Trial Outcomes & Findings for A Study of SI-6603 in Patients With Lumbar Disc Herniation (NCT NCT02421601)

NCT ID: NCT02421601

Last Updated: 2023-03-23

Results Overview

A treatment-emergent adverse event (TEAE) was defined as an adverse event (AE) that began or that worsened in severity after the investigational drug had been administered. All AEs, including intercurrent illnesses and regardless of the relationship to investigational drug, occurring during the study were documented from the signing of the informed consent form until completion of final visit. Concomitant illnesses, which existed before entry into the study, were not considered AEs unless they worsened during the treatment period. All AEs, regardless of the source of identification (e.g., physical examination, laboratory assessment, or reported by patient), had to be documented.

Recruitment status

COMPLETED

Study phase

PHASE3

Target enrollment

1011 participants

Primary outcome timeframe

26 weeks

Results posted on

2023-03-23

Participant Flow

Patients are enrolled in the study once eligibility is determined, but after enrollment, injection to the intervertebral disc may not be feasible due to anatomical reasons and patient condition during injection procedure. Therefore, Enrollment number in the Protocol Section (1011) and patients who Started the study (991) are not necessarily the same.

Participant milestones

Participant milestones
Measure
SI-6603
Patients received a single-dose injection of SI-6603 1.25 U into an intervertebral disc.
Overall Study
STARTED
991
Overall Study
COMPLETED
909
Overall Study
NOT COMPLETED
82

Reasons for withdrawal

Reasons for withdrawal
Measure
SI-6603
Patients received a single-dose injection of SI-6603 1.25 U into an intervertebral disc.
Overall Study
Adverse Event
4
Overall Study
Lack of Efficacy
5
Overall Study
Physician Decision
1
Overall Study
Withdrawal by Subject
31
Overall Study
Others
41

Baseline Characteristics

Number analyzed differs from overall population, due to data availability for analysis.

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
SI-6603
n=991 Participants
Patients received a single-dose injection of SI-6603 1.25 U into an intervertebral disc.
Age, Customized
49.1 years
STANDARD_DEVIATION 9.69 • n=991 Participants
Sex: Female, Male
Female
539 Participants
n=991 Participants
Sex: Female, Male
Male
452 Participants
n=991 Participants
Race/Ethnicity, Customized
Race · Asian
4 Participants
n=991 Participants
Race/Ethnicity, Customized
Race · White
862 Participants
n=991 Participants
Race/Ethnicity, Customized
Race · Black
103 Participants
n=991 Participants
Race/Ethnicity, Customized
Race · Other
22 Participants
n=991 Participants
Region of Enrollment
United States
824 participants
n=991 Participants
Region of Enrollment
Germany
70 participants
n=991 Participants
Region of Enrollment
Spain
75 participants
n=991 Participants
Region of Enrollment
Romania
22 participants
n=991 Participants
Body Mass Index (BMI)
29.44 kg/m^2
STANDARD_DEVIATION 6.172 • n=989 Participants • Number analyzed differs from overall population, due to data availability for analysis.
Leg Pain (VAS)
67.9 mm
STANDARD_DEVIATION 18.48 • n=990 Participants • Number analyzed differs from overall population, due to data availability for analysis.

PRIMARY outcome

Timeframe: 26 weeks

Population: Number of Patients with at Least 1 Treatment-Emergent Adverse Event N (%)

A treatment-emergent adverse event (TEAE) was defined as an adverse event (AE) that began or that worsened in severity after the investigational drug had been administered. All AEs, including intercurrent illnesses and regardless of the relationship to investigational drug, occurring during the study were documented from the signing of the informed consent form until completion of final visit. Concomitant illnesses, which existed before entry into the study, were not considered AEs unless they worsened during the treatment period. All AEs, regardless of the source of identification (e.g., physical examination, laboratory assessment, or reported by patient), had to be documented.

Outcome measures

Outcome measures
Measure
SI-6603
n=991 Participants
Patients received a single-dose injection of SI-6603 1.25 U into an intervertebral disc.
Number of Participants With Treatment-Emergent Adverse Events (TEAE)
615 Participants

SECONDARY outcome

Timeframe: 26 weeks

Worst leg pain intensity during the past 24 hours assessed by Visual Analog Scale (VAS). Scores are recorded by making a handwritten mark on a 100 mm line that represents a continuum between "no pain" (0 mm) and "extreme pain" (100 mm).

Outcome measures

Outcome measures
Measure
SI-6603
n=900 Participants
Patients received a single-dose injection of SI-6603 1.25 U into an intervertebral disc.
Worst Leg Pain as Assessed by Visual Analog Scale (VAS)
28.6 units on a scale
Standard Deviation 29.61

Adverse Events

SI-6603

Serious events: 36 serious events
Other events: 615 other events
Deaths: 4 deaths

Serious adverse events

Serious adverse events
Measure
SI-6603
n=991 participants at risk
Patients received a single-dose injection of SI-6603 1.25 U into an intervertebral disc.
Infections and infestations
Pneumonia
0.10%
1/991 • 26 Weeks
Infections and infestations
Urinary tract infection bacterial
0.10%
1/991 • 26 Weeks
Infections and infestations
Urosepsis
0.10%
1/991 • 26 Weeks
Infections and infestations
Wound infection
0.10%
1/991 • 26 Weeks
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Bladder cancer
0.10%
1/991 • 26 Weeks
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Breast cancer
0.10%
1/991 • 26 Weeks
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Hodgkin's disease recurrent
0.10%
1/991 • 26 Weeks
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Small intestine adenocarcinoma
0.10%
1/991 • 26 Weeks
Metabolism and nutrition disorders
Hyponatraemia
0.10%
1/991 • 26 Weeks
Psychiatric disorders
Drug dependence
0.10%
1/991 • 26 Weeks
Psychiatric disorders
Panic attack
0.10%
1/991 • 26 Weeks
Nervous system disorders
Transient ischaemic attack
0.20%
2/991 • 26 Weeks
Nervous system disorders
Cerebral ischaemia
0.10%
1/991 • 26 Weeks
Nervous system disorders
Sciatica
0.10%
1/991 • 26 Weeks
Nervous system disorders
Syncope
0.10%
1/991 • 26 Weeks
Cardiac disorders
Acute myocardial infarction
0.10%
1/991 • 26 Weeks
Cardiac disorders
Cardio-respiratory arrest
0.10%
1/991 • 26 Weeks
Vascular disorders
Hypertensive crisis
0.10%
1/991 • 26 Weeks
Respiratory, thoracic and mediastinal disorders
Asthma
0.20%
2/991 • 26 Weeks
Respiratory, thoracic and mediastinal disorders
Chronic obstructive pulmonary disease
0.10%
1/991 • 26 Weeks
Gastrointestinal disorders
Ascites
0.10%
1/991 • 26 Weeks
Gastrointestinal disorders
Colitis
0.10%
1/991 • 26 Weeks
Hepatobiliary disorders
Cholecystitis
0.10%
1/991 • 26 Weeks
Hepatobiliary disorders
Cholelithiasis
0.10%
1/991 • 26 Weeks
Musculoskeletal and connective tissue disorders
Intervertebral disc protrusion
0.30%
3/991 • 26 Weeks
Musculoskeletal and connective tissue disorders
Arthralgia
0.10%
1/991 • 26 Weeks
Musculoskeletal and connective tissue disorders
Back pain
0.10%
1/991 • 26 Weeks
Musculoskeletal and connective tissue disorders
Osteoarthritis
0.10%
1/991 • 26 Weeks
Musculoskeletal and connective tissue disorders
Pain in extremity
0.10%
1/991 • 26 Weeks
Musculoskeletal and connective tissue disorders
Paraspinal abscess
0.10%
1/991 • 26 Weeks
Reproductive system and breast disorders
Uterine haemorrhage
0.10%
1/991 • 26 Weeks
General disorders
Non-cardiac chest pain
0.20%
2/991 • 26 Weeks
General disorders
Pain
0.10%
1/991 • 26 Weeks
Investigations
Nuclear magnetic resonance imaging abnormal
0.10%
1/991 • 26 Weeks
Injury, poisoning and procedural complications
Ankle fracture
0.20%
2/991 • 26 Weeks
Injury, poisoning and procedural complications
Road traffic accident
0.20%
2/991 • 26 Weeks
Injury, poisoning and procedural complications
Spinal compression fracture
0.10%
1/991 • 26 Weeks
Injury, poisoning and procedural complications
Toxicity to various agents
0.10%
1/991 • 26 Weeks
Injury, poisoning and procedural complications
Wound dehiscence
0.10%
1/991 • 26 Weeks

Other adverse events

Other adverse events
Measure
SI-6603
n=991 participants at risk
Patients received a single-dose injection of SI-6603 1.25 U into an intervertebral disc.
Investigations
Nuclear magnetic resonance imaging spinal abnormal
20.8%
206/991 • 26 Weeks
Musculoskeletal and connective tissue disorders
Back pain
15.9%
158/991 • 26 Weeks
Investigations
Spinal X-ray abnormal
7.7%
76/991 • 26 Weeks
Musculoskeletal and connective tissue disorders
Pain in extremity
5.4%
54/991 • 26 Weeks
Investigations
C-reactive protein increased
4.0%
40/991 • 26 Weeks
Nervous system disorders
Sciatica
2.7%
27/991 • 26 Weeks
Musculoskeletal and connective tissue disorders
Arthralgia
2.5%
25/991 • 26 Weeks
Infections and infestations
Nasopharyngitis
2.0%
20/991 • 26 Weeks
Musculoskeletal and connective tissue disorders
Muscle spasms
1.7%
17/991 • 26 Weeks
Gastrointestinal disorders
Nausea
1.5%
15/991 • 26 Weeks
Metabolism and nutrition disorders
Hypertriglyceridaemia
1.4%
14/991 • 26 Weeks
Nervous system disorders
Headache
1.4%
14/991 • 26 Weeks
Infections and infestations
Sinusitis
1.3%
13/991 • 26 Weeks
Investigations
White blood cell count increased
1.2%
12/991 • 26 Weeks
Skin and subcutaneous tissue disorders
Rash
1.1%
11/991 • 26 Weeks
Investigations
Blood triglycerides increased
1.0%
10/991 • 26 Weeks
Infections and infestations
Upper respiratory tract infection
1.0%
10/991 • 26 Weeks
Infections and infestations
Influenza
1.0%
10/991 • 26 Weeks

Additional Information

Clinical Development Department

Seikagaku Corporation

Phone: (81)3-5220-8948

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place

Restriction type: OTHER