Trial Outcomes & Findings for A Study of Oral Testosterone Undecanoate (TU) in Hypogonadal Men (NCT NCT02722278)

NCT ID: NCT02722278

Last Updated: 2018-02-23

Results Overview

Recruitment status

COMPLETED

Study phase

PHASE3

Target enrollment

222 participants

Primary outcome timeframe

Day 105

Results posted on

2018-02-23

Participant Flow

Participant milestones

Participant milestones
Measure
Oral Testosterone Undecanoate
166 subjects received oral TU treatment during the study for approximately 3.5 months. Subjects randomly assigned to the oral TU treatment group will begin treatment at a dose of 237 mg TU twice daily (BID). Oral Testosterone Undecanoate: Subjects assigned to oral TU treatment will begin at 237 mg TU twice daily. Serial PK samples over 24 hours will be obtained after 21 days and 56 days of treatment. Dose adjustments may be made on Day 35 and Day 70, based on the T Cavg results obtained at Day 21 and Day 56, respectively. Dose will be increased if Cavg \< 350 ng/dL, decreased if \> 800 ng/dL and maintained if Cavg = 350 ng/dL to 800 ng/dL.
Axiron Testosterone Topical Solution
56 subjects were randomly assigned to the Axiron treatment group and began treatment at a dose of 60 mg every morning. Axiron Testosterone Topical Solution: Subjects assigned to Axiron treatment will begin at 60 mg Axiron every morning. Axiron is applied to the axilla only. Serial PK samples over 24 hours will be obtained after 21 days and 56 days of treatment. Dose adjustments may be made on Day 35 and Day 70, based on the T Cavg results obtained at Day 21 and Day 56, respectively. Dose will be increased if Cavg \< 350 ng/dL, decreased if \> 800 ng/dL and maintained if Cavg = 350 ng/dL to 800 ng/dL.
Overall Study
STARTED
166
56
Overall Study
COMPLETED
154
49
Overall Study
NOT COMPLETED
12
7

Reasons for withdrawal

Reasons for withdrawal
Measure
Oral Testosterone Undecanoate
166 subjects received oral TU treatment during the study for approximately 3.5 months. Subjects randomly assigned to the oral TU treatment group will begin treatment at a dose of 237 mg TU twice daily (BID). Oral Testosterone Undecanoate: Subjects assigned to oral TU treatment will begin at 237 mg TU twice daily. Serial PK samples over 24 hours will be obtained after 21 days and 56 days of treatment. Dose adjustments may be made on Day 35 and Day 70, based on the T Cavg results obtained at Day 21 and Day 56, respectively. Dose will be increased if Cavg \< 350 ng/dL, decreased if \> 800 ng/dL and maintained if Cavg = 350 ng/dL to 800 ng/dL.
Axiron Testosterone Topical Solution
56 subjects were randomly assigned to the Axiron treatment group and began treatment at a dose of 60 mg every morning. Axiron Testosterone Topical Solution: Subjects assigned to Axiron treatment will begin at 60 mg Axiron every morning. Axiron is applied to the axilla only. Serial PK samples over 24 hours will be obtained after 21 days and 56 days of treatment. Dose adjustments may be made on Day 35 and Day 70, based on the T Cavg results obtained at Day 21 and Day 56, respectively. Dose will be increased if Cavg \< 350 ng/dL, decreased if \> 800 ng/dL and maintained if Cavg = 350 ng/dL to 800 ng/dL.
Overall Study
Withdrawal by Subject
5
3
Overall Study
Adverse Event
4
1
Overall Study
Lost to Follow-up
2
0
Overall Study
Protocol Violation
1
0
Overall Study
High PSA pre-study/ not eligible
0
1
Overall Study
Subject declined after tx assignment
0
1
Overall Study
Site closure not study related
0
1

Baseline Characteristics

A Study of Oral Testosterone Undecanoate (TU) in Hypogonadal Men

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Oral Testosterone Undecanoate
n=166 Participants
Approximately 135 subjects will receive oral TU treatment during the study for approximately 3.5 months. Subjects randomly assigned to the oral TU treatment group will begin treatment at a dose of 237 mg TU twice daily (BID). Oral Testosterone Undecanoate: Subjects assigned to oral TU treatment will begin at 237 mg TU twice daily. Serial PK samples over 24 hours will be obtained after 21 days and 56 days of treatment. Dose adjustments may be made on Day 35 and Day 70, based on the T Cavg results obtained at Day 21 and Day 56, respectively. Dose will be increased if Cavg \< 350 ng/dL, decreased if \> 800 ng/dL and maintained if Cavg = 350 ng/dL to 800 ng/dL.
Axiron Testosterone Topical Solution
n=56 Participants
Subjects randomly assigned to the Axiron treatment group will begin treatment at a dose of 60 mg every morning. Axiron Testosterone Topical Solution: Subjects assigned to Axiron treatment will begin at 60 mg Axiron every morning. Axiron is applied to the axilla only. Serial PK samples over 24 hours will be obtained after 21 days and 56 days of treatment. Dose adjustments may be made on Day 35 and Day 70, based on the T Cavg results obtained at Day 21 and Day 56, respectively. Dose will be increased if Cavg \< 350 ng/dL, decreased if \> 800 ng/dL and maintained if Cavg = 350 ng/dL to 800 ng/dL.
Total
n=222 Participants
Total of all reporting groups
Age, Categorical
<=18 years
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
160 Participants
n=5 Participants
54 Participants
n=7 Participants
214 Participants
n=5 Participants
Age, Categorical
>=65 years
6 Participants
n=5 Participants
2 Participants
n=7 Participants
8 Participants
n=5 Participants
Age, Continuous
51.6 years
STANDARD_DEVIATION 9.08 • n=5 Participants
53.4 years
STANDARD_DEVIATION 7.86 • n=7 Participants
52 years
STANDARD_DEVIATION 8.81 • n=5 Participants
Sex: Female, Male
Female
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Sex: Female, Male
Male
166 Participants
n=5 Participants
56 Participants
n=7 Participants
222 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
25 Participants
n=5 Participants
15 Participants
n=7 Participants
40 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
141 Participants
n=5 Participants
41 Participants
n=7 Participants
182 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
1 Participants
n=7 Participants
1 Participants
n=5 Participants
Race (NIH/OMB)
Asian
3 Participants
n=5 Participants
2 Participants
n=7 Participants
5 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
29 Participants
n=5 Participants
11 Participants
n=7 Participants
40 Participants
n=5 Participants
Race (NIH/OMB)
White
133 Participants
n=5 Participants
42 Participants
n=7 Participants
175 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
1 Participants
n=5 Participants
0 Participants
n=7 Participants
1 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Region of Enrollment
United States
166 Participants
n=5 Participants
56 Participants
n=7 Participants
222 Participants
n=5 Participants

PRIMARY outcome

Timeframe: Day 105

Population: Intent-to-treat study population All subjects randomized to either Oral TU or Axiron

Outcome measures

Outcome measures
Measure
Oral Testosterone Undecanoate
n=166 Participants
166 subjects received oral TU treatment during the study for approximately 3.5 months. Subjects randomly assigned to the oral TU treatment group will begin treatment at a dose of 237 mg TU twice daily (BID). Oral Testosterone Undecanoate: Subjects assigned to oral TU treatment will begin at 237 mg TU twice daily. Serial PK samples over 24 hours will be obtained after 21 days and 56 days of treatment. Dose adjustments may be made on Day 35 and Day 70, based on the T Cavg results obtained at Day 21 and Day 56, respectively. Dose will be increased if Cavg \< 350 ng/dL, decreased if \> 800 ng/dL and maintained if Cavg = 350 ng/dL to 800 ng/dL.
Axiron Testosterone Topical Solution
n=56 Participants
56 subjects were randomly assigned to the Axiron treatment group and began treatment at a dose of 60 mg every morning. Axiron Testosterone Topical Solution: Subjects assigned to Axiron treatment will begin at 60 mg Axiron every morning. Axiron is applied to the axilla only. Serial PK samples over 24 hours will be obtained after 21 days and 56 days of treatment. Dose adjustments may be made on Day 35 and Day 70, based on the T Cavg results obtained at Day 21 and Day 56, respectively. Dose will be increased if Cavg \< 350 ng/dL, decreased if \> 800 ng/dL and maintained if Cavg = 350 ng/dL to 800 ng/dL.
Number of Oral TU Treated Subjects Who Have a Total T Cavg in the Eugonadal Range of 252 to 907 ng/dL at Visit 7
145 Participants
48 Participants

OTHER_PRE_SPECIFIED outcome

Timeframe: Approximately 4.5 months

Compare the Oral TU-treated subjects and the Topical Axiron®-treated subjects with respect to number of subjects in the cosyntropin stimulation test substudy with a normal maximum post-stimulation (cosyntropin stimulation) cortisol level at Visit 8.

Outcome measures

Outcome measures
Measure
Oral Testosterone Undecanoate
n=24 Participants
166 subjects received oral TU treatment during the study for approximately 3.5 months. Subjects randomly assigned to the oral TU treatment group will begin treatment at a dose of 237 mg TU twice daily (BID). Oral Testosterone Undecanoate: Subjects assigned to oral TU treatment will begin at 237 mg TU twice daily. Serial PK samples over 24 hours will be obtained after 21 days and 56 days of treatment. Dose adjustments may be made on Day 35 and Day 70, based on the T Cavg results obtained at Day 21 and Day 56, respectively. Dose will be increased if Cavg \< 350 ng/dL, decreased if \> 800 ng/dL and maintained if Cavg = 350 ng/dL to 800 ng/dL.
Axiron Testosterone Topical Solution
n=8 Participants
56 subjects were randomly assigned to the Axiron treatment group and began treatment at a dose of 60 mg every morning. Axiron Testosterone Topical Solution: Subjects assigned to Axiron treatment will begin at 60 mg Axiron every morning. Axiron is applied to the axilla only. Serial PK samples over 24 hours will be obtained after 21 days and 56 days of treatment. Dose adjustments may be made on Day 35 and Day 70, based on the T Cavg results obtained at Day 21 and Day 56, respectively. Dose will be increased if Cavg \< 350 ng/dL, decreased if \> 800 ng/dL and maintained if Cavg = 350 ng/dL to 800 ng/dL.
Number of Participants With Post-stimulation Cortisol Level of >18 ug/dL at Visit 8
19 Participants
8 Participants

Adverse Events

Oral Testosterone Undecanoate

Serious events: 2 serious events
Other events: 31 other events
Deaths: 0 deaths

Axiron Testosterone Topical Solution

Serious events: 0 serious events
Other events: 8 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Oral Testosterone Undecanoate
n=166 participants at risk
166 subjects received oral TU treatment during the study for approximately 3.5 months. Subjects randomly assigned to the oral TU treatment group will begin treatment at a dose of 237 mg TU twice daily (BID). Oral Testosterone Undecanoate: Subjects assigned to oral TU treatment will begin at 237 mg TU twice daily. Serial PK samples over 24 hours will be obtained after 21 days and 56 days of treatment. Dose adjustments may be made on Day 35 and Day 70, based on the T Cavg results obtained at Day 21 and Day 56, respectively. Dose will be increased if Cavg \< 350 ng/dL, decreased if \> 800 ng/dL and maintained if Cavg = 350 ng/dL to 800 ng/dL.
Axiron Testosterone Topical Solution
n=55 participants at risk
56 subjects were randomly assigned to the Axiron treatment group and began treatment at a dose of 60 mg every morning. Axiron Testosterone Topical Solution: Subjects assigned to Axiron treatment will begin at 60 mg Axiron every morning. Axiron is applied to the axilla only. Serial PK samples over 24 hours will be obtained after 21 days and 56 days of treatment. Dose adjustments may be made on Day 35 and Day 70, based on the T Cavg results obtained at Day 21 and Day 56, respectively. Dose will be increased if Cavg \< 350 ng/dL, decreased if \> 800 ng/dL and maintained if Cavg = 350 ng/dL to 800 ng/dL.
Gastrointestinal disorders
Small intestinal obstruction
0.60%
1/166 • Number of events 1 • 9 months
0.00%
0/55 • 9 months
Infections and infestations
Periumbilical abscess
0.60%
1/166 • Number of events 1 • 9 months
0.00%
0/55 • 9 months

Other adverse events

Other adverse events
Measure
Oral Testosterone Undecanoate
n=166 participants at risk
166 subjects received oral TU treatment during the study for approximately 3.5 months. Subjects randomly assigned to the oral TU treatment group will begin treatment at a dose of 237 mg TU twice daily (BID). Oral Testosterone Undecanoate: Subjects assigned to oral TU treatment will begin at 237 mg TU twice daily. Serial PK samples over 24 hours will be obtained after 21 days and 56 days of treatment. Dose adjustments may be made on Day 35 and Day 70, based on the T Cavg results obtained at Day 21 and Day 56, respectively. Dose will be increased if Cavg \< 350 ng/dL, decreased if \> 800 ng/dL and maintained if Cavg = 350 ng/dL to 800 ng/dL.
Axiron Testosterone Topical Solution
n=55 participants at risk
56 subjects were randomly assigned to the Axiron treatment group and began treatment at a dose of 60 mg every morning. Axiron Testosterone Topical Solution: Subjects assigned to Axiron treatment will begin at 60 mg Axiron every morning. Axiron is applied to the axilla only. Serial PK samples over 24 hours will be obtained after 21 days and 56 days of treatment. Dose adjustments may be made on Day 35 and Day 70, based on the T Cavg results obtained at Day 21 and Day 56, respectively. Dose will be increased if Cavg \< 350 ng/dL, decreased if \> 800 ng/dL and maintained if Cavg = 350 ng/dL to 800 ng/dL.
Investigations
High Density Lipoprotein Decreased
3.0%
5/166 • Number of events 5 • 9 months
0.00%
0/55 • 9 months
Investigations
Blood triglycerides increased
0.60%
1/166 • Number of events 1 • 9 months
0.00%
0/55 • 9 months
Investigations
Blood pressure increased
1.2%
2/166 • Number of events 2 • 9 months
1.8%
1/55 • Number of events 1 • 9 months
Investigations
Prostatic specific antigen increased
1.2%
2/166 • Number of events 2 • 9 months
0.00%
0/55 • 9 months
Gastrointestinal disorders
Nausea
2.4%
4/166 • Number of events 4 • 9 months
0.00%
0/55 • 9 months
Gastrointestinal disorders
Dyspepsia
1.8%
3/166 • Number of events 3 • 9 months
0.00%
0/55 • 9 months
Gastrointestinal disorders
Gastrooesophageal reflux disease
1.8%
3/166 • Number of events 3 • 9 months
0.00%
0/55 • 9 months
Gastrointestinal disorders
Abdominal distension
1.2%
2/166 • Number of events 2 • 9 months
0.00%
0/55 • 9 months
Gastrointestinal disorders
Diarrhoea
1.2%
2/166 • Number of events 2 • 9 months
0.00%
0/55 • 9 months
Gastrointestinal disorders
Dry mouth
1.2%
2/166 • Number of events 2 • 9 months
0.00%
0/55 • 9 months
Gastrointestinal disorders
Eructation
1.2%
2/166 • Number of events 2 • 9 months
0.00%
0/55 • 9 months
Infections and infestations
Upper respiratory tract infection
3.6%
6/166 • Number of events 6 • 9 months
0.00%
0/55 • 9 months
Infections and infestations
Atypical pneumonia
1.2%
2/166 • Number of events 2 • 9 months
0.00%
0/55 • 9 months
Investigations
Haematocrit Increased
4.8%
8/166 • Number of events 8 • 9 months
0.00%
0/55 • 9 months
Nervous system disorders
Headache
4.8%
8/166 • Number of events 8 • 9 months
1.8%
1/55 • Number of events 1 • 9 months
Nervous system disorders
Hypoaesthesia
1.2%
2/166 • Number of events 2 • 9 months
0.00%
0/55 • 9 months
Musculoskeletal and connective tissue disorders
Musculoskeletal Pain
1.2%
2/166 • Number of events 2 • 9 months
0.00%
0/55 • 9 months
Musculoskeletal and connective tissue disorders
Myalgia
1.2%
2/166 • Number of events 2 • 9 months
0.00%
0/55 • 9 months
Musculoskeletal and connective tissue disorders
Osteoarthritis
1.2%
2/166 • Number of events 2 • 9 months
0.00%
0/55 • 9 months
Injury, poisoning and procedural complications
Contusion
1.2%
2/166 • Number of events 2 • 9 months
0.00%
0/55 • 9 months
Psychiatric disorders
Insomnia
1.8%
3/166 • Number of events 3 • 9 months
0.00%
0/55 • 9 months
Psychiatric disorders
Anxiety
1.2%
2/166 • Number of events 2 • 9 months
1.8%
1/55 • Number of events 1 • 9 months
Psychiatric disorders
Depression
1.2%
2/166 • Number of events 2 • 9 months
0.00%
0/55 • 9 months
Skin and subcutaneous tissue disorders
Rash
1.2%
2/166 • Number of events 3 • 9 months
3.6%
2/55 • Number of events 2 • 9 months
Vascular disorders
Hypertension
3.0%
5/166 • Number of events 5 • 9 months
0.00%
0/55 • 9 months
Vascular disorders
Flushing
1.2%
2/166 • Number of events 2 • 9 months
0.00%
0/55 • 9 months
General disorders
Oedema Peripheral
1.8%
3/166 • Number of events 3 • 9 months
1.8%
1/55 • Number of events 1 • 9 months
Investigations
Weight Increased
0.60%
1/166 • Number of events 1 • 9 months
1.8%
1/55 • Number of events 1 • 9 months
Infections and infestations
Cellulitis
0.60%
1/166 • Number of events 1 • 9 months
1.8%
1/55 • Number of events 1 • 9 months
Infections and infestations
Sinusitis
0.60%
1/166 • Number of events 1 • 9 months
1.8%
1/55 • Number of events 1 • 9 months
Infections and infestations
Acute Sinusitis
0.00%
0/166 • 9 months
1.8%
1/55 • Number of events 1 • 9 months
Infections and infestations
Otitis Externa
0.00%
0/166 • 9 months
1.8%
1/55 • Number of events 1 • 9 months
Nervous system disorders
Dizziness
0.60%
1/166 • Number of events 1 • 9 months
1.8%
1/55 • Number of events 1 • 9 months
Nervous system disorders
Presyncope
0.60%
1/166 • Number of events 1 • 9 months
1.8%
1/55 • Number of events 1 • 9 months
Nervous system disorders
Disturbance in attention
0.00%
0/166 • 9 months
1.8%
1/55 • Number of events 1 • 9 months
Nervous system disorders
Nerve Compression
0.00%
0/166 • 9 months
1.8%
1/55 • Number of events 1 • 9 months
Musculoskeletal and connective tissue disorders
Muscle Spasms
0.00%
0/166 • 9 months
1.8%
1/55 • Number of events 1 • 9 months
Musculoskeletal and connective tissue disorders
Neck Pain
0.00%
0/166 • 9 months
1.8%
1/55 • Number of events 1 • 9 months
Musculoskeletal and connective tissue disorders
Rotator Cuff Syndrome
0.00%
0/166 • 9 months
1.8%
1/55 • Number of events 1 • 9 months
Injury, poisoning and procedural complications
Muscle Strain
0.60%
1/166 • Number of events 1 • 9 months
1.8%
1/55 • Number of events 1 • 9 months
Injury, poisoning and procedural complications
Overdose
0.60%
1/166 • Number of events 1 • 9 months
3.6%
2/55 • Number of events 3 • 9 months
Injury, poisoning and procedural complications
Pelvic Facture
0.00%
0/166 • 9 months
1.8%
1/55 • Number of events 1 • 9 months
Psychiatric disorders
Libido increases
0.00%
0/166 • 9 months
1.8%
1/55 • Number of events 1 • 9 months
Skin and subcutaneous tissue disorders
Drug Eruption
0.00%
0/166 • 9 months
1.8%
1/55 • Number of events 1 • 9 months
Skin and subcutaneous tissue disorders
Rash maculo-papular
0.00%
0/166 • 9 months
1.8%
1/55 • Number of events 1 • 9 months
Skin and subcutaneous tissue disorders
Sunburn
0.00%
0/166 • 9 months
1.8%
1/55 • Number of events 1 • 9 months
General disorders
Application site pain
0.00%
0/166 • 9 months
1.8%
1/55 • Number of events 1 • 9 months
General disorders
Feeling jittery
0.00%
0/166 • 9 months
1.8%
1/55 • Number of events 1 • 9 months
General disorders
Infusion site thrombosis
0.00%
0/166 • 9 months
1.8%
1/55 • Number of events 1 • 9 months
Respiratory, thoracic and mediastinal disorders
Cough
1.2%
2/166 • Number of events 2 • 9 months
0.00%
0/55 • 9 months
Metabolism and nutrition disorders
Diabetes mellitus
0.60%
1/166 • Number of events 1 • 9 months
1.8%
1/55 • Number of events 1 • 9 months
Renal and urinary disorders
Hematuria
1.2%
2/166 • Number of events 2 • 9 months
0.00%
0/55 • 9 months
Renal and urinary disorders
Pollakiuria
0.60%
1/166 • Number of events 1 • 9 months
1.8%
1/55 • Number of events 1 • 9 months
Renal and urinary disorders
Urinary incontinence
0.00%
0/166 • 9 months
1.8%
1/55 • Number of events 1 • 9 months
Eye disorders
Vitreous floaters
0.00%
0/166 • 9 months
1.8%
1/55 • Number of events 1 • 9 months
Reproductive system and breast disorders
Ejaculation disorder
0.00%
0/166 • 9 months
1.8%
1/55 • Number of events 1 • 9 months
Blood and lymphatic system disorders
Anaemia
0.60%
1/166 • Number of events 1 • 9 months
1.8%
1/55 • Number of events 1 • 9 months
Surgical and medical procedures
Tooth extraction
0.00%
0/166 • 9 months
1.8%
1/55 • Number of events 1 • 9 months

Additional Information

Theodore Danoff, MD, PhD

Clarus Therapeutics

Phone: 847-562-4300

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place

Restriction type: GT60