Trial Outcomes & Findings for 3-year Follow-up Study to Assess the Viral Activity in Hepatitis C Patients Who Failed Feeder DEB025/Alisporivir Study (NCT NCT02465203)

NCT ID: NCT02465203

Last Updated: 2018-01-12

Results Overview

Persistence of resistance associated variants

Recruitment status

TERMINATED

Study phase

PHASE3

Target enrollment

105 participants

Primary outcome timeframe

27 months

Results posted on

2018-01-12

Participant Flow

Participant milestones

Participant milestones
Measure
From Study 2210 (N=56)
Follow up from feeder study NCT01183169
From Study 2301 (N=36)
Follow up from withdrawn feeder study NCT01318694
From Study 2211 - Overall (N=13)
Follow up from feeder study NCT01215643
Overall Study
STARTED
56
36
13
Overall Study
COMPLETED
0
0
0
Overall Study
NOT COMPLETED
56
36
13

Reasons for withdrawal

Reasons for withdrawal
Measure
From Study 2210 (N=56)
Follow up from feeder study NCT01183169
From Study 2301 (N=36)
Follow up from withdrawn feeder study NCT01318694
From Study 2211 - Overall (N=13)
Follow up from feeder study NCT01215643
Overall Study
Protocol Violation
1
1
1
Overall Study
Study terminated by sponsor
50
34
11
Overall Study
New therapy for study indication
4
0
0
Overall Study
Patient/guardian decision
1
1
1

Baseline Characteristics

3-year Follow-up Study to Assess the Viral Activity in Hepatitis C Patients Who Failed Feeder DEB025/Alisporivir Study

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
From Study 2210 (N=56)
n=56 Participants
Follow up from feeder study NCT01183169
From Study 2301 (N=36)
n=36 Participants
Follow up from withdrawn feeder study NCT01318694
Study 2211 - Overall (N=13)
n=13 Participants
Follow up from feeder study NCT01215643
Total
n=105 Participants
Total of all reporting groups
Age, Continuous
52.7 years
STANDARD_DEVIATION 9.86 • n=5 Participants
53.8 years
STANDARD_DEVIATION 10.57 • n=7 Participants
46.5 years
STANDARD_DEVIATION 7.88 • n=5 Participants
52.3 years
STANDARD_DEVIATION 10.06 • n=4 Participants
Sex: Female, Male
Female
23 Participants
n=5 Participants
22 Participants
n=7 Participants
4 Participants
n=5 Participants
49 Participants
n=4 Participants
Sex: Female, Male
Male
33 Participants
n=5 Participants
14 Participants
n=7 Participants
9 Participants
n=5 Participants
56 Participants
n=4 Participants
Race/Ethnicity, Customized
Caucasian
40 participants
n=5 Participants
24 participants
n=7 Participants
6 participants
n=5 Participants
70 participants
n=4 Participants
Race/Ethnicity, Customized
Black
3 participants
n=5 Participants
0 participants
n=7 Participants
1 participants
n=5 Participants
4 participants
n=4 Participants
Race/Ethnicity, Customized
Asian
12 participants
n=5 Participants
12 participants
n=7 Participants
6 participants
n=5 Participants
30 participants
n=4 Participants
Race/Ethnicity, Customized
Native American
0 participants
n=5 Participants
0 participants
n=7 Participants
0 participants
n=5 Participants
0 participants
n=4 Participants
Race/Ethnicity, Customized
Pacific Islander
0 participants
n=5 Participants
0 participants
n=7 Participants
0 participants
n=5 Participants
0 participants
n=4 Participants
Race/Ethnicity, Customized
Other
1 participants
n=5 Participants
0 participants
n=7 Participants
0 participants
n=5 Participants
1 participants
n=4 Participants
BMI
26.35 kg/m^2
STANDARD_DEVIATION 3.76 • n=5 Participants
25.54 kg/m^2
STANDARD_DEVIATION 4.08 • n=7 Participants
26.24 kg/m^2
STANDARD_DEVIATION 4.12 • n=5 Participants
26.06 kg/m^2
STANDARD_DEVIATION 3.89 • n=4 Participants
Baseline HCV RNA Load (log10 IU/mL)
6.32 log10 IU/mL
STANDARD_DEVIATION 1.3375 • n=5 Participants
6.19 log10 IU/mL
STANDARD_DEVIATION 0.5171 • n=7 Participants
6.17 log10 IU/mL
STANDARD_DEVIATION 1.1974 • n=5 Participants
6.26 log10 IU/mL
STANDARD_DEVIATION 1.0959 • n=4 Participants

PRIMARY outcome

Timeframe: 27 months

Population: There was no hypothesis testing in this study, as the study was prematurely terminated. 4 patients with resistance associated variants have been identified at study start. Study was not powered for 105 participants

Persistence of resistance associated variants

Outcome measures

Outcome measures
Measure
All Arms
n=105 Participants
All participants in study
HCV RNA Sequencing
4 Number of particiants

SECONDARY outcome

Timeframe: 27 months

Population: There was no hypothesis testing in this study, as the study was prematurely terminated. Study was powered for efficacy of 650 participants, and only 105 were randomized No data are available because data were not collected

Phenotypic analysis of HCV isolates to determine the patients susceptibility/resistance to alisporivir in vitro

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: 27 months

Population: There was no hypothesis testing in this study, as the study was prematurely terminated. No data for any pre-specified Outcomes were analyzed. There was no hypothesis testing in this study, as the study was prematurely terminated. Study was powered for 105 participants, not 650 No data are available because data were not collected

Changes in liver function and disease over time

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: 27 months

Population: There was no hypothesis testing in this study, as the study was prematurely terminated. No data for any pre-specified Outcomes were analyzed. There was no hypothesis testing in this study, as the study was prematurely terminated. Study was powered for 105 participants, not 650 No data are available because data were not collected

Development of hepatocellular carcinoma (HCC)

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: 27 months

Population: There was no hypothesis testing as the study was prematurely terminated. AE and SAE data are provided in the "Adverse Events" section There was no hypothesis testing in this study, as the study was prematurely terminated. Study was powered for 105 participants, not 650 No data are available because data were not collected

Safety over time of previous alisporivir exposure

Outcome measures

Outcome data not reported

Adverse Events

A2210

Serious events: 3 serious events
Other events: 1 other events
Deaths: 0 deaths

A2301

Serious events: 0 serious events
Other events: 1 other events
Deaths: 0 deaths

A2211 IFN-free

Serious events: 0 serious events
Other events: 2 other events
Deaths: 0 deaths

A2211 Overall

Serious events: 0 serious events
Other events: 4 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
A2210
n=53 participants at risk
From Study A2210 (3 patients did not receive alisporivir in the feeder study and were excluded from Safety Set)
A2301
n=33 participants at risk
From Study A2301 (3 patients did not receive alisporivir in the feeder study and were excluded from Safety Set)
A2211 IFN-free
n=6 participants at risk
From Study A2211 IFN-free (subset of Study 2211 overall)
A2211 Overall
n=12 participants at risk
From Study A2211 Overall (1 patient did not receive alisporivir in the feeder study and was excluded from Safety Set)
Hepatobiliary disorders
CHOLECYSTITIS
1.9%
1/53
0.00%
0/33
0.00%
0/6
0.00%
0/12
Hepatobiliary disorders
CHOLELITHIASIS
1.9%
1/53
0.00%
0/33
0.00%
0/6
0.00%
0/12
Injury, poisoning and procedural complications
HAND FRACTURE
1.9%
1/53
0.00%
0/33
0.00%
0/6
0.00%
0/12
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
HEPATOCELLULAR CARCINOMA
1.9%
1/53
0.00%
0/33
0.00%
0/6
0.00%
0/12

Other adverse events

Other adverse events
Measure
A2210
n=53 participants at risk
From Study A2210 (3 patients did not receive alisporivir in the feeder study and were excluded from Safety Set)
A2301
n=33 participants at risk
From Study A2301 (3 patients did not receive alisporivir in the feeder study and were excluded from Safety Set)
A2211 IFN-free
n=6 participants at risk
From Study A2211 IFN-free (subset of Study 2211 overall)
A2211 Overall
n=12 participants at risk
From Study A2211 Overall (1 patient did not receive alisporivir in the feeder study and was excluded from Safety Set)
Gastrointestinal disorders
ABDOMINAL PAIN UPPER
0.00%
0/53
0.00%
0/33
0.00%
0/6
8.3%
1/12
Hepatobiliary disorders
HEPATIC STEATOSIS
1.9%
1/53
3.0%
1/33
16.7%
1/6
16.7%
2/12
Investigations
BLOOD TRIGLYCERIDES INCREASED
0.00%
0/53
0.00%
0/33
0.00%
0/6
8.3%
1/12
Investigations
TOTAL BILE ACIDS INCREASED
0.00%
0/53
0.00%
0/33
0.00%
0/6
8.3%
1/12
Musculoskeletal and connective tissue disorders
NECK PAIN
0.00%
0/53
0.00%
0/33
16.7%
1/6
8.3%
1/12

Additional Information

Study Director

Novartis

Phone: +41613241111

Results disclosure agreements

  • Principal investigator is a sponsor employee The terms and conditions of Novartis' agreements with its investigators may vary. However, Novartis does not prohibit any investigator from publishing. Publications from a single site are postponed until publication of the pooled clinical trial data (i.e., data from all sites) or disclosure of trial results in their entirety.
  • Publication restrictions are in place

Restriction type: OTHER