Trial Outcomes & Findings for A Clinical Trial to Assess the Efficacy and Safety of MK-0653C in Japanese Participants With Hypercholesterolemia (MK-0653C-383) (NCT NCT02550288)

NCT ID: NCT02550288

Last Updated: 2024-05-16

Results Overview

Participants had LDL-C levels assessed at baseline and after 12 weeks of study drug administration. The change from baseline was calculated.

Recruitment status

COMPLETED

Study phase

PHASE3

Target enrollment

309 participants

Primary outcome timeframe

Baseline and Week 12

Results posted on

2024-05-16

Participant Flow

Study consisted of screening, a 2-week placebo run-in and a 12-week treatment period.

Participant milestones

Participant milestones
Measure
Ezetimibe 10 mg
1 ezetimide 10 mg tablet, 2 atorvastatin 10 mg placebo capsules orally once daily for 12 weeks.
Atorvastatin 10 mg
1 atorvastatin 10 mg capsule, 1 ezetimide 10 mg placebo tablet, and 1 atorvastatin 10 mg placebo capsule orally once daily for 12 weeks.
Atorvastatin 20 mg
2 atorvastatin 10 mg capsules and 1 ezetimide 10 mg placebo tablet orally, once daily for 12 weeks.
Ezetimibe 10 mg + Atorvastatin 10 mg
1 Ezetimibe 10 mg tablet, 1 atorvastatin 10 mg capsule and 1 atorvastatin 10 mg placebo capsule orally, once daily for 12 weeks
Ezetimibe 10 mg + Atorvastatin 20 mg
1 Ezetimibe 10 mg tablet and 2 atorvastatin 10 mg capsules orally, once daily for 12 weeks
Overall Study
STARTED
35
68
69
68
69
Overall Study
COMPLETED
33
65
68
65
66
Overall Study
NOT COMPLETED
2
3
1
3
3

Reasons for withdrawal

Reasons for withdrawal
Measure
Ezetimibe 10 mg
1 ezetimide 10 mg tablet, 2 atorvastatin 10 mg placebo capsules orally once daily for 12 weeks.
Atorvastatin 10 mg
1 atorvastatin 10 mg capsule, 1 ezetimide 10 mg placebo tablet, and 1 atorvastatin 10 mg placebo capsule orally once daily for 12 weeks.
Atorvastatin 20 mg
2 atorvastatin 10 mg capsules and 1 ezetimide 10 mg placebo tablet orally, once daily for 12 weeks.
Ezetimibe 10 mg + Atorvastatin 10 mg
1 Ezetimibe 10 mg tablet, 1 atorvastatin 10 mg capsule and 1 atorvastatin 10 mg placebo capsule orally, once daily for 12 weeks
Ezetimibe 10 mg + Atorvastatin 20 mg
1 Ezetimibe 10 mg tablet and 2 atorvastatin 10 mg capsules orally, once daily for 12 weeks
Overall Study
Adverse Event
0
1
0
0
0
Overall Study
Physician Decision
0
0
0
1
0
Overall Study
Protocol Violation
2
2
1
0
3
Overall Study
Participant moved
0
0
0
1
0
Overall Study
Withdrawal by Subject
0
0
0
1
0

Baseline Characteristics

A Clinical Trial to Assess the Efficacy and Safety of MK-0653C in Japanese Participants With Hypercholesterolemia (MK-0653C-383)

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Ezetimibe 10 mg
n=35 Participants
1 ezetimide 10 mg tablet, 2 atorvastatin 10 mg placebo capsules orally once daily for 12 weeks.
Atorvastatin 10 mg
n=68 Participants
1 atorvastatin 10 mg capsule, 1 ezetimide 10 mg placebo tablet, and 1 atorvastatin 10 mg placebo capsule orally once daily for 12 weeks.
Atorvastatin 20 mg
n=69 Participants
2 atorvastatin 10 mg capsules and 1 ezetimide 10 mg placebo tablet orally, once daily for 12 weeks.
Ezetimibe 10 mg + Atorvastatin 10 mg
n=68 Participants
1 Ezetimibe 10 mg tablet, 1 atorvastatin 10 mg capsule and 1 atorvastatin 10 mg placebo capsule orally, once daily for 12 weeks
Ezetimibe 10 mg + Atorvastatin 20 mg
n=69 Participants
1 Ezetimibe 10 mg tablet and 2 atorvastatin 10 mg capsules orally, once daily for 12 weeks
Total
n=309 Participants
Total of all reporting groups
Age, Continuous
57.1 years
STANDARD_DEVIATION 9.8 • n=5 Participants
58.9 years
STANDARD_DEVIATION 8.6 • n=7 Participants
58.3 years
STANDARD_DEVIATION 10.3 • n=5 Participants
58.7 years
STANDARD_DEVIATION 10.4 • n=4 Participants
57.9 years
STANDARD_DEVIATION 11.0 • n=21 Participants
58.3 years
STANDARD_DEVIATION 10.0 • n=8 Participants
Sex: Female, Male
Female
18 Participants
n=5 Participants
34 Participants
n=7 Participants
39 Participants
n=5 Participants
34 Participants
n=4 Participants
37 Participants
n=21 Participants
162 Participants
n=8 Participants
Sex: Female, Male
Male
17 Participants
n=5 Participants
34 Participants
n=7 Participants
30 Participants
n=5 Participants
34 Participants
n=4 Participants
32 Participants
n=21 Participants
147 Participants
n=8 Participants

PRIMARY outcome

Timeframe: Baseline and Week 12

Population: All participants who received at least 1 dose of study treatment, and had a baseline observation or at least 1 post-baseline observation. One participant who received misallocated study medication during placebo run-in period was excluded from the main population for the analysis of efficacy data.

Participants had LDL-C levels assessed at baseline and after 12 weeks of study drug administration. The change from baseline was calculated.

Outcome measures

Outcome measures
Measure
Ezetimibe 10 mg
n=35 Participants
1 ezetimide 10 mg tablet, 2 atorvastatin 10 mg placebo capsules orally once daily for 12 weeks.
Atorvastatin 10 mg
n=68 Participants
1 atorvastatin 10 mg capsule, 1 ezetimide 10 mg placebo tablet, and 1 atorvastatin 10 mg placebo capsule orally once daily for 12 weeks.
Atorvastatin 20 mg
n=68 Participants
2 atorvastatin 10 mg capsules and 1 ezetimide 10 mg placebo tablet orally, once daily for 12 weeks.
Ezetimibe 10 mg + Atorvastatin 10 mg
n=68 Participants
1 Ezetimibe 10 mg tablet, 1 atorvastatin 10 mg capsule and 1 atorvastatin 10 mg placebo capsule orally, once daily for 12 weeks
Ezetimibe 10 mg + Atorvastatin 20 mg
n=69 Participants
1 Ezetimibe 10 mg tablet and 2 atorvastatin 10 mg capsules orally, once daily for 12 weeks
Percent Change From Baseline in Low-density Lipoprotein Cholesterol (LDL-C) at Week 12
-19.3 Percentage Change
Interval -22.7 to -15.8
-44.0 Percentage Change
Interval -46.5 to -41.6
-49.1 Percentage Change
Interval -51.5 to -46.7
-55.6 Percentage Change
Interval -58.0 to -53.2
-59.2 Percentage Change
Interval -61.6 to -56.8

PRIMARY outcome

Timeframe: up to 14 weeks

Population: All randomized participants who received at least 1 dose of actual study treatment.

Gastrointestinal-related AEs included all preferred terms within system organ class of Gastrointestinal Disorders except Chapped Lips and Toothache.

Outcome measures

Outcome measures
Measure
Ezetimibe 10 mg
n=35 Participants
1 ezetimide 10 mg tablet, 2 atorvastatin 10 mg placebo capsules orally once daily for 12 weeks.
Atorvastatin 10 mg
n=68 Participants
1 atorvastatin 10 mg capsule, 1 ezetimide 10 mg placebo tablet, and 1 atorvastatin 10 mg placebo capsule orally once daily for 12 weeks.
Atorvastatin 20 mg
n=69 Participants
2 atorvastatin 10 mg capsules and 1 ezetimide 10 mg placebo tablet orally, once daily for 12 weeks.
Ezetimibe 10 mg + Atorvastatin 10 mg
n=68 Participants
1 Ezetimibe 10 mg tablet, 1 atorvastatin 10 mg capsule and 1 atorvastatin 10 mg placebo capsule orally, once daily for 12 weeks
Ezetimibe 10 mg + Atorvastatin 20 mg
n=69 Participants
1 Ezetimibe 10 mg tablet and 2 atorvastatin 10 mg capsules orally, once daily for 12 weeks
Percentage of Participants Who Experience 1 or More Gastrointestinal-related Adverse Events (AEs)
5.7 Percentage of Participants
0.0 Percentage of Participants
8.7 Percentage of Participants
7.4 Percentage of Participants
7.2 Percentage of Participants

PRIMARY outcome

Timeframe: up to 14 weeks

Population: All randomized participants who received at least 1 dose of actual study treatment.

Gallbladder-related AEs included Bile Duct Obstruction, Bile Duct Stone, Bile Duct Stenosis, Biliary Colic, Cholangitis, Cholecystectomy, Cholecystitis, Cholelithiasis, Gallbladder Disorder, Gallbladder Perforation, Hepatic Pain, and Hydrocholecystis.

Outcome measures

Outcome measures
Measure
Ezetimibe 10 mg
n=35 Participants
1 ezetimide 10 mg tablet, 2 atorvastatin 10 mg placebo capsules orally once daily for 12 weeks.
Atorvastatin 10 mg
n=68 Participants
1 atorvastatin 10 mg capsule, 1 ezetimide 10 mg placebo tablet, and 1 atorvastatin 10 mg placebo capsule orally once daily for 12 weeks.
Atorvastatin 20 mg
n=69 Participants
2 atorvastatin 10 mg capsules and 1 ezetimide 10 mg placebo tablet orally, once daily for 12 weeks.
Ezetimibe 10 mg + Atorvastatin 10 mg
n=68 Participants
1 Ezetimibe 10 mg tablet, 1 atorvastatin 10 mg capsule and 1 atorvastatin 10 mg placebo capsule orally, once daily for 12 weeks
Ezetimibe 10 mg + Atorvastatin 20 mg
n=69 Participants
1 Ezetimibe 10 mg tablet and 2 atorvastatin 10 mg capsules orally, once daily for 12 weeks
Percentage of Participants Who Experience 1 or More Gallbladder-related AEs
0.0 Percentage of Participants
1.5 Percentage of Participants
0.0 Percentage of Participants
0.0 Percentage of Participants
0.0 Percentage of Participants

PRIMARY outcome

Timeframe: up to 14 weeks

Population: All randomized participants who received at least 1 dose of actual study treatment.

Allergic Reaction or Rash AEs included Allergy to Arthropod Sting, Anaphylactoid Reaction, Anaphylactic Reaction, Anaphylatic Shock, Anaphylactoid Shock, Angioedema, Conjunctivitis Allergic, Contrast Media Reaction, Dermatitis, Dermatitis Allergic, Dermatitis Atopic, Dermatitis Bullous, Dermatitis Contact, Dermatitis Psoriasiform, Drug Hypersensitivity, Eczema, Eosinophila, Erythema, Eye Allergy, Face Oedema, Hypersensitivity, Mechanical Urticaria, Palmar Erythema, Periorbital Oedema, Photodermatosis, Photosensitivity Allergic reaction, Photosensitivity Reaction, Pigmentation Disorder, Pruritus, Pruritus Generalised, Rash, Rash Erythematous, Rash Follicular, Rash Generalised, Rash Maculo-Papular, Rash Papulosquamous, Rash Pruritic, Rash Pustular, Rash Vesicular, Rhinitis, Rhinitis Allergic, Rosacea, Skin Exfoliation, Skin Disorder, Skin Hyperpigmentation, Skin Lesion, Skin Mass, Skin Ulcer, Subcutaneous Nodule, Swelling Face, Systemic Lupus Erythematosus Rash, Urticaria.

Outcome measures

Outcome measures
Measure
Ezetimibe 10 mg
n=35 Participants
1 ezetimide 10 mg tablet, 2 atorvastatin 10 mg placebo capsules orally once daily for 12 weeks.
Atorvastatin 10 mg
n=68 Participants
1 atorvastatin 10 mg capsule, 1 ezetimide 10 mg placebo tablet, and 1 atorvastatin 10 mg placebo capsule orally once daily for 12 weeks.
Atorvastatin 20 mg
n=69 Participants
2 atorvastatin 10 mg capsules and 1 ezetimide 10 mg placebo tablet orally, once daily for 12 weeks.
Ezetimibe 10 mg + Atorvastatin 10 mg
n=68 Participants
1 Ezetimibe 10 mg tablet, 1 atorvastatin 10 mg capsule and 1 atorvastatin 10 mg placebo capsule orally, once daily for 12 weeks
Ezetimibe 10 mg + Atorvastatin 20 mg
n=69 Participants
1 Ezetimibe 10 mg tablet and 2 atorvastatin 10 mg capsules orally, once daily for 12 weeks
Percentage of Participants Who Experience 1 or More Allergic Reaction or Rash AEs
0.0 Percentage of Participants
2.9 Percentage of Participants
2.9 Percentage of Participants
0.0 Percentage of Participants
1.4 Percentage of Participants

PRIMARY outcome

Timeframe: up to 14 weeks

Population: All randomized participants who received at least 1 dose of actual study treatment.

Hepatitis-related AEs included Cholestasis, Cytolytic Hepatitis, Hepatic Cyst, Hepatic Failure, Hepatic Lesion, Hepatic Necrosis, Hepatitis, Hepatitis Cholestatic, Hepatitis Fulminant, Hepatitis Infectious, Hepatocellular Injury, Hepatomegaly, Jaundice, Jaundice Cholestatic.

Outcome measures

Outcome measures
Measure
Ezetimibe 10 mg
n=35 Participants
1 ezetimide 10 mg tablet, 2 atorvastatin 10 mg placebo capsules orally once daily for 12 weeks.
Atorvastatin 10 mg
n=68 Participants
1 atorvastatin 10 mg capsule, 1 ezetimide 10 mg placebo tablet, and 1 atorvastatin 10 mg placebo capsule orally once daily for 12 weeks.
Atorvastatin 20 mg
n=69 Participants
2 atorvastatin 10 mg capsules and 1 ezetimide 10 mg placebo tablet orally, once daily for 12 weeks.
Ezetimibe 10 mg + Atorvastatin 10 mg
n=68 Participants
1 Ezetimibe 10 mg tablet, 1 atorvastatin 10 mg capsule and 1 atorvastatin 10 mg placebo capsule orally, once daily for 12 weeks
Ezetimibe 10 mg + Atorvastatin 20 mg
n=69 Participants
1 Ezetimibe 10 mg tablet and 2 atorvastatin 10 mg capsules orally, once daily for 12 weeks
Percentage of Participants Who Experience 1 or More Hepatitis-related AEs
0.0 Percentage of Participants
0.0 Percentage of Participants
0.0 Percentage of Participants
0.0 Percentage of Participants
0.0 Percentage of Participants

PRIMARY outcome

Timeframe: up to 12 weeks

Population: All randomized participants who received at least 1 dose of actual study treatment.

Participants had ALT levels assessed throughout the 12 week treatment period. Participants who had 2 consecutive assessments of ALT that were 3 x ULN or greater were recorded. The ALT ULN was 40 U/L.

Outcome measures

Outcome measures
Measure
Ezetimibe 10 mg
n=35 Participants
1 ezetimide 10 mg tablet, 2 atorvastatin 10 mg placebo capsules orally once daily for 12 weeks.
Atorvastatin 10 mg
n=68 Participants
1 atorvastatin 10 mg capsule, 1 ezetimide 10 mg placebo tablet, and 1 atorvastatin 10 mg placebo capsule orally once daily for 12 weeks.
Atorvastatin 20 mg
n=69 Participants
2 atorvastatin 10 mg capsules and 1 ezetimide 10 mg placebo tablet orally, once daily for 12 weeks.
Ezetimibe 10 mg + Atorvastatin 10 mg
n=68 Participants
1 Ezetimibe 10 mg tablet, 1 atorvastatin 10 mg capsule and 1 atorvastatin 10 mg placebo capsule orally, once daily for 12 weeks
Ezetimibe 10 mg + Atorvastatin 20 mg
n=69 Participants
1 Ezetimibe 10 mg tablet and 2 atorvastatin 10 mg capsules orally, once daily for 12 weeks
Percentage of Participants Who Experience Consecutive Elevations in Alanine Aminotransferase (ALT) ≥3 Times Upper Limit of Normal (ULN)
0.0 Percentage of Participants
0.0 Percentage of Participants
0.0 Percentage of Participants
1.5 Percentage of Participants
0.0 Percentage of Participants

PRIMARY outcome

Timeframe: up to 12 weeks

Population: All randomized participants who received at least 1 dose of actual study treatment.

Participants had AST levels assessed throughout the 12 week treatment period. Participants who had 2 consecutive assessments of AST that were 3 x ULN or greater were recorded. The AST ULN was 40 U/L.

Outcome measures

Outcome measures
Measure
Ezetimibe 10 mg
n=35 Participants
1 ezetimide 10 mg tablet, 2 atorvastatin 10 mg placebo capsules orally once daily for 12 weeks.
Atorvastatin 10 mg
n=68 Participants
1 atorvastatin 10 mg capsule, 1 ezetimide 10 mg placebo tablet, and 1 atorvastatin 10 mg placebo capsule orally once daily for 12 weeks.
Atorvastatin 20 mg
n=69 Participants
2 atorvastatin 10 mg capsules and 1 ezetimide 10 mg placebo tablet orally, once daily for 12 weeks.
Ezetimibe 10 mg + Atorvastatin 10 mg
n=68 Participants
1 Ezetimibe 10 mg tablet, 1 atorvastatin 10 mg capsule and 1 atorvastatin 10 mg placebo capsule orally, once daily for 12 weeks
Ezetimibe 10 mg + Atorvastatin 20 mg
n=69 Participants
1 Ezetimibe 10 mg tablet and 2 atorvastatin 10 mg capsules orally, once daily for 12 weeks
Percentage of Participants Who Experience Consecutive Elevations in Aspartate Aminotransferase (AST) ≥3 Times ULN
0.0 Percentage of Participants
0.0 Percentage of Participants
0.0 Percentage of Participants
1.5 Percentage of Participants
0.0 Percentage of Participants

PRIMARY outcome

Timeframe: up to 12 weeks

Population: All randomized participants who received at least 1 dose of actual study treatment.

Participants had ALT and AST levels assessed throughout the 12 week treatment period. Participants who had 2 consecutive assessments of ALT and/or AST that were 3 x ULN or greater were recorded. The ALT and AST ULNs were 40 U/L.

Outcome measures

Outcome measures
Measure
Ezetimibe 10 mg
n=35 Participants
1 ezetimide 10 mg tablet, 2 atorvastatin 10 mg placebo capsules orally once daily for 12 weeks.
Atorvastatin 10 mg
n=68 Participants
1 atorvastatin 10 mg capsule, 1 ezetimide 10 mg placebo tablet, and 1 atorvastatin 10 mg placebo capsule orally once daily for 12 weeks.
Atorvastatin 20 mg
n=69 Participants
2 atorvastatin 10 mg capsules and 1 ezetimide 10 mg placebo tablet orally, once daily for 12 weeks.
Ezetimibe 10 mg + Atorvastatin 10 mg
n=68 Participants
1 Ezetimibe 10 mg tablet, 1 atorvastatin 10 mg capsule and 1 atorvastatin 10 mg placebo capsule orally, once daily for 12 weeks
Ezetimibe 10 mg + Atorvastatin 20 mg
n=69 Participants
1 Ezetimibe 10 mg tablet and 2 atorvastatin 10 mg capsules orally, once daily for 12 weeks
Percentage of Participants Who Experience Consecutive Elevations in ALT and/or AST ≥3 Times ULN
0.0 Percentage of Participants
0.0 Percentage of Participants
0.0 Percentage of Participants
1.5 Percentage of Participants
0.0 Percentage of Participants

PRIMARY outcome

Timeframe: up to 12 weeks

Population: All randomized participants who received at least 1 dose of actual study treatment.

Participants had ALT levels assessed throughout the 12 week treatment period. Participants who had an assessment of ALT that was 5x ULN or greater were recorded. The ALT ULN was 40 U/L.

Outcome measures

Outcome measures
Measure
Ezetimibe 10 mg
n=35 Participants
1 ezetimide 10 mg tablet, 2 atorvastatin 10 mg placebo capsules orally once daily for 12 weeks.
Atorvastatin 10 mg
n=68 Participants
1 atorvastatin 10 mg capsule, 1 ezetimide 10 mg placebo tablet, and 1 atorvastatin 10 mg placebo capsule orally once daily for 12 weeks.
Atorvastatin 20 mg
n=69 Participants
2 atorvastatin 10 mg capsules and 1 ezetimide 10 mg placebo tablet orally, once daily for 12 weeks.
Ezetimibe 10 mg + Atorvastatin 10 mg
n=68 Participants
1 Ezetimibe 10 mg tablet, 1 atorvastatin 10 mg capsule and 1 atorvastatin 10 mg placebo capsule orally, once daily for 12 weeks
Ezetimibe 10 mg + Atorvastatin 20 mg
n=69 Participants
1 Ezetimibe 10 mg tablet and 2 atorvastatin 10 mg capsules orally, once daily for 12 weeks
Percentage of Participants Who Experience Consecutive Elevations in ALT ≥5 Times ULN
0.0 Percentage of Participants
0.0 Percentage of Participants
0.0 Percentage of Participants
1.5 Percentage of Participants
0.0 Percentage of Participants

PRIMARY outcome

Timeframe: up to 12 weeks

Population: All randomized participants who received at least 1 dose of actual study treatment.

Participants had AST levels assessed throughout the 12 week treatment period. Participants who had an assessment of AST that was 5x ULN or greater were recorded. AST ULN was 40 U/L.

Outcome measures

Outcome measures
Measure
Ezetimibe 10 mg
n=35 Participants
1 ezetimide 10 mg tablet, 2 atorvastatin 10 mg placebo capsules orally once daily for 12 weeks.
Atorvastatin 10 mg
n=68 Participants
1 atorvastatin 10 mg capsule, 1 ezetimide 10 mg placebo tablet, and 1 atorvastatin 10 mg placebo capsule orally once daily for 12 weeks.
Atorvastatin 20 mg
n=69 Participants
2 atorvastatin 10 mg capsules and 1 ezetimide 10 mg placebo tablet orally, once daily for 12 weeks.
Ezetimibe 10 mg + Atorvastatin 10 mg
n=69 Participants
1 Ezetimibe 10 mg tablet, 1 atorvastatin 10 mg capsule and 1 atorvastatin 10 mg placebo capsule orally, once daily for 12 weeks
Ezetimibe 10 mg + Atorvastatin 20 mg
n=69 Participants
1 Ezetimibe 10 mg tablet and 2 atorvastatin 10 mg capsules orally, once daily for 12 weeks
Percentage of Participants Who Experience Consecutive Elevations in AST ≥5 Times ULN
0.0 Percentage of Participants
0.0 Percentage of Participants
0.0 Percentage of Participants
1.5 Percentage of Participants
0.0 Percentage of Participants

PRIMARY outcome

Timeframe: up to 12 weeks

Population: All randomized participants who received at least 1 dose of actual study treatment.

Participants had ALT and AST levels assessed throughout the 12 week treatment period. Participants who had 2 consecutive assessments of ALT and/or AST that were 5 x ULN or greater were recorded. The ALT and AST ULNs were 40 U/L.

Outcome measures

Outcome measures
Measure
Ezetimibe 10 mg
n=35 Participants
1 ezetimide 10 mg tablet, 2 atorvastatin 10 mg placebo capsules orally once daily for 12 weeks.
Atorvastatin 10 mg
n=68 Participants
1 atorvastatin 10 mg capsule, 1 ezetimide 10 mg placebo tablet, and 1 atorvastatin 10 mg placebo capsule orally once daily for 12 weeks.
Atorvastatin 20 mg
n=69 Participants
2 atorvastatin 10 mg capsules and 1 ezetimide 10 mg placebo tablet orally, once daily for 12 weeks.
Ezetimibe 10 mg + Atorvastatin 10 mg
n=68 Participants
1 Ezetimibe 10 mg tablet, 1 atorvastatin 10 mg capsule and 1 atorvastatin 10 mg placebo capsule orally, once daily for 12 weeks
Ezetimibe 10 mg + Atorvastatin 20 mg
n=69 Participants
1 Ezetimibe 10 mg tablet and 2 atorvastatin 10 mg capsules orally, once daily for 12 weeks
Percentage of Participants Who Have Consecutive Elevations in ALT and/or AST ≥5 Times ULN
0.0 Percentage of Participants
0.0 Percentage of Participants
0.0 Percentage of Participants
1.5 Percentage of Participants
0.0 Percentage of Participants

PRIMARY outcome

Timeframe: up to 12 weeks

Population: All randomized participants who received at least 1 dose of actual study treatment.

Participants had ALT levels assessed throughout the 12 week treatment period. Participants who had an assessment of ALT that was 10x ULN or greater were recorded. The ALT ULN was 40 U/L.

Outcome measures

Outcome measures
Measure
Ezetimibe 10 mg
n=35 Participants
1 ezetimide 10 mg tablet, 2 atorvastatin 10 mg placebo capsules orally once daily for 12 weeks.
Atorvastatin 10 mg
n=68 Participants
1 atorvastatin 10 mg capsule, 1 ezetimide 10 mg placebo tablet, and 1 atorvastatin 10 mg placebo capsule orally once daily for 12 weeks.
Atorvastatin 20 mg
n=69 Participants
2 atorvastatin 10 mg capsules and 1 ezetimide 10 mg placebo tablet orally, once daily for 12 weeks.
Ezetimibe 10 mg + Atorvastatin 10 mg
n=68 Participants
1 Ezetimibe 10 mg tablet, 1 atorvastatin 10 mg capsule and 1 atorvastatin 10 mg placebo capsule orally, once daily for 12 weeks
Ezetimibe 10 mg + Atorvastatin 20 mg
n=69 Participants
1 Ezetimibe 10 mg tablet and 2 atorvastatin 10 mg capsules orally, once daily for 12 weeks
Percentage of Participants Who Experience Consecutive Elevations in ALT ≥10 Times ULN
0.0 Percentage of Participants
0.0 Percentage of Participants
0.0 Percentage of Participants
0.0 Percentage of Participants
0.0 Percentage of Participants

PRIMARY outcome

Timeframe: up to 12 weeks

Population: All randomized participants who received at least 1 dose of actual study treatment.

Participants had AST levels assessed throughout the 12 week treatment period. Participants who had 2 consecutive assessments of AST that were 10x ULN or greater were recorded. The AST ULN was 40 U/L.

Outcome measures

Outcome measures
Measure
Ezetimibe 10 mg
n=35 Participants
1 ezetimide 10 mg tablet, 2 atorvastatin 10 mg placebo capsules orally once daily for 12 weeks.
Atorvastatin 10 mg
n=68 Participants
1 atorvastatin 10 mg capsule, 1 ezetimide 10 mg placebo tablet, and 1 atorvastatin 10 mg placebo capsule orally once daily for 12 weeks.
Atorvastatin 20 mg
n=69 Participants
2 atorvastatin 10 mg capsules and 1 ezetimide 10 mg placebo tablet orally, once daily for 12 weeks.
Ezetimibe 10 mg + Atorvastatin 10 mg
n=68 Participants
1 Ezetimibe 10 mg tablet, 1 atorvastatin 10 mg capsule and 1 atorvastatin 10 mg placebo capsule orally, once daily for 12 weeks
Ezetimibe 10 mg + Atorvastatin 20 mg
n=69 Participants
1 Ezetimibe 10 mg tablet and 2 atorvastatin 10 mg capsules orally, once daily for 12 weeks
Percentage of Participants Who Experience Consecutive Elevations in AST ≥10 Times ULN
0.0 Percentage of Participants
0.0 Percentage of Participants
0.0 Percentage of Participants
1.5 Percentage of Participants
0.0 Percentage of Participants

PRIMARY outcome

Timeframe: up to 12 weeks

Population: All randomized participants who received at least 1 dose of actual study treatment.

Participants had ALT and AST levels assessed throughout the 12 week treatment period. Participants who had 2 consecutive assessments of ALT and/or AST that were 10x ULN or greater were recorded. The ALT and AST ULNs were 40 U/L.

Outcome measures

Outcome measures
Measure
Ezetimibe 10 mg
n=35 Participants
1 ezetimide 10 mg tablet, 2 atorvastatin 10 mg placebo capsules orally once daily for 12 weeks.
Atorvastatin 10 mg
n=68 Participants
1 atorvastatin 10 mg capsule, 1 ezetimide 10 mg placebo tablet, and 1 atorvastatin 10 mg placebo capsule orally once daily for 12 weeks.
Atorvastatin 20 mg
n=69 Participants
2 atorvastatin 10 mg capsules and 1 ezetimide 10 mg placebo tablet orally, once daily for 12 weeks.
Ezetimibe 10 mg + Atorvastatin 10 mg
n=69 Participants
1 Ezetimibe 10 mg tablet, 1 atorvastatin 10 mg capsule and 1 atorvastatin 10 mg placebo capsule orally, once daily for 12 weeks
Ezetimibe 10 mg + Atorvastatin 20 mg
n=69 Participants
1 Ezetimibe 10 mg tablet and 2 atorvastatin 10 mg capsules orally, once daily for 12 weeks
Percentage of Participants Who Have Consecutive Elevations in ALT and/or AST ≥10 Times ULN
0.0 Percentage of Participants
0.0 Percentage of Participants
0.0 Percentage of Participants
1.5 Percentage of Participants
0.0 Percentage of Participants

PRIMARY outcome

Timeframe: up to 12 weeks

Population: All randomized participants who received at least 1 dose of actual study treatment.

Percentage of Participants with Potential Hy's Law Condition (defined as serum ALT or serum AST elevations \>3xULN, with serum alkaline phosphatase \<2xULN and total bilirubin (TBL) ≥2xULN) was summarized. The ALT and AST ULNs were 40 U/L. The ULN for alkaline phosphatase was 359 IU/L and the ULN for total bilirubin was 1.2 mg/dL.

Outcome measures

Outcome measures
Measure
Ezetimibe 10 mg
n=35 Participants
1 ezetimide 10 mg tablet, 2 atorvastatin 10 mg placebo capsules orally once daily for 12 weeks.
Atorvastatin 10 mg
n=68 Participants
1 atorvastatin 10 mg capsule, 1 ezetimide 10 mg placebo tablet, and 1 atorvastatin 10 mg placebo capsule orally once daily for 12 weeks.
Atorvastatin 20 mg
n=69 Participants
2 atorvastatin 10 mg capsules and 1 ezetimide 10 mg placebo tablet orally, once daily for 12 weeks.
Ezetimibe 10 mg + Atorvastatin 10 mg
n=68 Participants
1 Ezetimibe 10 mg tablet, 1 atorvastatin 10 mg capsule and 1 atorvastatin 10 mg placebo capsule orally, once daily for 12 weeks
Ezetimibe 10 mg + Atorvastatin 20 mg
n=69 Participants
1 Ezetimibe 10 mg tablet and 2 atorvastatin 10 mg capsules orally, once daily for 12 weeks
Percentage of Participants With Potential Hy's Law Condition
0.0 Percentage of Participants
0.0 Percentage of Participants
0.0 Percentage of Participants
0.0 Percentage of Participants
0.0 Percentage of Participants

PRIMARY outcome

Timeframe: up to 12 weeks

Population: All randomized participants who received at least 1 dose of actual study treatment.

Participants had creatine phosphokinase (CK) levels assessed throughout the 12 week treatment period. Participants who had any CK level that was ≥10 x ULN were recorded. The CK ULNs for males and females were 287 IU/L and 163 IU/L, respectively.

Outcome measures

Outcome measures
Measure
Ezetimibe 10 mg
n=35 Participants
1 ezetimide 10 mg tablet, 2 atorvastatin 10 mg placebo capsules orally once daily for 12 weeks.
Atorvastatin 10 mg
n=68 Participants
1 atorvastatin 10 mg capsule, 1 ezetimide 10 mg placebo tablet, and 1 atorvastatin 10 mg placebo capsule orally once daily for 12 weeks.
Atorvastatin 20 mg
n=69 Participants
2 atorvastatin 10 mg capsules and 1 ezetimide 10 mg placebo tablet orally, once daily for 12 weeks.
Ezetimibe 10 mg + Atorvastatin 10 mg
n=68 Participants
1 Ezetimibe 10 mg tablet, 1 atorvastatin 10 mg capsule and 1 atorvastatin 10 mg placebo capsule orally, once daily for 12 weeks
Ezetimibe 10 mg + Atorvastatin 20 mg
n=69 Participants
1 Ezetimibe 10 mg tablet and 2 atorvastatin 10 mg capsules orally, once daily for 12 weeks
Percentage of Participants Who Have Elevations in Creatine Kinase (CK) ≥10xULN
0.0 Percentage of Participants
0.0 Percentage of Participants
1.4 Percentage of Participants
0.0 Percentage of Participants
0.0 Percentage of Participants

PRIMARY outcome

Timeframe: up to 12 weeks

Population: All randomized participants who received at least 1 dose of actual study treatment.

Participants had CK levels assessed throughout the 12 week treatment period. Participants who had any CK level that was ≥10 x ULN and had associated muscle symptoms present within +/- 7 days were recorded. The CK ULNs for males and females were 287 IU/L and 163 IU/L, respectively.

Outcome measures

Outcome measures
Measure
Ezetimibe 10 mg
n=35 Participants
1 ezetimide 10 mg tablet, 2 atorvastatin 10 mg placebo capsules orally once daily for 12 weeks.
Atorvastatin 10 mg
n=68 Participants
1 atorvastatin 10 mg capsule, 1 ezetimide 10 mg placebo tablet, and 1 atorvastatin 10 mg placebo capsule orally once daily for 12 weeks.
Atorvastatin 20 mg
n=69 Participants
2 atorvastatin 10 mg capsules and 1 ezetimide 10 mg placebo tablet orally, once daily for 12 weeks.
Ezetimibe 10 mg + Atorvastatin 10 mg
n=68 Participants
1 Ezetimibe 10 mg tablet, 1 atorvastatin 10 mg capsule and 1 atorvastatin 10 mg placebo capsule orally, once daily for 12 weeks
Ezetimibe 10 mg + Atorvastatin 20 mg
n=69 Participants
1 Ezetimibe 10 mg tablet and 2 atorvastatin 10 mg capsules orally, once daily for 12 weeks
Percentage of Participants Who Have Elevations in CK ≥10xULN With Muscle Symptoms
0.0 Percentage of Participants
0.0 Percentage of Participants
0.0 Percentage of Participants
0.0 Percentage of Participants
0.0 Percentage of Participants

PRIMARY outcome

Timeframe: up to 12 weeks

Population: All randomized participants who received at least 1 dose of actual study treatment.

Participants had CK levels assessed throughout the 12 week treatment period. Participants who had any CK level that was ≥10 x ULN and had associated muscle symptoms present within +/- 7 days that were reported as at least possibly-related to study drug were recorded. The CK ULNs for males and females were 287 IU/L and 163 IU/L, respectively.

Outcome measures

Outcome measures
Measure
Ezetimibe 10 mg
n=35 Participants
1 ezetimide 10 mg tablet, 2 atorvastatin 10 mg placebo capsules orally once daily for 12 weeks.
Atorvastatin 10 mg
n=68 Participants
1 atorvastatin 10 mg capsule, 1 ezetimide 10 mg placebo tablet, and 1 atorvastatin 10 mg placebo capsule orally once daily for 12 weeks.
Atorvastatin 20 mg
n=69 Participants
2 atorvastatin 10 mg capsules and 1 ezetimide 10 mg placebo tablet orally, once daily for 12 weeks.
Ezetimibe 10 mg + Atorvastatin 10 mg
n=68 Participants
1 Ezetimibe 10 mg tablet, 1 atorvastatin 10 mg capsule and 1 atorvastatin 10 mg placebo capsule orally, once daily for 12 weeks
Ezetimibe 10 mg + Atorvastatin 20 mg
n=69 Participants
1 Ezetimibe 10 mg tablet and 2 atorvastatin 10 mg capsules orally, once daily for 12 weeks
Percentage of Participants Who Have Elevations in CK ≥10xULN and Drug-Related Muscle Symptoms
0.0 Percentage of Participants
0.0 Percentage of Participants
0.0 Percentage of Participants
0.0 Percentage of Participants
0.0 Percentage of Participants

Adverse Events

Ezetimibe 10 mg

Serious events: 0 serious events
Other events: 5 other events
Deaths: 0 deaths

Atorvastatin 10 mg

Serious events: 1 serious events
Other events: 5 other events
Deaths: 0 deaths

Atorvastatin 20 mg

Serious events: 0 serious events
Other events: 9 other events
Deaths: 0 deaths

Ezetimibe 10 mg + Atorvastatin 10 mg

Serious events: 0 serious events
Other events: 11 other events
Deaths: 0 deaths

Ezetimibe 10 mg + Atorvastatin 20 mg

Serious events: 0 serious events
Other events: 16 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Ezetimibe 10 mg
n=35 participants at risk
1 ezetimide 10 mg tablet, 2 atorvastatin 10 mg placebo capsules orally once daily for 12 weeks.
Atorvastatin 10 mg
n=68 participants at risk
1 atorvastatin 10 mg capsule, 1 ezetimide 10 mg placebo tablet, and 1 atorvastatin 10 mg placebo capsule orally once daily for 12 weeks.
Atorvastatin 20 mg
n=69 participants at risk
2 atorvastatin 10 mg capsules and 1 ezetimide 10 mg placebo tablet orally, once daily for 12 weeks.
Ezetimibe 10 mg + Atorvastatin 10 mg
n=68 participants at risk
1 Ezetimibe 10 mg tablet, 1 atorvastatin 10 mg capsule and 1 atorvastatin 10 mg placebo capsule orally, once daily for 12 weeks
Ezetimibe 10 mg + Atorvastatin 20 mg
n=69 participants at risk
1 Ezetimibe 10 mg tablet and 2 atorvastatin 10 mg capsules orally, once daily for 12 weeks
Cardiac disorders
Myocardial infarction
0.00%
0/35 • up to 14 weeks
1.5%
1/68 • Number of events 1 • up to 14 weeks
0.00%
0/69 • up to 14 weeks
0.00%
0/68 • up to 14 weeks
0.00%
0/69 • up to 14 weeks

Other adverse events

Other adverse events
Measure
Ezetimibe 10 mg
n=35 participants at risk
1 ezetimide 10 mg tablet, 2 atorvastatin 10 mg placebo capsules orally once daily for 12 weeks.
Atorvastatin 10 mg
n=68 participants at risk
1 atorvastatin 10 mg capsule, 1 ezetimide 10 mg placebo tablet, and 1 atorvastatin 10 mg placebo capsule orally once daily for 12 weeks.
Atorvastatin 20 mg
n=69 participants at risk
2 atorvastatin 10 mg capsules and 1 ezetimide 10 mg placebo tablet orally, once daily for 12 weeks.
Ezetimibe 10 mg + Atorvastatin 10 mg
n=68 participants at risk
1 Ezetimibe 10 mg tablet, 1 atorvastatin 10 mg capsule and 1 atorvastatin 10 mg placebo capsule orally, once daily for 12 weeks
Ezetimibe 10 mg + Atorvastatin 20 mg
n=69 participants at risk
1 Ezetimibe 10 mg tablet and 2 atorvastatin 10 mg capsules orally, once daily for 12 weeks
Infections and infestations
Nasopharyngitis
14.3%
5/35 • Number of events 7 • up to 14 weeks
5.9%
4/68 • Number of events 4 • up to 14 weeks
11.6%
8/69 • Number of events 8 • up to 14 weeks
14.7%
10/68 • Number of events 11 • up to 14 weeks
17.4%
12/69 • Number of events 15 • up to 14 weeks
Investigations
Alanine aminotransferase increased
0.00%
0/35 • up to 14 weeks
1.5%
1/68 • Number of events 1 • up to 14 weeks
1.4%
1/69 • Number of events 1 • up to 14 weeks
1.5%
1/68 • Number of events 1 • up to 14 weeks
5.8%
4/69 • Number of events 4 • up to 14 weeks

Additional Information

Senior Vice President, Global Clinical Development

Merck Sharp & Dohme Corp.

Phone: 1-800-672-6372

Results disclosure agreements

  • Principal investigator is a sponsor employee The Sponsor must have the opportunity to review all proposed abstracts, manuscripts or presentations regarding this trial 45 days prior to submission for publication/presentation. Any information identified by the Sponsor as confidential must be deleted prior to submission; this confidentiality does not include efficacy and safety results. Sponsor review can be expedited to meet publication timelines.
  • Publication restrictions are in place

Restriction type: OTHER