Using MRI-Guided Laser Heat Ablation to Induce Disruption of the Peritumoral Blood Brain Barrier to Enhance Delivery and Efficacy of Treatment of Pediatric Brain Tumors

NCT ID: NCT02372409

Last Updated: 2024-11-01

Study Results

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE2

Total Enrollment

6 participants

Study Classification

INTERVENTIONAL

Study Start Date

2015-08-14

Study Completion Date

2023-03-23

Brief Summary

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By employing a combination of advanced MRI techniques and correlative serum biomarkers of blood brain barrier (BBB) disruption, the investigators plan to develop a powerful, first of its kind clinical algorithm in pediatrics whereby the investigators can measure and identify the window of maximal BBB disruption post MLA to 1) allow for an alternative to surgery in incompletely resected tumors, 2) allow for optimal chemotherapeutic dosing to achieve the greatest benefits and the least systemic side effects and 3) distinguish subsequent tumor progression from long-term MLA treatment effects. Preliminary data in adult imaging studies have shown that the BBB disruption lasts for several weeks following treatment before returning to a low baseline. This pilot therapeutic study will provide preliminary validation in pediatric patients.

Detailed Description

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Conditions

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Glioma Pilocytic Astrocytoma Anaplastic Astrocytoma Glioblastoma Mixed Oligoastrocytoma Mixed Glioma Oligodendroglioma Optic Glioma Astrocytoma

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Arm A (MRI-guided laser ablation)

* MLA is a minimally invasive laser surgery currently FDA approved for cytoreductive treatment of brain tumors, both primary and metastatic. MLA employs a small incision in the scalp and skull, through which a thin laser probe is inserted and guided by MR imaging to the core of a tumor mass where it delivers hyperthermic ablation from the core to the rim.
* Participants will undergo DCE and DSC-MRI imaging at the following time points:

* no more than 3 weeks prior to MLA (OPTIONAL)
* within approximately 4 days after MLA
* 2-4 weeks after MLA
* Every 12 weeks (+/- 7 days) for the first year or until disease progression

Group Type EXPERIMENTAL

MRI-guided laser ablation

Intervention Type DEVICE

Dynamic contrast-enhanced (DCE) MRI

Intervention Type DEVICE

Dynamic susceptibility contrast (DSC) MRI

Intervention Type DEVICE

Arm B (MRI-guided laser ablation, doxorubicin, etoposide)

* MLA is a minimally invasive laser surgery currently FDA approved for cytoreductive treatment of brain tumors, both primary and metastatic. MLA employs a small incision in the scalp and skull, through which a thin laser probe is inserted and guided by MR imaging to the core of a tumor mass where it delivers hyperthermic ablation from the core to the rim.
* Within 7 days of MLA (range 2-14 days) doxorubicin will be given intravenously on an outpatient basis weekly for 6 weeks at a dose of 25 mg/m\^2 over 5-30 minutes
* Following the completion of doxorubin, etoposide 50 mg/m\^2/day will be given orally for 21 days of each 28-day cycle (treatment can continue up to 24 cycles)
* Participants will undergo DCE and DSC-MRI imaging at the following time points:

* no more than 3 weeks prior to MLA (OPTIONAL)
* within approximately 4 days after MLA
* 2-4 weeks after MLA
* every 8 weeks (+/- 7 days) until 2 years have elapsed or disease progression, whichever comes first

Group Type EXPERIMENTAL

MRI-guided laser ablation

Intervention Type DEVICE

Doxorubicin

Intervention Type DRUG

Etoposide

Intervention Type DRUG

Dynamic contrast-enhanced (DCE) MRI

Intervention Type DEVICE

Dynamic susceptibility contrast (DSC) MRI

Intervention Type DEVICE

Interventions

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MRI-guided laser ablation

Intervention Type DEVICE

Doxorubicin

Intervention Type DRUG

Etoposide

Intervention Type DRUG

Dynamic contrast-enhanced (DCE) MRI

Intervention Type DEVICE

Dynamic susceptibility contrast (DSC) MRI

Intervention Type DEVICE

Other Intervention Names

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MLA Adriamycin Etoposide phosphate VP-16 Toposar Etopophos VePesid DCE-MRI DSC-MRI

Eligibility Criteria

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Inclusion Criteria

ARM A

* Presumed pediatric gliomas (grades I-IV) on MRI that are determined to be candidates for MLA by the treating neurosurgeon
* Age 3 to ≤ 21
* Karnofsky/Lansky performance status ≥ 60%

ARM B

* Recurrent pediatric brain tumors determined candidates for MLA as determined by the treating neurosurgeon.
* Unequivocal evidence of tumor progression by MRI
* There must be an interval of at least 12 weeks from the completion of radiotherapy to study registration except if there is unequivocal evidence for tumor recurrence per RANO criteria. When the interval is less than 12 weeks from the completion of radiotherapy, the use of PET scan is allowed to differentiate between evidence of tumor recurrence and pseudoprogression.
* Recurrent lesions with dimension and contour that are determined by the treating neurosurgeon to be appropriate for MLA.
* Age 3 to ≤ 21
* Karnofsky/Lansky performance status ≥ 60%
* Adequate cardiac function as determined by a shortening fraction ≥ 27% or left ventricular ejection fraction ≥ 50% by echocardiogram within the past 1 year prior to registration.
* Prior anthracycline therapy does not exceed 200 mg/m\^2 total cumulative dose.
* Adequate bone marrow and hepatic function as defined below (must be within 7 days of MLA):

* Absolute neutrophil count (ANC) ≥ 1000/mcl (G-CSF is allowed)
* Platelets ≥ 100 K/cumm
* Hemoglobin ≥ 9 g/dL (pRBC transfusion +/- ESA are allowed)
* ALT ≤ 3 x ULN
* AST ≤ 3 x ULN
* ALP ≤ 3 x ULN. If ALP is \> 3 x ULN, GGT must be checked and be ≤ 3 x ULN.
* Bilirubin ≤ 2 x ULN
* At the time of registration, patient must have recovered from the toxic effects of prior therapy to no more than grade 1 toxicity.
* At the time of registration, patient must be at least 4 weeks from other prior cytotoxic chemotherapy.
* Women of childbearing potential and men must agree to use adequate contraception (hormonal or barrier method of birth control, abstinence) prior to study entry and for the duration of study participation. Should a woman become pregnant or suspect she is pregnant while participating in this study, she must inform her treating physician immediately.
* Ability to understand and willingness to sign an IRB approved written informed consent document (or that of legally authorized representative, if applicable).

Exclusion Criteria

ARM A

* Currently receiving or scheduled to receive any other therapies intended to treat the newly diagnosed glioma prior to MLA and the first post-MLA blood collection for correlative studies.
* Multi-focal or metastatic disease.
* Pregnant and/or breastfeeding. Premenopausal women must have a negative serum or urine pregnancy test within 14 days of study entry.
* Inability to undergo MRI due to personal or medical reasons.
* Known history of HIV or autoimmune diseases requiring immunosuppressant drugs.

ARM B

* Prior treatment with bevacizumab within 12 weeks of study entry.
* Previous treatment with complete cumulative doses of daunorubicin, idarubicin, and/or other anthracyclines and anthracenediones that is equivalent to a total dose of \> 200 mg/m2 doxorubicin.
* More than 2 prior relapses (not counting the current relapse being treated on this study).
* Currently receiving any other investigational agents that are intended as treatments of the relapsed tumor.
* Multi-focal or metastatic disease.
* A history of allergic reactions attributed to compounds of similar chemical or biologic composition to doxorubicin or other agents used in the study.
* Uncontrolled intercurrent illness including, but not limited to, ongoing or active infection, symptomatic congestive heart failure, unstable angina pectoris, cardiac arrhythmia, recent heart attack within the previous 12 months or severe heart problems, or psychiatric illness/social situations that would limit compliance with study requirements.
* Pregnant and/or breastfeeding. Premenopausal women must have a negative serum or urine pregnancy test within 14 days of study entry.
* Inability to undergo MRI due to personal or medical reasons.
* Known history of HIV or autoimmune diseases requiring immunosuppressant drugs.
Minimum Eligible Age

3 Years

Maximum Eligible Age

21 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Washington University School of Medicine

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Andrew Cluster, M.D.

Role: PRINCIPAL_INVESTIGATOR

Washington University School of Medicine

Locations

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Washington University School of Medicine

St Louis, Missouri, United States

Site Status

Countries

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United States

References

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Holodny AI, Nusbaum AO, Festa S, Pronin IN, Lee HJ, Kalnin AJ. Correlation between the degree of contrast enhancement and the volume of peritumoral edema in meningiomas and malignant gliomas. Neuroradiology. 1999 Nov;41(11):820-5. doi: 10.1007/s002340050848.

Reference Type BACKGROUND
PMID: 10602854 (View on PubMed)

Kassner A, Thornhill R. Measuring the integrity of the human blood-brain barrier using magnetic resonance imaging. Methods Mol Biol. 2011;686:229-45. doi: 10.1007/978-1-60761-938-3_10.

Reference Type BACKGROUND
PMID: 21082374 (View on PubMed)

Hawasli AH, Ray WZ, Murphy RK, Dacey RG Jr, Leuthardt EC. Magnetic resonance imaging-guided focused laser interstitial thermal therapy for subinsular metastatic adenocarcinoma: technical case report. Neurosurgery. 2012 Jun;70(2 Suppl Operative):332-7; discussion 338. doi: 10.1227/NEU.0b013e318232fc90.

Reference Type BACKGROUND
PMID: 21869722 (View on PubMed)

Gong W, Wang Z, Liu N, Lin W, Wang X, Xu D, Liu H, Zeng C, Xie X, Mei X, Lu W. Improving efficiency of adriamycin crossing blood brain barrier by combination of thermosensitive liposomes and hyperthermia. Biol Pharm Bull. 2011;34(7):1058-64. doi: 10.1248/bpb.34.1058.

Reference Type BACKGROUND
PMID: 21720013 (View on PubMed)

Quick J, Gessler F, Dutzmann S, Hattingen E, Harter PN, Weise LM, Franz K, Seifert V, Senft C. Benefit of tumor resection for recurrent glioblastoma. J Neurooncol. 2014 Apr;117(2):365-72. doi: 10.1007/s11060-014-1397-2. Epub 2014 Feb 15.

Reference Type BACKGROUND
PMID: 24535317 (View on PubMed)

Ashley DM, Meier L, Kerby T, Zalduondo FM, Friedman HS, Gajjar A, Kun L, Duffner PK, Smith S, Longee D. Response of recurrent medulloblastoma to low-dose oral etoposide. J Clin Oncol. 1996 Jun;14(6):1922-7. doi: 10.1200/JCO.1996.14.6.1922.

Reference Type BACKGROUND
PMID: 8656261 (View on PubMed)

Davidson A, Gowing R, Lowis S, Newell D, Lewis I, Dicks-Mireaux C, Pinkerton CR. Phase II study of 21 day schedule oral etoposide in children. New Agents Group of the United Kingdom Children's Cancer Study Group (UKCCSG). Eur J Cancer. 1997 Oct;33(11):1816-22. doi: 10.1016/s0959-8049(97)00201-3.

Reference Type BACKGROUND
PMID: 9470839 (View on PubMed)

Fulton D, Urtasun R, Forsyth P. Phase II study of prolonged oral therapy with etoposide (VP16) for patients with recurrent malignant glioma. J Neurooncol. 1996 Feb;27(2):149-55. doi: 10.1007/BF00177478.

Reference Type BACKGROUND
PMID: 8699237 (View on PubMed)

Law M, Young R, Babb J, Rad M, Sasaki T, Zagzag D, Johnson G. Comparing perfusion metrics obtained from a single compartment versus pharmacokinetic modeling methods using dynamic susceptibility contrast-enhanced perfusion MR imaging with glioma grade. AJNR Am J Neuroradiol. 2006 Oct;27(9):1975-82.

Reference Type BACKGROUND
PMID: 17032878 (View on PubMed)

Blyth BJ, Farhavar A, Gee C, Hawthorn B, He H, Nayak A, Stocklein V, Bazarian JJ. Validation of serum markers for blood-brain barrier disruption in traumatic brain injury. J Neurotrauma. 2009 Sep;26(9):1497-1507. doi: 10.1089/neu.2008.0738.

Reference Type BACKGROUND
PMID: 19257803 (View on PubMed)

Dunn GP, Dunn IF, Curry WT. Focus on TILs: Prognostic significance of tumor infiltrating lymphocytes in human glioma. Cancer Immun. 2007 Aug 13;7:12.

Reference Type BACKGROUND
PMID: 17691714 (View on PubMed)

Dunn GP, Fecci PE, Curry WT. Cancer immunoediting in malignant glioma. Neurosurgery. 2012 Aug;71(2):201-22; discussion 222-3. doi: 10.1227/NEU.0b013e31824f840d.

Reference Type BACKGROUND
PMID: 22353795 (View on PubMed)

Provided Documents

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Document Type: Study Protocol and Statistical Analysis Plan

View Document

Related Links

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http://www.siteman.wustl.edu

Alvin J. Siteman Cancer Center at Barnes-Jewish Hospital and Washington University School of Medicine

Other Identifiers

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201502062

Identifier Type: -

Identifier Source: org_study_id

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