Trial Outcomes & Findings for An Observational Study of Patient Cohorts Who Previously Received Long-term Treatment With Pioglitazone or Placebo in Addition to Existing Antidiabetic Medications (NCT NCT02678676)

NCT ID: NCT02678676

Last Updated: 2016-07-07

Results Overview

The composite macro-vascular event or death included all-cause mortality, non-fatal myocardial infarction, cardiac intervention, stroke, major leg amputation (above the ankle), bypass surgery or revascularization in the leg. The percentage of participants in the observational study population having first occurrence of macro-vascular event or death during the 10-year observational study period was analyzed. The data were analyzed using the Cox regression with respect to time to the first occurrence of macro-vascular event or death.

Recruitment status

COMPLETED

Target enrollment

3599 participants

Primary outcome timeframe

Up to Year 10

Results posted on

2016-07-07

Participant Flow

Participants took part at 228 sites in 18 European countries including Austria, Belgium, Czech Republic, Denmark, Estonia, Finland, France, Germany, Hungary, Latvia, Lithuania, Netherlands, Norway, Poland, Slovakia, Sweden, Switzerland, and the United Kingdom from 02 November 2004 to 10 March 2015.

Participants with a historical diagnosis of Type 2 diabetes mellitus (T2DM) who were previously treated with pioglitazone or placebo in the PROactive study (NCT00174993) were enrolled in this observational study according to their originally assigned treatment group.

Participant milestones

Participant milestones
Measure
Pioglitazone
Participants who were previously treated with pioglitazone 15, 30, or 45 milligram tablets, orally, once daily during the PROactive study (NCT00174993) were followed up to 10 years in this observational study.
Placebo
Participants who were previously treated with placebo-matching pioglitazone tablets, orally, once daily during the PROactive (NCT00174993) study were followed up to 10 years.
Overall Study
STARTED
1820
1779
Overall Study
COMPLETED
932
907
Overall Study
NOT COMPLETED
888
872

Reasons for withdrawal

Reasons for withdrawal
Measure
Pioglitazone
Participants who were previously treated with pioglitazone 15, 30, or 45 milligram tablets, orally, once daily during the PROactive study (NCT00174993) were followed up to 10 years in this observational study.
Placebo
Participants who were previously treated with placebo-matching pioglitazone tablets, orally, once daily during the PROactive (NCT00174993) study were followed up to 10 years.
Overall Study
Death
619
649
Overall Study
Withdrawal by Subject
13
5
Overall Study
Lost to Follow-up
171
151
Overall Study
Unconfirmed for lost to follow-up
85
67

Baseline Characteristics

An Observational Study of Patient Cohorts Who Previously Received Long-term Treatment With Pioglitazone or Placebo in Addition to Existing Antidiabetic Medications

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Pioglitazone
n=1820 Participants
Participants who were previously treated with pioglitazone 15, 30, or 45 milligram tablets, orally, once daily during the PROactive study (NCT00174993) were followed up to 10 years in this observational study.
Placebo
n=1779 Participants
Participants who were previously treated with placebo-matching pioglitazone tablets, orally, once daily during the PROactive (NCT00174993) study were followed up to 10 years.
Total
n=3599 Participants
Total of all reporting groups
Age, Continuous
61.8 years
STANDARD_DEVIATION 7.51 • n=5 Participants
61.4 years
STANDARD_DEVIATION 7.80 • n=7 Participants
61.6 years
STANDARD_DEVIATION 7.66 • n=5 Participants
Sex: Female, Male
Female
632 Participants
n=5 Participants
626 Participants
n=7 Participants
1258 Participants
n=5 Participants
Sex: Female, Male
Male
1188 Participants
n=5 Participants
1153 Participants
n=7 Participants
2341 Participants
n=5 Participants
Race/Ethnicity, Customized
White
1794 Participants
n=5 Participants
1760 Participants
n=7 Participants
3554 Participants
n=5 Participants
Race/Ethnicity, Customized
Black
7 Participants
n=5 Participants
3 Participants
n=7 Participants
10 Participants
n=5 Participants
Race/Ethnicity, Customized
Asian/Oriental
18 Participants
n=5 Participants
14 Participants
n=7 Participants
32 Participants
n=5 Participants
Race/Ethnicity, Customized
Other
1 Participants
n=5 Participants
2 Participants
n=7 Participants
3 Participants
n=5 Participants
Region of Enrollment
Austria
45 Participants
n=5 Participants
47 Participants
n=7 Participants
92 Participants
n=5 Participants
Region of Enrollment
Belgium
21 Participants
n=5 Participants
18 Participants
n=7 Participants
39 Participants
n=5 Participants
Region of Enrollment
Czech Republic
40 Participants
n=5 Participants
40 Participants
n=7 Participants
80 Participants
n=5 Participants
Region of Enrollment
Denmark
32 Participants
n=5 Participants
27 Participants
n=7 Participants
59 Participants
n=5 Participants
Region of Enrollment
Estonia
50 Participants
n=5 Participants
53 Participants
n=7 Participants
103 Participants
n=5 Participants
Region of Enrollment
Finland
138 Participants
n=5 Participants
124 Participants
n=7 Participants
262 Participants
n=5 Participants
Region of Enrollment
France
28 Participants
n=5 Participants
30 Participants
n=7 Participants
58 Participants
n=5 Participants
Region of Enrollment
Germany
104 Participants
n=5 Participants
104 Participants
n=7 Participants
208 Participants
n=5 Participants
Region of Enrollment
Hungary
356 Participants
n=5 Participants
360 Participants
n=7 Participants
716 Participants
n=5 Participants
Region of Enrollment
Latvia
178 Participants
n=5 Participants
175 Participants
n=7 Participants
353 Participants
n=5 Participants
Region of Enrollment
Lithuania
120 Participants
n=5 Participants
115 Participants
n=7 Participants
235 Participants
n=5 Participants
Region of Enrollment
Netherlands
16 Participants
n=5 Participants
18 Participants
n=7 Participants
34 Participants
n=5 Participants
Region of Enrollment
Norway
44 Participants
n=5 Participants
47 Participants
n=7 Participants
91 Participants
n=5 Participants
Region of Enrollment
Poland
374 Participants
n=5 Participants
366 Participants
n=7 Participants
740 Participants
n=5 Participants
Region of Enrollment
Slovakia
39 Participants
n=5 Participants
42 Participants
n=7 Participants
81 Participants
n=5 Participants
Region of Enrollment
Sweden
56 Participants
n=5 Participants
58 Participants
n=7 Participants
114 Participants
n=5 Participants
Region of Enrollment
Switzerland
11 Participants
n=5 Participants
7 Participants
n=7 Participants
18 Participants
n=5 Participants
Region of Enrollment
United Kingdom
168 Participants
n=5 Participants
148 Participants
n=7 Participants
316 Participants
n=5 Participants
Duration of T2DM
9.3 Years
STANDARD_DEVIATION 6.81 • n=5 Participants
9.3 Years
STANDARD_DEVIATION 6.96 • n=7 Participants
9.3 Years
STANDARD_DEVIATION 6.88 • n=5 Participants
Weight
87.72 Kilograms (kg)
STANDARD_DEVIATION 15.607 • n=5 Participants
88.62 Kilograms (kg)
STANDARD_DEVIATION 15.451 • n=7 Participants
88.17 Kilograms (kg)
STANDARD_DEVIATION 15.534 • n=5 Participants
Body mass index (BMI)
30.834 kilogram per square meter (kg/m^2)
STANDARD_DEVIATION 4.7978 • n=5 Participants
31.078 kilogram per square meter (kg/m^2)
STANDARD_DEVIATION 4.7135 • n=7 Participants
30.955 kilogram per square meter (kg/m^2)
STANDARD_DEVIATION 4.7572 • n=5 Participants

PRIMARY outcome

Timeframe: Up to Year 10

Population: The observational study population consisted of participants who enrolled in this study after completing the final visit of PROactive study (NCT00174993).

The composite macro-vascular event or death included all-cause mortality, non-fatal myocardial infarction, cardiac intervention, stroke, major leg amputation (above the ankle), bypass surgery or revascularization in the leg. The percentage of participants in the observational study population having first occurrence of macro-vascular event or death during the 10-year observational study period was analyzed. The data were analyzed using the Cox regression with respect to time to the first occurrence of macro-vascular event or death.

Outcome measures

Outcome measures
Measure
Pioglitazone
n=1820 Participants
Participants who were previously treated with pioglitazone 15, 30, or 45 milligram tablets, orally, once daily during the PROactive study (NCT00174993) were followed up to 10 years in this observational study.
Placebo
n=1779 Participants
Participants who were previously treated with placebo-matching pioglitazone tablets, orally, once daily during the PROactive (NCT00174993) study were followed up to 10 years.
Percentage of Participants With First Occurrence of Macro-vascular Event or Death
58 percentage of participants
NA
60.3 percentage of participants
NA

SECONDARY outcome

Timeframe: Up to Year 10

Population: The observational study population consisted of participants who enrolled in this study after completing the final visit of PROactive study (NCT00174993).

Percentage of participants with incidences of at least 1 malignancy was reported. All malignancies included adrenal, biliary, bladder, brain, breast, cervix, colon/rectal, gastric, hematological, hepatic, lung, mesothelioma, metastases, oesophageal, oropharyngeal, ovarian/uterine, pancreas, prostate, renal, skin and others.

Outcome measures

Outcome measures
Measure
Pioglitazone
n=1820 Participants
Participants who were previously treated with pioglitazone 15, 30, or 45 milligram tablets, orally, once daily during the PROactive study (NCT00174993) were followed up to 10 years in this observational study.
Placebo
n=1779 Participants
Participants who were previously treated with placebo-matching pioglitazone tablets, orally, once daily during the PROactive (NCT00174993) study were followed up to 10 years.
Incidences With Malignancies
12.9 percentage of participants
13.2 percentage of participants

Adverse Events

Pioglitazone

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Placebo

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Adverse event data not reported

Additional Information

Medical Director

Takeda

Phone: +1-877-825-3327

Results disclosure agreements

  • Principal investigator is a sponsor employee No publication related to study results will be published prior to publication of a multi-center report submitted for publication within 18 months after conclusion or termination of a study at all study sites. Results publications will be submitted to sponsor for review 60 days in advance of publication. Sponsor can require removal of confidential information unrelated to study results. Sponsor can embargo a proposed publication for another 60 days to preserve intellectual property.
  • Publication restrictions are in place

Restriction type: OTHER