PF-05208756, Moroctocog Alfa (AF-CC), Xyntha For Hemophilia A

NCT ID: NCT02492984

Last Updated: 2017-04-04

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE4

Total Enrollment

85 participants

Study Classification

INTERVENTIONAL

Study Start Date

2015-04-30

Study Completion Date

2016-08-31

Brief Summary

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An open-label, single-arm, post- authorization pragmatic clinical trial on the safety and efficacy of Xyntha (Moroctocog-alfa (AF-CC), Recombinant FVIII) in subjects with hemophilia A in usual care settings in China for approximately 6 months or or approximately 50 exposure days whichever occurs first

Detailed Description

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The purpose of this post-approval study is to provide supplementary information relating to the use of Xyntha (Moroctocog-alfa (AF-CC), Recombinant FVIII) in Chinese subjects with hemophilia A, especially on the safety and efficacy in different populations of Chinese hemophilia A patients, in particular in pediatric patients \<6 years of age, pediatric patients ≥6 to ≤12 years of age, Previously Untreated Patients (PUPs) , subjects receiving prophylaxis treatment after enrollment in the study, and severe patients (FVIII:C \<1%).

Conditions

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Hemophilia A

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Intravenous infusions of Xyntha

Enrolled subjects will be treated with intravenous infusions of Xyntha for: • On-Demand treatment, • Surgical Prophylaxis at a dose and frequency prescribed by the subject's treating physician in accordance with the Xyntha label and will be adjusted solely according to medical and therapeutic necessity.

Group Type EXPERIMENTAL

Intravenous infusions of Xyntha

Intervention Type DRUG

Enrolled subjects will be treated with intravenous infusions of Xyntha for: • On-Demand treatment, • Surgical Prophylaxis at a dose and frequency prescribed by the subject's treating physician in accordance with the Xyntha label and will be adjusted solely according to medical and therapeutic necessity.

Interventions

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Intravenous infusions of Xyntha

Enrolled subjects will be treated with intravenous infusions of Xyntha for: • On-Demand treatment, • Surgical Prophylaxis at a dose and frequency prescribed by the subject's treating physician in accordance with the Xyntha label and will be adjusted solely according to medical and therapeutic necessity.

Intervention Type DRUG

Other Intervention Names

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Xyntha (Moroctocog-alfa (AF-CC)

Eligibility Criteria

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Inclusion Criteria

* Male and/or Female subjects with Hemophilia A.
* Subjects/parents/legal representatives must be able to comply with registry procedures (informed consent/assent process, clinical visits, reporting of infusion and bleed data, reporting of adverse events, etc).
* Evidence of a personally signed and dated informed consent document indicating that the subject (or a legally acceptable representative, parent(s)/legal guardian) has been informed of all pertinent aspects of the study.

Exclusion Criteria

* Presence of any other bleeding disorder in addition to hemophilia A.
* Treatment with immunomodulatory therapy (e.g., intravenous immunoglobulin, routine systemic corticosteroids, cyclosporins, anti-TNF agents) within 30 days prior to study entry or planned use for the duration of their study participation.
* Subjects with a past history of, or current factor VIII inhibitor. For laboratory-based assessments, any Bethesda inhibitor titer greater than the laboratory's normal range or ≥0.6 BU/mL.
* Subjects with known hypersensitivity to the active substance or to any of the excipients of Xyntha.
* Subjects with a known hypersensitivity to Chinese Hamster Ovary cell proteins.
* Unwilling or unable to follow the terms of the protocol.
* Any condition which may compromise the subject's ability to comply with and/or perform study-related activities or that poses a clinical contraindication to study participation (these conditions include, but are not limited to, inadequate medical history to assure study eligibility; expectation of poor compliance in provision of observations for study-related documentation), in the opinion of the Investigator.
* Participation in other studies involving investigational drug(s) (Phases 1-4) within 30 days before the current study begins and/or during study participation (exception for studies on Xyntha).
* Subjects who are investigational site staff members directly involved in the conduct of the study and their family members, site staff members otherwise supervised by the Investigator, or subjects who are Pfizer employees directly involved in the conduct of the study.
Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Pfizer

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Pfizer CT.gov Call Center

Role: STUDY_DIRECTOR

Pfizer

Locations

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The Affiliated Hospital of Guizhou Medical University

Guiyang, Guizhou, China

Site Status

Henan Provincial People's Hospital

Zhengzhou, Henan, China

Site Status

Tongji Hospital of Tongji Medical College of Huazhong University of Science and Technology

Wuhan, Hubei, China

Site Status

Department of Hematology,The First Affiliated Hospital of Soochow University

Suzhou, Jiangsu, China

Site Status

Department of Hematology,Jiangxi Provincial People's Hospital

Nanchang, Jiangxi, China

Site Status

Blood Center of Shandong Province

Jinan, Shandong, China

Site Status

Chengdu Women's and Children's Central Hospital

Chengdu, Sichuan, China

Site Status

Blood Diseases Hospital, Chinese Academy of Medical Science (Institute of Hematology)

Tianjin, Tianjin Municipality, China

Site Status

Department of Hematology,The First Affiliated Hospital of Kunming Medical University

Kunming, Yunnan, China

Site Status

Beijing Children's hospital

Beijing, , China

Site Status

The second affiliated hospital of chongqing medical university

Chongqing, , China

Site Status

Children's Hospital of Chongqing Medical University

Chongqing, , China

Site Status

Hematology Department, Nanfang Hospital, Southern Medical University

Guangzhou, , China

Site Status

Ruijin Hospital Affiliated to Shanghai Jiao Tong University School of Medicine/Hematology Department

Shanghai, , China

Site Status

Department of Hematology/Children's Hospital of Shanghai

Shanghai, , China

Site Status

Countries

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China

References

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Yang R, Zhao Y, Wang X, Sun J, Wu R, Jin C, Jin J, Wu D, Rendo P, Sun F, Rupon J, Huard F, Korth-Bradley JM, Xu L, Luo B, Liu YC. Safety and Efficacy of Moroctocog Alfa (AF-CC) in Chinese Patients with Hemophilia A: Results of Two Open-Label Studies. J Blood Med. 2020 Nov 25;11:439-448. doi: 10.2147/JBM.S241605. eCollection 2020.

Reference Type DERIVED
PMID: 33269010 (View on PubMed)

Related Links

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https://trialinfoemail.pfizer.com

To obtain contact information for a study center near you, click here.

Other Identifiers

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2015-005040-33

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

B1831083

Identifier Type: -

Identifier Source: org_study_id

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