Trial Outcomes & Findings for Clinical Trial of the Safety and Efficacy of the Addition of Ramucirumab to Nab-paclitaxel in Previously Treated Patients With Advanced Non-small Cell Lung Cancer (NSCLC) (NCT NCT02730247)

NCT ID: NCT02730247

Last Updated: 2020-11-19

Results Overview

The duration of time from start of treatment to time of progression or death. Progression as defined by RECIST v1.1 for target lesions: Progressive Disease (PD): At least a 20% increase in the sum of the diameters of target lesions, taking as reference the smallest sum on study (this includes the baseline sum if that is the smallest on study). In addition to the relative increase of 20%, the sum must also demonstrate an absolute increase of at least 5 mm. (Note: the appearance of one or more new lesions is also considered progressions). For non-target lesions: Progressive Disease (PD): Appearance of one or more new lesions and/or unequivocal progression of existing non-target lesions. Unequivocal progression should not normally trump target lesion status. It must be representative of overall disease status change, not a single lesion increase.

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

7 participants

Primary outcome timeframe

Up to 26 months

Results posted on

2020-11-19

Participant Flow

Participant milestones

Participant milestones
Measure
Ramucirumab + Nab-paclitaxel
8 mg/kg IV ramucirumab on days 1 and 15 of a 28-day treatment cycle 100 mg/m\^2 IV nab-paclitaxel on days 1, 8 and 15 of a 28 day cycle
Overall Study
STARTED
7
Overall Study
COMPLETED
7
Overall Study
NOT COMPLETED
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Clinical Trial of the Safety and Efficacy of the Addition of Ramucirumab to Nab-paclitaxel in Previously Treated Patients With Advanced Non-small Cell Lung Cancer (NSCLC)

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Ramucirumab + Nab-paclitaxel
n=7 Participants
8 mg/kg IV ramucirumab on days 1 and 15 of a 28-day treatment cycle 100 mg/m\^2 IV nab-paclitaxel on days 1, 8 and 15 of a 28 day cycle
Race (NIH/OMB)
Black or African American
0 Participants
n=93 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=93 Participants
Race (NIH/OMB)
White
7 Participants
n=93 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=93 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=93 Participants
Stage of Disease
Stage IV
5 Participants
n=93 Participants
Stage of Disease
Stage IV B
2 Participants
n=93 Participants
ECOG Performance Status
Grade 1
6 Participants
n=93 Participants
ECOG Performance Status
Grade 2
1 Participants
n=93 Participants
Age, Continuous
63 years
n=93 Participants
Sex: Female, Male
Female
4 Participants
n=93 Participants
Sex: Female, Male
Male
3 Participants
n=93 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=93 Participants
Race (NIH/OMB)
Asian
0 Participants
n=93 Participants

PRIMARY outcome

Timeframe: Up to 26 months

Population: Patients evaluable for clinical response who have received at least one cycle of therapy.

The duration of time from start of treatment to time of progression or death. Progression as defined by RECIST v1.1 for target lesions: Progressive Disease (PD): At least a 20% increase in the sum of the diameters of target lesions, taking as reference the smallest sum on study (this includes the baseline sum if that is the smallest on study). In addition to the relative increase of 20%, the sum must also demonstrate an absolute increase of at least 5 mm. (Note: the appearance of one or more new lesions is also considered progressions). For non-target lesions: Progressive Disease (PD): Appearance of one or more new lesions and/or unequivocal progression of existing non-target lesions. Unequivocal progression should not normally trump target lesion status. It must be representative of overall disease status change, not a single lesion increase.

Outcome measures

Outcome measures
Measure
Ramucirumab + Nab-paclitaxel
n=7 Participants
8 mg/kg IV ramucirumab on days 1 and 15 of a 28-day treatment cycle 100 mg/m\^2 IV nab-paclitaxel on days 1, 8 and 15 of a 28 day cycle
Progression-free Survival (PFS)
8.16 months
Interval 3.68 to
Upper bound not able to be reached due to low patient accrual.

PRIMARY outcome

Timeframe: Up to 26 months

Population: Patients that received at least one dose of study treatment.

Percentage of patients that experienced Grade 3-5 adverse events as their highest Grade event, irrespective of relatedness to treatment, per NCI CTCAE v2.0 (National Cancer Institute Common Terminology Criteria for Adverse Events).

Outcome measures

Outcome measures
Measure
Ramucirumab + Nab-paclitaxel
n=7 Participants
8 mg/kg IV ramucirumab on days 1 and 15 of a 28-day treatment cycle 100 mg/m\^2 IV nab-paclitaxel on days 1, 8 and 15 of a 28 day cycle
Worst Grade of Adverse Event Experienced
Grade 3 adverse event
57.1 percentage of participants
Interval 20.0 to 87.6
Worst Grade of Adverse Event Experienced
Grade 4 adverse event
28.6 percentage of participants
Interval 6.2 to 70.7
Worst Grade of Adverse Event Experienced
Grade 5 adverse event
14.3 percentage of participants
Interval 1.8 to 59.7

PRIMARY outcome

Timeframe: Up to 26 months

Population: Patients that received at least one dose of study treatment.

Percentage of patients who experienced Grade 2-5 adverse events as their highest Grade event, that were at least possibly related to treatment, per NCI CTCAE v2.0 (National Cancer Institute Common Terminology Criteria for Adverse Events).

Outcome measures

Outcome measures
Measure
Ramucirumab + Nab-paclitaxel
n=7 Participants
8 mg/kg IV ramucirumab on days 1 and 15 of a 28-day treatment cycle 100 mg/m\^2 IV nab-paclitaxel on days 1, 8 and 15 of a 28 day cycle
Worst Grade of Adverse Event Experienced, at Least Possibly Related to Treatment
Grade 2
14.3 percentage of participants
Interval 1.5 to 64.8
Worst Grade of Adverse Event Experienced, at Least Possibly Related to Treatment
Grade 3
42.9 percentage of participants
Interval 10.5 to 82.8
Worst Grade of Adverse Event Experienced, at Least Possibly Related to Treatment
Grade 4
28.6 percentage of participants
Interval 5.2 to 74.6
Worst Grade of Adverse Event Experienced, at Least Possibly Related to Treatment
Grade 5
14.3 percentage of participants
Interval 1.5 to 64.8

PRIMARY outcome

Timeframe: Up to 26 months

Population: Patients that received at least one dose of study treatment.

Percentage of patients who experienced Grade 0-4 adverse events as their highest Grade event, that were at least probably related to treatment, per NCI CTCAE v2.0 (National Cancer Institute Common Terminology Criteria for Adverse Events).

Outcome measures

Outcome measures
Measure
Ramucirumab + Nab-paclitaxel
n=7 Participants
8 mg/kg IV ramucirumab on days 1 and 15 of a 28-day treatment cycle 100 mg/m\^2 IV nab-paclitaxel on days 1, 8 and 15 of a 28 day cycle
Worst Grade of Adverse Event Experienced, at Least Probably Related to Treatment
Grade 0
14.3 percentage of participants
Interval 1.3 to 68.4
Worst Grade of Adverse Event Experienced, at Least Probably Related to Treatment
Grade 1
28.6 percentage of participants
Interval 4.5 to 77.3
Worst Grade of Adverse Event Experienced, at Least Probably Related to Treatment
Grade 2
28.6 percentage of participants
Interval 4.5 to 77.3
Worst Grade of Adverse Event Experienced, at Least Probably Related to Treatment
Grade 3
14.3 percentage of participants
Interval 1.3 to 68.4
Worst Grade of Adverse Event Experienced, at Least Probably Related to Treatment
Grade 4
14.3 percentage of participants
Interval 1.3 to 68.4

PRIMARY outcome

Timeframe: Up to 26 months

Population: Patients that received at least one dose of study treatment.

Percentage of patients that experienced Grade 0-2 adverse events as their highest Grade event, that were definitely related to treatment, per NCI CTCAE v2.0 (National Cancer Institute Common Terminology Criteria for Adverse Events.

Outcome measures

Outcome measures
Measure
Ramucirumab + Nab-paclitaxel
n=7 Participants
8 mg/kg IV ramucirumab on days 1 and 15 of a 28-day treatment cycle 100 mg/m\^2 IV nab-paclitaxel on days 1, 8 and 15 of a 28 day cycle
Worst Grade of Adverse Event Experienced, Definitely Related to Treatment
Grade 0
71.4 proportion of participants
Interval 29.3 to 93.8
Worst Grade of Adverse Event Experienced, Definitely Related to Treatment
Grade 1
14.3 proportion of participants
Interval 1.8 to 59.7
Worst Grade of Adverse Event Experienced, Definitely Related to Treatment
Grade 2
14.3 proportion of participants
Interval 1.8 to 59.7

SECONDARY outcome

Timeframe: Up to 26 months

Population: Patients evaluable for response who received at least one cycle of therapy.

Median percentage of patients who experienced a best response of partial or complete response (PR + CR) / total number of patients (PR + CR + Stable Disease (SD) + Progressive Disease (PD)), per RECIST v1.1. Complete Response (CR): Disappearance of all target lesions. Any pathological lymph nodes (whether target or non-target) must have reduction in short axis to \<10 mm. Partial Response (PR): At least a 30% decrease in the sum of the diameters of target lesions, taking as reference the baseline sum diameters. Stable Disease (SD): Neither sufficient shrinkage to qualify for PR nor sufficient increase to qualify for PD, taking as reference the smallest sum diameters while on study. Progressive Disease (PD): At least a 20% increase in the sum of diameters of target lesions, taking as reference the smallest sum on study (this includes the baseline sum if that is the smallest on study). The sum must also demonstrate an absolute increase of at least 5 mm; appearance new lesions.

Outcome measures

Outcome measures
Measure
Ramucirumab + Nab-paclitaxel
n=6 Participants
8 mg/kg IV ramucirumab on days 1 and 15 of a 28-day treatment cycle 100 mg/m\^2 IV nab-paclitaxel on days 1, 8 and 15 of a 28 day cycle
Best Overall Response
Best Response - Stable Disease
67.7 percentage of participants
Interval 22.3 to 95.7
Best Overall Response
Best Response - Partial Response
33.3 percentage of participants
Interval 4.3 to 77.8

SECONDARY outcome

Timeframe: Up to 26 months

Population: All enrolled participants.

The duration of time from the start of treatment to death.

Outcome measures

Outcome measures
Measure
Ramucirumab + Nab-paclitaxel
n=7 Participants
8 mg/kg IV ramucirumab on days 1 and 15 of a 28-day treatment cycle 100 mg/m\^2 IV nab-paclitaxel on days 1, 8 and 15 of a 28 day cycle
Overall Survival (OS)
7.42 months
Interval 3.48 to
Upper bound not able to be reached due to low patient accrual.

SECONDARY outcome

Timeframe: Baseline through up to 26 months

Population: Patients that received at least one dose of study treatment and who completed at least one questionnaire.

The EuroQol Five Dimension questionnaire (EQ-5D-5L) score is a descriptive system that comprises five dimensions: mobility, self-care, usual activities, pain/discomfort and anxiety/depression. Each dimension has 5 levels: level 0=no problems, level 1=slight problems, level 2=moderate problems, level 3=severe problems and level 4= extreme problems. The patient is asked to indicate his/her health state by ticking the box next to the most appropriate statement in each of the five dimensions. This decision results in a 1-digit number that expresses the level selected for that dimension. The digits for the five dimensions can be combined into a 5-digit number that describes the patient's health state. Data is presented as a health profile table reporting a proportion of reported problems for each level for each dimension and/or dichotomised levels - 'no problems' (i.e. level 1) and 'problems' (i.e. levels 2 to 5)

Outcome measures

Outcome measures
Measure
Ramucirumab + Nab-paclitaxel
n=7 Participants
8 mg/kg IV ramucirumab on days 1 and 15 of a 28-day treatment cycle 100 mg/m\^2 IV nab-paclitaxel on days 1, 8 and 15 of a 28 day cycle
Median EuroQol Five Dimension Questionnaire (EQ-5D-5L) Score
Walking
1 EQ-5D-5L score
Interval 0.0 to 2.0
Median EuroQol Five Dimension Questionnaire (EQ-5D-5L) Score
Dressing
1 EQ-5D-5L score
Interval 0.0 to 2.0
Median EuroQol Five Dimension Questionnaire (EQ-5D-5L) Score
Active
1 EQ-5D-5L score
Interval 0.0 to 4.0
Median EuroQol Five Dimension Questionnaire (EQ-5D-5L) Score
Pain
1 EQ-5D-5L score
Interval 0.0 to 4.0
Median EuroQol Five Dimension Questionnaire (EQ-5D-5L) Score
Anxious
1 EQ-5D-5L score
Interval 0.0 to 3.0

Adverse Events

Ramucirumab + Nab-paclitaxel

Serious events: 7 serious events
Other events: 7 other events
Deaths: 5 deaths

Serious adverse events

Serious adverse events
Measure
Ramucirumab + Nab-paclitaxel
n=7 participants at risk
8 mg/kg IV ramucirumab on days 1 and 15 of a 28-day treatment cycle 100 mg/m\^2 IV nab-paclitaxel on days 1, 8 and 15 of a 28 day cycle
Blood and lymphatic system disorders
Anemia
14.3%
1/7 • Number of events 4 • Up to 26 months
Cardiac disorders
Cardiac arrest
14.3%
1/7 • Number of events 2 • Up to 26 months
Respiratory, thoracic and mediastinal disorders
Dyspnea
14.3%
1/7 • Number of events 2 • Up to 26 months
Blood and lymphatic system disorders
Febrile neutropenia
14.3%
1/7 • Number of events 2 • Up to 26 months
Vascular disorders
Hypertension
14.3%
1/7 • Number of events 2 • Up to 26 months
Metabolism and nutrition disorders
Hypoalbuminemia
14.3%
1/7 • Number of events 2 • Up to 26 months
Metabolism and nutrition disorders
Hyponatremia
28.6%
2/7 • Number of events 8 • Up to 26 months
Investigations
Lymphocyte count decreased
42.9%
3/7 • Number of events 16 • Up to 26 months
Investigations
Neutrophil count decreased
42.9%
3/7 • Number of events 24 • Up to 26 months
Injury, poisoning and procedural complications
Spinal fracture
14.3%
1/7 • Number of events 2 • Up to 26 months
Nervous system disorders
Syncope
14.3%
1/7 • Number of events 2 • Up to 26 months
Vascular disorders
Thromboembolic event
14.3%
1/7 • Number of events 2 • Up to 26 months
Investigations
Weight loss
14.3%
1/7 • Number of events 2 • Up to 26 months
Investigations
White blood cell decreased
28.6%
2/7 • Number of events 16 • Up to 26 months

Other adverse events

Other adverse events
Measure
Ramucirumab + Nab-paclitaxel
n=7 participants at risk
8 mg/kg IV ramucirumab on days 1 and 15 of a 28-day treatment cycle 100 mg/m\^2 IV nab-paclitaxel on days 1, 8 and 15 of a 28 day cycle
Investigations
Alkaline phosphatase increased
42.9%
3/7 • Number of events 14 • Up to 26 months
Blood and lymphatic system disorders
Anemia
85.7%
6/7 • Number of events 56 • Up to 26 months
Metabolism and nutrition disorders
Anorexia
57.1%
4/7 • Number of events 8 • Up to 26 months
Psychiatric disorders
Anxiety
14.3%
1/7 • Number of events 2 • Up to 26 months
Injury, poisoning and procedural complications
Arterial injury
14.3%
1/7 • Number of events 2 • Up to 26 months
Investigations
Aspartate aminotransferase increased
42.9%
3/7 • Number of events 20 • Up to 26 months
Investigations
Blood bilirubin increased
28.6%
2/7 • Number of events 14 • Up to 26 months
Cardiac disorders
Cardiac arrest
14.3%
1/7 • Number of events 2 • Up to 26 months
Gastrointestinal disorders
Constipation
28.6%
2/7 • Number of events 4 • Up to 26 months
Respiratory, thoracic and mediastinal disorders
Cough
14.3%
1/7 • Number of events 2 • Up to 26 months
Investigations
Creatinine increased
14.3%
1/7 • Number of events 6 • Up to 26 months
Metabolism and nutrition disorders
Dehydration
14.3%
1/7 • Number of events 4 • Up to 26 months
Psychiatric disorders
Depression
14.3%
1/7 • Number of events 2 • Up to 26 months
Gastrointestinal disorders
Diarrhea
28.6%
2/7 • Number of events 8 • Up to 26 months
Nervous system disorders
Dysgeusia
14.3%
1/7 • Number of events 2 • Up to 26 months
Respiratory, thoracic and mediastinal disorders
Dyspnea
57.1%
4/7 • Number of events 12 • Up to 26 months
General disorders
Edema limbs
14.3%
1/7 • Number of events 2 • Up to 26 months
Eye disorders
Eye disorders - Other, specify
14.3%
1/7 • Number of events 2 • Up to 26 months
General disorders
Fatigue
71.4%
5/7 • Number of events 16 • Up to 26 months
Blood and lymphatic system disorders
Febrile neutropenia
14.3%
1/7 • Number of events 2 • Up to 26 months
General disorders
Gait disturbance
14.3%
1/7 • Number of events 2 • Up to 26 months
Gastrointestinal disorders
Gastrointestinal disorders - Other, specify
14.3%
1/7 • Number of events 2 • Up to 26 months
General disorders
General disorders and administration site conditions - Other, specify
14.3%
1/7 • Number of events 4 • Up to 26 months
Musculoskeletal and connective tissue disorders
Generalized muscle weakness
28.6%
2/7 • Number of events 4 • Up to 26 months
Nervous system disorders
Headache
14.3%
1/7 • Number of events 2 • Up to 26 months
Metabolism and nutrition disorders
Hypercalcemia
14.3%
1/7 • Number of events 4 • Up to 26 months
Metabolism and nutrition disorders
Hyperglycemia
42.9%
3/7 • Number of events 30 • Up to 26 months
Vascular disorders
Hypertension
28.6%
2/7 • Number of events 8 • Up to 26 months
Metabolism and nutrition disorders
Hypoalbuminemia
71.4%
5/7 • Number of events 48 • Up to 26 months
Metabolism and nutrition disorders
Hypocalcemia
28.6%
2/7 • Number of events 16 • Up to 26 months
Metabolism and nutrition disorders
Hypoglycemia
28.6%
2/7 • Number of events 4 • Up to 26 months
Metabolism and nutrition disorders
Hypokalemia
42.9%
3/7 • Number of events 10 • Up to 26 months
Metabolism and nutrition disorders
Hypomagnesemia
14.3%
1/7 • Number of events 2 • Up to 26 months
Metabolism and nutrition disorders
Hyponatremia
85.7%
6/7 • Number of events 36 • Up to 26 months
Metabolism and nutrition disorders
Hypophosphatemia
57.1%
4/7 • Number of events 14 • Up to 26 months
Vascular disorders
Hypotension
14.3%
1/7 • Number of events 4 • Up to 26 months
Respiratory, thoracic and mediastinal disorders
Hypoxia
14.3%
1/7 • Number of events 2 • Up to 26 months
Investigations
INR increased
14.3%
1/7 • Number of events 4 • Up to 26 months
Investigations
Investigations - Other, specify
42.9%
3/7 • Number of events 14 • Up to 26 months
Investigations
Lymphocyte count decreased
42.9%
3/7 • Number of events 30 • Up to 26 months
Metabolism and nutrition disorders
Metabolism and nutrition disorders - Other, specify
28.6%
2/7 • Number of events 10 • Up to 26 months
Infections and infestations
Mucosal infection
14.3%
1/7 • Number of events 2 • Up to 26 months
Musculoskeletal and connective tissue disorders
Myalgia
28.6%
2/7 • Number of events 4 • Up to 26 months
Gastrointestinal disorders
Nausea
14.3%
1/7 • Number of events 2 • Up to 26 months
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Neoplasms benign, malignant and unspecified (incl cysts and polyps) - Other, specify
14.3%
1/7 • Number of events 2 • Up to 26 months
Investigations
Neutrophil count decreased
71.4%
5/7 • Number of events 84 • Up to 26 months
General disorders
Non-cardiac chest pain
14.3%
1/7 • Number of events 2 • Up to 26 months
Musculoskeletal and connective tissue disorders
Pain in extremity
14.3%
1/7 • Number of events 4 • Up to 26 months
Nervous system disorders
Peripheral sensory neuropathy
28.6%
2/7 • Number of events 4 • Up to 26 months
Investigations
Platelet count decreased
42.9%
3/7 • Number of events 22 • Up to 26 months
Renal and urinary disorders
Proteinuria
57.1%
4/7 • Number of events 8 • Up to 26 months
Skin and subcutaneous tissue disorders
Rash maculo-papular
14.3%
1/7 • Number of events 2 • Up to 26 months
Cardiac disorders
Sinus tachycardia
28.6%
2/7 • Number of events 8 • Up to 26 months
Infections and infestations
Skin infection
28.6%
2/7 • Number of events 4 • Up to 26 months
Injury, poisoning and procedural complications
Spinal fracture
14.3%
1/7 • Number of events 2 • Up to 26 months
Nervous system disorders
Syncope
14.3%
1/7 • Number of events 2 • Up to 26 months
Vascular disorders
Thromboembolic event
14.3%
1/7 • Number of events 2 • Up to 26 months
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Tumor pain
14.3%
1/7 • Number of events 4 • Up to 26 months
Infections and infestations
Upper respiratory infection
14.3%
1/7 • Number of events 2 • Up to 26 months
Renal and urinary disorders
Urinary frequency
14.3%
1/7 • Number of events 2 • Up to 26 months
Infections and infestations
Urinary tract infection
14.3%
1/7 • Number of events 2 • Up to 26 months
Vascular disorders
Vascular disorders - Other, specify
14.3%
1/7 • Number of events 2 • Up to 26 months
Gastrointestinal disorders
Vomiting
14.3%
1/7 • Number of events 2 • Up to 26 months
Investigations
Weight loss
28.6%
2/7 • Number of events 6 • Up to 26 months
Investigations
White blood cell decreased
57.1%
4/7 • Number of events 68 • Up to 26 months

Additional Information

Barbara Stadterman, MPH, MCCR; CRS Regulatory Supervisor

UPMC Hillman Cancer Center

Phone: 412-647-5554

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place