Efficacy and Safety Study of Squalamine Ophthalmic Solution in Subjects With Neovascular AMD

NCT ID: NCT02727881

Last Updated: 2017-04-27

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

UNKNOWN

Clinical Phase

PHASE3

Total Enrollment

230 participants

Study Classification

INTERVENTIONAL

Study Start Date

2016-04-12

Study Completion Date

2017-12-31

Brief Summary

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A Phase 3 Study of the Efficacy and Safety of Squalamine Lactate Ophthalmic Solution 0.2% Twice Daily in Subjects with Neovascular Age-Related Macular Degeneration. Patients will receive injections of ranibizumab. In addition, patients will receive either Squalamine lactate 0.2% eye drops or Placebo eye drops. The study duration is approximately 9 months to primary endpoint

Detailed Description

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Phase 3 Study of the Efficacy and Safety of Squalamine Lactate Ophthalmic Solution 0.2% Twice Daily in Subjects with Neovascular Age-Related Macular Degeneration Methodology: Phase III, multicenter, randomized, double-masked, placebo-controlled study conducted over 9 months

(Screening/Baseline to Week 36): Patients will be randomly assigned to one of 2 treatment groups in a 1:1 ratio:

* Squalamine lactate ophthalmic solution, 0.2% BID + ranibizumab every 4 weeks
* Placebo ophthalmic solution BID + monthly ranibizumab every 4 weeks

Conditions

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Age-related Macular Degeneration

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Squalamine solution, 0.2% BID

Squalamine lactate ophthalmic solution, 0.2% bis in die (BID) + ranibizumab every 4 weeks

Group Type EXPERIMENTAL

Squalamine lactate ophthalmic solution, 0.2%

Intervention Type DRUG

Squalamine lactate ophthalmic solution, 0.2%

ranibizumab

Intervention Type DRUG

ranibizumab

Placebo solution BID

Placebo ophthalmic solution BID + ranibizumab every 4 weeks

Group Type PLACEBO_COMPARATOR

Placebo Ophthalmic solution

Intervention Type DRUG

Placebo Ophthalmic solution

ranibizumab

Intervention Type DRUG

ranibizumab

Interventions

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Squalamine lactate ophthalmic solution, 0.2%

Squalamine lactate ophthalmic solution, 0.2%

Intervention Type DRUG

Placebo Ophthalmic solution

Placebo Ophthalmic solution

Intervention Type DRUG

ranibizumab

ranibizumab

Intervention Type DRUG

Other Intervention Names

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active placebo Lucentis

Eligibility Criteria

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Inclusion Criteria

* Age ≥ 50 years
* A diagnosis of choroid neovascularization (CNV) secondary to AMD with CNV comprising at least 50% of the total lesion area on fluorescein angiography (FA)
* Central subfield thickness (spectral domain (SD)-OCT central 1 mm) of ≥ 300 μm
* Best-corrected visual acuity (BCVA) 20/40 to 20/320 (73- to 24-letter score on the Early Treatment of Diabetic Retinopathy Study \[ETDRS\] chart)

Exclusion Criteria

* Neovascularization secondary to any other condition than AMD in the study eye; Blood occupying greater than 50% of the AMD lesion, or blood \> 1.0 sq. mm underlying the fovea
* Pigment epithelial detachment (PED) without associated subretinal fluid and/or cystic retinal changes
* Clinical evidence of diabetic retinopathy or diabetic macular edema in the study eye
* Confounding ocular conditions in the study eye which will affect interpretation of OCT, VA or assessment of macular appearance (e.g., cataract, epiretinal membrane, retinal vascular occlusive disease)
* Fibrosis or atrophy, retinal epithelial tear in the center of the fovea in the study eye or any condition preventing VA improvement
* Uncontrolled glaucoma in the study eye, or currently receiving topical glaucoma medication in the study eye
Minimum Eligible Age

50 Years

Maximum Eligible Age

110 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Ohr Pharmaceutical Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Avner Ingerman, MD

Role: STUDY_DIRECTOR

Ohr Pharmaceutical

Locations

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Investigational Site

Mobile, Alabama, United States

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Phoenix, Arizona, United States

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Phoenix, Arizona, United States

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Phoenix, Arizona, United States

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Tucson, Arizona, United States

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Arcadia, California, United States

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Beverly Hills, California, United States

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Campbell, California, United States

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Fullerton, California, United States

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Glendale, California, United States

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Glendora, California, United States

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La Jolla, California, United States

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Laguna Hills, California, United States

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Loma Linda, California, United States

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Los Angeles, California, United States

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Oceanside, California, United States

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Orange, California, United States

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Palm Desert, California, United States

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Palo Alto, California, United States

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Pasadena, California, United States

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Poway, California, United States

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Redlands, California, United States

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Sacramento, California, United States

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Bridgeport, Connecticut, United States

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Hamden, Connecticut, United States

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New London, Connecticut, United States

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Altamonte Springs, Florida, United States

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Boynton Beach, Florida, United States

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Fort Myers, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Naples, Florida, United States

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Sarasota, Florida, United States

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Stuart, Florida, United States

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Augusta, Georgia, United States

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‘Aiea, Hawaii, United States

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Berwyn, Illinois, United States

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Bloomington, Illinois, United States

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Chicago, Illinois, United States

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Sycamore, Illinois, United States

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New Albany, Indiana, United States

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Leawood, Kansas, United States

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Louisville, Kentucky, United States

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Paducah, Kentucky, United States

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Portland, Maine, United States

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Baltimore, Maryland, United States

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Baltimore, Maryland, United States

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Glen Burnie, Maryland, United States

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Hagerstown, Maryland, United States

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Pikesville, Maryland, United States

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Rockville, Maryland, United States

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Detroit, Michigan, United States

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Grand Rapids, Michigan, United States

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Jackson, Michigan, United States

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Royal Oak, Michigan, United States

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Southfield, Michigan, United States

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Traverse City, Michigan, United States

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Biloxi, Mississippi, United States

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Chesterfield, Missouri, United States

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Florissant, Missouri, United States

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Henderson, Nevada, United States

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Las Vegas, Nevada, United States

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Portsmouth, New Hampshire, United States

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Bloomfield, New Jersey, United States

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Lawrenceville, New Jersey, United States

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New Brunswick, New Jersey, United States

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Northfield, New Jersey, United States

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Ramsey, New Jersey, United States

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Teaneck, New Jersey, United States

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Toms River, New Jersey, United States

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Brooklyn, New York, United States

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Great Neck, New York, United States

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Hauppauge, New York, United States

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Lynbrook, New York, United States

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New York, New York, United States

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New York, New York, United States

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Rochester, New York, United States

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Rockville Centre, New York, United States

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Syracuse, New York, United States

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Charlotte, North Carolina, United States

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Concord, North Carolina, United States

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Cleveland, Ohio, United States

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Cleveland, Ohio, United States

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Cleveland, Ohio, United States

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Toledo, Ohio, United States

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Youngstown, Ohio, United States

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Ashland, Oregon, United States

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Camp Hill, Pennsylvania, United States

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Kingston, Pennsylvania, United States

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Lancaster, Pennsylvania, United States

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Philadelphia, Pennsylvania, United States

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Philadelphia, Pennsylvania, United States

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Philadelphia, Pennsylvania, United States

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Pittsburgh, Pennsylvania, United States

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Columbia, South Carolina, United States

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Greenville, South Carolina, United States

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Mt. Pleasant, South Carolina, United States

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Rapid City, South Dakota, United States

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Kingsport, Tennessee, United States

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Nashville, Tennessee, United States

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Fort Worth, Texas, United States

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Grapevine, Texas, United States

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Harlingen, Texas, United States

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Houston, Texas, United States

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Katy, Texas, United States

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Kingwood, Texas, United States

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McAllen, Texas, United States

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Plano, Texas, United States

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San Antonio, Texas, United States

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The Woodlands, Texas, United States

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Salt Lake City, Utah, United States

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Burlington, Vermont, United States

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Fairfax, Virginia, United States

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Warrenton, Virginia, United States

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Bellevue, Washington, United States

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Spokane, Washington, United States

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Morgantown, West Virginia, United States

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Madison, Wisconsin, United States

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Countries

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United States

Other Identifiers

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OHR-1601

Identifier Type: -

Identifier Source: org_study_id

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