Trial Outcomes & Findings for A Phase I/II Study of Ganetespib in Combination With Doxorubicin (NCT NCT02261805)

NCT ID: NCT02261805

Last Updated: 2018-04-23

Results Overview

The dose of ganetespib at which 1 or more out of 3-6 patients experiences a dose-limiting toxicity

Recruitment status

TERMINATED

Study phase

PHASE1/PHASE2

Target enrollment

11 participants

Primary outcome timeframe

1 year

Results posted on

2018-04-23

Participant Flow

Participant milestones

Participant milestones
Measure
Ganetespib and Doxorubicin - Phase Ib Dose Level 1
Ganetespib 100 mg/m2 IV on days 1 and 8 of a 21-day cycle Doxorubicin 50 mg/m2 IV on day 1 of a 21-day cycle
Ganetespib and Doxorubicin - Phase Ib Dose Level 2
Ganetespib 150 mg/m2 IV on days 1 and 8 of a 21-day cycle Doxorubicin 50 mg/m2 IV on day 1 of a 21-day cycle
Ganetespib and Doxorubicin - Phase II Expansion
Ganetespib 150 mg/m2 IV on days 1 and 8 of a 21-day cycle Doxorubicin 50 mg/m2 IV on day 1 of a 21-day cycle
Overall Study
STARTED
3
6
2
Overall Study
COMPLETED
3
6
2
Overall Study
NOT COMPLETED
0
0
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

A Phase I/II Study of Ganetespib in Combination With Doxorubicin

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Ganetespib and Doxorubicin
n=11 Participants
Ganetespib 100 or 150 mg/m2 IV on days 1 and 8 of a 21-day cycle Doxorubicin 50 mg/m2 IV on day 1 of a 21-day cycle Ganetespib and doxorubicin Ganetespib and doxorubicin: IV ganetespib and doxorubicin
Age, Categorical
<=18 years
0 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
9 Participants
n=5 Participants
Age, Categorical
>=65 years
2 Participants
n=5 Participants
Sex: Female, Male
Female
4 Participants
n=5 Participants
Sex: Female, Male
Male
7 Participants
n=5 Participants

PRIMARY outcome

Timeframe: 1 year

The dose of ganetespib at which 1 or more out of 3-6 patients experiences a dose-limiting toxicity

Outcome measures

Outcome measures
Measure
Ganetespib and Doxorubicin - Phase Ib Dose Level 1
n=3 Participants
Ganetespib 100 mg/m2 IV on days 1 and 8 of a 21-day cycle Doxorubicin 50 mg/m2 IV on day 1 of a 21-day cycle
Ganetespib and Doxorubicin - Phase Ib Dose Level 2
n=6 Participants
Ganetespib 150 mg/m2 IV on days 1 and 8 of a 21-day cycle Doxorubicin 50 mg/m2 IV on day 1 of a 21-day cycle
Ganetespib and Doxorubicin - Phase II Expansion
Ganetespib 150 mg/m2 IV on days 1 and 8 of a 21-day cycle Doxorubicin 50 mg/m2 IV on day 1 of a 21-day cycle
Maximum Tolerated Dose
100 mg/m^2
150 mg/m^2

SECONDARY outcome

Timeframe: 2 years

Objective response rate included the count of confirmed complete responses (CR) and partial responses (PR) and was based on Response Evaluation Criteria in Solid Tumors (RECIST) version 1.1.

Outcome measures

Outcome measures
Measure
Ganetespib and Doxorubicin - Phase Ib Dose Level 1
n=3 Participants
Ganetespib 100 mg/m2 IV on days 1 and 8 of a 21-day cycle Doxorubicin 50 mg/m2 IV on day 1 of a 21-day cycle
Ganetespib and Doxorubicin - Phase Ib Dose Level 2
n=6 Participants
Ganetespib 150 mg/m2 IV on days 1 and 8 of a 21-day cycle Doxorubicin 50 mg/m2 IV on day 1 of a 21-day cycle
Ganetespib and Doxorubicin - Phase II Expansion
n=2 Participants
Ganetespib 150 mg/m2 IV on days 1 and 8 of a 21-day cycle Doxorubicin 50 mg/m2 IV on day 1 of a 21-day cycle
Objective Response Rate
1 Participants
1 Participants
0 Participants

Adverse Events

Ganetespib and Doxorubicin

Serious events: 1 serious events
Other events: 11 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Ganetespib and Doxorubicin
n=11 participants at risk
Ganetespib 100 or 150 mg/m2 IV on days 1 and 8 of a 21-day cycle Doxorubicin 50 mg/m2 IV on day 1 of a 21-day cycle
Immune system disorders
Neutrophil count decreased
9.1%
1/11 • Number of events 1
Adverse events were reported as pooling all subjects together and were not broken out by group.

Other adverse events

Other adverse events
Measure
Ganetespib and Doxorubicin
n=11 participants at risk
Ganetespib 100 or 150 mg/m2 IV on days 1 and 8 of a 21-day cycle Doxorubicin 50 mg/m2 IV on day 1 of a 21-day cycle
Gastrointestinal disorders
Constipation
27.3%
3/11 • Number of events 3
Adverse events were reported as pooling all subjects together and were not broken out by group.
Nervous system disorders
Dysgeusia
9.1%
1/11 • Number of events 1
Adverse events were reported as pooling all subjects together and were not broken out by group.
General disorders
Fatigue
54.5%
6/11 • Number of events 7
Adverse events were reported as pooling all subjects together and were not broken out by group.
Skin and subcutaneous tissue disorders
Rash maculo-papular
18.2%
2/11 • Number of events 2
Adverse events were reported as pooling all subjects together and were not broken out by group.
Blood and lymphatic system disorders
Alkaline phosphatase increased
18.2%
2/11 • Number of events 2
Adverse events were reported as pooling all subjects together and were not broken out by group.
Blood and lymphatic system disorders
Anemia
27.3%
3/11 • Number of events 4
Adverse events were reported as pooling all subjects together and were not broken out by group.
Psychiatric disorders
Depression
9.1%
1/11 • Number of events 1
Adverse events were reported as pooling all subjects together and were not broken out by group.
Gastrointestinal disorders
Diarrhea
45.5%
5/11 • Number of events 10
Adverse events were reported as pooling all subjects together and were not broken out by group.
Gastrointestinal disorders
Dyspepsia
9.1%
1/11 • Number of events 1
Adverse events were reported as pooling all subjects together and were not broken out by group.
Respiratory, thoracic and mediastinal disorders
Dyspnea
18.2%
2/11 • Number of events 2
Adverse events were reported as pooling all subjects together and were not broken out by group.
Nervous system disorders
Headache
9.1%
1/11 • Number of events 1
Adverse events were reported as pooling all subjects together and were not broken out by group.
General disorders
Nausea
72.7%
8/11 • Number of events 8
Adverse events were reported as pooling all subjects together and were not broken out by group.
Immune system disorders
Neutrophil count decreased
36.4%
4/11 • Number of events 4
Adverse events were reported as pooling all subjects together and were not broken out by group.
Nervous system disorders
Pain
18.2%
2/11 • Number of events 2
Adverse events were reported as pooling all subjects together and were not broken out by group.
General disorders
Anorexia
27.3%
3/11 • Number of events 4
Adverse events were reported as pooling all subjects together and were not broken out by group.
Hepatobiliary disorders
Aspartate aminotransferase increased
18.2%
2/11 • Number of events 3
Adverse events were reported as pooling all subjects together and were not broken out by group.
Blood and lymphatic system disorders
Hyponatremia
9.1%
1/11 • Number of events 1
Adverse events were reported as pooling all subjects together and were not broken out by group.
General disorders
Insomnia
9.1%
1/11 • Number of events 1
Adverse events were reported as pooling all subjects together and were not broken out by group.
Immune system disorders
Lymphocyte count decreased
9.1%
1/11 • Number of events 2
Adverse events were reported as pooling all subjects together and were not broken out by group.
Respiratory, thoracic and mediastinal disorders
Cough
9.1%
1/11 • Number of events 1
Adverse events were reported as pooling all subjects together and were not broken out by group.
Gastrointestinal disorders
Gastrointestinal anastomotic leak
9.1%
1/11 • Number of events 1
Adverse events were reported as pooling all subjects together and were not broken out by group.
Hepatobiliary disorders
Hypoalbuminemia
9.1%
1/11 • Number of events 1
Adverse events were reported as pooling all subjects together and were not broken out by group.
Gastrointestinal disorders
Weight loss
27.3%
3/11 • Number of events 3
Adverse events were reported as pooling all subjects together and were not broken out by group.
Respiratory, thoracic and mediastinal disorders
Hoarseness
9.1%
1/11 • Number of events 1
Adverse events were reported as pooling all subjects together and were not broken out by group.
Blood and lymphatic system disorders
Hypokalemia
27.3%
3/11 • Number of events 3
Adverse events were reported as pooling all subjects together and were not broken out by group.
Blood and lymphatic system disorders
Hypophosphatemia
18.2%
2/11 • Number of events 2
Adverse events were reported as pooling all subjects together and were not broken out by group.
Musculoskeletal and connective tissue disorders
Joint effusion
9.1%
1/11 • Number of events 1
Adverse events were reported as pooling all subjects together and were not broken out by group.
Blood and lymphatic system disorders
Platelet count decreased
9.1%
1/11 • Number of events 1
Adverse events were reported as pooling all subjects together and were not broken out by group.
Immune system disorders
White blood cell decreased
9.1%
1/11 • Number of events 1
Adverse events were reported as pooling all subjects together and were not broken out by group.
Hepatobiliary disorders
AST elevation
18.2%
2/11 • Number of events 2
Adverse events were reported as pooling all subjects together and were not broken out by group.
Skin and subcutaneous tissue disorders
Alopecia
9.1%
1/11 • Number of events 1
Adverse events were reported as pooling all subjects together and were not broken out by group.
Eye disorders
Blurred vision
9.1%
1/11 • Number of events 1
Adverse events were reported as pooling all subjects together and were not broken out by group.
Gastrointestinal disorders
Epigastric pain
9.1%
1/11 • Number of events 1
Adverse events were reported as pooling all subjects together and were not broken out by group.
General disorders
Infusion related reaction
9.1%
1/11 • Number of events 1
Adverse events were reported as pooling all subjects together and were not broken out by group.
Respiratory, thoracic and mediastinal disorders
Shortness of Breath
9.1%
1/11 • Number of events 1
Adverse events were reported as pooling all subjects together and were not broken out by group.
Blood and lymphatic system disorders
Thrombocytopenia
9.1%
1/11 • Number of events 1
Adverse events were reported as pooling all subjects together and were not broken out by group.
Gastrointestinal disorders
Vomiting
9.1%
1/11 • Number of events 2
Adverse events were reported as pooling all subjects together and were not broken out by group.
Blood and lymphatic system disorders
Elavated LDH
9.1%
1/11 • Number of events 1
Adverse events were reported as pooling all subjects together and were not broken out by group.
Blood and lymphatic system disorders
Hypermagnesemia
9.1%
1/11 • Number of events 1
Adverse events were reported as pooling all subjects together and were not broken out by group.
Skin and subcutaneous tissue disorders
Mucositis oral
9.1%
1/11 • Number of events 1
Adverse events were reported as pooling all subjects together and were not broken out by group.
Musculoskeletal and connective tissue disorders
Back stiffness
9.1%
1/11 • Number of events 1
Adverse events were reported as pooling all subjects together and were not broken out by group.
Blood and lymphatic system disorders
Hypomagnesemia
18.2%
2/11 • Number of events 2
Adverse events were reported as pooling all subjects together and were not broken out by group.
Blood and lymphatic system disorders
Leukopenia
9.1%
1/11 • Number of events 1
Adverse events were reported as pooling all subjects together and were not broken out by group.

Additional Information

Giuseppe Giaccone

Lombardi Comprehensive Cancer Center

Phone: 202-687-7072

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place