Trial Outcomes & Findings for A Randomized Trial Evaluating Rapid Delivery of Dose Escalated Hypofractionated Radiotherapy for Patients Diagnosed With Bone Metastases for Effective Palliation of Symptoms (NCT NCT02163226)

NCT ID: NCT02163226

Last Updated: 2021-11-08

Results Overview

Evaluate single fraction stereotactic regimen for pain response in terms of time to failure. Pain response was defined by international consensus criteria as a combination of pain score and analgesic use (daily morphine-equivalent dose). Pain failure (ie, lack of response) was defined as worsening pain score (2 points on a 0-to-10 scale), an increase in morphine-equivalent opioid dose of 50% or more, reirradiation, or pathologic fracture. Time to failure was defined as the first occurrence of any of the following events: worsening in pain score by at least 2 categories by MDASI survey. Statistical tests in treatment group were based on the Wilcoxon rank sum test to compare changes in pain scores and analgesic use at each assessment point relative to baseline. Increases or decreases of 2 or more points on a scale of 0 to 10 indicated improving or worsening pain. Fisher exact tests were used to compare the distribution of pain responders (CR + PR) and nonresponders (PP + IR).

Recruitment status

COMPLETED

Study phase

PHASE2/PHASE3

Target enrollment

167 participants

Primary outcome timeframe

From date of registration until the date of first documented Pain failure or death from any cause, or lost to follow up, whichever came first, assessed up to 9 months

Results posted on

2021-11-08

Participant Flow

There was total 167 patients enrolled in this phase II 2013-0640 palliation of symptoms study. Eligible criteria: pathologic diagnosis of malignancy; any radiographic evidence of bone metastases; with pain or dysathesia; life expectancy of more than 3 months; should not treat more than 3 separate radiation treatment fields concurrently.

A total of 167 patients were consented to this study, but 1 patient withdrew consent prior to protocol treatment, 3 patients insurance denied, 2 Patient condition deteriorated, 1 Pathologic fracture on reevaluation, only 160 patients was randomized and treated under this protocol.

Participant milestones

Participant milestones
Measure
Arm 1: the Standard Hypofractionated Regimen (MFRT Group)
3 Gy x 10 fractions; Patients can be treated with 2-D, 3-D, or intensity modulated radiation therapy (IMRT)
Arm 2: Single-fraction Stereotactic Radiation (SBRT Group)
12 Gy x 1 fraction or 16 Gy x 1 fractions, depending on the size of the metastases or gross tumor volume (GTV), treated with 2-D, 3-D, or IMRT
Overall Study
STARTED
79
81
Overall Study
COMPLETED
63
70
Overall Study
NOT COMPLETED
16
11

Reasons for withdrawal

Reasons for withdrawal
Measure
Arm 1: the Standard Hypofractionated Regimen (MFRT Group)
3 Gy x 10 fractions; Patients can be treated with 2-D, 3-D, or intensity modulated radiation therapy (IMRT)
Arm 2: Single-fraction Stereotactic Radiation (SBRT Group)
12 Gy x 1 fraction or 16 Gy x 1 fractions, depending on the size of the metastases or gross tumor volume (GTV), treated with 2-D, 3-D, or IMRT
Overall Study
Death
2
1
Overall Study
Withdrawal by Subject
5
2
Overall Study
Returned home, local radiotherapy
3
0
Overall Study
Repeat imaging showed no disease
2
0
Overall Study
Incomplete radiotherapy
3
0
Overall Study
Treatment was to >3 radiotherapy fields
1
0
Overall Study
"Insurance denied for single-fraction treatment"
0
5
Overall Study
ineligible
0
3

Baseline Characteristics

A Randomized Trial Evaluating Rapid Delivery of Dose Escalated Hypofractionated Radiotherapy for Patients Diagnosed With Bone Metastases for Effective Palliation of Symptoms

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Arm 1: the Standard Hypofractionated Regimen (MFRT Group)
n=79 Participants
3 Gy x 10 fractions; Patients can be treated with 2-D, 3-D, or intensity modulated radiation therapy (IMRT)
Arm 2: Single-fraction Stereotactic Radiation (SBRT Group)
n=81 Participants
12 Gy x 1 fraction or 16 Gy x 1 fractions, depending on the size of the metastases or gross tumor volume (GTV), treated with 2-D, 3-D, or IMRT
Total
n=160 Participants
Total of all reporting groups
Age, Categorical
<=18 years
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
40 Participants
n=5 Participants
36 Participants
n=7 Participants
76 Participants
n=5 Participants
Age, Categorical
>=65 years
39 Participants
n=5 Participants
45 Participants
n=7 Participants
84 Participants
n=5 Participants
Age, Continuous
63 years
n=5 Participants
63 years
n=7 Participants
63 years
n=5 Participants
Sex: Female, Male
Female
32 Participants
n=5 Participants
32 Participants
n=7 Participants
64 Participants
n=5 Participants
Sex: Female, Male
Male
47 Participants
n=5 Participants
49 Participants
n=7 Participants
96 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
4 Participants
n=5 Participants
7 Participants
n=7 Participants
11 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
69 Participants
n=5 Participants
73 Participants
n=7 Participants
142 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
6 Participants
n=5 Participants
1 Participants
n=7 Participants
7 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Asian
2 Participants
n=5 Participants
3 Participants
n=7 Participants
5 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
8 Participants
n=5 Participants
2 Participants
n=7 Participants
10 Participants
n=5 Participants
Race (NIH/OMB)
White
59 Participants
n=5 Participants
68 Participants
n=7 Participants
127 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
10 Participants
n=5 Participants
8 Participants
n=7 Participants
18 Participants
n=5 Participants
Region of Enrollment
United States
79 participants
n=5 Participants
81 participants
n=7 Participants
160 participants
n=5 Participants
Number of Lesions
≤4
41 Participants
n=5 Participants
42 Participants
n=7 Participants
83 Participants
n=5 Participants
Number of Lesions
>4
38 Participants
n=5 Participants
39 Participants
n=7 Participants
77 Participants
n=5 Participants
Site of Bony Mets
Abdomen
4 Participants
n=5 Participants
3 Participants
n=7 Participants
7 Participants
n=5 Participants
Site of Bony Mets
Thorax
9 Participants
n=5 Participants
10 Participants
n=7 Participants
19 Participants
n=5 Participants
Site of Bony Mets
Extremities
13 Participants
n=5 Participants
15 Participants
n=7 Participants
28 Participants
n=5 Participants
Site of Bony Mets
Head/Neck
2 Participants
n=5 Participants
4 Participants
n=7 Participants
6 Participants
n=5 Participants
Site of Bony Mets
Pelvis
48 Participants
n=5 Participants
46 Participants
n=7 Participants
94 Participants
n=5 Participants
Site of Bony Mets
Spine
3 Participants
n=5 Participants
3 Participants
n=7 Participants
6 Participants
n=5 Participants
Numbers of Sites Irradiated
1
64 Participants
n=5 Participants
61 Participants
n=7 Participants
125 Participants
n=5 Participants
Numbers of Sites Irradiated
>1
15 Participants
n=5 Participants
20 Participants
n=7 Participants
35 Participants
n=5 Participants
Karnofsky performance score (KPS)
KPS 50-60
10 Participants
n=5 Participants
9 Participants
n=7 Participants
19 Participants
n=5 Participants
Karnofsky performance score (KPS)
KPS 70-80
58 Participants
n=5 Participants
57 Participants
n=7 Participants
115 Participants
n=5 Participants
Karnofsky performance score (KPS)
KPS 90-100
11 Participants
n=5 Participants
15 Participants
n=7 Participants
26 Participants
n=5 Participants
Primary Cancer Site
Adrenal-cortical
1 Participants
n=5 Participants
0 Participants
n=7 Participants
1 Participants
n=5 Participants
Primary Cancer Site
Bladder
4 Participants
n=5 Participants
3 Participants
n=7 Participants
7 Participants
n=5 Participants
Primary Cancer Site
Breast
3 Participants
n=5 Participants
11 Participants
n=7 Participants
14 Participants
n=5 Participants
Primary Cancer Site
Esophagus
4 Participants
n=5 Participants
4 Participants
n=7 Participants
8 Participants
n=5 Participants
Primary Cancer Site
Head and Neck
1 Participants
n=5 Participants
2 Participants
n=7 Participants
3 Participants
n=5 Participants
Primary Cancer Site
Liver
0 Participants
n=5 Participants
3 Participants
n=7 Participants
3 Participants
n=5 Participants
Primary Cancer Site
Lung
47 Participants
n=5 Participants
32 Participants
n=7 Participants
79 Participants
n=5 Participants
Primary Cancer Site
Pancreas
0 Participants
n=5 Participants
1 Participants
n=7 Participants
1 Participants
n=5 Participants
Primary Cancer Site
Prostate
9 Participants
n=5 Participants
14 Participants
n=7 Participants
23 Participants
n=5 Participants
Primary Cancer Site
Renal Cell
5 Participants
n=5 Participants
9 Participants
n=7 Participants
14 Participants
n=5 Participants
Primary Cancer Site
Thymoma
1 Participants
n=5 Participants
0 Participants
n=7 Participants
1 Participants
n=5 Participants
Primary Cancer Site
Thyroid
2 Participants
n=5 Participants
0 Participants
n=7 Participants
2 Participants
n=5 Participants
Primary Cancer Site
Unknown/Lung
0 Participants
n=5 Participants
1 Participants
n=7 Participants
1 Participants
n=5 Participants
Primary Cancer Site
Uveal Melanoma
1 Participants
n=5 Participants
0 Participants
n=7 Participants
1 Participants
n=5 Participants
Primary Cancer Site
Multiple Myeloma
1 Participants
n=5 Participants
1 Participants
n=7 Participants
2 Participants
n=5 Participants
Primary Tumor Histology
Adenocarcinoma
50 Participants
n=5 Participants
51 Participants
n=7 Participants
101 Participants
n=5 Participants
Primary Tumor Histology
Adenoid Cystic
1 Participants
n=5 Participants
0 Participants
n=7 Participants
1 Participants
n=5 Participants
Primary Tumor Histology
Adrenal Cortical Carcinoma
1 Participants
n=5 Participants
0 Participants
n=7 Participants
1 Participants
n=5 Participants
Primary Tumor Histology
Atypical Carcinoid
1 Participants
n=5 Participants
1 Participants
n=7 Participants
2 Participants
n=5 Participants
Primary Tumor Histology
Carcinoma
1 Participants
n=5 Participants
1 Participants
n=7 Participants
2 Participants
n=5 Participants
Primary Tumor Histology
Clear Cell
5 Participants
n=5 Participants
9 Participants
n=7 Participants
14 Participants
n=5 Participants
Primary Tumor Histology
Ductal Carcinoma
0 Participants
n=5 Participants
4 Participants
n=7 Participants
4 Participants
n=5 Participants
Primary Tumor Histology
Lobular Carcinoma
1 Participants
n=5 Participants
1 Participants
n=7 Participants
2 Participants
n=5 Participants
Primary Tumor Histology
Melanoma
1 Participants
n=5 Participants
0 Participants
n=7 Participants
1 Participants
n=5 Participants
Primary Tumor Histology
Neuroendocrine
1 Participants
n=5 Participants
3 Participants
n=7 Participants
4 Participants
n=5 Participants
Primary Tumor Histology
Papillary
2 Participants
n=5 Participants
0 Participants
n=7 Participants
2 Participants
n=5 Participants
Primary Tumor Histology
Pleiomorphic Carcinoma
1 Participants
n=5 Participants
0 Participants
n=7 Participants
1 Participants
n=5 Participants
Primary Tumor Histology
Poorly Diff Carcinoma
1 Participants
n=5 Participants
0 Participants
n=7 Participants
1 Participants
n=5 Participants
Primary Tumor Histology
Sarcomatoid
1 Participants
n=5 Participants
0 Participants
n=7 Participants
1 Participants
n=5 Participants
Primary Tumor Histology
Small Cell
1 Participants
n=5 Participants
3 Participants
n=7 Participants
4 Participants
n=5 Participants
Primary Tumor Histology
Squamous
6 Participants
n=5 Participants
5 Participants
n=7 Participants
11 Participants
n=5 Participants
Primary Tumor Histology
Urothelial Carcinoma
4 Participants
n=5 Participants
4 Participants
n=7 Participants
8 Participants
n=5 Participants
Primary Tumor Histology
Other
1 Participants
n=5 Participants
2 Participants
n=7 Participants
3 Participants
n=5 Participants

PRIMARY outcome

Timeframe: From date of registration until the date of first documented Pain failure or death from any cause, or lost to follow up, whichever came first, assessed up to 9 months

Evaluate single fraction stereotactic regimen for pain response in terms of time to failure. Pain response was defined by international consensus criteria as a combination of pain score and analgesic use (daily morphine-equivalent dose). Pain failure (ie, lack of response) was defined as worsening pain score (2 points on a 0-to-10 scale), an increase in morphine-equivalent opioid dose of 50% or more, reirradiation, or pathologic fracture. Time to failure was defined as the first occurrence of any of the following events: worsening in pain score by at least 2 categories by MDASI survey. Statistical tests in treatment group were based on the Wilcoxon rank sum test to compare changes in pain scores and analgesic use at each assessment point relative to baseline. Increases or decreases of 2 or more points on a scale of 0 to 10 indicated improving or worsening pain. Fisher exact tests were used to compare the distribution of pain responders (CR + PR) and nonresponders (PP + IR).

Outcome measures

Outcome measures
Measure
Arm 1: the Standard Hypofractionated Regimen (MFRT Group)
n=79 Participants
3 Gy x 10 fractions; Patients can be treated with 2-D, 3-D, or intensity modulated radiation therapy (IMRT)
Arm 2: Single-fraction Stereotactic Radiation (SBRT Group)
n=81 Participants
12 Gy x 1 fraction or 16 Gy x 1 fractions, depending on the size of the metastases or gross tumor volume (GTV), treated with 2-D, 3-D, or IMRT
Number of Intent- to- Treat Patients With Pain Response by Treatment
Pain Response (CR+PR) at 2 weeks
19 Participants
34 Participants
Number of Intent- to- Treat Patients With Pain Response by Treatment
Pain Response (CR+PR) at 1 month
24 Participants
36 Participants
Number of Intent- to- Treat Patients With Pain Response by Treatment
Pain Response (CR+PR) at 3 months
17 Participants
31 Participants
Number of Intent- to- Treat Patients With Pain Response by Treatment
Pain Response (CR+PR) at 6 months
17 Participants
19 Participants
Number of Intent- to- Treat Patients With Pain Response by Treatment
Pain Response (CR+PR) at 9 months
12 Participants
17 Participants

PRIMARY outcome

Timeframe: From date of registration until the date of first documented Pain failure or death from any cause, or lost to follow up, whichever came first, assessed up to 9 months

Evaluate single fraction stereotactic regimen for pain response in terms of time to failure. Pain response was defined by international consensus criteria as a combination of pain score and analgesic use (daily morphine-equivalent dose). Pain failure (ie, lack of response) was defined as worsening pain score (2 points on a 0-to-10 scale), an increase in morphine-equivalent opioid dose of 50% or more, reirradiation, or pathologic fracture. Time to failure was defined as the first occurrence of any of the following events: worsening in pain score by at least 2 categories by MDASI survey. Complete response (CR) is a pain score of 0 at the treated site and no increase in analgesic. Partial response (PR): reduction in pain score of 2 or more points above baseline with no increase in analgesic. Pain progression (PP): Increases of 2 or more points on a scale of 0 to 10 or worsening pain. indeterminate response (IR): were all other responses.

Outcome measures

Outcome measures
Measure
Arm 1: the Standard Hypofractionated Regimen (MFRT Group)
n=52 Participants
3 Gy x 10 fractions; Patients can be treated with 2-D, 3-D, or intensity modulated radiation therapy (IMRT)
Arm 2: Single-fraction Stereotactic Radiation (SBRT Group)
n=55 Participants
12 Gy x 1 fraction or 16 Gy x 1 fractions, depending on the size of the metastases or gross tumor volume (GTV), treated with 2-D, 3-D, or IMRT
Number of Evaluable Participants With Pain Response by Treatment
Pain Response (CR+PR) at 2 weeks
19 Participants
34 Participants
Number of Evaluable Participants With Pain Response by Treatment
Pain Response (CR+PR) at 1 month
24 Participants
36 Participants
Number of Evaluable Participants With Pain Response by Treatment
Pain Response (CR+PR) at 3 months
17 Participants
32 Participants
Number of Evaluable Participants With Pain Response by Treatment
Pain Response (CR+PR) at 6 months
17 Participants
19 Participants
Number of Evaluable Participants With Pain Response by Treatment
Pain Response (CR+PR) at 9 months
12 Participants
17 Participants

SECONDARY outcome

Timeframe: From date of registration until the date of documented death from any cause, or lost to follow up, whichever came first, assessed up to 2 years.

Report grade 3 acute (skin, fatigue, flare reaction) and long term (sclerosis, bone ossification, bone fracture rate) toxicity associated with treatment. During radiotherapy, the patient will be examined weekly and acute reactions recorded and toxicity occurring after 3 months of radiation therapy.

Outcome measures

Outcome measures
Measure
Arm 1: the Standard Hypofractionated Regimen (MFRT Group)
n=79 Participants
3 Gy x 10 fractions; Patients can be treated with 2-D, 3-D, or intensity modulated radiation therapy (IMRT)
Arm 2: Single-fraction Stereotactic Radiation (SBRT Group)
n=81 Participants
12 Gy x 1 fraction or 16 Gy x 1 fractions, depending on the size of the metastases or gross tumor volume (GTV), treated with 2-D, 3-D, or IMRT
Number of Participants With Toxicity Associated With Treatment
Nausea
4 Participants
1 Participants
Number of Participants With Toxicity Associated With Treatment
Vomiting
2 Participants
0 Participants
Number of Participants With Toxicity Associated With Treatment
Fatigue
4 Participants
9 Participants
Number of Participants With Toxicity Associated With Treatment
Radiation Dermatitis
2 Participants
1 Participants
Number of Participants With Toxicity Associated With Treatment
Fracture
0 Participants
1 Participants

Adverse Events

Arm 1: the Standard Hypofractionated Regimen (MFRT Group)

Serious events: 19 serious events
Other events: 0 other events
Deaths: 49 deaths

Arm 2: Single-fraction Stereotactic Radiation (SBRT Group)

Serious events: 11 serious events
Other events: 0 other events
Deaths: 42 deaths

Serious adverse events

Serious adverse events
Measure
Arm 1: the Standard Hypofractionated Regimen (MFRT Group)
n=79 participants at risk
3 Gy x 10 fractions; Patients can be treated with 2-D, 3-D, or intensity modulated radiation therapy (IMRT)
Arm 2: Single-fraction Stereotactic Radiation (SBRT Group)
n=81 participants at risk
12 Gy x 1 fraction or 16 Gy x 1 fractions, depending on the size of the metastases or gross tumor volume (GTV), treated with 2-D, 3-D, or IMRT
Musculoskeletal and connective tissue disorders
Bone pain
19.0%
15/79 • Number of events 18 • From the time of registration to the time of the adverse events (AEs) start date, assessed up to 2 years
6.2%
5/81 • Number of events 6 • From the time of registration to the time of the adverse events (AEs) start date, assessed up to 2 years
General disorders
Fatigue
5.1%
4/79 • Number of events 4 • From the time of registration to the time of the adverse events (AEs) start date, assessed up to 2 years
11.1%
9/81 • Number of events 9 • From the time of registration to the time of the adverse events (AEs) start date, assessed up to 2 years
Gastrointestinal disorders
Nausea
5.1%
4/79 • Number of events 4 • From the time of registration to the time of the adverse events (AEs) start date, assessed up to 2 years
1.2%
1/81 • Number of events 1 • From the time of registration to the time of the adverse events (AEs) start date, assessed up to 2 years
Gastrointestinal disorders
Vomiting
2.5%
2/79 • Number of events 2 • From the time of registration to the time of the adverse events (AEs) start date, assessed up to 2 years
0.00%
0/81 • From the time of registration to the time of the adverse events (AEs) start date, assessed up to 2 years

Other adverse events

Adverse event data not reported

Additional Information

Dr. Quynh-Nhu Nguyen, MD,Associate Professor, Radiation Oncology Department

UT MD Anderson Cancer Center

Phone: (713) 563-2450

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place