A Study of Oral Vismodegib for the Treatment of Idiopathic Pulmonary Fibrosis (IPF)

NCT ID: NCT02168530

Last Updated: 2016-11-02

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

WITHDRAWN

Clinical Phase

PHASE2

Study Classification

INTERVENTIONAL

Study Start Date

2014-10-31

Study Completion Date

2017-01-31

Brief Summary

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This is a randomized, multicenter, double-blind, placebo-controlled, parallel-group study of vismodegib in patients with IPF. Eligible patients will be randomized in a 2:1 ratio to one of two treatment arms: vismodegib or placebo. The duration of treatment will be 52 weeks. Study drug will be administered daily by the oral route. An 8-week safety follow-up period is included for all patients who receive at least one dose of study drug.

Detailed Description

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Conditions

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Idiopathic Pulmonary Fibrosis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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Placebo

Group Type PLACEBO_COMPARATOR

placebo

Intervention Type DRUG

matching placebo administered daily orally

Vismodegib

Group Type EXPERIMENTAL

vismodegib

Intervention Type DRUG

vismodegib 150 mg administered daily orally

Interventions

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placebo

matching placebo administered daily orally

Intervention Type DRUG

vismodegib

vismodegib 150 mg administered daily orally

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Adult patients aged \>/=40 years at Visit 1
* Diagnosis of IPF within the previous 5 years from time of screening and confirmed at baseline
* Patients from countries where a treatment is licensed/approved for IPF must additionally meet at least one of the following criteria to be eligible: (1) be unable to access a licensed therapy for IPF; (2) treatment with a licensed therapy/therapies has been stopped for lack of efficacy or because of safety/tolerability reasons (a washout period will be required); (3) be unwilling to be treated with a licensed therapy and study enrollment considered appropriate.
* Forced vital capacity (FVC) \>/=40% and \</=90% of predicted at screening
* Stable baseline lung function as evidenced by a difference of \<10% in absolute FVC measurements (in liters) between screening and Day 1/Visit 2 prior to randomization
* Diffusion capacity of the lung for carbon dioxide (DLCO) \>/=25% of predicted at screening
* Adequate hematopoietic capacity, liver and renal function
* Female patients of childbearing potential must use two methods of acceptable contraception, including one highly effective method and a barrier method, during treatment and for 7 months after completion of study treatment (or as per local requirement)
* Male patients must agree to remain abstinent or use a condom, even after a vasectomy, during sexual intercourse with female partners while being treated with vismodegib/placebo, and for 2 months after completion of study treatment
* Agreement not to donate blood or blood products during the study and for at least 7 months (or as per local requirements) after the last dose of study treatment

Exclusion Criteria

* Pregnant or lactating
* Known hypersensitivity to any of the study drug excipients or the drug itself
* Prior treatment with vismodegib or any Hh-pathway inhibitor
* Evidence of other known causes of interstitial lung disease
* Hospitalization due to an exacerbation of IPF within 4 weeks prior to, or during, screening
* Lung transplant expected within 12 months of screening
* Evidence of clinically significant lung disease other than IPF
* Substantial emphysema on high resolution computed tomography (HRCT) with degree of emphysema greater than fibrosis
* Post bronchodilator forced expiratory volume in 1 second/FVC ratio \<0.7 at screening
* Class IV New York Heart Association chronic heart failure or historical evidence of left ventricular ejection fraction \<35%
* Known current malignancy or current evaluation for a potential malignancy
* Known immunodeficiency, including but not limited to HIV infection
* Any clinically significant medical disease (other than IPF) that is associated with an expected survival of \<12 months, likely to require a change in therapy during the study, or likely to impact the ability of the patient to participate in the study in the opinion of the investigator, or impact the study efficacy or safety assessments
Minimum Eligible Age

40 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Hoffmann-La Roche

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clinical Trials

Role: STUDY_DIRECTOR

Hoffmann-La Roche

Countries

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Australia France Germany Israel Mexico Peru South Korea United States

Other Identifiers

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2014-000963-42

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

GB29298

Identifier Type: -

Identifier Source: org_study_id