Safety And Efficacy Study Of Palbociclib Plus Cetuximab Versus Cetuximab To Treat Head And Neck Cancer

NCT ID: NCT02499120

Last Updated: 2023-09-08

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

125 participants

Study Classification

INTERVENTIONAL

Study Start Date

2015-09-10

Study Completion Date

2022-09-07

Brief Summary

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The purpose of this study is to determine whether the combination of palbociclib with cetuximab is superior to cetuximab in prolonging overall survival in HPV-negative, cetuximab-naive patients with recurrent/metastatic squamous cell carcinoma of the head and neck.

Detailed Description

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Conditions

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Squamous Cell Carcinoma of the Head and Neck (SCCHN)

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Palbociclib plus Cetuximab

Palbociclib, 125 mg, orally once daily (QD) with food on Day 1 to Day 21 followed by 7 days off treatment in a 28-day cycle; in combination with Cetuximab, 400 mg/m2 initial dose as a 120-minute IV infusion followed by 250 mg/m2 weekly infused over 60 minutes.

Group Type EXPERIMENTAL

palbociclib

Intervention Type DRUG

Palbociclib will be supplied as capsules containing 75 mg, 100 mg, or 125 mg equivalents of palbociclib free base. Administered with food on Day 1 to Day 21 followed by 7 days off treatment in a 28-day cycle.

Cetuximab

Intervention Type DRUG

Cetuximab injection for IV infusion will be provided in 100 mg/50 mL, single-use vials, and 200 mg/100 mL, single-use vials. In Japan, cetuximab will be provided in 100 mg/20 mL, single-use vials. Administered, 400 mg/m2 initial dose as a 120-minute IV infusion followed by 250 mg/m2 weekly infused over 60 minutes.

Placebo plus Cetuximab

Placebo orally QD with food on Day 1 to Day 21 followed by 7 days off treatment in a 28-day cycle; in combination with Cetuximab, 400 mg/m2 initial dose as a 120-minute IV infusion followed by 250 mg/m2 weekly infused over 60 minutes.

Group Type ACTIVE_COMPARATOR

Cetuximab

Intervention Type DRUG

Cetuximab injection for IV infusion will be provided in 100 mg/50 mL, single-use vials, and 200 mg/100 mL, single-use vials. In Japan, cetuximab will be provided in 100 mg/20 mL, single-use vials. Administered, 400 mg/m2 initial dose as a 120-minute IV infusion followed by 250 mg/m2 weekly infused over 60 minutes.

Placebo

Intervention Type DRUG

Placebo for palbociclib will be indistinguishable from the palbociclib capsules and will be supplied as capsules matching in size and color the various palbociclib formulations.

Administered with food on Day 1 to Day 21 followed by 7 days off treatment in a 28-day cycle.

Interventions

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palbociclib

Palbociclib will be supplied as capsules containing 75 mg, 100 mg, or 125 mg equivalents of palbociclib free base. Administered with food on Day 1 to Day 21 followed by 7 days off treatment in a 28-day cycle.

Intervention Type DRUG

Cetuximab

Cetuximab injection for IV infusion will be provided in 100 mg/50 mL, single-use vials, and 200 mg/100 mL, single-use vials. In Japan, cetuximab will be provided in 100 mg/20 mL, single-use vials. Administered, 400 mg/m2 initial dose as a 120-minute IV infusion followed by 250 mg/m2 weekly infused over 60 minutes.

Intervention Type DRUG

Placebo

Placebo for palbociclib will be indistinguishable from the palbociclib capsules and will be supplied as capsules matching in size and color the various palbociclib formulations.

Administered with food on Day 1 to Day 21 followed by 7 days off treatment in a 28-day cycle.

Intervention Type DRUG

Other Intervention Names

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IBRANCE, PD-0332991 ERBITUX

Eligibility Criteria

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Inclusion Criteria

* Histologically or cytologically confirmed squamous cell carcinoma of the oral cavity, oropharynx, hypopharynx or larynx, not amenable for salvage surgery or radiotherapy.
* Measurable disease as defined per RECIST v. 1.1. Tumor lesions previously irradiated or subjected to other locoregional therapy will only be deemed measureable if disease progression at the treated site after completion of therapy is clearly documented.
* HPV- negative SCCHN tumor as determined per institutional standard (eg, p16 IHC; multiplex nucleic acid sequence based amplification \[NASBA\] or other polymerase chain reaction \[PCR\]-based assays).
* Documented progressive disease according to RECIST v1.1 (Appendix 2) following receipt of at least 2 cycles of one platinum-containing chemotherapy regimen administered for R/M disease (min. 50 mg/m2 for cisplatin, minimum area under the curve \[AUC\] \> 4 for carboplatin).
* Availability of a tumor tissue specimen (ie, archived formalin fixed paraffin embedded tissue \[block preferred, or 15 unstained slides\]), which will be used for centralized, retrospective biomarker analysis. If archived tumor tissue is not available, then a de novo biopsy will be required for patient participation.

Exclusion Criteria

* Prior nasopharyngeal cancer, salivary gland or sinus tumors.
* More than one chemotherapeutic regimen given for R/M disease. Prior treatment with immunotherapy is allowed.
* Known active uncontrolled or symptomatic central nervous system (CNS) metastases, carcinomatous meningitis, or leptomeningeal disease as indicated by clinical symptoms, cerebral edema, and/or progressive growth. Patients with a history of CNS metastases or cord compression are eligible if they have been definitively treated with local therapy (eg, radiotherapy, stereotactic surgery) and are clinically stable off anticonvulsants and steroids for at least 4 weeks before randomization.
* Progressive disease within 3 months after completion of curatively intended treatment for locoregionally advanced SCCHN.
* Difficulty swallowing capsules.
* Prior use of cetuximab in the R/M disease treatment setting (except cetuximab during curative radiotherapy)
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Pfizer

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Pfizer CT.gov Call Center

Role: STUDY_DIRECTOR

Pfizer

Locations

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UC San Diego Medical Center - La Jolla (Thornton Hospital)

La Jolla, California, United States

Site Status

UC San Diego Moores Cancer Center

La Jolla, California, United States

Site Status

UC San Diego Medical Center- Hillcrest

San Diego, California, United States

Site Status

University Medical Center, lnc.:DBA University of Louisville Hospital

Louisville, Kentucky, United States

Site Status

Mayo Clinic

Rochester, Minnesota, United States

Site Status

Siteman Cancer Center

City of Saint Peters, Missouri, United States

Site Status

Siteman Cancer Center - West County

Creve Coeur, Missouri, United States

Site Status

Barnes-Jewish Hospital

St Louis, Missouri, United States

Site Status

Washington University School of Medicine, Siteman Cancer Center

St Louis, Missouri, United States

Site Status

Siteman Cancer Center - South County

St Louis, Missouri, United States

Site Status

University of Cincinnati Investigational Pharmacy

Cincinnati, Ohio, United States

Site Status

University of Cincinnati Medical Center

Cincinnati, Ohio, United States

Site Status

UC Health Physicians Office South

West Chester, Ohio, United States

Site Status

Henry Joyce Cancer Clinic

Nashville, Tennessee, United States

Site Status

Fakultni nemocnice Olomouc

Olomouc, , Czechia

Site Status

Fakultni nemocnice Olomouc, Lekarna

Olomouc, , Czechia

Site Status

Nemocnice Na Bulovce, Centralni laboratore Pavilon c. 8

Prague, , Czechia

Site Status

Nemocnice Na Bulovce, Lekarna, Oddeleni Centralni pripravy

Prague, , Czechia

Site Status

Nemocnice Na Bulovce, Ustav radiacni onkologie

Prague, , Czechia

Site Status

Debreceni Egyetem klinikai Koezpont Onkologiai Intezet

Debrecen, , Hungary

Site Status

Neuro CT Kft

Pécs, , Hungary

Site Status

Pecsi Tudomanyegyetem, Klinikai Kozpont, Laboratoriumi

Pécs, , Hungary

Site Status

Pecsi Tudomanyegyetem, Klinikai Kozpont,

Pécs, , Hungary

Site Status

Jasz-Nagykun-Szolnok Megyei Hetenyi Geza Korhaz-Rendelointezet,Onkologiai Kozpont

Szolnok, , Hungary

Site Status

Istituto Nazionale Tumori Napoli

Napoli, , Italy

Site Status

Aichi cancer center Central hospital

Nagoya, Aichi-ken, Japan

Site Status

National Cancer Center Hospital East

Kashiwa, Chiba, Japan

Site Status

Hokkaido University Hospital/Otolaryngology

Sapporo, Hokkaido, Japan

Site Status

Shizuoka Cancer Center

Sunto-gun, Shizuoka, Japan

Site Status

Instituto Nacional de Cancerologia

Mexico City, Mexico City, Mexico

Site Status

Hospital Universitario Dr. Jose Eleuterio Gonzalez

Monterrey, Nuevo León, Mexico

Site Status

Cirugia y Ginecobstetricia de Oaxaca S.A de C.V Hospital Reforma

Oaxaca City, Oaxaca DE Juarez, Mexico

Site Status

Diaz San Juan Noe, Imagenologia Siglo XXI San Felipe

Oaxaca City, Oaxaca DE Juarez, Mexico

Site Status

Daniel Javier Mendez Lopez Imagen y Diagnostico Medico IDM

Oaxaca City, Oaxaca DE Juarez, Mexico

Site Status

Oaxaca Site Management Organization S C

Oaxaca City, , Mexico

Site Status

Szpital Specjalistyczny w Brzozowie Podkarpacki Osrodek Onkologiczny im. ks. B. Markiewicza

Brzozów, , Poland

Site Status

Uniwersyteckie Centrum Kliniczne Klinika Onkologii i Radioterapii

Gdansk, , Poland

Site Status

Wojewodzki Szpital Specjalistyczny im. M. Kopernika w Lodzi Oddzial Chemioterapii

Lodz, , Poland

Site Status

SPZOZ MSWiA z Warminsko-Mazurskim Centrum Onkologii w Olsztynie Oddzial Kliniczny Onkologii

Olsztyn, , Poland

Site Status

SC Medisprof SRL

Cluj-Napoca, Cluj, Romania

Site Status

Centrul de Oncologie Sf. Nectarie SRL

Craiova, Dolj, Romania

Site Status

SC Oncolab SRL

Craiova, Dolj, Romania

Site Status

S.C. ONCOCENTER Oncologie Clinica S.R.L.

Timișoara, Timiș County, Romania

Site Status

Spitalul Clinic Judetean de Urgenta Sibiu, Clinica Oncologie Medicala

Sibiu, , Romania

Site Status

State Budgetary Healthcare Institution of Arkhangelsk Region

Arkhangelsk, Arkhangelskaya oblast, Russia

Site Status

State Budgetary Healthcare Institution "Oncology Center #2" of the Ministry of

Sochi, Krasnodarskiy Kray, Russia

Site Status

State Autonomous Healthcare Institution Republican Clinical Oncology Dispensary of the Ministry

Kazan', Tatarstan Republic, Russia

Site Status

FSBI "National Medical Scientific Centre of Oncology n.a.N.N.Petrov" of the MOH of Russia

Saint Petersburg, , Russia

Site Status

Institute for Oncology and Radiology of Serbia

Belgrade, , Serbia

Site Status

Military Medical Academy

Belgrade, , Serbia

Site Status

Narodny onkologicky ustav

Bratislava, , Slovakia

Site Status

POKO Poprad, s.r.o.

Poprad, , Slovakia

Site Status

Seoul National University Hospital

Seoul, , South Korea

Site Status

Asan Medical Center

Seoul, , South Korea

Site Status

Samsung Medical Center

Seoul, , South Korea

Site Status

Servicio de Oncologia

Pamplona, Navarre, Spain

Site Status

Hospital Universitario Vall d'Hebron

Barcelona, , Spain

Site Status

Hospital Universitario 12 de Octubre

Madrid, , Spain

Site Status

China Medical University Hospital

Taichung, , Taiwan

Site Status

Taichung Veterans General Hospital

Taichung, , Taiwan

Site Status

National Cheng Kung University Hospital

Tainan City, , Taiwan

Site Status

National Cheng Kung University Hospital Department of Pathology

Tainan City, , Taiwan

Site Status

Tri-Service General Hospital

Taipei, , Taiwan

Site Status

Communal Institution of Kherson Regional Council Kherson Regional Oncological Dispensary

Antonivka, Kherson Oblast, Ukraine

Site Status

Communal Institution "Chernivtsi Regional clinical oncology dispensary",

Chernivtsy, , Ukraine

Site Status

SI Dnipropetrovsk Medical Academy of MoH of Ukraine, Chair of Oncology and Medical Radiology

Dnipropetrovsk, , Ukraine

Site Status

CI Dnipropetrovsk City Multifunctional Clinical Hospital #4 of Dnipropetrovsk Regional Council

Dnipropetrovsk, , Ukraine

Site Status

Regional Clinical Hospital, Department of microsurgery of otolaryngology organs

Ivano-Frankivsk, , Ukraine

Site Status

Communal Institution "Krivorizhskiy Oncology Dispensary" of Dnipropetrovsk Regional Council,

Kryvyi Rih, , Ukraine

Site Status

Clinic of SI "Institute of Otolaryngology n.a. Prof. O.S. Kolomyichenka of NAMSU"

Kyiv, , Ukraine

Site Status

Podilskiy Regional Center of Oncology, Chemotherapy Department

Vinnytsia, , Ukraine

Site Status

Countries

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United States Czechia Hungary Italy Japan Mexico Poland Romania Russia Serbia Slovakia South Korea Spain Taiwan Ukraine

References

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Adkins DR, Lin JC, Sacco A, Ley J, Oppelt P, Vanchenko V, Komashko N, Yen CJ, Wise-Draper T, Lopez-Picazo Gonzalez J, Radulovic S, Shen Q, Thurm H, Martini JF, Hoffman J, Huang X, Melichar B, Tahara M. Palbociclib and cetuximab compared with placebo and cetuximab in platinum-resistant, cetuximab-naive, human papillomavirus-unrelated recurrent or metastatic head and neck squamous cell carcinoma: A double-blind, randomized, phase 2 trial. Oral Oncol. 2021 Apr;115:105192. doi: 10.1016/j.oraloncology.2021.105192. Epub 2021 Feb 8.

Reference Type DERIVED
PMID: 33571736 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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https://trialinfoemail.pfizer.com

To obtain contact information for a study center near you, click here.

Other Identifiers

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2015-000515-41

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

PALATINUS

Identifier Type: OTHER

Identifier Source: secondary_id

A5481044

Identifier Type: -

Identifier Source: org_study_id

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