Trial Outcomes & Findings for Treatments Against RA and Effect on FDG-PET/CT (NCT NCT02374021)

NCT ID: NCT02374021

Last Updated: 2022-10-26

Results Overview

The primary outcome was the change in the mean of the maximum of the target to background ratio (TBR) in the most diseased segment (MDS) of of the index vessel as measured by FDG-PET/CT scans conducted at baseline and after 24 weeks of randomized treatment allocation (MDS meanmaxTBR). The index vessel is the vessel (either aorta, left carotid, or right carotid) with the highest meanmaxTBR at baseline. Higher values indicate greater vascular inflammation. FDG uptake measurement: PET-CT images were batch-analyzed by an investigator blinded to the patients' clinical information. FDG uptake was evaluated within the wall of the ascending aorta and bilateral carotid arteries (as maximum and mean standardized FDG uptake value \[SUVmax and SUVmean, respectively\]) approximately every 5 mm on axial images. Subsequently, the target-to-background ratio (TBR) was reported (ratio of the average arterial to blood axial slice SUVmax) to correct for the blood compartment contribution.

Recruitment status

COMPLETED

Study phase

PHASE4

Target enrollment

159 participants

Primary outcome timeframe

0, 6 months

Results posted on

2022-10-26

Participant Flow

Participant milestones

Participant milestones
Measure
Triple Therapy (MTX+SSZ+HCQ)
Sulfasalazine (SSZ) 1 g bid and hydroxychloroquine (HCQ) 200 mg twice daily, not to exceed 6.5mg/kg HCQ (in addition to concomitant methotrexate \[MTX\]). Methotrexate: Subjects entering trial will continue on MTX dose of at least 15mg MTX/week. At the discretion of the treating rheumatologist, may be switched to SQ route. Sulfasalazine: 1 gm bid Hydroxychloroquine: 200 mg twice daily, not to exceed 6.5mg/kg
TNF Inhibitor (Etanercept or Adalimumab)
etanercept 50 mg subcutaneously weekly or adalimumab 40 mg subcutaneously every other week (in addition to concomitant methotrexate, plus hydroxychloroquine, for subjects who were taking this at screening). Biologic treatment will be assigned randomly. Methotrexate: Subjects entering trial will continue on MTX dose of at least 15mg MTX/week. At the discretion of the treating rheumatologist, may be switched to SQ route. Etanercept: 50 mg SC weekly Adalimumab: 40 mg SQ every other week
Overall Study
STARTED
80
79
Overall Study
COMPLETED
57
58
Overall Study
NOT COMPLETED
23
21

Reasons for withdrawal

Reasons for withdrawal
Measure
Triple Therapy (MTX+SSZ+HCQ)
Sulfasalazine (SSZ) 1 g bid and hydroxychloroquine (HCQ) 200 mg twice daily, not to exceed 6.5mg/kg HCQ (in addition to concomitant methotrexate \[MTX\]). Methotrexate: Subjects entering trial will continue on MTX dose of at least 15mg MTX/week. At the discretion of the treating rheumatologist, may be switched to SQ route. Sulfasalazine: 1 gm bid Hydroxychloroquine: 200 mg twice daily, not to exceed 6.5mg/kg
TNF Inhibitor (Etanercept or Adalimumab)
etanercept 50 mg subcutaneously weekly or adalimumab 40 mg subcutaneously every other week (in addition to concomitant methotrexate, plus hydroxychloroquine, for subjects who were taking this at screening). Biologic treatment will be assigned randomly. Methotrexate: Subjects entering trial will continue on MTX dose of at least 15mg MTX/week. At the discretion of the treating rheumatologist, may be switched to SQ route. Etanercept: 50 mg SC weekly Adalimumab: 40 mg SQ every other week
Overall Study
Adverse Event
1
0
Overall Study
Lost to Follow-up
3
2
Overall Study
Physician Decision
0
3
Overall Study
Withdrawal by Subject
6
5
Overall Study
Poor Adherence
0
1
Overall Study
Scan protocol not followed
0
1
Overall Study
Poor quality scan/scan not able to be analyzed
13
9

Baseline Characteristics

Treatments Against RA and Effect on FDG-PET/CT

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Triple Therapy (MTX+SSZ+HCQ)
n=57 Participants
Sulfasalazine (SSZ) 1 g bid and hydroxychloroquine (HCQ) 200 mg twice daily, not to exceed 6.5mg/kg HCQ (in addition to concomitant methotrexate \[MTX\]). Methotrexate: Subjects entering trial will continue on MTX dose of at least 15mg MTX/week. At the discretion of the treating rheumatologist, may be switched to SQ route. Sulfasalazine: 1 gm bid Hydroxychloroquine: 200 mg twice daily, not to exceed 6.5mg/kg
TNF Inhibitor (Etanercept or Adalimumab)
n=58 Participants
etanercept 50 mg subcutaneously weekly or adalimumab 40 mg subcutaneously every other week (in addition to concomitant methotrexate, plus hydroxychloroquine, for subjects who were taking this at screening). Biologic treatment will be assigned randomly. Methotrexate: Subjects entering trial will continue on MTX dose of at least 15mg MTX/week. At the discretion of the treating rheumatologist, may be switched to SQ route. Etanercept: 50 mg SC weekly Adalimumab: 40 mg SQ every other week
Total
n=115 Participants
Total of all reporting groups
Age, Continuous
59.0 years
n=93 Participants
58.0 years
n=4 Participants
58.0 years
n=27 Participants
Sex: Female, Male
Female
43 Participants
n=93 Participants
39 Participants
n=4 Participants
82 Participants
n=27 Participants
Sex: Female, Male
Male
14 Participants
n=93 Participants
19 Participants
n=4 Participants
33 Participants
n=27 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
16 Participants
n=93 Participants
15 Participants
n=4 Participants
31 Participants
n=27 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
41 Participants
n=93 Participants
43 Participants
n=4 Participants
84 Participants
n=27 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=93 Participants
0 Participants
n=4 Participants
0 Participants
n=27 Participants
DAS28-CRP
4.6 units on a scale
n=93 Participants
4.9 units on a scale
n=4 Participants
4.8 units on a scale
n=27 Participants

PRIMARY outcome

Timeframe: 0, 6 months

Population: Participants with a FDG-PET/CT at baseline and six months for whom the primary outcome could be assessed

The primary outcome was the change in the mean of the maximum of the target to background ratio (TBR) in the most diseased segment (MDS) of of the index vessel as measured by FDG-PET/CT scans conducted at baseline and after 24 weeks of randomized treatment allocation (MDS meanmaxTBR). The index vessel is the vessel (either aorta, left carotid, or right carotid) with the highest meanmaxTBR at baseline. Higher values indicate greater vascular inflammation. FDG uptake measurement: PET-CT images were batch-analyzed by an investigator blinded to the patients' clinical information. FDG uptake was evaluated within the wall of the ascending aorta and bilateral carotid arteries (as maximum and mean standardized FDG uptake value \[SUVmax and SUVmean, respectively\]) approximately every 5 mm on axial images. Subsequently, the target-to-background ratio (TBR) was reported (ratio of the average arterial to blood axial slice SUVmax) to correct for the blood compartment contribution.

Outcome measures

Outcome measures
Measure
Triple Therapy (MTX+SSZ+HCQ)
n=57 Participants
Sulfasalazine (SSZ) 1 g bid and hydroxychloroquine (HCQ) 200 mg twice daily, not to exceed 6.5mg/kg HCQ (in addition to concomitant methotrexate \[MTX\]). Methotrexate: Subjects entering trial will continue on MTX dose of at least 15mg MTX/week. At the discretion of the treating rheumatologist, may be switched to SQ route. Sulfasalazine: 1 gm bid Hydroxychloroquine: 200 mg twice daily, not to exceed 6.5mg/kg
TNF Inhibitor (Etanercept or Adalimumab)
n=58 Participants
etanercept 50 mg subcutaneously weekly or adalimumab 40 mg subcutaneously every other week (in addition to concomitant methotrexate, plus hydroxychloroquine, for subjects who were taking this at screening). Biologic treatment will be assigned randomly. Methotrexate: Subjects entering trial will continue on MTX dose of at least 15mg MTX/week. At the discretion of the treating rheumatologist, may be switched to SQ route. Etanercept: 50 mg SC weekly Adalimumab: 40 mg SQ every other week
Change From Baseline in Vascular Inflammation as Measured by FDG-PET/CT at 6 Months
-0.19 ratio
Standard Deviation 0.51
-0.24 ratio
Standard Deviation 0.51

SECONDARY outcome

Timeframe: 0, 6 months

Population: Participants with a FDG-PET/CT at baseline and six months for whom the outcome could be assessed

The outcome was the change in the mean of the maximum of the target to background ratio (TBR) in the most diseased segment (MDS) of the aorta as measured by FDG-PET/CT scans conducted at baseline and after 24 weeks of randomized treatment allocation (MDS meanmaxTBR). Higher values indicate greater vascular inflammation. FDG uptake measurement: PET-CT images were batch-analyzed by an investigator blinded to the patients' clinical information. FDG uptake was evaluated within the wall of the ascending aorta and bilateral carotid arteries (as maximum and mean standardized FDG uptake value \[SUVmax and SUVmean, respectively\]) approximately every 5 mm on axial images. Subsequently, the target-to-background ratio (TBR) was reported (ratio of the average arterial to blood axial slice SUVmax) to correct for the blood compartment contribution.

Outcome measures

Outcome measures
Measure
Triple Therapy (MTX+SSZ+HCQ)
n=52 Participants
Sulfasalazine (SSZ) 1 g bid and hydroxychloroquine (HCQ) 200 mg twice daily, not to exceed 6.5mg/kg HCQ (in addition to concomitant methotrexate \[MTX\]). Methotrexate: Subjects entering trial will continue on MTX dose of at least 15mg MTX/week. At the discretion of the treating rheumatologist, may be switched to SQ route. Sulfasalazine: 1 gm bid Hydroxychloroquine: 200 mg twice daily, not to exceed 6.5mg/kg
TNF Inhibitor (Etanercept or Adalimumab)
n=56 Participants
etanercept 50 mg subcutaneously weekly or adalimumab 40 mg subcutaneously every other week (in addition to concomitant methotrexate, plus hydroxychloroquine, for subjects who were taking this at screening). Biologic treatment will be assigned randomly. Methotrexate: Subjects entering trial will continue on MTX dose of at least 15mg MTX/week. At the discretion of the treating rheumatologist, may be switched to SQ route. Etanercept: 50 mg SC weekly Adalimumab: 40 mg SQ every other week
Change From Baseline in the MDS of the Aorta
-0.17 Ratio
Standard Deviation 0.39
-0.17 Ratio
Standard Deviation 0.52

SECONDARY outcome

Timeframe: 0, 6 months

Population: Participants with a FDG-PET/CT at baseline and six months for whom the outcome could be assessed

The outcome was the change in the target to background ratio (TBR) of the aorta as measured by FDG-PET/CT scans conducted at baseline and after 24 weeks of randomized treatment allocation (MDS meanmaxTBR). Higher values indicate greater vascular inflammation. FDG uptake measurement: PET-CT images were batch-analyzed by an investigator blinded to the patients' clinical information. FDG uptake was evaluated within the wall of the ascending aorta and bilateral carotid arteries (as maximum and mean standardized FDG uptake value \[SUVmax and SUVmean, respectively\]) approximately every 5 mm on axial images. Subsequently, the target-to-background ratio (TBR) was reported (ratio of the average arterial to blood axial slice SUVmax) to correct for the blood compartment contribution.

Outcome measures

Outcome measures
Measure
Triple Therapy (MTX+SSZ+HCQ)
n=52 Participants
Sulfasalazine (SSZ) 1 g bid and hydroxychloroquine (HCQ) 200 mg twice daily, not to exceed 6.5mg/kg HCQ (in addition to concomitant methotrexate \[MTX\]). Methotrexate: Subjects entering trial will continue on MTX dose of at least 15mg MTX/week. At the discretion of the treating rheumatologist, may be switched to SQ route. Sulfasalazine: 1 gm bid Hydroxychloroquine: 200 mg twice daily, not to exceed 6.5mg/kg
TNF Inhibitor (Etanercept or Adalimumab)
n=56 Participants
etanercept 50 mg subcutaneously weekly or adalimumab 40 mg subcutaneously every other week (in addition to concomitant methotrexate, plus hydroxychloroquine, for subjects who were taking this at screening). Biologic treatment will be assigned randomly. Methotrexate: Subjects entering trial will continue on MTX dose of at least 15mg MTX/week. At the discretion of the treating rheumatologist, may be switched to SQ route. Etanercept: 50 mg SC weekly Adalimumab: 40 mg SQ every other week
Change From Baseline in the Average TBR of the Aorta
-0.06 Ratio
Standard Deviation 0.34
-0.02 Ratio
Standard Deviation 0.43

SECONDARY outcome

Timeframe: 0, 6 months

Population: Participants with a FDG-PET/CT at baseline and six months for whom the outcome could be assessed

The outcome was the change in the target to background ratio (TBR) of the average of the left and right carotids as measured by FDG-PET/CT scans conducted at baseline and after 24 weeks of randomized treatment allocation (MDS meanmaxTBR). The baseline values of the left and right carotids were averaged and then the follow-up values of the left and right carotids were averaged resulting in one value at each time point. Higher values indicate greater vascular inflammation. FDG uptake measurement: PET-CT images were batch-analyzed by an investigator blinded to the patients' clinical information. FDG uptake was evaluated within the wall of the ascending aorta and bilateral carotid arteries (as maximum and mean standardized FDG uptake value \[SUVmax and SUVmean, respectively\]) approximately every 5 mm on axial images. Subsequently, the target-to-background ratio (TBR) was reported (ratio of the average arterial to blood axial slice SUVmax) to correct for the blood compartment contribution.

Outcome measures

Outcome measures
Measure
Triple Therapy (MTX+SSZ+HCQ)
n=43 Participants
Sulfasalazine (SSZ) 1 g bid and hydroxychloroquine (HCQ) 200 mg twice daily, not to exceed 6.5mg/kg HCQ (in addition to concomitant methotrexate \[MTX\]). Methotrexate: Subjects entering trial will continue on MTX dose of at least 15mg MTX/week. At the discretion of the treating rheumatologist, may be switched to SQ route. Sulfasalazine: 1 gm bid Hydroxychloroquine: 200 mg twice daily, not to exceed 6.5mg/kg
TNF Inhibitor (Etanercept or Adalimumab)
n=45 Participants
etanercept 50 mg subcutaneously weekly or adalimumab 40 mg subcutaneously every other week (in addition to concomitant methotrexate, plus hydroxychloroquine, for subjects who were taking this at screening). Biologic treatment will be assigned randomly. Methotrexate: Subjects entering trial will continue on MTX dose of at least 15mg MTX/week. At the discretion of the treating rheumatologist, may be switched to SQ route. Etanercept: 50 mg SC weekly Adalimumab: 40 mg SQ every other week
Change From Baseline in the Average TBR of the Bilateral Carotids
-0.10 Ratio
Standard Deviation 0.51
-0.06 Ratio
Standard Deviation 0.48

SECONDARY outcome

Timeframe: 0, 6 months

Population: Participants with a FDG-PET/CT at baseline and six months for whom the outcome could be assessed

The outcome was the change in the target to background ratio (TBR) in the index vessel as measured by FDG-PET/CT scans conducted at baseline and after 24 weeks of randomized treatment allocation (MDS meanmaxTBR). Higher values indicate greater vascular inflammation. FDG uptake measurement: PET-CT images were batch-analyzed by an investigator blinded to the patients' clinical information. FDG uptake was evaluated within the wall of the ascending aorta and bilateral carotid arteries (as maximum and mean standardized FDG uptake value \[SUVmax and SUVmean, respectively\]) approximately every 5 mm on axial images. Subsequently, the target-to-background ratio (TBR) was reported (ratio of the average arterial to blood axial slice SUVmax) to correct for the blood compartment contribution.

Outcome measures

Outcome measures
Measure
Triple Therapy (MTX+SSZ+HCQ)
n=57 Participants
Sulfasalazine (SSZ) 1 g bid and hydroxychloroquine (HCQ) 200 mg twice daily, not to exceed 6.5mg/kg HCQ (in addition to concomitant methotrexate \[MTX\]). Methotrexate: Subjects entering trial will continue on MTX dose of at least 15mg MTX/week. At the discretion of the treating rheumatologist, may be switched to SQ route. Sulfasalazine: 1 gm bid Hydroxychloroquine: 200 mg twice daily, not to exceed 6.5mg/kg
TNF Inhibitor (Etanercept or Adalimumab)
n=58 Participants
etanercept 50 mg subcutaneously weekly or adalimumab 40 mg subcutaneously every other week (in addition to concomitant methotrexate, plus hydroxychloroquine, for subjects who were taking this at screening). Biologic treatment will be assigned randomly. Methotrexate: Subjects entering trial will continue on MTX dose of at least 15mg MTX/week. At the discretion of the treating rheumatologist, may be switched to SQ route. Etanercept: 50 mg SC weekly Adalimumab: 40 mg SQ every other week
Change From Baseline in the Average TBR of the Index Vessel
-0.07 Ratio
Standard Deviation 0.47
-0.09 Ratio
Standard Deviation 0.43

Adverse Events

Triple Therapy (MTX+SSZ+HCQ)

Serious events: 4 serious events
Other events: 0 other events
Deaths: 0 deaths

TNF Inhibitor (Etanercept or Adalimumab)

Serious events: 10 serious events
Other events: 0 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Triple Therapy (MTX+SSZ+HCQ)
n=80 participants at risk
Sulfasalazine (SSZ) 1 g bid and hydroxychloroquine (HCQ) 200 mg twice daily, not to exceed 6.5mg/kg HCQ (in addition to concomitant methotrexate \[MTX\]). Methotrexate: Subjects entering trial will continue on MTX dose of at least 15mg MTX/week. At the discretion of the treating rheumatologist, may be switched to SQ route. Sulfasalazine: 1 gm bid Hydroxychloroquine: 200 mg twice daily, not to exceed 6.5mg/kg
TNF Inhibitor (Etanercept or Adalimumab)
n=79 participants at risk
etanercept 50 mg subcutaneously weekly or adalimumab 40 mg subcutaneously every other week (in addition to concomitant methotrexate, plus hydroxychloroquine, for subjects who were taking this at screening). Biologic treatment will be assigned randomly. Methotrexate: Subjects entering trial will continue on MTX dose of at least 15mg MTX/week. At the discretion of the treating rheumatologist, may be switched to SQ route. Etanercept: 50 mg SC weekly Adalimumab: 40 mg SQ every other week
Renal and urinary disorders
Renal Calculi
0.00%
0/80 • 24 weeks
2.5%
2/79 • Number of events 2 • 24 weeks
Gastrointestinal disorders
Dysphagia
0.00%
0/80 • 24 weeks
1.3%
1/79 • Number of events 1 • 24 weeks
Musculoskeletal and connective tissue disorders
Myalgia
0.00%
0/80 • 24 weeks
1.3%
1/79 • Number of events 1 • 24 weeks
Cardiac disorders
Myocardial Infarction
0.00%
0/80 • 24 weeks
1.3%
1/79 • Number of events 1 • 24 weeks
Gastrointestinal disorders
Vomiting
1.2%
1/80 • Number of events 1 • 24 weeks
0.00%
0/79 • 24 weeks
Musculoskeletal and connective tissue disorders
Back Pain
1.2%
1/80 • Number of events 1 • 24 weeks
0.00%
0/79 • 24 weeks
Gastrointestinal disorders
Abdominal Pain
1.2%
1/80 • Number of events 1 • 24 weeks
0.00%
0/79 • 24 weeks
Respiratory, thoracic and mediastinal disorders
Respiratory Failure
0.00%
0/80 • 24 weeks
1.3%
1/79 • Number of events 1 • 24 weeks
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Neoplasms Benign Malignant And Unspecified
0.00%
0/80 • 24 weeks
1.3%
1/79 • Number of events 1 • 24 weeks
Renal and urinary disorders
Urinary Tract Infection
0.00%
0/80 • 24 weeks
1.3%
1/79 • Number of events 1 • 24 weeks
Respiratory, thoracic and mediastinal disorders
Pneumonitis
1.2%
1/80 • Number of events 1 • 24 weeks
0.00%
0/79 • 24 weeks
Respiratory, thoracic and mediastinal disorders
Dyspnea
0.00%
0/80 • 24 weeks
2.5%
2/79 • Number of events 2 • 24 weeks

Other adverse events

Adverse event data not reported

Additional Information

Dr. Daniel Solomon

Brigham and Women's Hospital

Phone: 617-732-5356

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place