Trial Outcomes & Findings for Open Label Extension Study of Nalbuphine HCl ER in Hemodialysis Patients With Uremic Pruritus (NCT NCT02143973)

NCT ID: NCT02143973

Last Updated: 2025-05-21

Results Overview

The number of participants reporting at least one TEAE of a particular body system and preferred term are reported (incidence)

Recruitment status

COMPLETED

Study phase

PHASE2/PHASE3

Target enrollment

167 participants

Primary outcome timeframe

24 weeks

Results posted on

2025-05-21

Participant Flow

Participant milestones

Participant milestones
Measure
Nalbuphine HCl ER
nalbuphine HCl ER nalbuphine HCl ER BID: nalbuphine HCl ER titrated from 30 mg QD to 120 mg BID over three weeks based on tolerability and efficacy, then maintain dosing at that maximum achieved level; full titration and maintenance is 24 weeks.
Overall Study
STARTED
167
Overall Study
COMPLETED
101
Overall Study
NOT COMPLETED
66

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Open Label Extension Study of Nalbuphine HCl ER in Hemodialysis Patients With Uremic Pruritus

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Nalbuphine HCl ER
n=167 Participants
nalbuphine HCl ER
Age, Continuous
53.1 years
STANDARD_DEVIATION 12.2 • n=5 Participants
Sex: Female, Male
Female
75 Participants
n=5 Participants
Sex: Female, Male
Male
92 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
31 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
136 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
2 Participants
n=5 Participants
Race (NIH/OMB)
Asian
1 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
1 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
89 Participants
n=5 Participants
Race (NIH/OMB)
White
73 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
1 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
Region of Enrollment
United States
146 participants
n=5 Participants
Region of Enrollment
Europe
21 participants
n=5 Participants

PRIMARY outcome

Timeframe: 24 weeks

The number of participants reporting at least one TEAE of a particular body system and preferred term are reported (incidence)

Outcome measures

Outcome measures
Measure
Nalbuphine HCl ER
n=167 Participants
nalbuphine HCl ER
Number and Percetage of Participants With Treatment Emergent Adverse Events (TEAEs)
133 Participants

Adverse Events

Nalbuphine HCl ER

Serious events: 54 serious events
Other events: 0 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Nalbuphine HCl ER
n=167 participants at risk
nalbuphine HCl ER
Infections and infestations
Arteriovenous graft site infection
2.4%
4/167
Infections and infestations
Sepsis
1.8%
3/167
Infections and infestations
Diverticulitis
1.2%
2/167
Infections and infestations
Pneumonia
1.2%
2/167
Infections and infestations
Septic shock
1.2%
2/167
Infections and infestations
Abcess neck
0.60%
1/167
Infections and infestations
Arthritis bacterial
0.60%
1/167
Infections and infestations
Bronchitis bacterial
0.60%
1/167
Infections and infestations
Clostridium difficile infection
0.60%
1/167
Infections and infestations
Cystitis
0.60%
1/167
Infections and infestations
Endometritis
0.60%
1/167
Infections and infestations
Influenza
0.60%
1/167
Infections and infestations
Staphylococcal infection
0.60%
1/167
Infections and infestations
Urinary tract infection
0.60%
1/167
Infections and infestations
Urospesis
0.60%
1/167
Nervous system disorders
Syncope
1.2%
2/167
Nervous system disorders
Ataxia
0.60%
1/167
Nervous system disorders
Cerebrovascular accident
0.60%
1/167
Nervous system disorders
Convulsion
0.60%
1/167
Nervous system disorders
Haemorrhagic stroke
0.60%
1/167
Nervous system disorders
Headache
0.60%
1/167
Nervous system disorders
Presyncope
0.60%
1/167
Nervous system disorders
Speech disorder
0.60%
1/167
Respiratory, thoracic and mediastinal disorders
Chronic obstructive pulmonary disease
2.4%
4/167
Respiratory, thoracic and mediastinal disorders
Acute pulmonary oedema
1.2%
2/167
Respiratory, thoracic and mediastinal disorders
Pleural effusion
1.2%
2/167
Respiratory, thoracic and mediastinal disorders
Dyspnoea
0.60%
1/167
Respiratory, thoracic and mediastinal disorders
Hypoxia
0.60%
1/167
Vascular disorders
Hypotension
1.8%
3/167
Vascular disorders
Hypertension
1.2%
2/167
Vascular disorders
Orthostatic hypotension
1.2%
2/167
Vascular disorders
Hypertensive emergency
0.60%
1/167
Vascular disorders
Jugular vein thrombosis
0.60%
1/167
Vascular disorders
Malignant hypertension
0.60%
1/167
Gastrointestinal disorders
Constipation
1.2%
2/167
Gastrointestinal disorders
Colitis
0.60%
1/167
Gastrointestinal disorders
Gastritis
0.60%
1/167
Gastrointestinal disorders
Gastrointestinal inflammation
0.60%
1/167
Gastrointestinal disorders
Pancreatitis
0.60%
1/167
Gastrointestinal disorders
Proctitis
0.60%
1/167
Gastrointestinal disorders
Retroperitoneal haematoma
0.60%
1/167
Gastrointestinal disorders
Umbilical hernia
0.60%
1/167
Injury, poisoning and procedural complications
Arteriovenous fistula thrombosis
0.60%
1/167
Injury, poisoning and procedural complications
Arteriovenous graft site hemorrhage
0.60%
1/167
Injury, poisoning and procedural complications
Dialysis related complication
0.60%
1/167
Injury, poisoning and procedural complications
Femur fracture
0.60%
1/167
Injury, poisoning and procedural complications
Pelvic fracture
0.60%
1/167
Injury, poisoning and procedural complications
Tibia fracture
0.60%
1/167
Injury, poisoning and procedural complications
Traumatic intracranial haemorrhage
0.60%
1/167
Injury, poisoning and procedural complications
Vascular graft complication
0.60%
1/167
General disorders
Non-cardiac chest pain
2.4%
4/167
General disorders
Sudden cardiac death
0.60%
1/167
General disorders
Systemic inflammatory response syndrome
0.60%
1/167
Cardiac disorders
Cardiac arrest
0.60%
1/167
Cardiac disorders
Cardiac failure
0.60%
1/167
Cardiac disorders
Cardiac failure acute
0.60%
1/167
Cardiac disorders
Cardiac failure congestive
0.60%
1/167
Cardiac disorders
Myocardial infarction
0.60%
1/167
Metabolism and nutrition disorders
Fluid overload
1.2%
2/167
Metabolism and nutrition disorders
Hypocalcaemia
0.60%
1/167
Metabolism and nutrition disorders
Hyperglycaemia
0.60%
1/167
Hepatobiliary disorders
Cholecystitis acute
1.2%
2/167
Hepatobiliary disorders
Cholangitis
0.60%
1/167
Hepatobiliary disorders
Cholelithiasis
0.60%
1/167
Blood and lymphatic system disorders
Anaemia
0.60%
1/167
Endocrine disorders
Adrenal insufficiency
0.60%
1/167
Investigations
Anticoagulation drug level below therapeutic
0.60%
1/167
Pregnancy, puerperium and perinatal conditions
Abortion spontaneous
0.60%
1/167

Other adverse events

Adverse event data not reported

Additional Information

Thomas Sciascia, MD

Trevi Therapeutics

Phone: 203-304-2499

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place