Trial Outcomes & Findings for Inhibiting Fatty Acid Synthase to Improve Efficacy of Neoadjuvant Chemotherapy (NCT NCT02595372)

NCT ID: NCT02595372

Last Updated: 2021-12-15

Results Overview

pCR is defined as no invasive disease in the breast of axilla at the time of definitive surgery. A patient is considered to have FASN expression if the positivity was \>= 15% at the baseline or after 4-7 days of Omeprazole monotherapy. FASN expression is evaluated using immunohistochemistry in core biopsy samples. The percent of patients with FASN expression that have pCR will be calculated with an exact 95% confidence interval.

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

42 participants

Primary outcome timeframe

Up to 6 months

Results posted on

2021-12-15

Participant Flow

Participant milestones

Participant milestones
Measure
High Dose Omeprazole Treatment
Patients will be treated with omeprazole 80 mg orally BID beginning 4-7 days prior to chemotherapy and continuing until surgery.
Overall Study
STARTED
42
Overall Study
COMPLETED
33
Overall Study
NOT COMPLETED
9

Reasons for withdrawal

Reasons for withdrawal
Measure
High Dose Omeprazole Treatment
Patients will be treated with omeprazole 80 mg orally BID beginning 4-7 days prior to chemotherapy and continuing until surgery.
Overall Study
Adverse Event
6
Overall Study
Physician Decision
2
Overall Study
Disease Progression
1

Baseline Characteristics

Inhibiting Fatty Acid Synthase to Improve Efficacy of Neoadjuvant Chemotherapy

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
High Dose Omeprazole Treatment
n=42 Participants
Patients will be treated with omeprazole 80 mg orally BID beginning 4-7 days prior to chemotherapy and continuing until surgery.
Age, Categorical
<=18 years
0 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
36 Participants
n=5 Participants
Age, Categorical
>=65 years
6 Participants
n=5 Participants
Age, Continuous
52.6 years
STANDARD_DEVIATION 10.50 • n=5 Participants
Sex: Female, Male
Female
42 Participants
n=5 Participants
Sex: Female, Male
Male
0 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
3 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
38 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
1 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
Race (NIH/OMB)
Asian
0 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
14 Participants
n=5 Participants
Race (NIH/OMB)
White
24 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
1 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
3 Participants
n=5 Participants
Eastern Cooperative Oncology Group (ECOG) Performance Status
0-Fully active
36 Participants
n=5 Participants
Eastern Cooperative Oncology Group (ECOG) Performance Status
1-Restricted in physically strenuous activity
6 Participants
n=5 Participants

PRIMARY outcome

Timeframe: Up to 6 months

Population: Patients who had surgery and positive FASN expression

pCR is defined as no invasive disease in the breast of axilla at the time of definitive surgery. A patient is considered to have FASN expression if the positivity was \>= 15% at the baseline or after 4-7 days of Omeprazole monotherapy. FASN expression is evaluated using immunohistochemistry in core biopsy samples. The percent of patients with FASN expression that have pCR will be calculated with an exact 95% confidence interval.

Outcome measures

Outcome measures
Measure
High Dose Omeprazole Treatment
n=29 Participants
Patients will be treated with omeprazole 80 mg orally BID beginning 4-7 days prior to chemotherapy and continuing until surgery.
Percentage of Patients With Pathological Complete Response (pCR) in Patients Who Have Fatty Acid Synthase (FASN) Expression
72.4 percentage of participants
Interval 52.8 to 87.3

SECONDARY outcome

Timeframe: Up to 6 months

Population: Patients who received surgery

pCR is defined as no invasive disease in the breast or axilla at the time of definitive surgery. The percentage of patients who achieve pCR along with exact 95% confidence intervals were calculated.

Outcome measures

Outcome measures
Measure
High Dose Omeprazole Treatment
n=39 Participants
Patients will be treated with omeprazole 80 mg orally BID beginning 4-7 days prior to chemotherapy and continuing until surgery.
Percentage of Patients With Pathological Complete Response (pCR) in All Patients
74.4 percentage of participants
Interval 57.9 to 87.0

SECONDARY outcome

Timeframe: up to 1 week

Population: Patients with FASN positivity results at either baseline or after 4-7 days of treatment.

FASN expression was evaluated using immunohistochemistry in core biopsy samples. FASN expression was determined if the positivity was \>= 15%. The percent of patients who had FASN expression and the exact 95% confidence intervals were calculated.

Outcome measures

Outcome measures
Measure
High Dose Omeprazole Treatment
n=30 Participants
Patients will be treated with omeprazole 80 mg orally BID beginning 4-7 days prior to chemotherapy and continuing until surgery.
Percent of Patients With FASN Expression
93.3 percentage of participants
Interval 77.9 to 99.2

SECONDARY outcome

Timeframe: baseline and after 4-7 days

Population: Patients with FASN positivity expression at both baseline and after 4-7 days of treatment.

The mean and standard deviation of FASN positivity expression determined at baseline and after 4-7 days of Omeprazole treatment. FASN expression is evaluated using immunohistochemistry in core biopsy samples.

Outcome measures

Outcome measures
Measure
High Dose Omeprazole Treatment
n=24 Participants
Patients will be treated with omeprazole 80 mg orally BID beginning 4-7 days prior to chemotherapy and continuing until surgery.
FASN Positivity Expression at Baseline and After 4-7 Days of Omeprazole Treatment
Baseline
53.9 percentage of positivity
Standard Deviation 23.6
FASN Positivity Expression at Baseline and After 4-7 Days of Omeprazole Treatment
After 4-7 days
41.7 percentage of positivity
Standard Deviation 30.7

SECONDARY outcome

Timeframe: baseline and after 4-7 days

Population: Patients with FASN activity evaluated at baseline and after 4-7 days of treatment.

The mean and standard deviation of FASN activity determined at baseline and after 4-7 days of Omeprazole treatment. FASN activity was evaluated using immunohistochemistry in core biopsy samples.

Outcome measures

Outcome measures
Measure
High Dose Omeprazole Treatment
n=12 Participants
Patients will be treated with omeprazole 80 mg orally BID beginning 4-7 days prior to chemotherapy and continuing until surgery.
FASN Activity at Baseline and After 4-7 Days of Omeprazole Treatment
Baseline
2.1 ng/mg
Standard Deviation 1.61
FASN Activity at Baseline and After 4-7 Days of Omeprazole Treatment
After 4-7 days
1.3 ng/mg
Standard Deviation 0.93

SECONDARY outcome

Timeframe: up to 8 months

Population: Patients who received treatment

Number of unique patients who had an Omeprazole treatment related (possible, probable or definite) adverse event with grade \>= 3.

Outcome measures

Outcome measures
Measure
High Dose Omeprazole Treatment
n=42 Participants
Patients will be treated with omeprazole 80 mg orally BID beginning 4-7 days prior to chemotherapy and continuing until surgery.
Number of Patients With Treatment Related Adverse Events Grade 3 or Above
0 Participants

Adverse Events

High Dose Omeprazole Treatment

Serious events: 5 serious events
Other events: 37 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
High Dose Omeprazole Treatment
n=42 participants at risk
Patients will be treated with omeprazole 80 mg orally BID beginning 4-7 days prior to chemotherapy and continuing until surgery.
Blood and lymphatic system disorders
Febrile neutropenia
7.1%
3/42 • Up to 8 months
Gastrointestinal disorders
Constipation
2.4%
1/42 • Up to 8 months
Investigations
Neutrophil count decreased
2.4%
1/42 • Up to 8 months
Investigations
White blood cell decreased
2.4%
1/42 • Up to 8 months
Respiratory, thoracic and mediastinal disorders
Cough
2.4%
1/42 • Up to 8 months

Other adverse events

Other adverse events
Measure
High Dose Omeprazole Treatment
n=42 participants at risk
Patients will be treated with omeprazole 80 mg orally BID beginning 4-7 days prior to chemotherapy and continuing until surgery.
Blood and lymphatic system disorders
Anemia
31.0%
13/42 • Up to 8 months
Gastrointestinal disorders
Constipation
23.8%
10/42 • Up to 8 months
Gastrointestinal disorders
Diarrhea
26.2%
11/42 • Up to 8 months
Gastrointestinal disorders
Dry mouth
9.5%
4/42 • Up to 8 months
Gastrointestinal disorders
Dyspepsia
9.5%
4/42 • Up to 8 months
Gastrointestinal disorders
Mucositis oral
23.8%
10/42 • Up to 8 months
Gastrointestinal disorders
Nausea
33.3%
14/42 • Up to 8 months
Gastrointestinal disorders
Vomiting
16.7%
7/42 • Up to 8 months
General disorders
Edema limbs
7.1%
3/42 • Up to 8 months
General disorders
Fatigue
38.1%
16/42 • Up to 8 months
General disorders
Pain
14.3%
6/42 • Up to 8 months
Infections and infestations
Urinary tract infection
9.5%
4/42 • Up to 8 months
Investigations
Alanine aminotransferase increased
11.9%
5/42 • Up to 8 months
Investigations
Lymphocyte count decreased
23.8%
10/42 • Up to 8 months
Investigations
Neutrophil count decreased
19.0%
8/42 • Up to 8 months
Investigations
Platelet count decreased
7.1%
3/42 • Up to 8 months
Investigations
Weight loss
7.1%
3/42 • Up to 8 months
Investigations
White blood cell decreased
16.7%
7/42 • Up to 8 months
Metabolism and nutrition disorders
Anorexia
21.4%
9/42 • Up to 8 months
Metabolism and nutrition disorders
Hyperglycemia
7.1%
3/42 • Up to 8 months
Metabolism and nutrition disorders
Hypertriglyceridemia
7.1%
3/42 • Up to 8 months
Metabolism and nutrition disorders
Hypokalemia
14.3%
6/42 • Up to 8 months
Metabolism and nutrition disorders
Hypomagnesemia
9.5%
4/42 • Up to 8 months
Musculoskeletal and connective tissue disorders
Back pain
14.3%
6/42 • Up to 8 months
Musculoskeletal and connective tissue disorders
Myalgia
9.5%
4/42 • Up to 8 months
Musculoskeletal and connective tissue disorders
Pain in extremity
11.9%
5/42 • Up to 8 months
Nervous system disorders
Dizziness
7.1%
3/42 • Up to 8 months
Nervous system disorders
Dysgeusia
9.5%
4/42 • Up to 8 months
Nervous system disorders
Headache
19.0%
8/42 • Up to 8 months
Nervous system disorders
Peripheral motor neuropathy
9.5%
4/42 • Up to 8 months
Nervous system disorders
Peripheral sensory neuropathy
38.1%
16/42 • Up to 8 months
Psychiatric disorders
Anxiety
9.5%
4/42 • Up to 8 months
Psychiatric disorders
Insomnia
21.4%
9/42 • Up to 8 months
Respiratory, thoracic and mediastinal disorders
Cough
26.2%
11/42 • Up to 8 months
Respiratory, thoracic and mediastinal disorders
Dyspnea
16.7%
7/42 • Up to 8 months
Skin and subcutaneous tissue disorders
Alopecia
31.0%
13/42 • Up to 8 months
Skin and subcutaneous tissue disorders
Pruritus
16.7%
7/42 • Up to 8 months
Skin and subcutaneous tissue disorders
Skin and subcutaneous tissue disorders - Other
7.1%
3/42 • Up to 8 months
Skin and subcutaneous tissue disorders
Skin hyperpigmentation
11.9%
5/42 • Up to 8 months
Vascular disorders
Hot flashes
9.5%
4/42 • Up to 8 months

Additional Information

Dr. Kathy Miller

IndianaU

Phone: (317) 948-3855

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place