A Phase 2 Study of Ruxolitinib With Chemotherapy in Children With Acute Lymphoblastic Leukemia

NCT ID: NCT02723994

Last Updated: 2025-10-17

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE2

Total Enrollment

171 participants

Study Classification

INTERVENTIONAL

Study Start Date

2016-09-30

Study Completion Date

2026-02-01

Brief Summary

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This is a nonrandomized study of ruxolitinib in combination with a standard multi-agent chemotherapy regimen for the treatment of B-cell acute lymphoblastic leukemia. Part 1 of the study will optimize the dose of study drug (ruxolitinib) in combination with the chemotherapy regimen. Part 2 will evaluate the efficacy of combination chemotherapy and ruxolitinib at the recommended dose determined in Part 1.

Detailed Description

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Conditions

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Leukemia

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Ruxolitinib in combination with chemotherapy

Group Type EXPERIMENTAL

Ruxolitinib

Intervention Type DRUG

In Part 1, ruxolitinib will be administered at a protocol-defined starting dose in combination with chemotherapy, with dose escalation and de-escalation following the rolling 6 study design. The established recommended starting dose will be taken forward into Part 2.

Asparaginase Erwinia Chrysanthemi

Intervention Type DRUG

Cyclophosphamide

Intervention Type DRUG

Cytarabine

Intervention Type DRUG

Dexamethasone

Intervention Type DRUG

Doxorubicin

Intervention Type DRUG

Leucovorin Calcium

Intervention Type DRUG

Mercaptopurine

Intervention Type DRUG

Methotrexate

Intervention Type DRUG

Pegaspargase

Intervention Type DRUG

Prednisone

Intervention Type DRUG

Thioguanine

Intervention Type DRUG

Vincristine Sulfate

Intervention Type DRUG

Interventions

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Ruxolitinib

In Part 1, ruxolitinib will be administered at a protocol-defined starting dose in combination with chemotherapy, with dose escalation and de-escalation following the rolling 6 study design. The established recommended starting dose will be taken forward into Part 2.

Intervention Type DRUG

Asparaginase Erwinia Chrysanthemi

Intervention Type DRUG

Cyclophosphamide

Intervention Type DRUG

Cytarabine

Intervention Type DRUG

Dexamethasone

Intervention Type DRUG

Doxorubicin

Intervention Type DRUG

Leucovorin Calcium

Intervention Type DRUG

Mercaptopurine

Intervention Type DRUG

Methotrexate

Intervention Type DRUG

Pegaspargase

Intervention Type DRUG

Prednisone

Intervention Type DRUG

Thioguanine

Intervention Type DRUG

Vincristine Sulfate

Intervention Type DRUG

Other Intervention Names

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INCB018424

Eligibility Criteria

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Inclusion Criteria

* Eligible for study when participant is 1 year to 21 years at the time of diagnosis
* Eligible Ages in Canada; 2 years to 21 years
* De novo high-risk (HR) Ph-like B-ALL for which any of following criteria are present at diagnosis:

* Age ≥ 10 years
* White blood cell (WBC) ≥ 50 × 10\^3/μL
* CNS3 leukemia at diagnosis
* Systemic steroid pretreatment without presteroid WBC documentation
* Diagnostic bone marrow or peripheral blood sample must have gene expression profiling and downstream genetic testing performed by submitting diagnostic specimens under the COG AALL08B1 or APEC14B1 biology studies, or AALL1131 or its successor study. Specimens must demonstrate a Ph-like expression profile (ie, LDA-positive) as tested by low density microarray testing at the COG ALL reference laboratory or TriCore laboratory at the University of New Mexico AND must contain 1 of the following genetic lesions: (determined at COG ALL reference laboratories, or equivalent CAP/CLIA-certified laboratories approved by the medical monitor:

1. CRLF2 rearrangement with confirmed JAK1 or JAK2 mutation (JAK+)
2. CRLF2 rearrangement without JAK mutation
3. Other JAK pathway alterations (eg, JAK2 fusions, EPOR fusions, SH2B3 deletions, IL7RA mutations) with or without CRLF2-R, or CRLF2-R with unknown JAK status as determined by a COG ALL Reference Laboratory
* Completed a 4-drug Induction therapy regimen (modified aBFM regimen or equivalent) in Study AALL1131 or its successor study, or as per the institutional standard of care for HR B-ALL and have had end-Induction minimal residual disease (MRD) assessed
* Male and female subjects of reproductive non childbearing potential or willing to take appropriate precautions to avoid pregnancy or fathering a child for the duration of study participation

Exclusion Criteria

* Receipt of any other cytotoxic chemotherapy before Induction therapy, with exception of hydroxyurea or steroid pretreatment
* Trisomy 21 (Down syndrome)
* BCR-ABL1-rearranged (Ph+) ALL
* Calculated creatinine clearance or radioisotope glomerular filtration rate \< 70 mL/min/1.73 m\^2
* Alanine aminotransferase ≥ 5 × upper limit of normal (ULN) for age
* Direct bilirubin ≥ 1.5 × ULN (may be assumed if total bilirubin is below ULN)
* History or evidence of cirrhosis
* Platelet count \< 75 × 10\^3/μL
* Absolute neutrophil count (ANC) \< 750/μL
* Positive screen for hepatitis B or C
* Known human immunodeficiency virus infection
Minimum Eligible Age

1 Year

Maximum Eligible Age

21 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Incyte Corporation

INDUSTRY

Sponsor Role lead

Children's Oncology Group

NETWORK

Sponsor Role collaborator

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Albert Assad, MD

Role: STUDY_DIRECTOR

Incyte Corporation

Sarah Tasian, MD

Role: STUDY_CHAIR

Children's Hospital of Philadelphia, Philadelphia, PA

Locations

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The Childrens Hospital of Alabama

Birmingham, Alabama, United States

Site Status

Phoenix Children'S Hospital

Phoenix, Arizona, United States

Site Status

Arkansas Childrens Hospital

Little Rock, Arkansas, United States

Site Status

Kaiser Permanente

Fontana, California, United States

Site Status

Loma Linda University Cancer Center

Loma Linda, California, United States

Site Status

Miller Childrens Hospital Pharmacy

Long Beach, California, United States

Site Status

Children'S Hospital Los Angeles

Los Angeles, California, United States

Site Status

Kaiser Foundation Health Plan

Los Angeles, California, United States

Site Status

Southern California Permanente Medical Group

Los Angeles, California, United States

Site Status

Valley Childrens Hospital

Madera, California, United States

Site Status

Choc Children Hospital

Orange, California, United States

Site Status

Lucille Packard Childrens Hospital

Palo Alto, California, United States

Site Status

Kaiser Permanente

San Diego, California, United States

Site Status

Rady Children'S Hospital - San Diego

San Diego, California, United States

Site Status

Ucsf Pediatric Oncology

San Francisco, California, United States

Site Status

Kaiser Permanente Downey

Santa Fe Springs, California, United States

Site Status

Children'S Hospital Colorado

Aurora, Colorado, United States

Site Status

Connecticut Children'S Medical Ctr

Hartford, Connecticut, United States

Site Status

Smilow Cancer Center - Yale

New Haven, Connecticut, United States

Site Status

Alfred I. Dupont Hospital For Children

Wilmington, Delaware, United States

Site Status

Childrens Hospital of Southwest Florida

Fort Myers, Florida, United States

Site Status

Joe Dimaggio Children Hospital

Hollywood, Florida, United States

Site Status

Nemours Childrens Clinic

Jacksonville, Florida, United States

Site Status

University of Florida Health Shands Hospital

Jacksonville, Florida, United States

Site Status

Florida Hospital Orlando

Orlando, Florida, United States

Site Status

Arnold Palmer Hospital For Children

Orlando, Florida, United States

Site Status

Nemours Childrens Clinic

Pensacola, Florida, United States

Site Status

All Childrens Hospital

St. Petersburg, Florida, United States

Site Status

St Josephs Childrens Hospital Tampa

Tampa, Florida, United States

Site Status

Saint Marys Medical Center

West Palm Beach, Florida, United States

Site Status

Egleston Children'S Health

Atlanta, Georgia, United States

Site Status

Kapiolani Medical Center For Women and Children

Honolulu, Hawaii, United States

Site Status

Ann & Robert H. Lurie Children'S Hospital

Chicago, Illinois, United States

Site Status

Loyola University Medical Center

Maywood, Illinois, United States

Site Status

Southern Illinois University School of Medicine

Springfield, Illinois, United States

Site Status

Riley Hospital For Children

Indianapolis, Indiana, United States

Site Status

St Vincent Hospital

Indianapolis, Indiana, United States

Site Status

Blank Childrens Hospital

Des Moines, Iowa, United States

Site Status

University of Iowa Hospital and Clinics

Iowa City, Iowa, United States

Site Status

University of Kentucky

Lexington, Kentucky, United States

Site Status

Kosair Childrens Hospital

Louisville, Kentucky, United States

Site Status

Ochsner Clinic

New Orleans, Louisiana, United States

Site Status

Maine Center For Cancer Medicine

Scarborough, Maine, United States

Site Status

Sinai Hospital of Baltimore

Baltimore, Maryland, United States

Site Status

Johns Hopkins University

Baltimore, Maryland, United States

Site Status

Dana Farber Boston Children'S

Boston, Massachusetts, United States

Site Status

Cs Mott Childrens Hospital

Ann Arbor, Michigan, United States

Site Status

Helen Devos Childrens Hosp

Grand Rapids, Michigan, United States

Site Status

Michigan State University

Lansing, Michigan, United States

Site Status

Children'S Hospitals and Clinics of Minnesota

Minneapolis, Minnesota, United States

Site Status

University of Minnesota

Minneapolis, Minnesota, United States

Site Status

University of Mississippi Medical Center

Jackson, Mississippi, United States

Site Status

The Children'S Mercy Hospital Outpatient

Kansas City, Missouri, United States

Site Status

Washington University

St Louis, Missouri, United States

Site Status

Children'S Hospital & Medical Center

Omaha, Nebraska, United States

Site Status

Alliance For Childhood Diseases

Las Vegas, Nevada, United States

Site Status

Children'S Center For Cancer & Blood Dis

Las Vegas, Nevada, United States

Site Status

Hackensack University Medical Center

Hackensack, New Jersey, United States

Site Status

Morristown Medical Center

Morristown, New Jersey, United States

Site Status

Rutgers Cancer Institute of Nj

New Brunswick, New Jersey, United States

Site Status

Newark Beth Israel Medical Center

Newark, New Jersey, United States

Site Status

St Josephs Regional Medical Center

Paterson, New Jersey, United States

Site Status

University of New Mexico Hospital

Albuquerque, New Mexico, United States

Site Status

Albany Medical College

Albany, New York, United States

Site Status

Roswell Park Comprehensive Cancer Center

Buffalo, New York, United States

Site Status

Cohen Children'S Medical Center

New Hyde Park, New York, United States

Site Status

Weill Cornell Medical College

New York, New York, United States

Site Status

Nyu Clinical Cancer Center

New York, New York, United States

Site Status

University of Rochester Medical Center

Rochester, New York, United States

Site Status

Suny Upstate Medical University

Syracuse, New York, United States

Site Status

New York Medical College

Valhalla, New York, United States

Site Status

University of North Carolina At Chapel Hill

Chapel Hill, North Carolina, United States

Site Status

Carolinas Medical Center

Charlotte, North Carolina, United States

Site Status

Wake Forest University

Winston-Salem, North Carolina, United States

Site Status

Akron Children'S Hospital

Akron, Ohio, United States

Site Status

Cincinnati Childrens Hospital Medical Center

Cincinnati, Ohio, United States

Site Status

Rainbow Babies & Children Hosp

Cleveland, Ohio, United States

Site Status

Cleveland Clinic Foundation

Cleveland, Ohio, United States

Site Status

Nationwide Children'S Hospital

Columbus, Ohio, United States

Site Status

Dayton Children'S Hospital

Dayton, Ohio, United States

Site Status

Toledo Hospital

Toledo, Ohio, United States

Site Status

University of Oklahoma Health Sciences Center

Oklahoma City, Oklahoma, United States

Site Status

Legacy Emanuel Hospital and Health Center

Portland, Oregon, United States

Site Status

Doernbecher Childrens Hospital

Portland, Oregon, United States

Site Status

Penn State Hershey Medical Center

Hershey, Pennsylvania, United States

Site Status

Children'S Hospital of Philadelphia

Philadelphia, Pennsylvania, United States

Site Status

Childrens Hospital of Pittsburgh

Pittsburgh, Pennsylvania, United States

Site Status

Hasbro Childrens Hospital

Providence, Rhode Island, United States

Site Status

Medical University of South Carolina

Charleston, South Carolina, United States

Site Status

Vanderbilt University Medical Center

Nashville, Tennessee, United States

Site Status

Dell Childrens Medical Center of Central Texas

Austin, Texas, United States

Site Status

Driscoll Children'S Hospital

Corpus Christi, Texas, United States

Site Status

Medical City Dallas Hospital

Dallas, Texas, United States

Site Status

University of Texas Southwestern Medical Center

Dallas, Texas, United States

Site Status

El Paso Children'S Hospital Corporation

El Paso, Texas, United States

Site Status

Texas Childrens Hospital

Houston, Texas, United States

Site Status

University of Texas Health Science Cente

San Antonio, Texas, United States

Site Status

Primary Children'S Hospital

Salt Lake City, Utah, United States

Site Status

Children'S Hospital of the

Norfolk, Virginia, United States

Site Status

Seattle Children'S Hospital

Seattle, Washington, United States

Site Status

Providence Sacred Heart Medical Center & Children'S Hospital

Spokane, Washington, United States

Site Status

St Vincent Hospital

Green Bay, Wisconsin, United States

Site Status

Medical College of Wisconsin

Milwaukee, Wisconsin, United States

Site Status

Alberta'S Children Hospital

Calgary, Alberta, Canada

Site Status

Bc Children'S Hospital

Vancouver, British Columbia, Canada

Site Status

The Hospital For Sick Children

Toronto, Ontario, Canada

Site Status

Chu Sainte-Justine

Montreal, Quebec, Canada

Site Status

McGill University Health Centre/Glen Site/Cedars Cancer Centre

Montreal, Quebec, Canada

Site Status

McMaster University Medical Centre

Hamilton, , Canada

Site Status

University Pediatric Hospital

San Juan, PR, Puerto Rico

Site Status

San Jorge Childrens Hospital

San Juan, , Puerto Rico

Site Status

Countries

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United States Canada Puerto Rico

Other Identifiers

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AALL1521

Identifier Type: OTHER

Identifier Source: secondary_id

INCB 18424-269

Identifier Type: -

Identifier Source: org_study_id

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