Trial Outcomes & Findings for A Pilot Clinical Trial of Overminus Spectacle Therapy for Intermittent Exotropia (NCT NCT02223650)

NCT ID: NCT02223650

Last Updated: 2017-05-19

Results Overview

At each visit, control of the exodeviation was measured at distance (6 meters) and at near (1/3 meters) using the Office Control Score\* which ranges from 0 (phoria, best control) to 5 (constant exotropia, worst control). Due to the variability of single measures of control, we used a "triple control score," which is a mean of 3 measures obtained at specific time-points during a 20- to 40-minute office examination. The primary analysis was an intention-to-treat treatment group comparison of mean 8-week distance control using an analysis of covariance (ANCOVA) model which adjusted for baseline distance control. \*Mohney BG, Holmes JM. An office-based scale for assessing control in intermittent exotropia. Strabismus 2006;14(3):147-50.

Recruitment status

COMPLETED

Study phase

NA

Target enrollment

58 participants

Primary outcome timeframe

8 weeks

Results posted on

2017-05-19

Participant Flow

Between December 2014 and May 2015, 58 children were enrolled at 21 sites, with 31 participants assigned to observation and 27 to overminus treatment.

Participant milestones

Participant milestones
Measure
Overminus Treatment
2.50D overminus spectacles Overminus treatment: 2.50D overminus spectacles
Non-overminus Treatment
spectacles without overminus or no spectacles Non-overminus treatment: spectacles without overminus or no spectacles
Overall Study
STARTED
27
31
Overall Study
COMPLETED
27
31
Overall Study
NOT COMPLETED
0
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

A Pilot Clinical Trial of Overminus Spectacle Therapy for Intermittent Exotropia

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Overminus Treatment
n=27 Participants
2.50D overminus spectacles Overminus treatment: 2.50D overminus spectacles
Non-overminus Treatment
n=31 Participants
spectacles without overminus or no spectacles Non-overminus treatment: spectacles without overminus or no spectacles
Total
n=58 Participants
Total of all reporting groups
Age, Continuous
5.2 years
STANDARD_DEVIATION 1 • n=5 Participants
5.1 years
STANDARD_DEVIATION 1.2 • n=7 Participants
5.1 years
STANDARD_DEVIATION 1.1 • n=5 Participants
Age, Customized
3 to <4 years
7 participants
n=5 Participants
3 participants
n=7 Participants
10 participants
n=5 Participants
Age, Customized
4 to <5 years
4 participants
n=5 Participants
11 participants
n=7 Participants
15 participants
n=5 Participants
Age, Customized
5 to <6 years
9 participants
n=5 Participants
10 participants
n=7 Participants
19 participants
n=5 Participants
Age, Customized
6 to <7 years
7 participants
n=5 Participants
7 participants
n=7 Participants
14 participants
n=5 Participants
Sex: Female, Male
Female
18 Participants
n=5 Participants
18 Participants
n=7 Participants
36 Participants
n=5 Participants
Sex: Female, Male
Male
9 Participants
n=5 Participants
13 Participants
n=7 Participants
22 Participants
n=5 Participants
Race/Ethnicity, Customized
White
14 participants
n=5 Participants
15 participants
n=7 Participants
29 participants
n=5 Participants
Race/Ethnicity, Customized
Black/African American
2 participants
n=5 Participants
4 participants
n=7 Participants
6 participants
n=5 Participants
Race/Ethnicity, Customized
Hispanic or Latino
6 participants
n=5 Participants
9 participants
n=7 Participants
15 participants
n=5 Participants
Race/Ethnicity, Customized
Asian
5 participants
n=5 Participants
3 participants
n=7 Participants
8 participants
n=5 Participants
Refractive error in more myopic eye (spherical equivalent, D)
>+0.50 to +1.00
13 participants
n=5 Participants
15 participants
n=7 Participants
28 participants
n=5 Participants
Refractive error in more myopic eye (spherical equivalent, D)
0 to +0.50
5 participants
n=5 Participants
9 participants
n=7 Participants
14 participants
n=5 Participants
Refractive error in more myopic eye (spherical equivalent, D)
<0 to >-0.50
2 participants
n=5 Participants
1 participants
n=7 Participants
3 participants
n=5 Participants
Refractive error in more myopic eye (spherical equivalent, D)
-0.50 to >-1.00
4 participants
n=5 Participants
1 participants
n=7 Participants
5 participants
n=5 Participants
Refractive error in more myopic eye (spherical equivalent, D)
-1.00 to >-1.50
1 participants
n=5 Participants
0 participants
n=7 Participants
1 participants
n=5 Participants
Refractive error in more myopic eye (spherical equivalent, D)
-1.50 to >-2.00
1 participants
n=5 Participants
0 participants
n=7 Participants
1 participants
n=5 Participants
Refractive error in more myopic eye (spherical equivalent, D)
-2.00 to >-2.50
0 participants
n=5 Participants
2 participants
n=7 Participants
2 participants
n=5 Participants
Refractive error in more myopic eye (spherical equivalent, D)
-2.50 to >-3.00
0 participants
n=5 Participants
2 participants
n=7 Participants
2 participants
n=5 Participants
Refractive error in more myopic eye (spherical equivalent, D)
<=-3.00
1 participants
n=5 Participants
1 participants
n=7 Participants
2 participants
n=5 Participants
Accommodative convergence over accommodation (AC/A) ratio
<2.5
12 participants
n=5 Participants
13 participants
n=7 Participants
25 participants
n=5 Participants
Accommodative convergence over accommodation (AC/A) ratio
2.5 to 6.0
12 participants
n=5 Participants
15 participants
n=7 Participants
27 participants
n=5 Participants
Accommodative convergence over accommodation (AC/A) ratio
>6.0
3 participants
n=5 Participants
3 participants
n=7 Participants
6 participants
n=5 Participants

PRIMARY outcome

Timeframe: 8 weeks

At each visit, control of the exodeviation was measured at distance (6 meters) and at near (1/3 meters) using the Office Control Score\* which ranges from 0 (phoria, best control) to 5 (constant exotropia, worst control). Due to the variability of single measures of control, we used a "triple control score," which is a mean of 3 measures obtained at specific time-points during a 20- to 40-minute office examination. The primary analysis was an intention-to-treat treatment group comparison of mean 8-week distance control using an analysis of covariance (ANCOVA) model which adjusted for baseline distance control. \*Mohney BG, Holmes JM. An office-based scale for assessing control in intermittent exotropia. Strabismus 2006;14(3):147-50.

Outcome measures

Outcome measures
Measure
Overminus Treatment
n=27 Participants
2.50D overminus spectacles Overminus treatment: 2.50D overminus spectacles
Non-overminus Treatment
n=31 Participants
spectacles without overminus or no spectacles Non-overminus treatment: spectacles without overminus or no spectacles
Mean Distance Exotropia Control Score
2.0 points on control score scale
Standard Deviation 1.4
2.8 points on control score scale
Standard Deviation 1.4

SECONDARY outcome

Timeframe: 8 weeks

At each visit, control of the exodeviation was measured at near (1/3 meters) using the Office Control Score which ranges from 0 (phoria, best control) to 5 (constant exotropia, worst control). Due to the variability of single measures of control, we used a "triple control score," which is a mean of 3 measures obtained at specific time-points during a 20- to 40-minute office examination. The secondary analysis was an intention-to-treat treatment group comparison of mean 8-week near control using an analysis of covariance (ANCOVA) model which adjusted for baseline near control.

Outcome measures

Outcome measures
Measure
Overminus Treatment
n=27 Participants
2.50D overminus spectacles Overminus treatment: 2.50D overminus spectacles
Non-overminus Treatment
n=31 Participants
spectacles without overminus or no spectacles Non-overminus treatment: spectacles without overminus or no spectacles
Mean Near Exotropia Control Score
0.9 points on control score scale
Standard Deviation 1.2
1.2 points on control score scale
Standard Deviation 1.1

SECONDARY outcome

Timeframe: 8 weeks

Control of exodeviation will be assessed in the habitual correction at distance (6 meters) and near (1/3 meter) using a standardized IXT control scale.

Outcome measures

Outcome measures
Measure
Overminus Treatment
n=27 Participants
2.50D overminus spectacles Overminus treatment: 2.50D overminus spectacles
Non-overminus Treatment
n=31 Participants
spectacles without overminus or no spectacles Non-overminus treatment: spectacles without overminus or no spectacles
Distribution of Distance Control Score at 8-week Outcome
0 to <1
4 participants
1 participants
Distribution of Distance Control Score at 8-week Outcome
1 to <2
11 participants
7 participants
Distribution of Distance Control Score at 8-week Outcome
2 to <3
5 participants
10 participants
Distribution of Distance Control Score at 8-week Outcome
3 to <4
1 participants
3 participants
Distribution of Distance Control Score at 8-week Outcome
4 to 5
6 participants
10 participants

SECONDARY outcome

Timeframe: 8 weeks

Control of exodeviation will be assessed in the habitual correction at distance (6 meters) and near (1/3 meter) using a standardized IXT control scale.

Outcome measures

Outcome measures
Measure
Overminus Treatment
n=27 Participants
2.50D overminus spectacles Overminus treatment: 2.50D overminus spectacles
Non-overminus Treatment
n=31 Participants
spectacles without overminus or no spectacles Non-overminus treatment: spectacles without overminus or no spectacles
Distribution of Near Control Score at 8-week Outcome
0 to <1
15 participants
10 participants
Distribution of Near Control Score at 8-week Outcome
1 to <2
7 participants
13 participants
Distribution of Near Control Score at 8-week Outcome
2 to <3
2 participants
3 participants
Distribution of Near Control Score at 8-week Outcome
3 to <4
2 participants
5 participants
Distribution of Near Control Score at 8-week Outcome
4 to 5
1 participants
0 participants

SECONDARY outcome

Timeframe: 8 weeks

A comparison of the proportion of subjects showing a "treatment response," defined as an improvement of at least 1 point in distance control (mean of the 3 assessments over the exam) between enrollment and 8 weeks.

Outcome measures

Outcome measures
Measure
Overminus Treatment
n=27 Participants
2.50D overminus spectacles Overminus treatment: 2.50D overminus spectacles
Non-overminus Treatment
n=31 Participants
spectacles without overminus or no spectacles Non-overminus treatment: spectacles without overminus or no spectacles
Proportion of Subjects With Distance Control Treatment Response
16 participants
12 participants

SECONDARY outcome

Timeframe: 8 weeks

Population: Spectacle-related questions at follow up apply only to observation participants prescribed correction (N=10 (32%) and to all overminus group participants N=27 (100%)).

A brief survey of symptoms that may be associated with overminus such as headaches, eye strain, and problems with spectacle wear will be administered to the parents of the subjects. Parents are asked to respond to the survey questions based on their observations of their child in the past 2 weeks. Response options are based on frequency of observations; never, rarely, sometimes, often, always, and not applicable. Survey items were derived based on expert opinion of pediatric ophthalmologists and optometrists on the study planning committee. The response options were a 5-point Likert-type scale based on frequency of observations: never = score of 0, almost never = 1, sometimes = 2, often = 3, and always = 4.

Outcome measures

Outcome measures
Measure
Overminus Treatment
n=27 Participants
2.50D overminus spectacles Overminus treatment: 2.50D overminus spectacles
Non-overminus Treatment
n=10 Participants
spectacles without overminus or no spectacles Non-overminus treatment: spectacles without overminus or no spectacles
Symptom Survey Response to Question: Has Child Looked Over His/Her Spectacles Since Enrollment?
Looked over specatcles: Always
0 participants
0 participants
Symptom Survey Response to Question: Has Child Looked Over His/Her Spectacles Since Enrollment?
Looked over specatcles: Often
3 participants
1 participants
Symptom Survey Response to Question: Has Child Looked Over His/Her Spectacles Since Enrollment?
Looked over specatcles: Sometimes
7 participants
2 participants
Symptom Survey Response to Question: Has Child Looked Over His/Her Spectacles Since Enrollment?
Looked over specatcles: Rarely
2 participants
2 participants
Symptom Survey Response to Question: Has Child Looked Over His/Her Spectacles Since Enrollment?
Looked over specatcles: Never
15 participants
5 participants

SECONDARY outcome

Timeframe: 8 weeks

Stereoacuity will be assessed with habitual correction using the Randot Preschool stereotest at near (performed at 40 cm). A specific level of stereoacuity is not required for eligibility.

Outcome measures

Outcome measures
Measure
Overminus Treatment
n=27 Participants
2.50D overminus spectacles Overminus treatment: 2.50D overminus spectacles
Non-overminus Treatment
n=31 Participants
spectacles without overminus or no spectacles Non-overminus treatment: spectacles without overminus or no spectacles
Stereoacuity
2.2 log arcsecond
Standard Deviation 0.5
2.2 log arcsecond
Standard Deviation 0.6

SECONDARY outcome

Timeframe: 8 weeks

Monocular distance visual acuity testing with the habitual correction and without cycloplegia was measured using the Amblyopia Treatment Study HOTV testing protocol on any certified visual acuity system. The treatment groups were not different with respect to 8-week control PACT at distance

Outcome measures

Outcome measures
Measure
Overminus Treatment
n=27 Participants
2.50D overminus spectacles Overminus treatment: 2.50D overminus spectacles
Non-overminus Treatment
n=31 Participants
spectacles without overminus or no spectacles Non-overminus treatment: spectacles without overminus or no spectacles
Distance Visual Acuity
21.1 prism diopters
Standard Deviation 11.2
23.0 prism diopters
Standard Deviation 6.3

SECONDARY outcome

Timeframe: 8 weeks

Binocular near visual acuity was tested in habitual correction using the ATS4 near visual acuity test. The treatment groups were not different with respect to 8-week control at near.

Outcome measures

Outcome measures
Measure
Overminus Treatment
n=27 Participants
2.50D overminus spectacles Overminus treatment: 2.50D overminus spectacles
Non-overminus Treatment
n=31 Participants
spectacles without overminus or no spectacles Non-overminus treatment: spectacles without overminus or no spectacles
Binocular Near Visual Acuity
12.8 prism diopters
Standard Deviation 8.3
16.9 prism diopters
Standard Deviation 8.4

SECONDARY outcome

Timeframe: 8 weeks

A brief survey of symptoms that may be associated with overminus such as headaches, eye strain, and problems with spectacle wear will be administered to the parents of the subjects. Parents are asked to respond to the survey questions based on their observations of their child in the past 2 weeks. Response options are based on frequency of observations; never, rarely, sometimes, often, always, and not applicable. Survey items were derived based on expert opinion of pediatric ophthalmologists and optometrists on the study planning committee. The response options were a 5-point Likert-type scale based on frequency of observations: never = score of 0, almost never = 1, sometimes = 2, often = 3, and always = 4.

Outcome measures

Outcome measures
Measure
Overminus Treatment
n=27 Participants
2.50D overminus spectacles Overminus treatment: 2.50D overminus spectacles
Non-overminus Treatment
n=31 Participants
spectacles without overminus or no spectacles Non-overminus treatment: spectacles without overminus or no spectacles
Symptom Survey Response to Question: Has Your Child Had Eyestrain (Tired, Sore, or Uncomfortable Eyes)?
Often
0 participants
0 participants
Symptom Survey Response to Question: Has Your Child Had Eyestrain (Tired, Sore, or Uncomfortable Eyes)?
Never
18 participants
24 participants
Symptom Survey Response to Question: Has Your Child Had Eyestrain (Tired, Sore, or Uncomfortable Eyes)?
Always
0 participants
0 participants
Symptom Survey Response to Question: Has Your Child Had Eyestrain (Tired, Sore, or Uncomfortable Eyes)?
Sometimes
4 participants
3 participants
Symptom Survey Response to Question: Has Your Child Had Eyestrain (Tired, Sore, or Uncomfortable Eyes)?
Rarely
5 participants
4 participants

SECONDARY outcome

Timeframe: 8 weeks

Population: Spectacle-related questions at follow up apply only to observation participants prescribed correction (N=10 (32%) and to all overminus group participants N=27 (100%)).

A brief survey of symptoms that may be associated with overminus such as headaches, eye strain, and problems with spectacle wear will be administered to the parents of the subjects. Parents are asked to respond to the survey questions based on their observations of their child in the past 2 weeks. Response options are based on frequency of observations; never, rarely, sometimes, often, always, and not applicable. Survey items were derived based on expert opinion of pediatric ophthalmologists and optometrists on the study planning committee. The response options were a 5-point Likert-type scale based on frequency of observations: never = score of 0, almost never = 1, sometimes = 2, often = 3, and always = 4.

Outcome measures

Outcome measures
Measure
Overminus Treatment
n=27 Participants
2.50D overminus spectacles Overminus treatment: 2.50D overminus spectacles
Non-overminus Treatment
n=31 Participants
spectacles without overminus or no spectacles Non-overminus treatment: spectacles without overminus or no spectacles
Symptom Survey Response to Question: Since Enrollment Has Your Child Avoided Reading or Doing Things up Close?
Always
0 participants
0 participants
Symptom Survey Response to Question: Since Enrollment Has Your Child Avoided Reading or Doing Things up Close?
Often
0 participants
0 participants
Symptom Survey Response to Question: Since Enrollment Has Your Child Avoided Reading or Doing Things up Close?
Sometimes
1 participants
1 participants
Symptom Survey Response to Question: Since Enrollment Has Your Child Avoided Reading or Doing Things up Close?
Rarely
0 participants
2 participants
Symptom Survey Response to Question: Since Enrollment Has Your Child Avoided Reading or Doing Things up Close?
Never
26 participants
28 participants

SECONDARY outcome

Timeframe: 8 weeks

A brief survey of symptoms that may be associated with overminus such as headaches, eye strain, and problems with spectacle wear will be administered to the parents of the subjects. Parents are asked to respond to the survey questions based on their observations of their child in the past 2 weeks. Response options are based on frequency of observations; never, rarely, sometimes, often, always, and not applicable. Survey items were derived based on expert opinion of pediatric ophthalmologists and optometrists on the study planning committee. The response options were a 5-point Likert-type scale based on frequency of observations: never = score of 0, almost never = 1, sometimes = 2, often = 3, and always = 4.

Outcome measures

Outcome measures
Measure
Overminus Treatment
n=27 Participants
2.50D overminus spectacles Overminus treatment: 2.50D overminus spectacles
Non-overminus Treatment
n=31 Participants
spectacles without overminus or no spectacles Non-overminus treatment: spectacles without overminus or no spectacles
Symptom Survey Response to Question: Has Your Child Reported Blurry Vision?
Sometimes
1 participants
1 participants
Symptom Survey Response to Question: Has Your Child Reported Blurry Vision?
Rarely
1 participants
1 participants
Symptom Survey Response to Question: Has Your Child Reported Blurry Vision?
Always
0 participants
0 participants
Symptom Survey Response to Question: Has Your Child Reported Blurry Vision?
Often
0 participants
0 participants
Symptom Survey Response to Question: Has Your Child Reported Blurry Vision?
Never
25 participants
29 participants

SECONDARY outcome

Timeframe: 8 weeks

A comparison of the proportion of subjects showing a "treatment response," defined as an improvement of at least 1 point in near control (mean of the 3 assessments over the exam) between enrollment and 8 weeks.

Outcome measures

Outcome measures
Measure
Overminus Treatment
n=27 Participants
2.50D overminus spectacles Overminus treatment: 2.50D overminus spectacles
Non-overminus Treatment
n=31 Participants
spectacles without overminus or no spectacles Non-overminus treatment: spectacles without overminus or no spectacles
Proportion of Subjects With Near Control Treatment Response
7 participants
8 participants

Adverse Events

Overminus Treatment

Serious events: 0 serious events
Other events: 3 other events
Deaths: 0 deaths

Non-overminus Treatment

Serious events: 0 serious events
Other events: 2 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
Overminus Treatment
n=27 participants at risk
2.50D overminus spectacles Overminus treatment: 2.50D overminus spectacles
Non-overminus Treatment
n=31 participants at risk
spectacles without overminus or no spectacles Non-overminus treatment: spectacles without overminus or no spectacles
Eye disorders
Development of esodeviation
3.7%
1/27 • Number of events 1 • Baseline to 8 weeks after randomization.
0.00%
0/31 • Baseline to 8 weeks after randomization.
Eye disorders
Reduction in monocular distance visual acuity >=2 lines
7.4%
2/27 • Number of events 2 • Baseline to 8 weeks after randomization.
3.2%
1/31 • Number of events 1 • Baseline to 8 weeks after randomization.
Eye disorders
Reduction in binocular near visual acuity >=2 lines
0.00%
0/27 • Baseline to 8 weeks after randomization.
3.2%
1/31 • Number of events 1 • Baseline to 8 weeks after randomization.

Additional Information

Ray Kraker, M.S.P.H., Director of PEDIG Coordinating Center

Jaeb Center for Health Research

Phone: (813) 975-8690

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place