Trial Outcomes & Findings for Dose Ranging Study of OTO-201 in AOMT (NCT NCT02719158)

NCT ID: NCT02719158

Last Updated: 2020-10-19

Results Overview

Number of subjects with adverse events during the study from dosing up to 1 month after dosing

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

95 participants

Primary outcome timeframe

Up to 1 month

Results posted on

2020-10-19

Participant Flow

Participant milestones

Participant milestones
Measure
6 mg OTO-201
6 mg ciprofloxacin: single administration of OTO-201
12 mg OTO-201
12 mg ciprofloxacin: single administration of OTO-201
Control
Sham Control: simulated, single administration
Overall Study
STARTED
38
38
19
Overall Study
COMPLETED
38
38
18
Overall Study
NOT COMPLETED
0
0
1

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Dose Ranging Study of OTO-201 in AOMT

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
6 mg OTO-201
n=37 Participants
6 mg ciprofloxacin: single administration of OTO-201
12 mg OTO-201
n=38 Participants
12 mg ciprofloxacin: single administration of OTO-201
Control
n=18 Participants
Sham Control: simulated, single administration
Total
n=93 Participants
Total of all reporting groups
Age, Continuous
3.004 years
STANDARD_DEVIATION 3.0546 • n=5 Participants
3.955 years
STANDARD_DEVIATION 2.9111 • n=7 Participants
3.551 years
STANDARD_DEVIATION 2.4583 • n=5 Participants
3.498 years
STANDARD_DEVIATION 2.8915 • n=4 Participants
Sex: Female, Male
Female
15 Participants
n=5 Participants
18 Participants
n=7 Participants
7 Participants
n=5 Participants
40 Participants
n=4 Participants
Sex: Female, Male
Male
22 Participants
n=5 Participants
20 Participants
n=7 Participants
11 Participants
n=5 Participants
53 Participants
n=4 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
3 Participants
n=5 Participants
3 Participants
n=7 Participants
2 Participants
n=5 Participants
8 Participants
n=4 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
33 Participants
n=5 Participants
35 Participants
n=7 Participants
16 Participants
n=5 Participants
84 Participants
n=4 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
1 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
1 Participants
n=4 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
Race (NIH/OMB)
Asian
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
Race (NIH/OMB)
Black or African American
8 Participants
n=5 Participants
9 Participants
n=7 Participants
5 Participants
n=5 Participants
22 Participants
n=4 Participants
Race (NIH/OMB)
White
29 Participants
n=5 Participants
27 Participants
n=7 Participants
11 Participants
n=5 Participants
67 Participants
n=4 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
2 Participants
n=7 Participants
1 Participants
n=5 Participants
3 Participants
n=4 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
0 Participants
n=7 Participants
1 Participants
n=5 Participants
1 Participants
n=4 Participants
Region of Enrollment
United States
37 participants
n=5 Participants
38 participants
n=7 Participants
18 participants
n=5 Participants
93 participants
n=4 Participants

PRIMARY outcome

Timeframe: Up to 1 month

Population: Safety analysis set: all subjects who received study drug.

Number of subjects with adverse events during the study from dosing up to 1 month after dosing

Outcome measures

Outcome measures
Measure
6 mg OTO-201
n=38 Participants
6 mg ciprofloxacin: single administration of OTO-201
12 mg OTO-201
n=38 Participants
12 mg ciprofloxacin: single administration of OTO-201
Control
n=19 Participants
Sham Control: simulated, single administration
Number of Subjects With Adverse Events
19 Participants
14 Participants
4 Participants

PRIMARY outcome

Timeframe: Up to 1 month

Population: Safety Population (19 sham, 38 6mg, 38 12 mg) who could have had one or 2 affected ears at Baseline (that is, it was not necessary for both ears to be infected to take part in the study). This is why the number of ears in each group do not equal twice the number of participants.

Number of affected ears (i.e., those ears that were infected) whose external ear and ear canal (auricle and meatus), when examined through an otoscope, appeared normal at Baseline and appeared abnormal at Day 29. The auricle and meatus of each infected ear was examined using an otoscope and was assessed as either normal or abnormal at every visit. This outcome looks to see if there was a worsening of the condition of the auricle and meatus with treatment (i.e., a safety measure).

Outcome measures

Outcome measures
Measure
6 mg OTO-201
n=38 Participants
6 mg ciprofloxacin: single administration of OTO-201
12 mg OTO-201
n=38 Participants
12 mg ciprofloxacin: single administration of OTO-201
Control
n=7 normal affected ears at Baseline
Sham Control: simulated, single administration
Otoscopic Examination: Auricle and Meatus
2 abnormal affected ears at Day 29
0 abnormal affected ears at Day 29
0 abnormal affected ears at Day 29

PRIMARY outcome

Timeframe: Up to 1 month

Population: Safety Population (19 sham, 38 6mg, 38 12 mg) who could have had one or 2 affected ears at Baseline (that is, it was not necessary for both ears to be infected to take part in the study). This is why the number of ears in each group do not equal twice the number of participants.

Number of affected ears (i.e., those ears that were infected) whose ear drum (tympanic membrane), when examined through an otoscope, appeared normal at Baseline and appeared abnormal at Day 29. The tympanic membrane of each infected ear was examined using an otoscope and was assessed as either normal or abnormal at every visit. This outcome looks to see if there was a worsening of the condition of the tympanic membrane with treatment (i.e., a safety measure).

Outcome measures

Outcome measures
Measure
6 mg OTO-201
n=23 normal affected ears at Baseline
6 mg ciprofloxacin: single administration of OTO-201
12 mg OTO-201
n=15 normal affected ears at Baseline
12 mg ciprofloxacin: single administration of OTO-201
Control
n=10 normal affected ears at Baseline
Sham Control: simulated, single administration
Otoscopic Examination: Tympanic Membrane
1 abnormal ears at Day 29
0 abnormal ears at Day 29
0 abnormal ears at Day 29

SECONDARY outcome

Timeframe: Up to Two Weeks

Population: Modified intent-to-treat analysis set: all subjects who were randomized, received treatment, did not have group A streptococci cultured on Visit 1 (Day 1), and had at least 1 on-therapy visit.

Absence of otorrhea (middle ear drainage)

Outcome measures

Outcome measures
Measure
6 mg OTO-201
n=37 Participants
6 mg ciprofloxacin: single administration of OTO-201
12 mg OTO-201
n=38 Participants
12 mg ciprofloxacin: single administration of OTO-201
Control
n=18 Participants
Sham Control: simulated, single administration
Absence of Otorrhea
20 Participants
23 Participants
2 Participants

Adverse Events

6 mg OTO-201

Serious events: 0 serious events
Other events: 5 other events
Deaths: 0 deaths

12 mg OTO-201

Serious events: 0 serious events
Other events: 6 other events
Deaths: 0 deaths

Control

Serious events: 0 serious events
Other events: 1 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
6 mg OTO-201
n=38 participants at risk
6 mg ciprofloxacin: single administration of OTO-201
12 mg OTO-201
n=38 participants at risk
12 mg ciprofloxacin: single administration of OTO-201
Control
n=19 participants at risk
Sham Control: simulated, single administration
Infections and infestations
Otitis media acute
10.5%
4/38 • Adverse events were reported during dosing and up to 1 month following dosing.
2.6%
1/38 • Adverse events were reported during dosing and up to 1 month following dosing.
5.3%
1/19 • Adverse events were reported during dosing and up to 1 month following dosing.
General disorders
Pyrexia
2.6%
1/38 • Adverse events were reported during dosing and up to 1 month following dosing.
13.2%
5/38 • Adverse events were reported during dosing and up to 1 month following dosing.
0.00%
0/19 • Adverse events were reported during dosing and up to 1 month following dosing.

Additional Information

Medical Information Call Center

Otonomy, Inc.

Phone: 1-800-826-6411

Results disclosure agreements

  • Principal investigator is a sponsor employee Publication subject to Sponsor consent.
  • Publication restrictions are in place

Restriction type: OTHER