Trial Outcomes & Findings for TARGTEPO Treatment for Anemia in PD US Trial (NCT NCT02468414)

NCT ID: NCT02468414

Last Updated: 2022-03-28

Results Overview

Recruitment status

TERMINATED

Study phase

PHASE2

Target enrollment

3 participants

Primary outcome timeframe

52 weeks

Results posted on

2022-03-28

Participant Flow

Participant milestones

Participant milestones
Measure
Group A
18-25 IU/Kg/day
Group B
35-45 IU/Kg/day
Overall Study
STARTED
3
0
Overall Study
Successfully Screened
2
0
Overall Study
Harvesting
1
0
Overall Study
Implantation
1
0
Overall Study
Safety Follow-up
0
0
Overall Study
COMPLETED
0
0
Overall Study
NOT COMPLETED
3
0

Reasons for withdrawal

Reasons for withdrawal
Measure
Group A
18-25 IU/Kg/day
Group B
35-45 IU/Kg/day
Overall Study
Early Study Termination by Sponsor
1
0
Overall Study
Poor in-vitro secreting TARGTs
1
0
Overall Study
Screen Failure
1
0

Baseline Characteristics

TARGTEPO Treatment for Anemia in PD US Trial

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Group A
n=3 Participants
TARGTEPO 18-25 IU/kg/day
Group B
TARGTEPO 35-45 IU/kg/day
Total
n=3 Participants
Total of all reporting groups
Age, Categorical
<=18 years
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
3 Participants
n=5 Participants
0 Participants
n=7 Participants
3 Participants
n=5 Participants
Age, Categorical
>=65 years
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Sex: Female, Male
Female
1 Participants
n=5 Participants
0 Participants
n=7 Participants
1 Participants
n=5 Participants
Sex: Female, Male
Male
2 Participants
n=5 Participants
0 Participants
n=7 Participants
2 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Asian
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
White
3 Participants
n=5 Participants
0 Participants
n=7 Participants
3 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants

PRIMARY outcome

Timeframe: 52 weeks

Population: No statistical analysis was performed as only one subject was treated with MDGN201 TARGTEPO due to the Sponsor's decision to discontinue study.

Outcome measures

Outcome measures
Measure
Group A
n=1 Participants
TARGTEPO 18-25 IU/kg/day
Group B
TARGTEPO 35-45 IU/kg/day
Patients Who Achieved Biological Activity of MDGN201 TARGTEPO Secretion as Measured by Serum EPO Levels Above Baseline.
1 Participants
0 Participants

Adverse Events

Group A

Serious events: 1 serious events
Other events: 2 other events
Deaths: 0 deaths

Group B

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Group A
n=2 participants at risk
TARGTEPO 18-25 IU/kg/day
Group B
TARGTEPO 35-45 IU/kg/day
Metabolism and nutrition disorders
Hyperkalemia
50.0%
1/2 • Number of events 1
0/0

Other adverse events

Other adverse events
Measure
Group A
n=2 participants at risk
TARGTEPO 18-25 IU/kg/day
Group B
TARGTEPO 35-45 IU/kg/day
Skin and subcutaneous tissue disorders
Local Contact Dermatitis, Right Upper Abdomen
50.0%
1/2 • Number of events 1
0/0
Gastrointestinal disorders
Acute Viral Gasritis
50.0%
1/2 • Number of events 1
0/0
Gastrointestinal disorders
Peritonitis
50.0%
1/2 • Number of events 1
0/0

Additional Information

Garry A. Neil, MD

Aevi Genomic Medicine

Phone: 610-254-4208

Results disclosure agreements

  • Principal investigator is a sponsor employee Should the Primary Investigator (PI) wish to publish the results of this study, the PI agrees to provide the Sponsor with a manuscript for review 60 days prior to submission for publication. The Sponsor retains the right to delete from the manuscript information that is confidential and proprietary and to object to suggested publication and/or its timing (at the Sponsor's sole discretion).
  • Publication restrictions are in place

Restriction type: OTHER