Treatment of Chronic Graft-Versus-Host Disease With Mesenchymal Stromal Cells

NCT ID: NCT02291770

Last Updated: 2014-11-14

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

UNKNOWN

Clinical Phase

PHASE3

Total Enrollment

130 participants

Study Classification

INTERVENTIONAL

Study Start Date

2014-10-31

Study Completion Date

2019-12-31

Brief Summary

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Chronic Graft-versus-Host Disease (cGvHD) is a potentially lethal disorder. A variety of second line immunosuppressive agents have been investigated but no optimal treatment has emerged. There is therefore a need for novel treatment strategies. Mesenchymal stromal cells (MSC) exhibit immunomodulatory properties and a recent pilot study suggests a response rate of 70% in steroid- refractory patients. In the present randomized study the efficacy and safety of MSC treatment will be further studied in patients with cGvHD.

Detailed Description

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Conditions

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Chronic Graft-Versus-Host Disease

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Mesenchymal stem cells (MSC)

Patients with newly diagnosed cGvHD receive primary treatment plus MSC:

1. MSC+prednisone+cyclosporine;
2. MSC+prednisone+tacrolimus;
3. MSC+prednisone+mycophenolate mofetil.

Group Type ACTIVE_COMPARATOR

Mesenchymal Stromal Cells

Intervention Type BIOLOGICAL

Mesenchymal stem cell(MSC). Patients with newly diagnosed cGvHD: prednisone 1mg/kg + cyclosporine or tacrolimus and MSC 2×1,000,000 MSC/kg, IV twice a week for the first two weeks and weekly for the following two weeks(6 doses totally).

Placebo

Patients with newly diagnosed cGvHD receive primary treatment:

1. Placebo+prednisone+cyclosporine;
2. Placebo+prednisone+tacrolimus;
3. Placebo+prednisone+mycophenolate mofetil.

Group Type PLACEBO_COMPARATOR

No interventions assigned to this group

Interventions

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Mesenchymal Stromal Cells

Mesenchymal stem cell(MSC). Patients with newly diagnosed cGvHD: prednisone 1mg/kg + cyclosporine or tacrolimus and MSC 2×1,000,000 MSC/kg, IV twice a week for the first two weeks and weekly for the following two weeks(6 doses totally).

Intervention Type BIOLOGICAL

Other Intervention Names

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MSC

Eligibility Criteria

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Inclusion Criteria

* Newly diagnosed cGvHD
* Informed consent obtained from patient and donor.
* Any patient who has undergone allogeneic stem cell transplantation with c GvHD.
* Have not received additional agent for cGVHD within 3 months.
* Expected life is more than 90 days.
* Adequate pulmonary function with no evidence of chronic obstructive or severe restrictive pulmonary disease.
* Adequate cardiac function with no evidence of uncontrolled high blood pressure,congestive heart failure, angina pectoris, acute myocardial infarction within 6 months prior to the process.

Exclusion Criteria

* Invasive fungal disease.
* Active cytomegalovirus (CMV)/Epstein-Barr virus(EBV)/varicella disease).
* Patient is with a history of hypersensitivity to bovine products.
* Relapsed malignancy.
Minimum Eligible Age

14 Years

Maximum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Sun Yat-sen University

OTHER

Sponsor Role collaborator

Nanfang Hospital, Southern Medical University

OTHER

Sponsor Role collaborator

Guangzhou General Hospital of Guangzhou Military Command

OTHER

Sponsor Role collaborator

Third Affiliated Hospital, Sun Yat-Sen University

OTHER

Sponsor Role collaborator

Guangzhou First People's Hospital

OTHER

Sponsor Role collaborator

Academy Military Medical Science, China

INDUSTRY

Sponsor Role collaborator

Guangdong Provincial People's Hospital

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Xin Du, Prof.

Role: PRINCIPAL_INVESTIGATOR

Guangdong Provincial People's Hospital

Locations

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Xin Du

Guangzhou, Guangdong, China

Site Status RECRUITING

Countries

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China

Central Contacts

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Xin Du, Prof.

Role: CONTACT

+86 02083827812-62122

Jianyu Weng, Prof.

Role: CONTACT

+86 02083827812-62122

Facility Contacts

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Xin Du, Prof.

Role: primary

Peilong Lai, Dr.

Role: backup

+86 02083827812-62121

References

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Weng J, He C, Lai P, Luo C, Guo R, Wu S, Geng S, Xiangpeng A, Liu X, Du X. Mesenchymal stromal cells treatment attenuates dry eye in patients with chronic graft-versus-host disease. Mol Ther. 2012 Dec;20(12):2347-54. doi: 10.1038/mt.2012.208. Epub 2012 Oct 16.

Reference Type BACKGROUND
PMID: 23070118 (View on PubMed)

Weng JY, Du X, Geng SX, Peng YW, Wang Z, Lu ZS, Wu SJ, Luo CW, Guo R, Ling W, Deng CX, Liao PJ, Xiang AP. Mesenchymal stem cell as salvage treatment for refractory chronic GVHD. Bone Marrow Transplant. 2010 Dec;45(12):1732-40. doi: 10.1038/bmt.2010.195. Epub 2010 Sep 6.

Reference Type BACKGROUND
PMID: 20818445 (View on PubMed)

Other Identifiers

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No.GRDEC 2014210H

Identifier Type: -

Identifier Source: org_study_id