Trial Outcomes & Findings for TEEL Study- Phase 1 Tamoxifen and Ribociclib (LEE011) in Advanced ER+ (HER2 Negative) Breast Cancer (NCT NCT02586675)

NCT ID: NCT02586675

Last Updated: 2022-01-21

Results Overview

400-600 mg of Ribociclib, when taken with Tamoxifen 20 mg. The Phase I portion of the study is a dose escalation to confirm the dose limiting toxicity (DLT) and the RP2D for ribociclib with Tamoxifen. DLT is defined as an adverse event or abnormal laboratory value assessed as having a reasonable possibility related to the study medication, unrelated to disease, disease progression, inter-current illness, or concomitant medications that occurs within the first 28 days of treatment (cycle 1) with LEE011 and Tamoxifen. National Cancer Institute Common Terminology Criteria for Adverse events (NCI CTCAE) version 4.03 will be used for all grading. In this study, a DLT will occur if CTCAE grade 4 neutropenia lasts more than 4 consecutive days, if CTCAE grade 3 thrombocytopenia is associated with clinically significant bleeding or if there is grade 4 thrombocytopenia.

Recruitment status

COMPLETED

Study phase

PHASE1

Target enrollment

7 participants

Primary outcome timeframe

Up to 12 months

Results posted on

2022-01-21

Participant Flow

Participants were enrolled at Moffitt Cancer Center March 2016 through September 2016. All participants were enrolled and treated on Cohort 1 (Ribociclib 400 mg PO D1-21; Tamoxifen 20 mg PO QD (1) only.

Participant milestones

Participant milestones
Measure
Tamoxifen and Ribociclib With Goserelin
Phase I dose escalation followed by Phase Ib dose expansion. Tamoxifen and Ribociclib, with Goserelin added for premenopausal or peri-menopausal participants. Ribociclib: Capsules/Tablets for oral use 400 mg OR 600 mg Days 1-21 of each 28 day cycle or daily. Tamoxifen: Tablets for oral use 20 mg daily (all days of every cycle without interruption). Goserelin: Subcutaneous injection 3.6 mg Day 1 of each 28 day cycle. Tamoxifen: Tamoxifen will be taken orally once daily on a continuous daily schedule (e.g., days 1-28 of each 28 day cycle). Ribociclib: Ribociclib (LEE011) will be taken orally once daily on days 1-21 of each 28 day cycle. Days 22-28 will be a "rest" period from dosing with Ribociclib. In the continuous cohort, 400 mg ribociclib will be given daily (QD). Goserelin: Goserelin will be given as an injectable subcutaneous implant on day 1 of every 28 day cycle. This will be given in pre-menopausal and peri-menopausal women.
Overall Study
STARTED
7
Overall Study
COMPLETED
7
Overall Study
NOT COMPLETED
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

TEEL Study- Phase 1 Tamoxifen and Ribociclib (LEE011) in Advanced ER+ (HER2 Negative) Breast Cancer

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Tamoxifen and Ribociclib With Goserelin
n=7 Participants
Phase I dose escalation followed by Phase Ib dose expansion.
Age, Continuous
54 years
STANDARD_DEVIATION 13.31 • n=93 Participants
Sex: Female, Male
Female
7 Participants
n=93 Participants
Sex: Female, Male
Male
0 Participants
n=93 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=93 Participants
Race (NIH/OMB)
Asian
0 Participants
n=93 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=93 Participants
Race (NIH/OMB)
Black or African American
1 Participants
n=93 Participants
Race (NIH/OMB)
White
6 Participants
n=93 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=93 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=93 Participants
Region of Enrollment
United States
7 participants
n=93 Participants

PRIMARY outcome

Timeframe: Up to 12 months

Population: All participants

400-600 mg of Ribociclib, when taken with Tamoxifen 20 mg. The Phase I portion of the study is a dose escalation to confirm the dose limiting toxicity (DLT) and the RP2D for ribociclib with Tamoxifen. DLT is defined as an adverse event or abnormal laboratory value assessed as having a reasonable possibility related to the study medication, unrelated to disease, disease progression, inter-current illness, or concomitant medications that occurs within the first 28 days of treatment (cycle 1) with LEE011 and Tamoxifen. National Cancer Institute Common Terminology Criteria for Adverse events (NCI CTCAE) version 4.03 will be used for all grading. In this study, a DLT will occur if CTCAE grade 4 neutropenia lasts more than 4 consecutive days, if CTCAE grade 3 thrombocytopenia is associated with clinically significant bleeding or if there is grade 4 thrombocytopenia.

Outcome measures

Outcome measures
Measure
Tamoxifen and Ribociclib With Goserelin
n=7 Participants
Phase I dose escalation followed by Phase Ib dose expansion.
Recommended Phase II Dose (RP2D)
400 dose in mg

SECONDARY outcome

Timeframe: 6 months

Population: All participants.

Occurrence of Progression Survival at 6 months. PFS: On study date to date of progression or the same as overall survival time if not progressed. Progressive Disease (PD): At least a 20% increase in the sum of the longest diameter (LD) of target lesions, taking as reference the smallest sum LD recorded since the treatment started or the appearance of one or more new lesions.

Outcome measures

Outcome measures
Measure
Tamoxifen and Ribociclib With Goserelin
n=7 Participants
Phase I dose escalation followed by Phase Ib dose expansion.
Progression-free Survival (PFS) at Six Months
57.1 percentage of participants
Interval 17.2 to 83.7

SECONDARY outcome

Timeframe: 6 months

Population: All participants.

Occurrence of Overall Survival at 6 months. OS: On study date to expired date or last visit date if not deceased.

Outcome measures

Outcome measures
Measure
Tamoxifen and Ribociclib With Goserelin
n=7 Participants
Phase I dose escalation followed by Phase Ib dose expansion.
Overall Survival (OS) at Six Months
83.3 percentage of participants
Interval 27.3 to 97.5

Adverse Events

Tamoxifen and Ribociclib With Goserelin

Serious events: 2 serious events
Other events: 7 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Tamoxifen and Ribociclib With Goserelin
n=7 participants at risk
All participants were enrolled and treated on Cohort 1 (Ribociclib 400 mg PO D1-21; Tamoxifen 20 mg PO QD (1) only.
Gastrointestinal disorders
Gastrointestinal - Other, Gastroenteritis
14.3%
1/7 • Number of events 1 • 1 year, 2 months
General disorders
Fatigue
14.3%
1/7 • Number of events 1 • 1 year, 2 months
Nervous system disorders
Syncope
14.3%
1/7 • Number of events 3 • 1 year, 2 months
Vascular disorders
Thromboembolic event
14.3%
1/7 • Number of events 1 • 1 year, 2 months

Other adverse events

Other adverse events
Measure
Tamoxifen and Ribociclib With Goserelin
n=7 participants at risk
All participants were enrolled and treated on Cohort 1 (Ribociclib 400 mg PO D1-21; Tamoxifen 20 mg PO QD (1) only.
Investigations
Neutrophil count decreased
57.1%
4/7 • Number of events 9 • 1 year, 2 months
Investigations
White blood cell decreased
57.1%
4/7 • Number of events 8 • 1 year, 2 months
Investigations
Alanine aminotransferase increased
42.9%
3/7 • Number of events 9 • 1 year, 2 months
Investigations
Aspartate aminotransferase increased
42.9%
3/7 • Number of events 9 • 1 year, 2 months
Investigations
Platelet count decreased
42.9%
3/7 • Number of events 3 • 1 year, 2 months
Investigations
Electrocardiogram QT corrected interval prolonged
28.6%
2/7 • Number of events 5 • 1 year, 2 months
Investigations
Alkaline phosphatase increased
14.3%
1/7 • Number of events 1 • 1 year, 2 months
Investigations
Cholesterol high
14.3%
1/7 • Number of events 1 • 1 year, 2 months
Investigations
Creatinine increased
14.3%
1/7 • Number of events 1 • 1 year, 2 months
Investigations
Weight loss
14.3%
1/7 • Number of events 1 • 1 year, 2 months
Metabolism and nutrition disorders
Dehydration
42.9%
3/7 • Number of events 4 • 1 year, 2 months
Metabolism and nutrition disorders
Hypomagnesemia
28.6%
2/7 • Number of events 2 • 1 year, 2 months
Metabolism and nutrition disorders
Anorexia
14.3%
1/7 • Number of events 1 • 1 year, 2 months
Metabolism and nutrition disorders
Hypokalemia
14.3%
1/7 • Number of events 2 • 1 year, 2 months
Metabolism and nutrition disorders
Hypophosphatemia
14.3%
1/7 • Number of events 3 • 1 year, 2 months
Nervous system disorders
Dizziness
28.6%
2/7 • Number of events 2 • 1 year, 2 months
Nervous system disorders
Dysgeusia
14.3%
1/7 • Number of events 1 • 1 year, 2 months
Nervous system disorders
Neuralgia
14.3%
1/7 • Number of events 1 • 1 year, 2 months
Nervous system disorders
Syncope
14.3%
1/7 • Number of events 1 • 1 year, 2 months
Gastrointestinal disorders
Vomiting
28.6%
2/7 • Number of events 2 • 1 year, 2 months
Gastrointestinal disorders
Constipation
14.3%
1/7 • Number of events 1 • 1 year, 2 months
Gastrointestinal disorders
Diarrhea
14.3%
1/7 • Number of events 2 • 1 year, 2 months
Gastrointestinal disorders
Dyspepsia
14.3%
1/7 • Number of events 1 • 1 year, 2 months
Gastrointestinal disorders
Flatulence
14.3%
1/7 • Number of events 1 • 1 year, 2 months
Gastrointestinal disorders
Mucositis oral
14.3%
1/7 • Number of events 1 • 1 year, 2 months
General disorders
Pain
28.6%
2/7 • Number of events 2 • 1 year, 2 months
General disorders
Non-cardiac chest pain
14.3%
1/7 • Number of events 1 • 1 year, 2 months
Infections and infestations
Otitis media
14.3%
1/7 • Number of events 1 • 1 year, 2 months
Infections and infestations
Sinusitis
14.3%
1/7 • Number of events 1 • 1 year, 2 months
Infections and infestations
Upper respiratory infection
14.3%
1/7 • Number of events 2 • 1 year, 2 months
Infections and infestations
Urinary tract infection
14.3%
1/7 • Number of events 1 • 1 year, 2 months
Musculoskeletal and connective tissue disorders
Arthralgia
14.3%
1/7 • Number of events 1 • 1 year, 2 months
Musculoskeletal and connective tissue disorders
Back pain
14.3%
1/7 • Number of events 1 • 1 year, 2 months
Musculoskeletal and connective tissue disorders
Bone pain
14.3%
1/7 • Number of events 1 • 1 year, 2 months
Musculoskeletal and connective tissue disorders
Flank pain
14.3%
1/7 • Number of events 1 • 1 year, 2 months
Musculoskeletal and connective tissue disorders
Generalized muscle weakness
14.3%
1/7 • Number of events 2 • 1 year, 2 months
Musculoskeletal and connective tissue disorders
Myalgia
14.3%
1/7 • Number of events 1 • 1 year, 2 months
Cardiac disorders
Cardiac disorders - Other, T Wave Inversion, Q Wave in II, on EKG
14.3%
1/7 • Number of events 1 • 1 year, 2 months
Cardiac disorders
Chest pain - cardiac
14.3%
1/7 • Number of events 1 • 1 year, 2 months
Cardiac disorders
Sinus bradycardia
14.3%
1/7 • Number of events 1 • 1 year, 2 months
Respiratory, thoracic and mediastinal disorders
Allergic rhinitis
14.3%
1/7 • Number of events 1 • 1 year, 2 months
Respiratory, thoracic and mediastinal disorders
Cough
14.3%
1/7 • Number of events 1 • 1 year, 2 months
Respiratory, thoracic and mediastinal disorders
Dyspnea
14.3%
1/7 • Number of events 1 • 1 year, 2 months
Respiratory, thoracic and mediastinal disorders
Laryngeal inflammation
14.3%
1/7 • Number of events 1 • 1 year, 2 months
Respiratory, thoracic and mediastinal disorders
Sore throat
14.3%
1/7 • Number of events 1 • 1 year, 2 months
Blood and lymphatic system disorders
Anemia
14.3%
1/7 • Number of events 1 • 1 year, 2 months
Eye disorders
Eyelid function disorder
14.3%
1/7 • Number of events 1 • 1 year, 2 months
Injury, poisoning and procedural complications
Fall
14.3%
1/7 • Number of events 1 • 1 year, 2 months
Injury, poisoning and procedural complications
Fracture
14.3%
1/7 • Number of events 1 • 1 year, 2 months
Renal and urinary disorders
Acute kidney injury
14.3%
1/7 • Number of events 1 • 1 year, 2 months
Vascular disorders
Hypotension
14.3%
1/7 • Number of events 4 • 1 year, 2 months
Vascular disorders
Lymphedema
14.3%
1/7 • Number of events 2 • 1 year, 2 months

Additional Information

Dr. Hatem Soliman

H. Lee Moffitt Cancer Center and Research Institute

Phone: 813-745-4933

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place