Trial Outcomes & Findings for A Phase 2a of RSLV-132 in Subjects With Systemic Lupus Erythematosus (SLE) (NCT NCT02660944)

NCT ID: NCT02660944

Last Updated: 2021-03-10

Results Overview

Mean change from baseline (from baseline to Day 85; or baseline to Day 169) in CLASI activity scores (Last Observation Carried Forward \[LOCF\] post censoring values). The CLASI is a single-page tool that separately quantifies disease activity and damage. For the activity score, points are given for the presence of erythema, scale, mucous membrane lesions, recent hair loss, and inflammatory alopecia. The total score represents the sum of the individual scores and ranges from 0 to 70. Higher scores are awarded for more severe manifestations.

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

64 participants

Primary outcome timeframe

Baseline and Days 29, 57, 85, 99, 113, 127, 141, 155, 169

Results posted on

2021-03-10

Participant Flow

Participant milestones

Participant milestones
Measure
RSLV-132
10 mg/kg RSLV-132 RSLV-132: RNase-Fc fusion protein
Placebo
Saline placebo Placebo: Saline placebo
Overall Study
STARTED
42
22
Overall Study
COMPLETED
25
12
Overall Study
NOT COMPLETED
17
10

Reasons for withdrawal

Reasons for withdrawal
Measure
RSLV-132
10 mg/kg RSLV-132 RSLV-132: RNase-Fc fusion protein
Placebo
Saline placebo Placebo: Saline placebo
Overall Study
Adverse Event
3
4
Overall Study
Physician Decision
3
1
Overall Study
Withdrawal by Subject
5
3
Overall Study
Lost to Follow-up
4
1
Overall Study
Subject schedule
0
1
Overall Study
Exclusion criteria met
2
0

Baseline Characteristics

A Phase 2a of RSLV-132 in Subjects With Systemic Lupus Erythematosus (SLE)

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
RSLV-132
n=42 Participants
10 mg/kg RSLV-132 RSLV-132: RNase-Fc fusion protein
Placebo
n=22 Participants
Saline placebo Placebo: Saline placebo
Total
n=64 Participants
Total of all reporting groups
Age, Continuous
45.3 years
STANDARD_DEVIATION 12.8 • n=5 Participants
45.2 years
STANDARD_DEVIATION 11.6 • n=7 Participants
45.3 years
STANDARD_DEVIATION 12.3 • n=5 Participants
Sex: Female, Male
Female
39 Participants
n=5 Participants
22 Participants
n=7 Participants
61 Participants
n=5 Participants
Sex: Female, Male
Male
3 Participants
n=5 Participants
0 Participants
n=7 Participants
3 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
13 Participants
n=5 Participants
4 Participants
n=7 Participants
17 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
29 Participants
n=5 Participants
18 Participants
n=7 Participants
47 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Asian
1 Participants
n=5 Participants
0 Participants
n=7 Participants
1 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
16 Participants
n=5 Participants
11 Participants
n=7 Participants
27 Participants
n=5 Participants
Race (NIH/OMB)
White
22 Participants
n=5 Participants
11 Participants
n=7 Participants
33 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
3 Participants
n=5 Participants
0 Participants
n=7 Participants
3 Participants
n=5 Participants
Region of Enrollment
United States
32 participants
n=5 Participants
22 participants
n=7 Participants
54 participants
n=5 Participants
CLASI Activity Total Score
24.1 Score on a scale
STANDARD_DEVIATION 9.9 • n=5 Participants
22.4 Score on a scale
STANDARD_DEVIATION 7.9 • n=7 Participants
23.5 Score on a scale
STANDARD_DEVIATION 9.2 • n=5 Participants
Oral corticosteroid dose
0
20 Participants
n=5 Participants
7 Participants
n=7 Participants
27 Participants
n=5 Participants
Oral corticosteroid dose
>0 and less than or equal to 7.5 mg/kg
6 Participants
n=5 Participants
5 Participants
n=7 Participants
11 Participants
n=5 Participants
Oral corticosteroid dose
>7.5
16 Participants
n=5 Participants
10 Participants
n=7 Participants
26 Participants
n=5 Participants

PRIMARY outcome

Timeframe: Baseline and Days 29, 57, 85, 99, 113, 127, 141, 155, 169

Mean change from baseline (from baseline to Day 85; or baseline to Day 169) in CLASI activity scores (Last Observation Carried Forward \[LOCF\] post censoring values). The CLASI is a single-page tool that separately quantifies disease activity and damage. For the activity score, points are given for the presence of erythema, scale, mucous membrane lesions, recent hair loss, and inflammatory alopecia. The total score represents the sum of the individual scores and ranges from 0 to 70. Higher scores are awarded for more severe manifestations.

Outcome measures

Outcome measures
Measure
RSLV-132
n=42 Participants
10 mg/kg RSLV-132 RSLV-132: RNase-Fc fusion protein
Placebo
n=22 Participants
Saline placebo Placebo: Saline placebo
Mean Cutaneous Lupus Erythematosus Disease Area and Severity Index (CLASI) Improvement Compared to Placebo.
Day 85
-6.2 Scores on a scale
Standard Deviation 6.7
-6.5 Scores on a scale
Standard Deviation 6.2
Mean Cutaneous Lupus Erythematosus Disease Area and Severity Index (CLASI) Improvement Compared to Placebo.
Day 169
-6.2 Scores on a scale
Standard Deviation 8.5
-5.7 Scores on a scale
Standard Deviation 7.0

SECONDARY outcome

Timeframe: Baseline and Days 29, 57, 85, 99, 113, 127, 141, 155, 169

Population: On Day 169, a post hoc exploratory subgroup analysis was performed on participants with severe CLASI and severe SLE Disease Activity Index (SLEDAI-2K) scores at baseline. The SLEDAI-2K is a clinical index for the assessment of lupus disease activity in the previous 30 days. It consists of 24 weighted clinical and laboratory variables of nine organ systems. Scores of the descriptors range from 1 to 8, the total possible score is 105. A higher score indicates more severe disease.

Percentage of participants achieving a 50% improvement in CLASI activity score at Day 85 and Day 169 (LOCF post censoring due to use of exclusionary medications)

Outcome measures

Outcome measures
Measure
RSLV-132
n=42 Participants
10 mg/kg RSLV-132 RSLV-132: RNase-Fc fusion protein
Placebo
n=22 Participants
Saline placebo Placebo: Saline placebo
Percentage of Participants Achieving a 50% Improvement in CLASI Activity Score
Day 85
11 Participants
2 Participants
Percentage of Participants Achieving a 50% Improvement in CLASI Activity Score
Day 169 All Participants
14 Participants
5 Participants
Percentage of Participants Achieving a 50% Improvement in CLASI Activity Score
Day 169 Participants with Severe CLASI >/=21
7 Participants
3 Participants
Percentage of Participants Achieving a 50% Improvement in CLASI Activity Score
Day 169 Participants with Severe SLEDAI >/=9
4 Participants
1 Participants

POST_HOC outcome

Timeframe: Baseline and Day 169

Population: A subgroup analysis was also performed on participants with severe CLASI and severe SLEDAI scores

Percentage of participants with an Systemic Lupus Erythematous Responder Index (SRI) 4 response on Day 169. This is a composite responder index incorporating the British Isles Lupus Assessment Group (BILAG) 2004, SLEDAI-2K and Physician Global Assessment (PGA) responses. The BILAG-2004 index, an organ-based transitional activity instrument, provides disease activity scorings across nine organ systems (constitutional, mucocutaneous, neuropsychiatry, musculoskeletal, cardiorespiratory, gastrointestinal, ophthalmic, renal and hematological) on an ordinal scale (A to E) based on the physician's intention-to-treat premise. Grade A represents the most active and Grade E the least active disease. The Physician's Global Assessment is measured on a 0 to 100 mm scale with score 0 to be No Disease Activity and score 100 to be the most Severe Disease Activity.

Outcome measures

Outcome measures
Measure
RSLV-132
n=42 Participants
10 mg/kg RSLV-132 RSLV-132: RNase-Fc fusion protein
Placebo
n=22 Participants
Saline placebo Placebo: Saline placebo
Percentage of Participants With SRI-4 Response
Day 169 All participants
11 Participants
7 Participants
Percentage of Participants With SRI-4 Response
Day 169 Participants with Severe CLASI >/=21
7 Participants
1 Participants
Percentage of Participants With SRI-4 Response
Day 169 Participants with Severe SLEDAI >/=9
8 Participants
4 Participants

POST_HOC outcome

Timeframe: Baseline and Day 169

Population: A subgroup analysis was also performed on participants with severe CLASI and severe SLEDAI scores

Percentage of participants with a BICLA response on Day 169. This is a composite responder index incorporating the BILAG-2004, SLEDAI-2K and PGA responses. The BILAG-2004 index, an organ-based transitional activity instrument, provides disease activity scorings across nine organ systems (constitutional, mucocutaneous, neuropsychiatry, musculoskeletal, cardiorespiratory, gastrointestinal, ophthalmic, renal and hematological) on an ordinal scale (A to E) based on the physician's intention-to-treat premise. Grade A represents the most active and Grade E the least active disease. The PGA is measured on a 0 to 100 mm scale with score 0 to be No Disease Activity and score 100 to be the most Severe Disease Activity.

Outcome measures

Outcome measures
Measure
RSLV-132
n=42 Participants
10 mg/kg RSLV-132 RSLV-132: RNase-Fc fusion protein
Placebo
n=22 Participants
Saline placebo Placebo: Saline placebo
Percentage of Participants With a British Isles Lupus Assessment Group-based Composite Lupus Assessment (BICLA) Response
Day 169 Participants with Severe SLEDAI >/=9
4 Participants
1 Participants
Percentage of Participants With a British Isles Lupus Assessment Group-based Composite Lupus Assessment (BICLA) Response
Day 169 All Participants
10 Participants
4 Participants
Percentage of Participants With a British Isles Lupus Assessment Group-based Composite Lupus Assessment (BICLA) Response
Day 169 Participants with Severe CLASI >/=21
5 Participants
1 Participants

Adverse Events

RSLV-132

Serious events: 3 serious events
Other events: 36 other events
Deaths: 0 deaths

Placebo

Serious events: 5 serious events
Other events: 20 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
RSLV-132
n=42 participants at risk
10 mg/kg RSLV-132 RSLV-132: RNase-Fc fusion protein
Placebo
n=22 participants at risk
Saline placebo Placebo: Saline placebo
Gastrointestinal disorders
Colitis
0.00%
0/42 • 215 days
Treatment emergent adverse events are summarized
4.5%
1/22 • Number of events 1 • 215 days
Treatment emergent adverse events are summarized
Gastrointestinal disorders
Diarrhoea
0.00%
0/42 • 215 days
Treatment emergent adverse events are summarized
4.5%
1/22 • Number of events 1 • 215 days
Treatment emergent adverse events are summarized
Infections and infestations
Appendicitis
2.4%
1/42 • Number of events 1 • 215 days
Treatment emergent adverse events are summarized
4.5%
1/22 • Number of events 1 • 215 days
Treatment emergent adverse events are summarized
Infections and infestations
Escherichia Sepsis
0.00%
0/42 • 215 days
Treatment emergent adverse events are summarized
4.5%
1/22 • Number of events 1 • 215 days
Treatment emergent adverse events are summarized
Infections and infestations
Pneumonia
0.00%
0/42 • 215 days
Treatment emergent adverse events are summarized
4.5%
1/22 • Number of events 1 • 215 days
Treatment emergent adverse events are summarized
Infections and infestations
Urinary Tract Infection
0.00%
0/42 • 215 days
Treatment emergent adverse events are summarized
4.5%
1/22 • Number of events 1 • 215 days
Treatment emergent adverse events are summarized
Infections and infestations
Flank Pain
0.00%
0/42 • 215 days
Treatment emergent adverse events are summarized
4.5%
1/22 • Number of events 1 • 215 days
Treatment emergent adverse events are summarized
Musculoskeletal and connective tissue disorders
Systemic Lupus Erythematosus
0.00%
0/42 • 215 days
Treatment emergent adverse events are summarized
4.5%
1/22 • Number of events 2 • 215 days
Treatment emergent adverse events are summarized
Nervous system disorders
Hypoaesthesia
2.4%
1/42 • Number of events 1 • 215 days
Treatment emergent adverse events are summarized
0.00%
0/22 • 215 days
Treatment emergent adverse events are summarized
Nervous system disorders
Syncope
0.00%
0/42 • 215 days
Treatment emergent adverse events are summarized
4.5%
1/22 • Number of events 1 • 215 days
Treatment emergent adverse events are summarized
Skin and subcutaneous tissue disorders
Cutaneous Lupus Erythematosus
2.4%
1/42 • Number of events 1 • 215 days
Treatment emergent adverse events are summarized
0.00%
0/22 • 215 days
Treatment emergent adverse events are summarized
Vascular disorders
Hypertension
0.00%
0/42 • 215 days
Treatment emergent adverse events are summarized
4.5%
1/22 • Number of events 1 • 215 days
Treatment emergent adverse events are summarized

Other adverse events

Other adverse events
Measure
RSLV-132
n=42 participants at risk
10 mg/kg RSLV-132 RSLV-132: RNase-Fc fusion protein
Placebo
n=22 participants at risk
Saline placebo Placebo: Saline placebo
Vascular disorders
Hypertension
14.3%
6/42 • Number of events 6 • 215 days
Treatment emergent adverse events are summarized
18.2%
4/22 • Number of events 4 • 215 days
Treatment emergent adverse events are summarized
Nervous system disorders
Headache
14.3%
6/42 • Number of events 7 • 215 days
Treatment emergent adverse events are summarized
13.6%
3/22 • Number of events 4 • 215 days
Treatment emergent adverse events are summarized
Gastrointestinal disorders
Nausea
11.9%
5/42 • Number of events 5 • 215 days
Treatment emergent adverse events are summarized
9.1%
2/22 • Number of events 3 • 215 days
Treatment emergent adverse events are summarized
Infections and infestations
Urinary Tract Infection
9.5%
4/42 • Number of events 5 • 215 days
Treatment emergent adverse events are summarized
18.2%
4/22 • Number of events 4 • 215 days
Treatment emergent adverse events are summarized
Skin and subcutaneous tissue disorders
Cutaneous Lupus Erythematosus
9.5%
4/42 • Number of events 5 • 215 days
Treatment emergent adverse events are summarized
0.00%
0/22 • 215 days
Treatment emergent adverse events are summarized
Infections and infestations
Sinusitis
9.5%
4/42 • Number of events 4 • 215 days
Treatment emergent adverse events are summarized
0.00%
0/22 • 215 days
Treatment emergent adverse events are summarized
Infections and infestations
Upper Respiratory Tract Infection
7.1%
3/42 • Number of events 4 • 215 days
Treatment emergent adverse events are summarized
18.2%
4/22 • Number of events 5 • 215 days
Treatment emergent adverse events are summarized
Renal and urinary disorders
Proteinuria
7.1%
3/42 • Number of events 4 • 215 days
Treatment emergent adverse events are summarized
0.00%
0/22 • 215 days
Treatment emergent adverse events are summarized
Infections and infestations
Bronchitis
4.8%
2/42 • Number of events 2 • 215 days
Treatment emergent adverse events are summarized
9.1%
2/22 • Number of events 2 • 215 days
Treatment emergent adverse events are summarized
Skin and subcutaneous tissue disorders
Rash
4.8%
2/42 • Number of events 2 • 215 days
Treatment emergent adverse events are summarized
9.1%
2/22 • Number of events 2 • 215 days
Treatment emergent adverse events are summarized
Musculoskeletal and connective tissue disorders
Systemic Lupus Erythematosus
2.4%
1/42 • Number of events 1 • 215 days
Treatment emergent adverse events are summarized
18.2%
4/22 • Number of events 4 • 215 days
Treatment emergent adverse events are summarized
Musculoskeletal and connective tissue disorders
Back Pain
2.4%
1/42 • Number of events 1 • 215 days
Treatment emergent adverse events are summarized
9.1%
2/22 • Number of events 2 • 215 days
Treatment emergent adverse events are summarized
Renal and urinary disorders
Dysuria
2.4%
1/42 • Number of events 1 • 215 days
Treatment emergent adverse events are summarized
9.1%
2/22 • Number of events 2 • 215 days
Treatment emergent adverse events are summarized

Additional Information

James Posada

Resolve Therapeutics LLC

Phone: (208)7277010

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place