Escalated Dose of Irinotecan in mCRC

NCT ID: NCT02256800

Last Updated: 2021-11-17

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

NA

Total Enrollment

213 participants

Study Classification

INTERVENTIONAL

Study Start Date

2014-08-13

Study Completion Date

2017-11-30

Brief Summary

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Metastatic diseases were found in 20-25% of patients with initial diagnosis of colorectal cancer and developed in up to 50% of patients. Owing to limited post-treatment response of 5-fluorouracil (5-FU) combined with leucovorin (LV) obtained in mCRC (metastatic colorectal cancer) patients, other therapeutic agents with different mechanisms were considered, such as irinotecan, a potent inhibitor of topoisomerase I, which is involved in the unwinding of DNA during replication. Bevacizumab is a humanized monoclonal antibody that inhibits tumor angiogenesis by blocking vascular endothelial growth factor (VEGF) and was the first antiangiogenic agent approved for the treatment of cancer.

Infusional fluorouracil/leucovorin plus irinotecan-based regimen (FOLFIRI) with bevacizumab has been widely used as first-line treatment for patients with metastatic colorectal cancer (mCRC). Recently, the investigators have shown that prospective analysis of uridine diphosphate glucuronosyl transferase 1A1 (UGT1A1) genotyping for irinotecan dose escalation (FOLFIRI regimen) with combination of bevacizumab biweekly as the first-line setting in mCRC patients (ASCO Abstract #491 - 2013 Gastrointestinal Cancers Symposium).

In this study, the investigators will enroll approximately 320 mCRC patients (It was considered that an increase of response rate of 15% compared to conventional irinotecan dose of 180 mg/m2, and these were chosen as parameters with which to calculate the study power. Initial power calculation was suggested that a minimum of 140 patients in each group would be required to achieve statistical significance with a power of 80% at the 5% significance level. It is estimated that about 10% of 320 mCRC patients fail to complete the study). For these enrolled patients, the investigators will randomize and divide these patients into two groups: control group and study group. Control group includes mCRC patients who will receive the conventional regimen of FOLFIRI plus bevacizumab. Otherwise, patients in the study group will have genotyping of UGT1A1 before therapy, and dose escalating of irinotecan will depend on results of genotyping.

Detailed Description

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Control group:

Regimen for treatment consisted of bevacizumab (Avastin) 5mg/Kg (IV infusion) on day 1, follow by irinotecan (180 mg/m2 as a 120-min IV infusion), LV (400 mg/m2 IV infusion over 2 hours), and 5-FU (2800 mg/m2 IV infusion over a 46-hour period), repeated every 2 weeks.

Study group: FOLFIRI (infusional fluorouracil/leucovorin plus irinotecan) + Bevacizumab. The dosage of irinotecan is adjusted to the UGT1A1 genotyping

The wild-type (6/6) of UGT1A1:

Regimen for treatment consisted of bevacizumab (Avastin) 5mg/Kg (IV infusion) on day 1, follow by irinotecan (180 mg/m2 as a 120-min IV infusion), LV (400 mg/m2 IV infusion over 2 hours), and 5-FU (2800 mg/m2 IV infusion over a 46-hour period), repeated every 2 weeks.

After 2 cycles of each different dose of irinotecan, we will observe the adverse effects (AEs) of hematological / non-hematological. If the grade is under the grade 2, we will escalate the dose of 30 mg/m2 gradually. The estimated maximal dose of irinotecan is 260 mg/m2.

The (6,7) type of UGT1A1:

Regimen for treatment consisted of bevacizumab (Avastin) 5mg/Kg (IV infusion) on day 1, follow by irinotecan (180 mg/m2 as a 120-min IV infusion), LV (400 mg/m2 IV infusion over 2 hours), and 5-FU (2800 mg/m2 IV infusion over a 46-hour period), repeated every 2 weeks.

After 2 cycles of each different dose of irinotecan, we will observe the adverse effects (AEs) of hematological / non-hematological. If the grade is under the grade 2, we will escalate the dose of 30 mg/m2 gradually. The estimated maximal dose of irinotecan is 240 mg/m2.

The (7,7) type of UGT1A1:

Regimen for treatment consisted of bevacizumab (Avastin) 5mg/Kg (IV infusion) on day 1, follow by irinotecan (120 mg/m2 as a 120-min IV infusion), LV (400 mg/m2 IV infusion over 2 hours), and 5-FU (2800 mg/m2 IV infusion over a 46-hour period), repeated every 2 weeks.

After 2 cycles of each different dose of irinotecan, we will observe the adverse effects (AEs) of hematological / non-hematological. If the grade is under the grade 2, we will escalate the dose of 30 mg/m2 gradually. The estimated maximal dose of irinotecan is 180 mg/m2.

Conditions

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Metastatic Colorectal Cancer

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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UGT1A1 genotyping (6,6)

The investigators will escalate the dosage of irinotecan from 180mg/m2 to 260 mg/m2

Group Type EXPERIMENTAL

UGT1A1 genotyping (6,6)

Intervention Type GENETIC

The investigators will use the regimen as following:

Regimen for treatment consisted of bevacizumab (Avastin) 5mg/Kg (IV infusion) on day 1, follow by irinotecan (180 mg/m2 as a 120-min IV infusion), Leucovorin (400 mg/m2 IV infusion over 2 hours), and 5-FU (2800 mg/m2 IV infusion over a 46-hour period), repeated every 2 weeks.

After 2 cycles of each different dose of irinotecan, we will observe the adverse effects (AEs) of hematological / non-hematological. If the grade is under the grade 2, we will escalate the dose of 30 mg/m2 gradually. The estimated maximal dose of irinotecan is 260 mg/m2.

bevacizumab (Avastin)

Intervention Type DRUG

bevacizumab as target therapy

irinotecan

Intervention Type DRUG

irinotecan as escalating dose according to UGT1A1 genotyping

Leucovorin

Intervention Type DRUG

combined with 5-FU

5-FU

Intervention Type DRUG

combined with irinotecan

UGTA1T1 genotyping (6,7)

The investigators will escalate the dosage of irinotecan from 180mg/m2 to 240 mg/m2

Group Type EXPERIMENTAL

UGTIA1 genotyping (6,7)

Intervention Type GENETIC

The investigators will use the regimen as following:

Regimen for treatment consisted of bevacizumab (Avastin) 5mg/Kg (IV infusion) on day 1, follow by irinotecan (180 mg/m2 as a 120-min IV infusion), Leucovorin (400 mg/m2 IV infusion over 2 hours), and 5-FU (2800 mg/m2 IV infusion over a 46-hour period), repeated every 2 weeks.

After 2 cycles of each different dose of irinotecan, we will observe the adverse effects (AEs) of hematological / non-hematological. If the grade is under the grade 2, we will escalate the dose of 30 mg/m2 gradually. The estimated maximal dose of irinotecan is 240 mg/m2.

bevacizumab (Avastin)

Intervention Type DRUG

bevacizumab as target therapy

irinotecan

Intervention Type DRUG

irinotecan as escalating dose according to UGT1A1 genotyping

Leucovorin

Intervention Type DRUG

combined with 5-FU

5-FU

Intervention Type DRUG

combined with irinotecan

UGTA1T1 genotyping (7,7)

The investigators will escalate the dosage of irinotecan from 120mg/m2 to 180 mg/m2

Group Type EXPERIMENTAL

UGTIA1 genotyping (7,7)

Intervention Type GENETIC

The investigators will use the regimen as following:

Regimen for treatment consisted of bevacizumab (Avastin) 5mg/Kg (IV infusion) on day 1, follow by irinotecan (120 mg/m2 as a 120-min IV infusion), Leucovorin (400 mg/m2 IV infusion over 2 hours), and 5-FU (2800 mg/m2 IV infusion over a 46-hour period), repeated every 2 weeks.

After 2 cycles of each different dose of irinotecan, we will observe the adverse effects (AEs) of hematological / non-hematological. If the grade is under the grade 2, we will escalate the dose of 30 mg/m2 gradually. The estimated maximal dose of irinotecan is 180 mg/m2.

bevacizumab (Avastin)

Intervention Type DRUG

bevacizumab as target therapy

irinotecan

Intervention Type DRUG

irinotecan as escalating dose according to UGT1A1 genotyping

Leucovorin

Intervention Type DRUG

combined with 5-FU

5-FU

Intervention Type DRUG

combined with irinotecan

UGT1A1 non-genotyping

The investigators will maintain the dosage of irinotecan by 180mg/m2

Group Type EXPERIMENTAL

UGT1A1 non-genotyping

Intervention Type GENETIC

The investigators will use the regimen as following:

Regimen for treatment consisted of bevacizumab (Avastin) 5mg/Kg (IV infusion) on day 1, follow by irinotecan (180 mg/m2 as a 120-min IV infusion), Leucovorin (400 mg/m2 IV infusion over 2 hours), and 5-FU (2800 mg/m2 IV infusion over a 46-hour period), repeated every 2 weeks.

bevacizumab (Avastin)

Intervention Type DRUG

bevacizumab as target therapy

irinotecan

Intervention Type DRUG

irinotecan as escalating dose according to UGT1A1 genotyping

Leucovorin

Intervention Type DRUG

combined with 5-FU

5-FU

Intervention Type DRUG

combined with irinotecan

Interventions

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UGT1A1 genotyping (6,6)

The investigators will use the regimen as following:

Regimen for treatment consisted of bevacizumab (Avastin) 5mg/Kg (IV infusion) on day 1, follow by irinotecan (180 mg/m2 as a 120-min IV infusion), Leucovorin (400 mg/m2 IV infusion over 2 hours), and 5-FU (2800 mg/m2 IV infusion over a 46-hour period), repeated every 2 weeks.

After 2 cycles of each different dose of irinotecan, we will observe the adverse effects (AEs) of hematological / non-hematological. If the grade is under the grade 2, we will escalate the dose of 30 mg/m2 gradually. The estimated maximal dose of irinotecan is 260 mg/m2.

Intervention Type GENETIC

UGTIA1 genotyping (6,7)

The investigators will use the regimen as following:

Regimen for treatment consisted of bevacizumab (Avastin) 5mg/Kg (IV infusion) on day 1, follow by irinotecan (180 mg/m2 as a 120-min IV infusion), Leucovorin (400 mg/m2 IV infusion over 2 hours), and 5-FU (2800 mg/m2 IV infusion over a 46-hour period), repeated every 2 weeks.

After 2 cycles of each different dose of irinotecan, we will observe the adverse effects (AEs) of hematological / non-hematological. If the grade is under the grade 2, we will escalate the dose of 30 mg/m2 gradually. The estimated maximal dose of irinotecan is 240 mg/m2.

Intervention Type GENETIC

UGTIA1 genotyping (7,7)

The investigators will use the regimen as following:

Regimen for treatment consisted of bevacizumab (Avastin) 5mg/Kg (IV infusion) on day 1, follow by irinotecan (120 mg/m2 as a 120-min IV infusion), Leucovorin (400 mg/m2 IV infusion over 2 hours), and 5-FU (2800 mg/m2 IV infusion over a 46-hour period), repeated every 2 weeks.

After 2 cycles of each different dose of irinotecan, we will observe the adverse effects (AEs) of hematological / non-hematological. If the grade is under the grade 2, we will escalate the dose of 30 mg/m2 gradually. The estimated maximal dose of irinotecan is 180 mg/m2.

Intervention Type GENETIC

UGT1A1 non-genotyping

The investigators will use the regimen as following:

Regimen for treatment consisted of bevacizumab (Avastin) 5mg/Kg (IV infusion) on day 1, follow by irinotecan (180 mg/m2 as a 120-min IV infusion), Leucovorin (400 mg/m2 IV infusion over 2 hours), and 5-FU (2800 mg/m2 IV infusion over a 46-hour period), repeated every 2 weeks.

Intervention Type GENETIC

bevacizumab (Avastin)

bevacizumab as target therapy

Intervention Type DRUG

irinotecan

irinotecan as escalating dose according to UGT1A1 genotyping

Intervention Type DRUG

Leucovorin

combined with 5-FU

Intervention Type DRUG

5-FU

combined with irinotecan

Intervention Type DRUG

Other Intervention Names

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UGT1A1*1*1 UGT1A1*1*28 UGT1A1*28*28 Avastin Campto

Eligibility Criteria

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Inclusion Criteria

1. 20 y/o ≦ Age ≦ 80y/o
2. Either metachronous or synchronous mCRC can be enrolled
3. Female patients need not ready to be pregnant or breastfeeding
4. No major underlying diseases (such as cardiovascular, cerebrovascular, malignant hypertension, kidney, liver and other major diseases)
5. mCRC be proven by pathologists or radiologists
6. Subjects are willing to sign an inform consent form

Exclusion Criteria

* Patients who do not meet the including criteria or unwilling to participate
Minimum Eligible Age

20 Years

Maximum Eligible Age

80 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Jaw-Yuan Wang, MD, PhD

OTHER

Sponsor Role lead

Responsible Party

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Jaw-Yuan Wang, MD, PhD

Professor

Responsibility Role SPONSOR_INVESTIGATOR

Locations

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Chung-Ho Memorial Hospital, Kaohsiung Medical University:

Kaohsiung City, , Taiwan

Site Status

Countries

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Taiwan

References

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Tsai HL, Huang CW, Lin YW, Wang JH, Wu CC, Sung YC, Chen TL, Wang HM, Tang HC, Chen JB, Ke TW, Tsai CS, Huang HY, Wang JY. Determination of the UGT1A1 polymorphism as guidance for irinotecan dose escalation in metastatic colorectal cancer treated with first-line bevacizumab and FOLFIRI (PURE FIST). Eur J Cancer. 2020 Oct;138:19-29. doi: 10.1016/j.ejca.2020.05.031. Epub 2020 Aug 20.

Reference Type DERIVED
PMID: 32829105 (View on PubMed)

Yeh YS, Tsai HL, Huang CW, Wang JH, Lin YW, Tang HC, Sung YC, Wu CC, Lu CY, Wang JY. Prospective analysis of UGT1A1 promoter polymorphism for irinotecan dose escalation in metastatic colorectal cancer patients treated with bevacizumab plus FOLFIRI as the first-line setting: study protocol for a randomized controlled trial. Trials. 2016 Jan 25;17:46. doi: 10.1186/s13063-016-1153-3.

Reference Type DERIVED
PMID: 26811156 (View on PubMed)

Other Identifiers

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KMUHIRB-20130020

Identifier Type: -

Identifier Source: org_study_id