Trial Outcomes & Findings for Modulation Of Airway Reactivity With Chronic Mechanical Strain (NCT NCT02396849)

NCT ID: NCT02396849

Last Updated: 2021-03-09

Results Overview

The change in airway reactivity measured prior to and after 4 weeks of either CPAP or SHAM treatment. Methacholine bronchial challenge was performed using the 5-breath protocol (DeVilbiss646 with KoKo dosimeter: 9 μL/breath) with quadrupling concentrations starting with 0.0625 mg/mL and continuing until FEV1 decreased by 20% (PC20) or Methacholine concentration of 16 mg/mL was inhaled.

Recruitment status

COMPLETED

Study phase

NA

Target enrollment

84 participants

Primary outcome timeframe

baseline (visit 1) and 4 weeks (visit 2)

Results posted on

2021-03-09

Participant Flow

25 were excluded based on screening criteria, two subjects (one in each group) were lost to follow-up, two (one in each group) did not tolerate the equipment and two (one in each group) did not undergo Methacholine challenge at V2 due to the presence of asthma symptoms.

Participant milestones

Participant milestones
Measure
Continuous Positive Airway Pressure (CPAP)
Use of a CPAP machine for at least 5 days per week for 28 days CPAP: Subjects assigned to this group will be asked to use the CPAP machine for a minimum of 4 hours/night at least 5 days/week for a total of 4 weeks.
Continuous Positive Airway Pressure (CPAP) Sham
Use of a sham CPAP machine for at least 5 days per week for 28 days CPAP Sham: Subjects assigned to this group will be asked to use the CPAP SHAM machine for a minimum of 4 hours/night at least 5 days/week for a total of 4 weeks.
Overall Study
STARTED
29
30
Overall Study
COMPLETED
27
28
Overall Study
NOT COMPLETED
2
2

Reasons for withdrawal

Reasons for withdrawal
Measure
Continuous Positive Airway Pressure (CPAP)
Use of a CPAP machine for at least 5 days per week for 28 days CPAP: Subjects assigned to this group will be asked to use the CPAP machine for a minimum of 4 hours/night at least 5 days/week for a total of 4 weeks.
Continuous Positive Airway Pressure (CPAP) Sham
Use of a sham CPAP machine for at least 5 days per week for 28 days CPAP Sham: Subjects assigned to this group will be asked to use the CPAP SHAM machine for a minimum of 4 hours/night at least 5 days/week for a total of 4 weeks.
Overall Study
Lost to Follow-up
1
1
Overall Study
Did not tolerate intervention
1
1

Baseline Characteristics

Modulation Of Airway Reactivity With Chronic Mechanical Strain

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
CPAP
n=27 Participants
Use of a CPAP machine for at least 5 days per week for 28 days CPAP: Subjects assigned to this group will be asked to use the CPAP machine for a minimum of 4 hours/night at least 5 days/week for a total of 4 weeks.
CPAP Sham
n=28 Participants
Use of a sham CPAP machine for at least 5 days per week for 28 days CPAP Sham: Subjects assigned to this group will be asked to use the CPAP SHAM machine for a minimum of 4 hours/night at least 5 days/week for a total of 4 weeks.
Total
n=55 Participants
Total of all reporting groups
Age, Continuous
11.1 years
STANDARD_DEVIATION 2.5 • n=5 Participants
11.7 years
STANDARD_DEVIATION 2.5 • n=7 Participants
11.5 years
STANDARD_DEVIATION 2.5 • n=5 Participants
Sex: Female, Male
Female
10 Participants
n=5 Participants
12 Participants
n=7 Participants
22 Participants
n=5 Participants
Sex: Female, Male
Male
17 Participants
n=5 Participants
16 Participants
n=7 Participants
33 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Asian
0 Participants
n=5 Participants
1 Participants
n=7 Participants
1 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
10 Participants
n=5 Participants
8 Participants
n=7 Participants
18 Participants
n=5 Participants
Race (NIH/OMB)
White
16 Participants
n=5 Participants
16 Participants
n=7 Participants
32 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
1 Participants
n=5 Participants
3 Participants
n=7 Participants
4 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Region of Enrollment
United States
27 Participants
n=5 Participants
28 Participants
n=7 Participants
55 Participants
n=5 Participants
Methacholine Bronchial Challenge
2.9 mg/mL
STANDARD_DEVIATION 4.5 • n=5 Participants
3.2 mg/mL
STANDARD_DEVIATION 4.3 • n=7 Participants
3.09 mg/mL
STANDARD_DEVIATION 4.38 • n=5 Participants

PRIMARY outcome

Timeframe: baseline (visit 1) and 4 weeks (visit 2)

Population: One subject in each group did not undergo Methacholine challenge at V2 due to the presence of asthma symptoms

The change in airway reactivity measured prior to and after 4 weeks of either CPAP or SHAM treatment. Methacholine bronchial challenge was performed using the 5-breath protocol (DeVilbiss646 with KoKo dosimeter: 9 μL/breath) with quadrupling concentrations starting with 0.0625 mg/mL and continuing until FEV1 decreased by 20% (PC20) or Methacholine concentration of 16 mg/mL was inhaled.

Outcome measures

Outcome measures
Measure
CPAP
n=26 Participants
Use of a CPAP machine for at least 5 days per week for 28 days CPAP: Subjects assigned to this group will be asked to use the CPAP machine for a minimum of 4 hours/night at least 5 days/week for a total of 4 weeks.
CPAP Sham
n=27 Participants
Use of a sham CPAP machine for at least 5 days per week for 28 days CPAP Sham: Subjects assigned to this group will be asked to use the CPAP SHAM machine for a minimum of 4 hours/night at least 5 days/week for a total of 4 weeks.
Change in Airway Reactivity From Baseline (Visit 1) and 4 Weeks (Visit 2)
Visit 1
3.0 mg/mL
Standard Deviation 4.6
3.2 mg/mL
Standard Deviation 4.4
Change in Airway Reactivity From Baseline (Visit 1) and 4 Weeks (Visit 2)
Visit 2
5.3 mg/mL
Standard Deviation 8.9
4.3 mg/mL
Standard Deviation 6.8

SECONDARY outcome

Timeframe: baseline (visit 1) and 4 weeks (visit 2)

Population: The overall success rate in obtaining quality sputum samples was 57%; however, only 10 CPAP and 12 sham subjects had quality samples at both study visits.

Airway Inflammation assessed as the change in the percentage eosinophils in the induced sputum measured prior to and after 4 weeks of Continuous Positive Airway Pressure (CPAP) or sham CPAP treatment.

Outcome measures

Outcome measures
Measure
CPAP
n=10 Participants
Use of a CPAP machine for at least 5 days per week for 28 days CPAP: Subjects assigned to this group will be asked to use the CPAP machine for a minimum of 4 hours/night at least 5 days/week for a total of 4 weeks.
CPAP Sham
n=12 Participants
Use of a sham CPAP machine for at least 5 days per week for 28 days CPAP Sham: Subjects assigned to this group will be asked to use the CPAP SHAM machine for a minimum of 4 hours/night at least 5 days/week for a total of 4 weeks.
Change in Airway Inflammation From Baseline (Visit 1) and 4 Weeks (Visit 2)
Study Visit 1
6.2 Percentage of sputum eosinophils
Standard Deviation 10.1
3.9 Percentage of sputum eosinophils
Standard Deviation 5.0
Change in Airway Inflammation From Baseline (Visit 1) and 4 Weeks (Visit 2)
Study Visit 2
3.6 Percentage of sputum eosinophils
Standard Deviation 6.4
5.4 Percentage of sputum eosinophils
Standard Deviation 8.2

Adverse Events

CPAP

Serious events: 0 serious events
Other events: 5 other events
Deaths: 0 deaths

CPAP Sham

Serious events: 0 serious events
Other events: 3 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
CPAP
n=29 participants at risk
Use of a CPAP machine for at least 5 days per week for 28 days CPAP: Subjects assigned to this group will be asked to use the CPAP machine for a minimum of 4 hours/night at least 5 days/week for a total of 4 weeks.
CPAP Sham
n=30 participants at risk
Use of a sham CPAP machine for at least 5 days per week for 28 days CPAP Sham: Subjects assigned to this group will be asked to use the CPAP SHAM machine for a minimum of 4 hours/night at least 5 days/week for a total of 4 weeks.
Respiratory, thoracic and mediastinal disorders
asthma exacerbation treated with oral corticosteroids
17.2%
5/29 • 4 weeks
Adverse event were described as an asthma exacerbation requiring oral corticosteroids during the study period.
10.0%
3/30 • 4 weeks
Adverse event were described as an asthma exacerbation requiring oral corticosteroids during the study period.

Additional Information

Christina Tiller

Indiana University

Phone: 317-044-4522

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place