Phase III Study Investigating the Efficacy and Safety of Ruxolitinib in Early Myelofibrosis Patients With High Molecular Risk Mutations.

NCT ID: NCT02598297

Last Updated: 2019-08-16

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

View full results

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

49 participants

Study Classification

INTERVENTIONAL

Study Start Date

2016-02-03

Study Completion Date

2017-10-23

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

Myelofibrosis patients with high molecular risk mutations have an intrinsically aggressive disease with increased risk of leukemic transformation and reduced overall survival. As there are no therapies currently established in the subset of high molecular risk patients with early myelofibrosis, the study aimed to evaluate ruxolitinib in this patient population.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Myelofibrosis With High Molecular Risk Mutations

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Ruxolitinib

Two tablets of ruxolitinib 5 mg were administered orally twice per day.

Group Type ACTIVE_COMPARATOR

Ruxolitinib

Intervention Type DRUG

5 mg tablet for oral use

Ruxolitinib Placebo

Two tablets of 5mg placebo were administered orally twice per day.

Group Type PLACEBO_COMPARATOR

Ruxolitinib Placebo

Intervention Type DRUG

5 mg placebo tablet for oral use

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Ruxolitinib

5 mg tablet for oral use

Intervention Type DRUG

Ruxolitinib Placebo

5 mg placebo tablet for oral use

Intervention Type DRUG

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

INC424

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Confirmed diagnosis of MF with bone marrow fibrosis of at least Grade 1; irrespective of JAK2 mutational status
* Patients with at least one mutation in one of the five HMR genes (ASXL1, EZH2, SRSF2 and IDH1/2)
* Patients with non-palpable spleen or spleen palpable ≤ 5 cm from the left costal margin to the point of greatest splenic protrusion
* Patients with MF-7 score of ≤ 15, with each individual symptom score of ≤ 3

Exclusion Criteria

* Patients with prior treatment with ruxolitinib or other JAK inhibitors.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Novartis Pharmaceuticals

Role: STUDY_DIRECTOR

Novartis Pharmaceuticals

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Novartis Investigative Site

Concord NSW, New South Wales, Australia

Site Status

Novartis Investigative Site

Liverpool, New South Wales, Australia

Site Status

Novartis Investigative Site

Wooloongabba, Queensland, Australia

Site Status

Novartis Investigative Site

Nedlands, Western Australia, Australia

Site Status

Novartis Investigative Site

Salzburg, , Austria

Site Status

Novartis Investigative Site

Vienna, , Austria

Site Status

Novartis Investigative Site

Antwerp, , Belgium

Site Status

Novartis Investigative Site

Leuven, , Belgium

Site Status

Novartis Investigative Site

Liège, , Belgium

Site Status

Novartis Investigative Site

São Paulo, São Paulo, Brazil

Site Status

Novartis Investigative Site

São Paulo, São Paulo, Brazil

Site Status

Novartis Investigative Site

São Paulo, , Brazil

Site Status

Novartis Investigative Site

Toronto, Ontario, Canada

Site Status

Novartis Investigative Site

Aalborg, , Denmark

Site Status

Novartis Investigative Site

Herlev, , Denmark

Site Status

Novartis Investigative Site

Bayonne, Bayonne Cedex, France

Site Status

Novartis Investigative Site

Angers, , France

Site Status

Novartis Investigative Site

Brest, , France

Site Status

Novartis Investigative Site

Chambéry, , France

Site Status

Novartis Investigative Site

Grenoble, , France

Site Status

Novartis Investigative Site

Lille, , France

Site Status

Novartis Investigative Site

Nice, , France

Site Status

Novartis Investigative Site

Rouen, , France

Site Status

Novartis Investigative Site

Vandœuvre-lès-Nancy, , France

Site Status

Novartis Investigative Site

Lübeck, Schleswig-Holstein, Germany

Site Status

Novartis Investigative Site

Aachen, , Germany

Site Status

Novartis Investigative Site

Bochum, , Germany

Site Status

Novartis Investigative Site

Bonn, , Germany

Site Status

Novartis Investigative Site

Chemnitz, , Germany

Site Status

Novartis Investigative Site

Cologne, , Germany

Site Status

Novartis Investigative Site

Dresden, , Germany

Site Status

Novartis Investigative Site

Essen, , Germany

Site Status

Novartis Investigative Site

Halle S, , Germany

Site Status

Novartis Investigative Site

Heilbronn, , Germany

Site Status

Novartis Investigative Site

Leipzig, , Germany

Site Status

Novartis Investigative Site

München, , Germany

Site Status

Novartis Investigative Site

Nordhorn, , Germany

Site Status

Novartis Investigative Site

Rostock, , Germany

Site Status

Novartis Investigative Site

Ulm, , Germany

Site Status

Novartis Investigative Site

Athens, GR, Greece

Site Status

Novartis Investigative Site

Thessaloniki, GR, Greece

Site Status

Novartis Investigative Site

Athens, , Greece

Site Status

Novartis Investigative Site

Athens, , Greece

Site Status

Novartis Investigative Site

Pátrai, , Greece

Site Status

Novartis Investigative Site

Hong Kong, , Hong Kong

Site Status

Novartis Investigative Site

Budapest, , Hungary

Site Status

Novartis Investigative Site

Debrecen, , Hungary

Site Status

Novartis Investigative Site

Kaposvár, , Hungary

Site Status

Novartis Investigative Site

Afula, , Israel

Site Status

Novartis Investigative Site

Haifa, , Israel

Site Status

Novartis Investigative Site

Jerusalem, , Israel

Site Status

Novartis Investigative Site

Tel Aviv, , Israel

Site Status

Novartis Investigative Site

Zrifin, , Israel

Site Status

Novartis Investigative Site

Bari, BA, Italy

Site Status

Novartis Investigative Site

Bologna, BO, Italy

Site Status

Novartis Investigative Site

Brescia, BS, Italy

Site Status

Novartis Investigative Site

Catania, CT, Italy

Site Status

Novartis Investigative Site

Florence, FI, Italy

Site Status

Novartis Investigative Site

Rome, Lazio, Italy

Site Status

Novartis Investigative Site

Milan, MI, Italy

Site Status

Novartis Investigative Site

Pavia, PV, Italy

Site Status

Novartis Investigative Site

Reggio Emilia, RE, Italy

Site Status

Novartis Investigative Site

Orbassano, TO, Italy

Site Status

Novartis Investigative Site

Terni, TR, Italy

Site Status

Novartis Investigative Site

Varese, VA, Italy

Site Status

Novartis Investigative Site

Nagoya, Aichi-ken, Japan

Site Status

Novartis Investigative Site

Fukuoka, Fukuoka, Japan

Site Status

Novartis Investigative Site

Maebashi, Gunma, Japan

Site Status

Novartis Investigative Site

Kobe, Hyōgo, Japan

Site Status

Novartis Investigative Site

Isehara, Kanagawa, Japan

Site Status

Novartis Investigative Site

Suita, Osaka, Japan

Site Status

Novartis Investigative Site

Bunkyo Ku, Tokyo, Japan

Site Status

Novartis Investigative Site

Shinjuku-ku, Tokyo, Japan

Site Status

Novartis Investigative Site

Chūō, Yamanashi, Japan

Site Status

Novartis Investigative Site

Osaka, , Japan

Site Status

Novartis Investigative Site

Bergen, , Norway

Site Status

Novartis Investigative Site

Loerenskog, , Norway

Site Status

Novartis Investigative Site

Lodz, , Poland

Site Status

Novartis Investigative Site

Torun, , Poland

Site Status

Novartis Investigative Site

Wroclaw, , Poland

Site Status

Novartis Investigative Site

Faro, , Portugal

Site Status

Novartis Investigative Site

Porto, , Portugal

Site Status

Novartis Investigative Site

Moscow, , Russia

Site Status

Novartis Investigative Site

Saint Petersburg, , Russia

Site Status

Novartis Investigative Site

Saint Petersburg, , Russia

Site Status

Novartis Investigative Site

Singapore, , Singapore

Site Status

Novartis Investigative Site

Singapore, , Singapore

Site Status

Novartis Investigative Site

Cadiz, Andalusia, Spain

Site Status

Novartis Investigative Site

Málaga, Andalusia, Spain

Site Status

Novartis Investigative Site

Madrid, , Spain

Site Status

Novartis Investigative Site

Gothenburg, , Sweden

Site Status

Novartis Investigative Site

Huddinge, , Sweden

Site Status

Novartis Investigative Site

Lund, , Sweden

Site Status

Novartis Investigative Site

Uddevalla, , Sweden

Site Status

Novartis Investigative Site

Basel, , Switzerland

Site Status

Novartis Investigative Site

Sankt Gallen, , Switzerland

Site Status

Novartis Investigative Site

Zurich, , Switzerland

Site Status

Novartis Investigative Site

Putzu City, Chiayi Hsien, Taiwan

Site Status

Novartis Investigative Site

Kaohsiung City, , Taiwan

Site Status

Novartis Investigative Site

Taipei, , Taiwan

Site Status

Novartis Investigative Site

Taoyuan District, , Taiwan

Site Status

Novartis Investigative Site

Ankara, , Turkey (Türkiye)

Site Status

Novartis Investigative Site

Istanbul, , Turkey (Türkiye)

Site Status

Novartis Investigative Site

Samsun, , Turkey (Türkiye)

Site Status

Novartis Investigative Site

Talas / Kayseri, , Turkey (Türkiye)

Site Status

Novartis Investigative Site

Edgbaston, Birmingham, United Kingdom

Site Status

Novartis Investigative Site

Westbruy on Trym, Bristol, United Kingdom

Site Status

Novartis Investigative Site

Leeds, , United Kingdom

Site Status

Novartis Investigative Site

London, , United Kingdom

Site Status

Novartis Investigative Site

Manchester, , United Kingdom

Site Status

Countries

Review the countries where the study has at least one active or historical site.

Australia Austria Belgium Brazil Canada Denmark France Germany Greece Hong Kong Hungary Israel Italy Japan Norway Poland Portugal Russia Singapore Spain Sweden Switzerland Taiwan Turkey (Türkiye) United Kingdom

Provided Documents

Download supplemental materials such as informed consent forms, study protocols, or participant manuals.

Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

2014-004928-21

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

CINC424A2353

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.

CINC424A2X01B Rollover Protocol
NCT02386800 ACTIVE_NOT_RECRUITING PHASE4