Trial Outcomes & Findings for Safety, Tolerability and Efficacy of AVP-786 for the Treatment of Disinhibition (NCT NCT02534038)

NCT ID: NCT02534038

Last Updated: 2020-10-26

Results Overview

Recruitment status

TERMINATED

Study phase

PHASE2

Target enrollment

1 participants

Primary outcome timeframe

Baseline; Week 6, Week 8, and Week 14

Results posted on

2020-10-26

Participant Flow

Participant milestones

Participant milestones
Measure
AVP-786; Placebo
In Period 1, participants were randomized to receive AVP-786 (deuterated \[d6\]-dextromethorphan hydrobromide \[d6-DM\]/quinidine sulfate \[Q\]) once a day (OD) in the morning and placebo in the evening for the first 7 days of the study. From Day 8, participants received AVP-786 twice a day (BID) for 14 days. From Day 22, participants received a target dose of d6-DM 28 milligrams (mg)/Q 4.9 mg (AVP-786-28/4.9) BID for the remaining 3 weeks of Period 1. In Period 2, participants were randomized to receive matching placebo. The periods were separated by a 2-week washout period.
Placebo; AVP-786
In Period 1, participants were randomized to receive matching placebo. In Period 2, participants were randomized to receive AVP-786 OD in the morning and placebo in the evening for the first 7 days of the study. From Day 8, participants received AVP-786 BID for 14 days. From Day 22, participants received a target dose of AVP-786-28/4.9 BID for the remaining 3 weeks of Period 2. The periods were separated by a 2-week washout period.
Period 1 (6 Weeks)
STARTED
1
0
Period 1 (6 Weeks)
COMPLETED
1
0
Period 1 (6 Weeks)
NOT COMPLETED
0
0
Period 2 (6 Weeks)
STARTED
1
0
Period 2 (6 Weeks)
COMPLETED
1
0
Period 2 (6 Weeks)
NOT COMPLETED
0
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Safety, Tolerability and Efficacy of AVP-786 for the Treatment of Disinhibition

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
AVP-786; Placebo
n=1 Participants
In Period 1, participants were randomized to receive AVP-786 (deuterated \[d6\]-dextromethorphan hydrobromide \[d6-DM\]/quinidine sulfate \[Q\]) once a day (OD) in the morning and placebo in the evening for the first 7 days of the study. From Day 8, participants received AVP-786 twice a day (BID) for 14 days. From Day 22, participants received a target dose of d6-DM 28 milligrams (mg)/Q 4.9 mg (AVP-786-28/4.9) BID for the remaining 3 weeks of Period 1. In Period 2, participants were randomized to receive matching placebo. The periods were separated by a 2-week washout period.
Placebo; AVP-786
In Period 1, participants were randomized to receive matching placebo. In Period 2, participants were randomized to receive AVP-786 OD in the morning and placebo in the evening for the first 7 days of the study. From Day 8, participants received AVP-786 BID for 14 days. From Day 22, participants received a target dose of AVP-786-28/4.9 BID for the remaining 3 weeks of Period 2. The periods were separated by a 2-week washout period.
Total
n=1 Participants
Total of all reporting groups
Age, Categorical
<=18 years
0 Participants
n=5 Participants
0 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
0 Participants
n=5 Participants
0 Participants
n=5 Participants
Age, Categorical
>=65 years
1 Participants
n=5 Participants
1 Participants
n=5 Participants
Sex: Female, Male
Female
NA Participants
n=5 Participants
NA Participants
n=5 Participants
Sex: Female, Male
Male
NA Participants
n=5 Participants
NA Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
NA Participants
n=5 Participants
NA Participants
n=5 Participants
Race (NIH/OMB)
Asian
NA Participants
n=5 Participants
NA Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
NA Participants
n=5 Participants
NA Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
NA Participants
n=5 Participants
NA Participants
n=5 Participants
Race (NIH/OMB)
White
NA Participants
n=5 Participants
NA Participants
n=5 Participants
Race (NIH/OMB)
More than one race
NA Participants
n=5 Participants
NA Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
NA Participants
n=5 Participants
NA Participants
n=5 Participants

PRIMARY outcome

Timeframe: Baseline; Week 6, Week 8, and Week 14

Population: No efficacy analyses were conducted due to the limited number of participants enrolled prior to study termination (N=1). In order to protect the privacy of participants, the results of enrolled participants cannot be reported.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Baseline; Week 6, Week 8, and Week 14

Population: No efficacy analyses were conducted due to the limited number of participants enrolled prior to study termination (N=1). In order to protect the privacy of participants, the results of enrolled participants cannot be reported.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Baseline; Week 6, Week 8, and Week 14

Population: No efficacy analyses were conducted due to the limited number of participants enrolled prior to study termination (N=1). In order to protect the privacy of participants, the results of enrolled participants cannot be reported.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Baseline; Week 1, Week 3, Week 6, Week 8, Week 9, Week 11, and Week 14

Population: No efficacy analyses were conducted due to the limited number of participants enrolled prior to study termination (N=1). In order to protect the privacy of participants, the results of enrolled participants cannot be reported.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Baseline; Week 1, Week 3, Week 6, Week 8, Week 9, Week 11, and Week 14

Population: No efficacy analyses were conducted due to the limited number of participants enrolled prior to study termination (N=1). In order to protect the privacy of participants, the results of enrolled participants cannot be reported.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Baseline; Week 1, Week 3, Week 6, Week 9, Week 11, and Week 14

Population: No efficacy analyses were conducted due to the limited number of participants enrolled prior to study termination (N=1). In order to protect the privacy of participants, the results of enrolled participants cannot be reported.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Week 3, Week 6, Week 11, and Week 14

Population: No efficacy analyses were conducted due to the limited number of participants enrolled prior to study termination (N=1). In order to protect the privacy of participants, the results of enrolled participants cannot be reported.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Week 3, Week 6, Week 11, and Week 14

Population: No efficacy analyses were conducted due to the limited number of participants enrolled prior to study termination (N=1). In order to protect the privacy of participants, the results of enrolled participants cannot be reported.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Baseline; Week 6, Week 8, and Week 14

Population: No efficacy analyses were conducted due to the limited number of participants enrolled prior to study termination (N=1). In order to protect the privacy of participants, the results of enrolled participants cannot be reported.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Baseline; Week 6, Week 8, and Week 14

Population: No efficacy analyses were conducted due to the limited number of participants enrolled prior to study termination (N=1). In order to protect the privacy of participants, the results of enrolled participants cannot be reported.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Baseline; Week 6, Week 8, and Week 14

Population: No efficacy analyses were conducted due to the limited number of participants enrolled prior to study termination (N=1). In order to protect the privacy of participants, the results of enrolled participants cannot be reported.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Baseline; Week 6, Week 8, and Week 14

Population: No efficacy analyses were conducted due to the limited number of participants enrolled prior to study termination (N=1). In order to protect the privacy of participants, the results of enrolled participants cannot be reported.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Baseline; Week 6, Week 8, and Week 14

Population: No efficacy analyses were conducted due to the limited number of participants enrolled prior to study termination (N=1). In order to protect the privacy of participants, the results of enrolled participants cannot be reported.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Baseline; Week 6, Week 8, and Week 14

Population: No efficacy analyses were conducted due to the limited number of participants enrolled prior to study termination (N=1). In order to protect the privacy of participants, the results of enrolled participants cannot be reported.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Baseline; Week 6, Week 8, and Week 14

Population: No efficacy analyses were conducted due to the limited number of participants enrolled prior to study termination (N=1). In order to protect the privacy of participants, the results of enrolled participants cannot be reported.

Outcome measures

Outcome data not reported

Adverse Events

Placebo

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

AVP-786

Serious events: 0 serious events
Other events: 1 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
Placebo
n=1 participants at risk
Participants received matching placebo for 6 weeks.
AVP-786
n=1 participants at risk
Participants received AVP-786 (up to a target dose of d6-DM 28 milligrams \[mg\]/Q 4.9 mg \[AVP-786-28/4.9\] twice a day \[BID\]) for 6 weeks.
Investigations
Blood bilirubin increased
0.00%
0/1 • up to 22 weeks
100.0%
1/1 • up to 22 weeks
Investigations
Blood creatine phosphokinase increased
0.00%
0/1 • up to 22 weeks
100.0%
1/1 • up to 22 weeks

Additional Information

Sanjay Dubé, M.D.

Avanir Pharmaceuticals, Inc.

Phone: 949-389-6700

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place

Restriction type: OTHER