Fibroblast Growth Factor Regeneration of Tympanic Membrane Perforations

NCT ID: NCT02307916

Last Updated: 2020-12-31

Study Results

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

57 participants

Study Classification

INTERVENTIONAL

Study Start Date

2016-10-31

Study Completion Date

2020-03-31

Brief Summary

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A Phase II randomized trial will be initiated to evaluate closure of the perforated tympanic membrane as the primary measureable outcome. The goal is to determine the safety and efficacy of Fibroblast Growth Factor-2 (FGF-2) in the closure of chronic tympanic membrane perforations (TMP). If FGF-2 is topically applied for the treatment of chronic TMP in humans, it is hypothesized it will be safe, tolerable and effective for use as treatment for tympanic membrane perforation. A total of 60 subjects will be recruited.

Detailed Description

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A Phase II randomized trial will be initiated to evaluate efficacy as the primary measureable outcome. Eligible and consented patients will be randomized in a 3:1 ratio to the optimal biologic dose (OBD) of FGF-2 or placebo (sterile water).

Application of the study treatment may occur at the initial Screening Visit (pending all eligibility requirements can be confirmed) or at Visit 1 and may be repeated at each follow up visit as needed for a maximum of three treatments per treatment arm. These follow up visits will occur three weeks (+/- 7 days) from the last treatment application. During these visits, the subject's tympanic membrane will be examined, photographed, and additional otologic tests will be performed. If the perforation is found to be closed during these visits, then the subject will report in 2 months (+/-7 days) for a final study visit.

If the subject's TMP has not closed after the third and final application of their assigned treatment group, then the subject will be crossed over to the other treatment group. Again, the subject may be given up to three additional treatments in this new group. The follow up visits will follow the same schedule, occurring three weeks (+/- 7 days) from the last treatment. The same otologic procedures will be performed as in the previous visits.

All subjects will report for a final study visit 2 months (+/- 7 days) after their last follow up visit when the perforation is determined to be closed or when the subject has completed the maximum number of study visits without perforation closure. The study will be completed for reporting purposes after all subjects have completed the 2 month (+/- 7 days) follow up final visit.

Conditions

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Tympanic Membrane Perforation

Keywords

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tympanic membrane perforation ear drum hole

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Investigators Outcome Assessors

Study Groups

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FGF-2

FGF-2 given a minimum of 1 and maximum of 3 times within, approximately, 60 days.

Group Type EXPERIMENTAL

FGF-2

Intervention Type DRUG

The FGF-2 method of use comprises a pledget of gelatin foam with human fibroblast growth factor-2 (FGF-2) added to the pledget just before topical application to the tympanic membrane, and the use of Tisseel, a fibrin glue used for applications in ear surgery.

Placebo

Equal concentration of saline is given a minimum of 1 and maximum of 3 times within, approximately, 60 days.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type OTHER

Placebo comparator using a sterile saline solution.

Interventions

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FGF-2

The FGF-2 method of use comprises a pledget of gelatin foam with human fibroblast growth factor-2 (FGF-2) added to the pledget just before topical application to the tympanic membrane, and the use of Tisseel, a fibrin glue used for applications in ear surgery.

Intervention Type DRUG

Placebo

Placebo comparator using a sterile saline solution.

Intervention Type OTHER

Other Intervention Names

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FGF2, Human Fibroblast Growth Factor 2 Placebo comparator; sterile saline

Eligibility Criteria

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Inclusion Criteria

1. Dry tympanic membrane perforation of greater than 3 months duration
2. If female, post-menopausal or sterile, or if she is of child-bearing potential, must have a negative beta-human chorionic gonadotropin (HCG) test and must be using an adequate form of birth control such as birth control pills, birth control implants, intrauterine devices (IUDs), diaphragms or condoms.

Exclusion Criteria

The presence of any of the following excludes a subject from study enrollment:

* Active otitis media or chronic otorrhea from the middle ear
* Subjects receiving radiation therapy, corticosteroids, immunosuppressive agents or chemotherapy
* Subjects who, at study entry, are taking systemic antibiotics
* Subjects who are immunosuppressed
* Subjects experiencing bacterial or viral infection or who may otherwise be febrile
* Life expectancy of less than 1 year
* Active alcohol or drug abuse within 6 months prior to study entry
* Significant medical condition that could prevent full participation in the procedures required for the study (See body of protocol for full list of exclusions)
* Known or suspected allergies to any components used in the study
* Subjects who have cholesteatoma mass in the tympanic cavity
* Subjects whose total perforation cannot be seen by an endoscope
* Subjects with inadequately controlled diabetes mellitus (NGSP: HbA1c 6.9% or higher)
* Subjects with a history of malignant ear canal tumors within 3 years of screening for eligibility
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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United States Department of Defense

FED

Sponsor Role collaborator

Dr. Bradley Welling

OTHER

Sponsor Role lead

Responsible Party

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Dr. Bradley Welling

Principal Investigator, M.D., Ph.D.

Responsibility Role SPONSOR_INVESTIGATOR

Principal Investigators

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D. B. Welling, M.D., Ph.D

Role: PRINCIPAL_INVESTIGATOR

Massachusetts Eye and Ear

Locations

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Massachusetts Eye and Ear

Boston, Massachusetts, United States

Site Status

Wilford Hall, Lackland Airforce Base

Lackland Air Force Base, Texas, United States

Site Status

Countries

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United States

Provided Documents

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Document Type: Study Protocol and Statistical Analysis Plan

View Document

Other Identifiers

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16-043

Identifier Type: -

Identifier Source: org_study_id