LEE011 for Patients With CDK4/6 Pathway Activated Tumors (SIGNATURE)

NCT ID: NCT02187783

Last Updated: 2019-07-18

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

106 participants

Study Classification

INTERVENTIONAL

Study Start Date

2014-08-25

Study Completion Date

2018-01-17

Brief Summary

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The purpose of this signal seeking study was to determine whether treatment with LEE011 demonstrates sufficient efficacy in CDK4/6 pathway activated solid tumors and/or hematologic malignancies to warrant further study.

Detailed Description

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Conditions

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Tumors With CDK4/6 Pathway Activation

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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LEE011

LEE011 600 mg (hard gelatin capsules) was administered orally once daily for 3 weeks on/1 week off. A complete treatment cycle was defined as 28 days.

Group Type EXPERIMENTAL

LEE011

Intervention Type DRUG

Study drug was provided in 200 mg and 50 mg hard gelatin capsules to be taken orally

Interventions

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LEE011

Study drug was provided in 200 mg and 50 mg hard gelatin capsules to be taken orally

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Patient had a confirmed diagnosis of a select solid tumor (except breast cancer (however, triple negative was included), liposarcoma, CRPC, melanoma and teratoma) or hematological malignancy (except mantle cell lymphoma).
* Patient must have been pre-identified as having a tumor with CDK4 amplification or mutation, CDK6 amplification or mutation, Cyclin D1 (CCND1) amplification, Cyclin D3 (CCND3) amplification, or p16 (CDKN2A) mutation
* Patient had received at least one prior treatment for recurrent, metastatic and /or locally advanced disease and for whom no standard therapy options are anticipated to result in a durable remission.
* Patient had progressive and measurable disease as per RECIST 1.1. or other appropriate hematological guidelines.
* Patient had an Eastern Cooperative Oncology Group (ECOG) performance status ≤ 1

Exclusion Criteria

* Patients had received prior treatment with LEE011.
* Patient had clinically significant resting bradycardia (heart rate \< 50 at rest), tachycardia (heart rate \> 90 at rest), PR interval \> 220 msec, QRS interval \> 109 msec, or QTcF \> 450 msec.
* Patients had primary CNS tumor or CNS tumor involvement
* Patient had received chemotherapy or anticancer therapy ≤ 4 weeks prior to starting study drug
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status

Alaska Clinical Research

Anchorage, Alaska, United States

Site Status

Arizona Oncology Associates Dept. Of Onc.

Phoenix, Arizona, United States

Site Status

University of Arkansas/ Arkansas Cancer Research Center UA Medical Sciences

Little Rock, Arkansas, United States

Site Status

PCR Oncology

Pismo Beach, California, United States

Site Status

University of California Davis Cancer Center UC Davis Cancer (3)

Sacramento, California, United States

Site Status

Sarah Cannon Research Institute

Denver, Colorado, United States

Site Status

Danbury Hospital

Danbury, Connecticut, United States

Site Status

Yale University School of Medicine Smilow Cancer Hospital

New Haven, Connecticut, United States

Site Status

Whittingham Cancer Center Norwalk Hospital

Norwalk, Connecticut, United States

Site Status

Stamford Hospital Med. Oncology Hematology Res.

Stamford, Connecticut, United States

Site Status

Florida Hospital Cancer Institute

Orlando, Florida, United States

Site Status

NorthWest Georgia Oncology Centers NW Georgia Oncology

Marietta, Georgia, United States

Site Status

Harbin Clinic Medical Oncology Clin. Res.

Rome, Georgia, United States

Site Status

Queen's Medical Center Queens Cancer Center

Honolulu, Hawaii, United States

Site Status

Northwestern Medicine Developmental Therapeutics Institute

Chicago, Illinois, United States

Site Status

Indiana University Indiana Univ. - Purdue Univ.

Indianapolis, Indiana, United States

Site Status

Northern Indiana Cancer Research Consortium No. Indiana Cancer Res.

South Bend, Indiana, United States

Site Status

University of Iowa Hospitals & Clinics Regulatory Contact 2

Iowa City, Iowa, United States

Site Status

New England Cancer Specialists

Scarborough, Maine, United States

Site Status

St. Agnes Hospital St. Agnes Hospital (2)

Baltimore, Maryland, United States

Site Status

Michigan Medicine University of Michigan Int. Medicine Oncology

Ann Arbor, Michigan, United States

Site Status

Cancer and Hematology Centers of West Michigan Dept. of Oncology

Grand Rapids, Michigan, United States

Site Status

Saint Luke's Hospital/Marion Bloch Neuroscience Institute St. Luke's Hospital (4)

Kansas City, Missouri, United States

Site Status

Research Medical Center Research Med Center (2)

Kansas City, Missouri, United States

Site Status

Comprehensive Cancer Centers of Nevada CCC of Nevada- Southwest (2)

Las Vegas, Nevada, United States

Site Status

Cooper Health System Cooper Health System (5)

Camden, New Jersey, United States

Site Status

Rutgers Cancer Institute of New Jersey

New Brunswick, New Jersey, United States

Site Status

New Mexico Cancer Care Alliance

Albuquerque, New Mexico, United States

Site Status

Cancer Center at Presbyterian

Albuquerque, New Mexico, United States

Site Status

Broome Oncology Broome Oncology (2)

Johnson City, New York, United States

Site Status

University of N C at Chapel Hill Physician Office Building

Chapel Hill, North Carolina, United States

Site Status

Carolina Oncology Specialists, PC

Hickory, North Carolina, United States

Site Status

Wake Forest University Baptist Medical Center

Winston-Salem, North Carolina, United States

Site Status

Oncology Hematology Care Inc Oncology Hematology Care 2

Cincinnati, Ohio, United States

Site Status

Cleveland Clinic Foundation Taussig Cancer Institute

Cleveland, Ohio, United States

Site Status

Ohio State University Medical Center Comprehensive Cancer Center

Columbus, Ohio, United States

Site Status

Oregon Health and Science University Oregon Health & Science U (56)

Portland, Oregon, United States

Site Status

Salem Health

Salem, Oregon, United States

Site Status

Fox Chase Cancer Center Dept of Medical Oncology

Philadelphia, Pennsylvania, United States

Site Status

Rhode Island Hospital Rhode Island Hosp. (2)

Providence, Rhode Island, United States

Site Status

Greenville Health System ITOR - Cancer Institute

Greenville, South Carolina, United States

Site Status

Sanford University of South Dakota Medical Center Sanford Health

Sioux Falls, South Dakota, United States

Site Status

Chattanooga Oncology and Hematology Assoicates, PC Chattanooga Oncology

Chattanooga, Tennessee, United States

Site Status

The West Clinic Dept. of the West Clinic

Memphis, Tennessee, United States

Site Status

Tennessee Oncology Tennessee Oncology (3)

Nashville, Tennessee, United States

Site Status

Coastal Bend Cancer Center

Corpus Christi, Texas, United States

Site Status

Oncology Consultants Oncology Group

Houston, Texas, United States

Site Status

MD Anderson Cancer Center/University of Texas MD Anderson Cancer Center (3)

Houston, Texas, United States

Site Status

University of Texas Health Science Center at San Antonio Cancer Therapy & Research Ctr.

San Antonio, Texas, United States

Site Status

Intermountain Medical Center Intermountain Healthcare

Murray, Utah, United States

Site Status

Utah Cancer Specialists Utah Cancer Specialists (11)

Salt Lake City, Utah, United States

Site Status

Shenandoah Oncology Shenadoah Oncology (2)

Winchester, Virginia, United States

Site Status

Kadlec Clinic Hematology and Oncology Kadlec Clinic Hematology & Onc

Kennewick, Washington, United States

Site Status

Vista Oncology Inc. PS

Olympia, Washington, United States

Site Status

Multicare Research Institute

Tacoma, Washington, United States

Site Status

Northwest Medical Specialties Rainier Physicians, PC

Tacoma, Washington, United States

Site Status

Providence St. Mary Regional Cancer Center

Walla Walla, Washington, United States

Site Status

Wenatchee Valley Medical Center Wenatchee Valley

Wenatchee, Washington, United States

Site Status

Aurora Research Institute Aurora Health Care

Milwaukee, Wisconsin, United States

Site Status

Medical College of Wisconsin Cancer Center

Milwaukee, Wisconsin, United States

Site Status

Countries

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United States

Provided Documents

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Document Type: Statistical Analysis Plan

View Document

Document Type: Study Protocol

View Document

Other Identifiers

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CLEE011XUS03

Identifier Type: -

Identifier Source: org_study_id

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