Study of Palbociclib in MLL-rearranged Acute Leukemias

NCT ID: NCT02310243

Last Updated: 2019-04-16

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

UNKNOWN

Clinical Phase

PHASE1/PHASE2

Total Enrollment

50 participants

Study Classification

INTERVENTIONAL

Study Start Date

2015-07-31

Study Completion Date

2019-07-31

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

Diagnosis: Acute myeloid leukemia; Acute lymphoblastic leukemia Age ≥ 18 years, no upper age limit Study drug: Palbociclib Phase Ib/IIa, open-label

* Phase Ib: Based on previous experience with 125 mg palbociclib once daily for 21 days followed by 7 days of rest in patients with breast cancer, liposarcoma, non-small cell lung cancer, hepatocellular carcinoma, ovarian cancer, mantle-cell lymphoma, and glioblastoma, this regimen will be chosen for the first dose to be evaluated in the phase Ib. Based on a 3 + 3 modified Fibonacci design, the tolerable dose of palbociclib for the phase IIa is defined.
* Phase IIa: single-agent palbociclib using the tolerable dose defined in the phase Ib part of the study is administered once daily for 21 days followed by 7 days of rest. Based on the optimal two-stage design of Simon, 21 patients are treated in the first stage. If results are positive, 29 additional patients will be recruited into the second stage of the study. An efficacy of the investigational therapy will be rejected in the first stage of 21 treated patients if two or less patients achieve complete remission (CR), CR with incomplete blood count recovery (CRi), partial remission (PR), or anti-leukemic effect (ALE). If three or more patients achieve CR, CRi, PR, or ALE during this first stage, the trial is intended to be continued in the second stage with a total sample size of 50 patients.

Start of recruitment: July 2015 End of recruitment: July 2017 End of study (last patient out): July 2018 The treatment duration of an individual patient is estimated to be 2-6 months, but may be unlimited in patients with sustained response ("case-by-case decision").

Observation time per patient after entry into the study (incl. treatment) is at least 12 months.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Acute Myeloid Leukemia Acute Lymphoblastic Leukemia

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Palbociclib

Phase1b: 125 mg palbociclib once daily for 21 days followed by 7 days of rest; this regimen will be chosen for the first dose to be evaluated.

phase IIa: single-agent palbociclib using the tolerable dose defined in the phase Ib part of the study is administered once daily for 21 days followed by 7 days of rest.

Group Type EXPERIMENTAL

Palbociclib

Intervention Type DRUG

oral, once daily (125mg, 100mg or 75mg) for 21 days

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Palbociclib

oral, once daily (125mg, 100mg or 75mg) for 21 days

Intervention Type DRUG

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

PD-0332991-00

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Patients with confirmed diagnosis of acute leukemia with MLL rearrangement according to the 2008 WHO Classification
* Patients with MLL-rearranged leukemia who are refractory to standard induction therapy and not immediate candidates for allogeneic HSCT (bridge to transplant is allowed)
* Patients with MLL-rearranged leukemia who relapsed after standard first-line treatment and are not immediate candidates for allogeneic HSCT (bridge to transplant is allowed)
* Patients with newly diagnosed MLL-rearranged leukemia who are not eligible for intensive first-line therapy
* Genetic/histologic/immunohistologic assessment in one of the central laboratories
* Age ≥ 18 years, no upper age limit
* WHO performance status of ≤ 2
* No prior chemotherapy two weeks before study entry except hydroxyurea to control hyperleukocytosis
* Non-pregnant and non-nursing. Women of child-bearing potential must have a negative serum or urine pregnancy test with a sensitivity of at least 25 mIU/mL within 72 hours prior to registration (WOCBP is defined as a sexually active mature woman who has not undergone a hysterectomy or who has had menses at any time in the preceding 24 months).
* Female patients in the reproductive age and male patients must agree to avoid getting pregnant or to father a child while on therapy and for three months after the last dose of therapy.
* Women of child-bearing potential must either commit to continued abstinence from heterosexual intercourse or begin one acceptable method of birth control (IUD, tubal ligation, or partner's vasectomy). Hormonal contraception is an inadequate method of birth control.
* Men must agree not to father a child and must use a latex condom during any sexual contact with WOCBP while receiving therapy and for three months after therapy is stopped, even if they have undergone successful vasectomy.
* Signed written informed consent

Exclusion Criteria

* Prior treatment with palbociclib
* Performance status \> 2 according to WHO criteria
* Organ insufficiency: creatinine \> 1.5 x upper normal serum level; bilirubin, AST, or AP \> 2.5 x upper normal serum level; heart failure NYHA III/IV; uncontrolled hypertension; unstable angina; serious cardiac arrhythmia; severe obstructive or restrictive ventilation disorder
* Uncontrolled infection
* Patients with a "currently active" second malignancy other than non-melanoma skin cancer. Patients are not considered to have a "currently active" malignancy if they have completed therapy and are considered by their physician to be at less than 30% risk of relapse within one year.
* Severe neurologic or psychiatric disorder interfering with ability of giving informed consent
* Known or suspected active alcohol or drug abuse
* Known positivity for HIV, active HAV, HBV, or HCV infection
* Bleeding disorder unrelated to leukemia
* Uncontrolled CNS involvement (treatment for CNS-involvement prior to inclusion is allowed)
* QTc \> 470 msec (based on the mean value of triplicate ECGs), family or personal history of long or short QT syndrome, Brugada syndrome, or known history of QTc prolongation or Torsade de Pointes
* Uncontrolled electrolyte disorders that can aggravate the effects of a QTc-prolonging drug (e.g., hypocalcemia, hypokalemia, hypomagnesemia)
* No consent for registration, storage, and processing of individual disease characteristics, information on the course of the disease, and information obtained from the family physician and/or other physicians involved in the treatment of the patient about study participation
* No consent for biobanking
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Pfizer

INDUSTRY

Sponsor Role collaborator

National Center for Tumor Diseases, Heidelberg

OTHER

Sponsor Role collaborator

University of Ulm

OTHER

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Peter Paschka

Prof. Dr. med.

Responsibility Role PRINCIPAL_INVESTIGATOR

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Klinikum Augsburg

Augsburg, , Germany

Site Status RECRUITING

Helios Klinikum Bad Saarow

Bad Saarow, , Germany

Site Status RECRUITING

Charité Campus Benjamin Franklin

Berlin, , Germany

Site Status RECRUITING

Vivantes Klinikum Neukölln

Berlin, , Germany

Site Status RECRUITING

Charité Campus Virchow-Klinikum

Berlin, , Germany

Site Status RECRUITING

Universitätsklinikum Bonn

Bonn, , Germany

Site Status RECRUITING

Städtisches Klinikum Braunschweig gGmbH

Braunschweig, , Germany

Site Status RECRUITING

Universitätsklinikum Düsseldorf

Düsseldorf, , Germany

Site Status RECRUITING

Kliniken Essen Süd, Ev. Krankenhaus Essen-Werden gGmbH

Essen, , Germany

Site Status RECRUITING

Malteser Krankenhaus St. Franziskus-Hospital

Flensburg, , Germany

Site Status RECRUITING

Universitätsklinikum Freiburg

Freiburg im Breisgau, , Germany

Site Status RECRUITING

MVZ Osthessen

Fulda, , Germany

Site Status RECRUITING

Universitätsklinikum Giessen

Giessen, , Germany

Site Status RECRUITING

Universitätsklinikum Hamburg-Eppendorf

Hamburg, , Germany

Site Status RECRUITING

Medizinische Hochschule Hannover

Hanover, , Germany

Site Status RECRUITING

Universitätsklinikum Heidelberg

Heidelberg, , Germany

Site Status RECRUITING

Städtisches Klinikum Karlsruhe gGmbH

Karlsruhe, , Germany

Site Status RECRUITING

Universitätsklinikum Schleswig-Holstein Campus Kiel

Kiel, , Germany

Site Status RECRUITING

Caritas-Krankenhaus Lebach

Lebach, , Germany

Site Status RECRUITING

Uni-Klinikum der Otto-von-Guericke-Universität

Magdeburg, , Germany

Site Status RECRUITING

Universitätsmedizin der Johannes Gutenberg-Universität

Mainz, , Germany

Site Status RECRUITING

Pius Hospital Oldenburg

Oldenburg, , Germany

Site Status RECRUITING

Medizinische Universitätsklinik Tübingen

Tübingen, , Germany

Site Status RECRUITING

University Hospital of Ulm

Ulm, , Germany

Site Status RECRUITING

Countries

Review the countries where the study has at least one active or historical site.

Germany

Facility Contacts

Find local site contact details for specific facilities participating in the trial.

Christoph Schmid, MD

Role: primary

Daniel Schöndube, MD

Role: primary

Claudia Bladus, MD

Role: primary

Maike de Wit, MD

Role: primary

Jörg Westermann, MD

Role: primary

Karin Tina Mayer, MD

Role: primary

Jürgen Krauter, MD

Role: primary

Thomas Schroeder, MD

Role: primary

Mohammed Wattad, MD

Role: primary

Nadezda Basara, MD

Role: primary

Ralph Wäsch, MD

Role: primary

Andrea Distelrath, MD

Role: primary

Maisun Abu Samara, MD

Role: primary

Walter Fiedler, MD

Role: primary

Michael Heuser, MD

Role: primary

Alwin Krämer, MD

Role: primary

Mark Ringhoffer, MD

Role: primary

Heinz-August Horst, MD

Role: primary

Stephan Kremers, MD

Role: primary

Denise Wolleschak, MD

Role: primary

Thomas Kindler, MD

Role: primary

Frank Griesinger, MD

Role: primary

Helmut Salih, MD

Role: primary

Peter Paschka, MD

Role: primary

0049-731-500 ext. 45521

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

AMLSG 23-14

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.