Trial Outcomes & Findings for Mirabegron and Urinary Urgency Incontinence (NCT NCT02495389)

NCT ID: NCT02495389

Last Updated: 2020-11-13

Results Overview

Response to therapy was measured using the Patient Perception of Bladder Control (PPBC) questionnaire which measures patients' perceived bladder condition on a 6-point ordinal scale ranging from 1 (no problems at all) to 6 (many severe problems). Women reporting a PPBC score of 4 or 5 by week 12 responded to therapy. Women reporting a PPBC score of 1, 2, or 3 by week 12 did not respond to therapy.

Recruitment status

COMPLETED

Study phase

PHASE4

Target enrollment

84 participants

Primary outcome timeframe

12 weeks

Results posted on

2020-11-13

Participant Flow

Patients were recruited from January 2015 through October 2018 (46 months) from a tertiary care female pelvic medicine and reconstructive surgery practice.

Participant milestones

Participant milestones
Measure
Mirabegron
This arm comprises women who received mirabegron
Overall Study
STARTED
84
Overall Study
COMPLETED
44
Overall Study
NOT COMPLETED
40

Reasons for withdrawal

Reasons for withdrawal
Measure
Mirabegron
This arm comprises women who received mirabegron
Overall Study
Withdrawal by Subject
40

Baseline Characteristics

One participant did not report her age

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Mirabegron
n=84 Participants
This arm comprises women who received mirabegron
Age, Continuous
66.67 years
STANDARD_DEVIATION 12.46 • n=83 Participants • One participant did not report her age
Sex: Female, Male
Female
84 Participants
n=84 Participants
Sex: Female, Male
Male
0 Participants
n=84 Participants
Race/Ethnicity, Customized
Race · Caucasian or White
65 Participants
n=84 Participants
Race/Ethnicity, Customized
Race · African American or Black
11 Participants
n=84 Participants
Race/Ethnicity, Customized
Race · Asian
1 Participants
n=84 Participants
Race/Ethnicity, Customized
Race · Multiracial
1 Participants
n=84 Participants
Race/Ethnicity, Customized
Race · Other
4 Participants
n=84 Participants
Race/Ethnicity, Customized
Race · Not Reported
2 Participants
n=84 Participants
Region of Enrollment
United States
84 Participants
n=84 Participants
Hormone Replacement Therapy
Taking hormone replacement therapy
7 Participants
n=84 Participants
Hormone Replacement Therapy
Not taking hormone replacement therapy
75 Participants
n=84 Participants
Hormone Replacement Therapy
Unknown
2 Participants
n=84 Participants
Type II Diabetes Status
Diabetic
16 Participants
n=84 Participants
Type II Diabetes Status
Non-Diabetic
67 Participants
n=84 Participants
Type II Diabetes Status
Not reported
1 Participants
n=84 Participants
Smoker Status
Smoker
8 Participants
n=84 Participants
Smoker Status
Non-smoker
74 Participants
n=84 Participants
Smoker Status
Not reported
2 Participants
n=84 Participants
Hypertension Status
Hypertensive
43 Participants
n=84 Participants
Hypertension Status
Non-hypertensive
40 Participants
n=84 Participants
Hypertension Status
Not reported
1 Participants
n=84 Participants
Cardiovascular Status
Heart disease
12 Participants
n=84 Participants
Cardiovascular Status
No heart disease
71 Participants
n=84 Participants
Cardiovascular Status
Not reported
1 Participants
n=84 Participants
Chronic Obstructive Pulmonary Disease (COPD)
Positive
4 Participants
n=84 Participants
Chronic Obstructive Pulmonary Disease (COPD)
Negative
78 Participants
n=84 Participants
Chronic Obstructive Pulmonary Disease (COPD)
Not reported
2 Participants
n=84 Participants
Asthma Status
Positive
13 Participants
n=84 Participants
Asthma Status
Negative
69 Participants
n=84 Participants
Asthma Status
Not reported
2 Participants
n=84 Participants

PRIMARY outcome

Timeframe: 12 weeks

Population: This analysis comprises women who received mirabegron and completed 12 weeks of therapy

Response to therapy was measured using the Patient Perception of Bladder Control (PPBC) questionnaire which measures patients' perceived bladder condition on a 6-point ordinal scale ranging from 1 (no problems at all) to 6 (many severe problems). Women reporting a PPBC score of 4 or 5 by week 12 responded to therapy. Women reporting a PPBC score of 1, 2, or 3 by week 12 did not respond to therapy.

Outcome measures

Outcome measures
Measure
Mirabegron
n=44 Participants
This arm comprises women who received mirabegron
Response to Therapy
Responded to therapy
15 Participants
Response to Therapy
Did not respond to therapy
29 Participants

SECONDARY outcome

Timeframe: 12 weeks

Population: This analysis comprises women who received mirabegron for 12 weeks and completed the Overactive Bladder Questionnaire at baseline and after 12 weeks of therapy

The Overactive Bladder Questionnaire (OAB-q) Health Related Quality of Life (HRQL) score is a measure of patients' bladder symptom severity. It ranges from 25 to 150 where higher scores indicate greater quality of life.

Outcome measures

Outcome measures
Measure
Mirabegron
n=40 Participants
This arm comprises women who received mirabegron
Change in Overactive Bladder Questionnaire (OAB-q) Health Related Quality of Life (HRQL)
Baseline
50.92 score on a scale
Standard Deviation 26.14
Change in Overactive Bladder Questionnaire (OAB-q) Health Related Quality of Life (HRQL)
After 12 weeks of therapy
74.88 score on a scale
Standard Deviation 25.35
Change in Overactive Bladder Questionnaire (OAB-q) Health Related Quality of Life (HRQL)
Change Score
23.96 score on a scale
Standard Deviation 17.54

SECONDARY outcome

Timeframe: 12 weeks

Population: This analysis comprises women who received mirabegron for 12 weeks and completed the Urinary Distress Inventory at baseline and after 12 weeks of therapy

The Urinary Distress Inventory is a 29-item questionnaire that asks patients to report how bothered they are by symptoms of urinary urgency on a scale from 1 (not at all) to 4 (quite a bit). The total score ranges from 0 to 300 where higher scores indicate worsening symptom severity.

Outcome measures

Outcome measures
Measure
Mirabegron
n=44 Participants
This arm comprises women who received mirabegron
Change in Urinary Distress Inventory (UDI)
Baseline
121.25 score on a scale
Standard Deviation 51.19
Change in Urinary Distress Inventory (UDI)
After 12 weeks of therapy
69.62 score on a scale
Standard Deviation 46.75
Change in Urinary Distress Inventory (UDI)
Change Score
-51.62 score on a scale
Standard Deviation 40.85

SECONDARY outcome

Timeframe: 12 weeks

Population: This analysis comprises women who received mirabegron for 12 weeks and completed the Prolapse Distress Inventory at baseline and after 12 weeks of therapy

The Pelvic Organ Prolapse Distress Inventory (POPDI) is a 16-item questionnaire that asks patients to report how bothered they are by symptoms of urinary urgency on a scale from 1 (not at all) to 4 (quite a bit). The total score ranges from 0 to 300 where higher scores indicate worsening symptom severity.

Outcome measures

Outcome measures
Measure
Mirabegron
n=44 Participants
This arm comprises women who received mirabegron
Change in Pelvic Organ Prolapse Distress Inventory (POPDI) Score
Change Score
-29.30 score on a scale
Standard Deviation 36.28
Change in Pelvic Organ Prolapse Distress Inventory (POPDI) Score
Baseline
77.85 score on a scale
Standard Deviation 64.80
Change in Pelvic Organ Prolapse Distress Inventory (POPDI) Score
After 12 weeks of therapy
48.55 score on a scale
Standard Deviation 50.91

SECONDARY outcome

Timeframe: 12 weeks

Population: This analysis comprises women who received mirabegron for 12 weeks and completed the Colo-Rectal-Anal Distress Inventory at baseline and after 12 weeks of therapy

The Colo-Rectal-Anal Distress Inventory (CRADI) is a 17-item questionnaire that asks patients to report how bothered they are by symptoms of urinary urgency on a scale from 1 (not at all) to 4 (quite a bit). The total score ranges from 0 to 400 where higher scores indicate worsening symptom severity.

Outcome measures

Outcome measures
Measure
Mirabegron
n=44 Participants
This arm comprises women who received mirabegron
Change in Colo-Rectal-Anal Distress Inventory (CRADI)
Baseline
94.50 score on a scale
Standard Deviation 82.18
Change in Colo-Rectal-Anal Distress Inventory (CRADI)
After 12 weeks of therapy
62.50 score on a scale
Standard Deviation 68.17
Change in Colo-Rectal-Anal Distress Inventory (CRADI)
Change Score
-32.00 score on a scale
Standard Deviation 40.61

Adverse Events

Mirabegron

Serious events: 2 serious events
Other events: 12 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Mirabegron
n=84 participants at risk
This arm comprises women who received mirabegron
Nervous system disorders
Stroke
1.2%
1/84 • Number of events 1 • Adverse event data were collected for 26 weeks
Immune system disorders
Breast Cancer
1.2%
1/84 • Number of events 1 • Adverse event data were collected for 26 weeks

Other adverse events

Other adverse events
Measure
Mirabegron
n=84 participants at risk
This arm comprises women who received mirabegron
Infections and infestations
Bacterial Infection
1.2%
1/84 • Number of events 1 • Adverse event data were collected for 26 weeks
Gastrointestinal disorders
Constipation
1.2%
1/84 • Number of events 1 • Adverse event data were collected for 26 weeks
Gastrointestinal disorders
Diarrhea
3.6%
3/84 • Number of events 3 • Adverse event data were collected for 26 weeks
General disorders
Somnolence
1.2%
1/84 • Number of events 1 • Adverse event data were collected for 26 weeks
General disorders
Leg pain
1.2%
1/84 • Number of events 1 • Adverse event data were collected for 26 weeks
Vascular disorders
Elevated Systolic Blood Pressure
2.4%
2/84 • Number of events 2 • Adverse event data were collected for 26 weeks
Gastrointestinal disorders
Abdominal Cramping
1.2%
1/84 • Number of events 1 • Adverse event data were collected for 26 weeks
General disorders
Nausea
1.2%
1/84 • Number of events 1 • Adverse event data were collected for 26 weeks
Product Issues
Allergic Reaction to mirabegron
1.2%
1/84 • Number of events 1 • Adverse event data were collected for 26 weeks

Additional Information

Alan Wolfe, Ph.D.

Loyola University Chicago

Phone: 708-216-5814

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place