A Study of APTO-253 in Patients With Relapsed or Refractory AML or MDS

NCT ID: NCT02267863

Last Updated: 2022-08-22

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE1

Total Enrollment

21 participants

Study Classification

INTERVENTIONAL

Study Start Date

2014-10-31

Study Completion Date

2021-09-30

Brief Summary

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This study is being done to evaluate the safety and effectiveness of APTO-253 for the treatment of patients with the condition of acute myelogenous leukemia (AML) or myelodysplastic syndrome (MDS) for which either the standard treatment has failed, is no longer effective, or can no longer be administered safely or poses a risk for your general well being.

Detailed Description

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This is a multicenter, open-label, Phase Ia/b dose escalation study of safety, pharmacodynamics, and pharmacokinetics of APTO-253 in ascending cohorts (3+3 design) to determine the MTD or recommended dose in patients with relapsed or refractory acute myelogenous leukemia (AML) or high-risk MDS patients. This is to be followed by a cohort expansion phase at the MTD or recommended dose.

Conditions

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Acute Myelogenous Leukemia in Relapse Acute Myelogenous Leukemia, Relapsed, Adult Acute Myelogenous Leukemia, Adult Acute Myelogenous Leukemia High Risk Myelodysplasia

Study Design

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Allocation Method

NA

Intervention Model

SEQUENTIAL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Dose Escalation and Expansion

APTO-253 will be given in ascending doses in patients with relapsed or refractory AML or high risk MDS (escalation cohort), until the maximum tolerated dose or recommended dose is reached. Followed by up to 30 patients enrolled in the expansion cohort at the recommended dose.

Group Type EXPERIMENTAL

APTO-253

Intervention Type DRUG

APTO-253 will be given in ascending doses starting at 20 mg/m2 until the maximum tolerated dose or recommended dose is reached.

Interventions

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APTO-253

APTO-253 will be given in ascending doses starting at 20 mg/m2 until the maximum tolerated dose or recommended dose is reached.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Patients ≥18 years old
* Life expectancy of at least 2 months
* Off previous cancer therapy for at least 14 days, or 5 half-lives for noncytotoxic agents prior to first study treatment administration
* Patients must have a calculated creatinine clearance \>60 mL/min
* Acceptable hematologic, renal and liver functions and coagulation status parameters

Exclusion Criteria

* Patients with GVHD requiring systemic immunosuppressive therapy
* Uncontrolled leptomeningeal disease, auto-immune hemolytic anemia and uncontrolled and clinical significant disease related metabolic disorder
* Clinically significant intravascular coagulation
* Treatment with other investigational drugs within 14 days prior to first study treatment administration
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Aptose Biosciences Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Rafael Bejar, MD., PhD.

Role: STUDY_DIRECTOR

Aptose Biosciences Inc.

Locations

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University of Arizona Cancer Center

Tucson, Arizona, United States

Site Status

UC San Diego Moores Cancer Center

La Jolla, California, United States

Site Status

University of California, Irvine

Orange, California, United States

Site Status

Emory University; Winship Cancer Institute

Atlanta, Georgia, United States

Site Status

Ochsner Cancer Institute

New Orleans, Louisiana, United States

Site Status

University of Michigan

Ann Arbor, Michigan, United States

Site Status

St. Vincent Frontier Cancer Center

Billings, Montana, United States

Site Status

University of Rochester; Wilmot Cancer Institute Clinical Trials Office

Rochester, New York, United States

Site Status

University Hospital

Cleveland, Ohio, United States

Site Status

Oregon Health & Science University

Portland, Oregon, United States

Site Status

Prisma Health, Institute for Translational Oncology Research

Greenville, South Carolina, United States

Site Status

Baylor Research Institute

Dallas, Texas, United States

Site Status

MD Anderson Cancer Center

Houston, Texas, United States

Site Status

Countries

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United States

Related Links

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Other Identifiers

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253-HEM1-01

Identifier Type: -

Identifier Source: org_study_id

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