Ublituximab + TGR-1202 Compared to Obinutuzumab + Chlorambucil in Participants With Untreated and Previously Treated Chronic Lymphocytic Leukemia

NCT ID: NCT02612311

Last Updated: 2024-12-13

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

603 participants

Study Classification

INTERVENTIONAL

Study Start Date

2015-11-19

Study Completion Date

2023-02-22

Brief Summary

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This study evaluates the combination of ublituximab, a novel monoclonal antibody, and TGR-1202, a novel PI3K delta inhibitor compared to obinutuzumab and chlorambucil, and compared to ublituximab or TGR-1202 alone in Chronic Lymphocytic Leukemia (CLL) participants.

Detailed Description

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Conditions

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Chronic Lymphocytic Leukemia

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Arm A: Ublituximab + Umbralisib

Participants received ublituximab, 150 milligrams (mg), intravenously (IV), on Day 1, 750 mg on Day 2, followed by 900 mg on Days 8 and 15 of Cycle 1 (cycle length=28 days), Day 1 of Cycles 2-6, and once every 3 cycles thereafter, along with umbralisib, 800 mg, orally, once daily during each cycle until disease progression, lack of tolerability, or until the treatment is commercially available or up to 87 months.

Group Type EXPERIMENTAL

Ublituximab

Intervention Type BIOLOGICAL

Ublituximab: IV infusion

TGR-1202

Intervention Type DRUG

TGR-1202: Oral daily dose

Arm B: Obinutuzumab + Chlorambucil

Participants received Obinutuzumab 100 mg, IV on Day 1, 900 mg on Day 2, followed by 1000 mg on Days 8 and 15 of cycle 1 (cycle length = 28 days), Day 1 of Cycle 2-6 along with Chlorambucil 0.5 milligram per kilogram (mg/kg) tablet orally on Days 1 and 15 once daily during each cycle until disease progression, lack of tolerability, or until the treatment is commercially available or up to 87 months.

Group Type ACTIVE_COMPARATOR

Obinutuzumab

Intervention Type BIOLOGICAL

Obinutuzumab: IV infusion

Chlorambucil

Intervention Type DRUG

Chlorambucil: Oral dose

Arm C: Ublituximab

Participants received ublituximab, 150 mg, IV, on Day 1, 750 mg on Day 2, followed by 900 mg on Days 8 and 15 of Cycle 1 (cycle length=28 days), Day 1 of Cycles 2-6, and once every 3 cycles thereafter, until disease progression, lack of tolerability, or until the treatment is commercially available or up to 87 months.

Group Type EXPERIMENTAL

Ublituximab

Intervention Type BIOLOGICAL

Ublituximab: IV infusion

Arm D: Umbralisib

Participants received umbralisib, 800 mg tablets, orally, once daily during each cycle (cycle length= 28 days) until removal from study or up to 87 months.

Group Type EXPERIMENTAL

TGR-1202

Intervention Type DRUG

TGR-1202: Oral daily dose

Interventions

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Obinutuzumab

Obinutuzumab: IV infusion

Intervention Type BIOLOGICAL

Ublituximab

Ublituximab: IV infusion

Intervention Type BIOLOGICAL

TGR-1202

TGR-1202: Oral daily dose

Intervention Type DRUG

Chlorambucil

Chlorambucil: Oral dose

Intervention Type DRUG

Other Intervention Names

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GAZYVA Leukeran

Eligibility Criteria

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Inclusion Criteria

* Treatment naïve or previously treated Chronic Lymphocytic Leukemia (CLL) requiring treatment
* Eastern Cooperative Oncology Group (ECOG) score of 0 to 2

Exclusion Criteria

* Any major surgery, chemotherapy or immunotherapy within the last 21 days
* Evidence of hepatitis B virus, hepatitis C virus or known HIV infection
* Autologous hematologic stem cell transplant within 3 months of study entry. Prior Allogeneic hematologic stem cell transplant is excluded
* Transformation of CLL to aggressive Non-Hodgkin's Lymphoma (NHL) (Richter's transformation)
* Prior therapy with obinutuzumab and/or chlorambucil or a PI3K delta inhibitor
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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TG Therapeutics, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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TG Therapeutics Investigational Trial Site

Huntsville, Alabama, United States

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Mobile, Alabama, United States

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Chandler, Arizona, United States

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Phoenix, Arizona, United States

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Tucson, Arizona, United States

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Fayetteville, Arkansas, United States

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Concord, California, United States

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Duarte, California, United States

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Greenbrae, California, United States

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Pismo Beach, California, United States

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Pleasanton, California, United States

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San Diego, California, United States

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Santa Barbara, California, United States

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Whittier, California, United States

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Aurora, Colorado, United States

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Denver, Colorado, United States

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Bridgeport, Connecticut, United States

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New Haven, Connecticut, United States

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Stamford, Connecticut, United States

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Newark, Delaware, United States

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Boca Raton, Florida, United States

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Fort Myers, Florida, United States

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Jacksonville, Florida, United States

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Jacksonville, Florida, United States

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Ocala, Florida, United States

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Pensacola, Florida, United States

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St. Petersburg, Florida, United States

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Tallahassee, Florida, United States

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Tampa, Florida, United States

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West Palm Beach, Florida, United States

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Albany, Georgia, United States

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Macon, Georgia, United States

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Chicago, Illinois, United States

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Decatur, Illinois, United States

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Maywood, Illinois, United States

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Niles, Illinois, United States

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Peoria, Illinois, United States

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Swansea, Illinois, United States

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Urbana, Illinois, United States

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Fort Wayne, Indiana, United States

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Indianapolis, Indiana, United States

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Ames, Iowa, United States

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Cedar Rapids, Iowa, United States

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Kansas City, Kansas, United States

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Westwood, Kansas, United States

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Louisville, Kentucky, United States

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Baltimore, Maryland, United States

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Baltimore, Maryland, United States

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Bethesda, Maryland, United States

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Columbia, Maryland, United States

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Boston, Massachusetts, United States

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Worcester, Massachusetts, United States

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Ann Arbor, Michigan, United States

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Detroit, Michigan, United States

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Jackson, Michigan, United States

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Saint Louis Park, Minnesota, United States

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Columbia, Missouri, United States

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Kansas City, Missouri, United States

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Lincoln, Nebraska, United States

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Las Vegas, Nevada, United States

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Lebanon, New Hampshire, United States

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Morristown, New Jersey, United States

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Somerville, New Jersey, United States

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East Setauket, New York, United States

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Glens Falls, New York, United States

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Syracuse, New York, United States

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Charlotte, North Carolina, United States

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Durham, North Carolina, United States

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Durham, North Carolina, United States

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Hickory, North Carolina, United States

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Kinston, North Carolina, United States

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Raleigh, North Carolina, United States

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Washington, North Carolina, United States

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Canton, Ohio, United States

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Cincinnati, Ohio, United States

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Toledo, Ohio, United States

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Portland, Oregon, United States

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Portland, Oregon, United States

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Springfield, Oregon, United States

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Camp Hill, Pennsylvania, United States

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Danville, Pennsylvania, United States

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Hershey, Pennsylvania, United States

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Philadelphia, Pennsylvania, United States

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Pittsburgh, Pennsylvania, United States

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Pittsburgh, Pennsylvania, United States

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Pawtucket, Rhode Island, United States

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Greenville, South Carolina, United States

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Sioux Falls, South Dakota, United States

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Watertown, South Dakota, United States

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Chattanooga, Tennessee, United States

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Nashville, Tennessee, United States

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Austin, Texas, United States

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Bedford, Texas, United States

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Fort Worth, Texas, United States

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Houston, Texas, United States

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San Antonio, Texas, United States

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San Antonio, Texas, United States

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Tyler, Texas, United States

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Ogden, Utah, United States

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Blacksburg, Virginia, United States

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Charlottesville, Virginia, United States

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Fort Belvoir, Virginia, United States

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Olympia, Washington, United States

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Seattle, Washington, United States

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Seattle, Washington, United States

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Spokane, Washington, United States

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Vancouver, Washington, United States

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Yakima, Washington, United States

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Milwaukee, Wisconsin, United States

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Wauwatosa, Wisconsin, United States

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Ashkelon, , Israel

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Beersheba, , Israel

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Haifa, , Israel

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Jerusalem, , Israel

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Nahariya, , Israel

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Petah Tikva, , Israel

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Tel Aviv, , Israel

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Bologna, , Italy

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Ferrara, , Italy

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Milan, , Italy

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Rome, , Italy

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Torino, , Italy

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Chorzów, , Poland

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Gdynia, , Poland

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Krakow, , Poland

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Lodz, , Poland

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Lublin, , Poland

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Słupsk, , Poland

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Warsaw, , Poland

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Wroclaw, , Poland

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Krasnozatonskiy, , Russia

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Moscow, , Russia

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Perm, , Russia

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Petrozavodsk, , Russia

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Rodionova, , Russia

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Saint Petersburg, , Russia

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Smolensk, , Russia

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Tula, , Russia

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Yaroslavl, , Russia

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Barcelona, , Spain

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Madrid, , Spain

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Valencia, , Spain

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Cambridge, , United Kingdom

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Cumbria, , United Kingdom

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Dudley West, , United Kingdom

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London, , United Kingdom

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Northbrook, , United Kingdom

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Northumbria, , United Kingdom

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Norwich, , United Kingdom

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Peterborough, , United Kingdom

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Southampton, , United Kingdom

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St. James, , United Kingdom

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Sunderland, , United Kingdom

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Wolverhampton, , United Kingdom

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Countries

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United States Israel Italy Poland Russia Spain United Kingdom

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2015-005758-36

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

UTX-TGR-304

Identifier Type: -

Identifier Source: org_study_id