Trial Outcomes & Findings for Randomized, Double-blind, Placebo Controlled, Multi-center and Tolerability of RBP-7000 in Schizophrenia Patients (NCT NCT02109562)

NCT ID: NCT02109562

Last Updated: 2018-10-26

Results Overview

The PANSS is a 30-item scale designed to assess various symptoms of schizophrenia including delusions, grandiosity, blunted affect, poor judgement, poor attention, and poor impulse control. The 30 symptoms are rated on a 7-point scale that ranges from 1 (absent) to 7 (extreme psychopathology). The PANSS total score is the sum of all 30 PANSS items and ranges from 30 to 210, with 30 indicating absence of symptoms of schizophrenia and 210 indicating extreme ratings of all 30 symptoms. Negative change from baseline scores indicate improvements in symptoms. Estimates (least square means and standard errors), 2-sided confidence intervals, and -1-sided P values are based on a repeated-measures linear regression model of the change from baseline score, with fixed effects for visit as a categorical variable, baseline score, treatment and treatment by visit interaction, assuming an unstructured covariance matrix.

Recruitment status

COMPLETED

Study phase

PHASE3

Target enrollment

354 participants

Primary outcome timeframe

Day 1 prior to treatment (Baseline), Days 15, 29, 43 and 57 or early discontinuation

Results posted on

2018-10-26

Participant Flow

A total of 538 subjects were screened for study participation at 33 sites in the US, including 354 subjects randomly assigned to treatment. Four subjects were found to be randomized incorrectly; therefore, they were withdrawn from the study and did not receive study drug (counted as 'Physician Decision' for reason d/c below).

Participant milestones

Participant milestones
Measure
RBP-7000 90 mg
Risperidone tablets given during the screening period to check for sensitivity. RBP-7000 administered as a 90 mg subcutaneous injection on Days 1 and 29 for a total of two injections.
RBP-7000 120 mg
Risperidone tablets given during the screening period to check for sensitivity. RBP-7000 administered as a 120 mg subcutaneous injection on Days 1 and 29 for a total of two injections.
Placebo
Risperidone tablets given during the screening period to check for sensitivity. Placebo administered by subcutaneous injection on Days 1 and 29 for a total of two injections.
Overall Study
STARTED
116
119
119
Overall Study
Safety
115
117
118
Overall Study
Intent to Treat (ITT)
111
114
112
Overall Study
COMPLETED
90
85
84
Overall Study
NOT COMPLETED
26
34
35

Reasons for withdrawal

Reasons for withdrawal
Measure
RBP-7000 90 mg
Risperidone tablets given during the screening period to check for sensitivity. RBP-7000 administered as a 90 mg subcutaneous injection on Days 1 and 29 for a total of two injections.
RBP-7000 120 mg
Risperidone tablets given during the screening period to check for sensitivity. RBP-7000 administered as a 120 mg subcutaneous injection on Days 1 and 29 for a total of two injections.
Placebo
Risperidone tablets given during the screening period to check for sensitivity. Placebo administered by subcutaneous injection on Days 1 and 29 for a total of two injections.
Overall Study
Insufficient clinical response
2
0
4
Overall Study
Adverse Event
0
2
3
Overall Study
Lost to Follow-up
1
0
1
Overall Study
Protocol Violation
0
3
1
Overall Study
Withdrawal by Subject
20
25
21
Overall Study
Physician Decision
3
4
5

Baseline Characteristics

Randomized, Double-blind, Placebo Controlled, Multi-center and Tolerability of RBP-7000 in Schizophrenia Patients

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
RBP-7000 90 mg
n=115 Participants
Risperidone tablets given during the screening period to check for sensitivity. RBP-7000 administered as a 90 mg subcutaneous injection on Days 1 and 29 for a total of two injections.
RBP-7000 120 mg
n=117 Participants
Risperidone tablets given during the screening period to check for sensitivity. RBP-7000 administered as a 120 mg subcutaneous injection on Days 1 and 29 for a total of two injections.
Placebo
n=118 Participants
Risperidone tablets given during the screening period to check for sensitivity. Placebo administered by subcutaneous injection on Days 1 and 29 for a total of two injections.
Total
n=350 Participants
Total of all reporting groups
Age, Continuous
40.5 years
STANDARD_DEVIATION 9.41 • n=93 Participants
40.6 years
STANDARD_DEVIATION 9.45 • n=4 Participants
42.4 years
STANDARD_DEVIATION 9.07 • n=27 Participants
41.1 years
STANDARD_DEVIATION 9.33 • n=483 Participants
Age, Customized
20 years and under
1 Participants
n=93 Participants
2 Participants
n=4 Participants
1 Participants
n=27 Participants
4 Participants
n=483 Participants
Age, Customized
21 to 30 years
16 Participants
n=93 Participants
20 Participants
n=4 Participants
16 Participants
n=27 Participants
52 Participants
n=483 Participants
Age, Customized
31 to 40 years
38 Participants
n=93 Participants
32 Participants
n=4 Participants
28 Participants
n=27 Participants
98 Participants
n=483 Participants
Age, Customized
41 to 50 years
41 Participants
n=93 Participants
43 Participants
n=4 Participants
49 Participants
n=27 Participants
133 Participants
n=483 Participants
Age, Customized
51 to 55 years
19 Participants
n=93 Participants
20 Participants
n=4 Participants
24 Participants
n=27 Participants
63 Participants
n=483 Participants
Sex: Female, Male
Female
20 Participants
n=93 Participants
31 Participants
n=4 Participants
31 Participants
n=27 Participants
82 Participants
n=483 Participants
Sex: Female, Male
Male
95 Participants
n=93 Participants
86 Participants
n=4 Participants
87 Participants
n=27 Participants
268 Participants
n=483 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
7 Participants
n=93 Participants
9 Participants
n=4 Participants
10 Participants
n=27 Participants
26 Participants
n=483 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
108 Participants
n=93 Participants
107 Participants
n=4 Participants
107 Participants
n=27 Participants
322 Participants
n=483 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=93 Participants
1 Participants
n=4 Participants
1 Participants
n=27 Participants
2 Participants
n=483 Participants
Race/Ethnicity, Customized
White
28 Participants
n=93 Participants
30 Participants
n=4 Participants
27 Participants
n=27 Participants
85 Participants
n=483 Participants
Race/Ethnicity, Customized
Black or African American
83 Participants
n=93 Participants
83 Participants
n=4 Participants
88 Participants
n=27 Participants
254 Participants
n=483 Participants
Race/Ethnicity, Customized
Asian
1 Participants
n=93 Participants
3 Participants
n=4 Participants
1 Participants
n=27 Participants
5 Participants
n=483 Participants
Race/Ethnicity, Customized
American Indian or Alaska Native
0 Participants
n=93 Participants
0 Participants
n=4 Participants
0 Participants
n=27 Participants
0 Participants
n=483 Participants
Race/Ethnicity, Customized
Native Hawaiian or Other Pacific Islander
1 Participants
n=93 Participants
1 Participants
n=4 Participants
1 Participants
n=27 Participants
3 Participants
n=483 Participants
Race/Ethnicity, Customized
Other
2 Participants
n=93 Participants
0 Participants
n=4 Participants
1 Participants
n=27 Participants
3 Participants
n=483 Participants
Weight
90.60 kg
STANDARD_DEVIATION 18.895 • n=93 Participants
89.01 kg
STANDARD_DEVIATION 20.462 • n=4 Participants
91.84 kg
STANDARD_DEVIATION 22.885 • n=27 Participants
90.49 kg
STANDARD_DEVIATION 20.802 • n=483 Participants
Height
175.1 cm
STANDARD_DEVIATION 9.09 • n=93 Participants
174.3 cm
STANDARD_DEVIATION 9.95 • n=4 Participants
173.1 cm
STANDARD_DEVIATION 10.91 • n=27 Participants
174.1 cm
STANDARD_DEVIATION 10.02 • n=483 Participants
Body Mass Index
29.576 kg/m^2
STANDARD_DEVIATION 5.938 • n=93 Participants
29.376 kg/m^2
STANDARD_DEVIATION 6.664 • n=4 Participants
30.706 kg/m^2
STANDARD_DEVIATION 7.293 • n=27 Participants
29.890 kg/m^2
STANDARD_DEVIATION 6.667 • n=483 Participants
Waist-to-Hip Ratio
0.947 ratio
STANDARD_DEVIATION 0.078 • n=93 Participants
0.936 ratio
STANDARD_DEVIATION 0.072 • n=4 Participants
0.944 ratio
STANDARD_DEVIATION 0.090 • n=27 Participants
0.942 ratio
STANDARD_DEVIATION 0.080 • n=483 Participants
Previous Antipsychotic Treatment
Yes
114 Participants
n=93 Participants
116 Participants
n=4 Participants
118 Participants
n=27 Participants
348 Participants
n=483 Participants
Previous Antipsychotic Treatment
No
1 Participants
n=93 Participants
1 Participants
n=4 Participants
0 Participants
n=27 Participants
2 Participants
n=483 Participants
Age at First Schizophrenia Diagnosis
25.5 years
STANDARD_DEVIATION 8.21 • n=93 Participants
26.9 years
STANDARD_DEVIATION 8.48 • n=4 Participants
26.6 years
STANDARD_DEVIATION 9.25 • n=27 Participants
26.3 years
STANDARD_DEVIATION 8.66 • n=483 Participants

PRIMARY outcome

Timeframe: Day 1 prior to treatment (Baseline), Days 15, 29, 43 and 57 or early discontinuation

Population: Intent to treat (ITT) population

The PANSS is a 30-item scale designed to assess various symptoms of schizophrenia including delusions, grandiosity, blunted affect, poor judgement, poor attention, and poor impulse control. The 30 symptoms are rated on a 7-point scale that ranges from 1 (absent) to 7 (extreme psychopathology). The PANSS total score is the sum of all 30 PANSS items and ranges from 30 to 210, with 30 indicating absence of symptoms of schizophrenia and 210 indicating extreme ratings of all 30 symptoms. Negative change from baseline scores indicate improvements in symptoms. Estimates (least square means and standard errors), 2-sided confidence intervals, and -1-sided P values are based on a repeated-measures linear regression model of the change from baseline score, with fixed effects for visit as a categorical variable, baseline score, treatment and treatment by visit interaction, assuming an unstructured covariance matrix.

Outcome measures

Outcome measures
Measure
RBP-7000 90 mg
n=111 Participants
Risperidone tablets given during the screening period to check for sensitivity. RBP-7000 administered as a 90 mg subcutaneous injection on Days 1 and 29 for a total of two injections.
RBP-7000 120 mg
n=114 Participants
Risperidone tablets given during the screening period to check for sensitivity. RBP-7000 administered as a 120 mg subcutaneous injection on Days 1 and 29 for a total of two injections.
Placebo
n=112 Participants
Risperidone tablets given during the screening period to check for sensitivity. Placebo administered by subcutaneous injection on Days 1 and 29 for a total of two injections.
Mixed Model for Repeated Measures (MMRM) Analysis of Change From Baseline to End of Treatment in the Positive and Negative Syndrome Scale (PANSS) Total Score
-15.367 units on a scale
Standard Error 1.2230
-16.456 units on a scale
Standard Error 1.2073
-9.219 units on a scale
Standard Error 1.2162

SECONDARY outcome

Timeframe: Day 1 prior to treatment (Baseline), Days 15, 29, 43 and 57 or early discontinuation

Population: Intent to treat population (ITT)

The CGI-S rating scale is a 7-point global assessment that measures the clinician's impression of the severity of illness exhibited by a participant. A rating of 1 is equivalent to "Normal, not at all ill" and a rating of 7 is equivalent to "Among the most extremely ill participants". Negative change from baseline scores indicate improvement in the severity of illness. Estimates (least square means and standard errors), 2-sided confidence intervals, and -1-sided P values are based on a repeated-measures linear regression model of the change from baseline score, with fixed effects for visit as a categorical variable, baseline score, treatment and treatment by visit interaction, assuming an unstructured covariance matrix.

Outcome measures

Outcome measures
Measure
RBP-7000 90 mg
n=111 Participants
Risperidone tablets given during the screening period to check for sensitivity. RBP-7000 administered as a 90 mg subcutaneous injection on Days 1 and 29 for a total of two injections.
RBP-7000 120 mg
n=114 Participants
Risperidone tablets given during the screening period to check for sensitivity. RBP-7000 administered as a 120 mg subcutaneous injection on Days 1 and 29 for a total of two injections.
Placebo
n=112 Participants
Risperidone tablets given during the screening period to check for sensitivity. Placebo administered by subcutaneous injection on Days 1 and 29 for a total of two injections.
Mixed Model for Repeated Measures (MMRM) Analysis of Change From Baseline to End of Treatment in Clinical Global Impression - Severity Scale (CGI-S)
-0.868 units on a scale
Standard Error 0.0662
-0.914 units on a scale
Standard Error 0.0654
-0.518 units on a scale
Standard Error 0.0659

SECONDARY outcome

Timeframe: Day 1 to Week 8

Population: Safety population

An adverse event (AE) is defined as any study-related event that represents a change (positive or negative) in frequency or severity from a baseline (prestudy) event (if any), regardless of the presence of causal relationship or medical significance. Treatment-emergent adverse events are defined as any adverse event with a start date on or after the first study dose date. AEs are determined by the Investigator to be related or not related to the study drug. A serious AE (SAE) is defined by federal regulation as any AE occurring at any dose that results in any of the following outcomes: death, life-threatening AE, hospitalization or prolongation of existing hospitalization, a persistent or significant disability/incapacity, or a congenital anomaly/birth defect. Although a subject may have had 2 or more adverse experiences the subject is counted only once in a category. The same subject may appear in different categories.

Outcome measures

Outcome measures
Measure
RBP-7000 90 mg
n=115 Participants
Risperidone tablets given during the screening period to check for sensitivity. RBP-7000 administered as a 90 mg subcutaneous injection on Days 1 and 29 for a total of two injections.
RBP-7000 120 mg
n=117 Participants
Risperidone tablets given during the screening period to check for sensitivity. RBP-7000 administered as a 120 mg subcutaneous injection on Days 1 and 29 for a total of two injections.
Placebo
n=118 Participants
Risperidone tablets given during the screening period to check for sensitivity. Placebo administered by subcutaneous injection on Days 1 and 29 for a total of two injections.
Summary of Participants With Treatment-Emergent Adverse Events (TEAE)
No TEAEs
34 Participants
26 Participants
37 Participants
Summary of Participants With Treatment-Emergent Adverse Events (TEAE)
1 or more TEAEs
81 Participants
91 Participants
81 Participants
Summary of Participants With Treatment-Emergent Adverse Events (TEAE)
Related TEAE
58 Participants
65 Participants
50 Participants
Summary of Participants With Treatment-Emergent Adverse Events (TEAE)
Serious TEAE
0 Participants
1 Participants
1 Participants
Summary of Participants With Treatment-Emergent Adverse Events (TEAE)
Serious, related TEAE
0 Participants
0 Participants
0 Participants
Summary of Participants With Treatment-Emergent Adverse Events (TEAE)
TEAE causing discontinuation
0 Participants
2 Participants
3 Participants
Summary of Participants With Treatment-Emergent Adverse Events (TEAE)
Death
0 Participants
0 Participants
0 Participants

Adverse Events

RBP-7000 90 mg

Serious events: 0 serious events
Other events: 65 other events
Deaths: 0 deaths

RBP-7000 120 mg

Serious events: 1 serious events
Other events: 70 other events
Deaths: 0 deaths

Placebo

Serious events: 1 serious events
Other events: 64 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
RBP-7000 90 mg
n=115 participants at risk
Risperidone tablets given during the screening period to check for sensitivity. RBP-7000 administered as a 90 mg subcutaneous injection on Days 1 and 29 for a total of two injections.
RBP-7000 120 mg
n=117 participants at risk
Risperidone tablets given during the screening period to check for sensitivity. RBP-7000 administered as a 120 mg subcutaneous injection on Days 1 and 29 for a total of two injections.
Placebo
n=118 participants at risk
Risperidone tablets given during the screening period to check for sensitivity. Placebo administered by subcutaneous injection on Days 1 and 29 for a total of two injections.
General disorders
Chest pain
0.00%
0/115 • Day 1 to Week 8
0.85%
1/117 • Day 1 to Week 8
0.00%
0/118 • Day 1 to Week 8
Gastrointestinal disorders
Dyspepsia
0.00%
0/115 • Day 1 to Week 8
0.00%
0/117 • Day 1 to Week 8
0.85%
1/118 • Day 1 to Week 8

Other adverse events

Other adverse events
Measure
RBP-7000 90 mg
n=115 participants at risk
Risperidone tablets given during the screening period to check for sensitivity. RBP-7000 administered as a 90 mg subcutaneous injection on Days 1 and 29 for a total of two injections.
RBP-7000 120 mg
n=117 participants at risk
Risperidone tablets given during the screening period to check for sensitivity. RBP-7000 administered as a 120 mg subcutaneous injection on Days 1 and 29 for a total of two injections.
Placebo
n=118 participants at risk
Risperidone tablets given during the screening period to check for sensitivity. Placebo administered by subcutaneous injection on Days 1 and 29 for a total of two injections.
General disorders
Injection site pain
15.7%
18/115 • Day 1 to Week 8
22.2%
26/117 • Day 1 to Week 8
19.5%
23/118 • Day 1 to Week 8
Nervous system disorders
Headache
17.4%
20/115 • Day 1 to Week 8
15.4%
18/117 • Day 1 to Week 8
23.7%
28/118 • Day 1 to Week 8
Investigations
Weight increased
13.0%
15/115 • Day 1 to Week 8
12.8%
15/117 • Day 1 to Week 8
3.4%
4/118 • Day 1 to Week 8
Gastrointestinal disorders
Constipation
7.0%
8/115 • Day 1 to Week 8
7.7%
9/117 • Day 1 to Week 8
5.1%
6/118 • Day 1 to Week 8
Gastrointestinal disorders
Toothache
7.8%
9/115 • Day 1 to Week 8
6.8%
8/117 • Day 1 to Week 8
5.9%
7/118 • Day 1 to Week 8
Musculoskeletal and connective tissue disorders
Back pain
3.5%
4/115 • Day 1 to Week 8
6.8%
8/117 • Day 1 to Week 8
4.2%
5/118 • Day 1 to Week 8
General disorders
Injection site erythema
6.1%
7/115 • Day 1 to Week 8
4.3%
5/117 • Day 1 to Week 8
5.1%
6/118 • Day 1 to Week 8
Musculoskeletal and connective tissue disorders
Musculoskeletal pain
5.2%
6/115 • Day 1 to Week 8
5.1%
6/117 • Day 1 to Week 8
2.5%
3/118 • Day 1 to Week 8
Nervous system disorders
Akathisia
2.6%
3/115 • Day 1 to Week 8
6.8%
8/117 • Day 1 to Week 8
4.2%
5/118 • Day 1 to Week 8
Psychiatric disorders
Anxiety
2.6%
3/115 • Day 1 to Week 8
6.8%
8/117 • Day 1 to Week 8
5.1%
6/118 • Day 1 to Week 8
Gastrointestinal disorders
Dyspepsia
3.5%
4/115 • Day 1 to Week 8
6.0%
7/117 • Day 1 to Week 8
9.3%
11/118 • Day 1 to Week 8
Gastrointestinal disorders
Nausea
4.3%
5/115 • Day 1 to Week 8
5.1%
6/117 • Day 1 to Week 8
8.5%
10/118 • Day 1 to Week 8
Skin and subcutaneous tissue disorders
Pruritus
5.2%
6/115 • Day 1 to Week 8
4.3%
5/117 • Day 1 to Week 8
7.6%
9/118 • Day 1 to Week 8
Nervous system disorders
Somnolence
5.2%
6/115 • Day 1 to Week 8
4.3%
5/117 • Day 1 to Week 8
0.00%
0/118 • Day 1 to Week 8
Musculoskeletal and connective tissue disorders
Pain in extremity
0.87%
1/115 • Day 1 to Week 8
7.7%
9/117 • Day 1 to Week 8
5.1%
6/118 • Day 1 to Week 8
Psychiatric disorders
Insomnia
3.5%
4/115 • Day 1 to Week 8
2.6%
3/117 • Day 1 to Week 8
5.9%
7/118 • Day 1 to Week 8
General disorders
Nodule
2.6%
3/115 • Day 1 to Week 8
3.4%
4/117 • Day 1 to Week 8
5.1%
6/118 • Day 1 to Week 8

Additional Information

Global Director, Clinical Development

Indivior, Inc.

Phone: 804-379-1090

Results disclosure agreements

  • Principal investigator is a sponsor employee Proposed publications shall be submitted to Sponsor 30 days prior to submission for publication, and may be withheld for an additional period, up to 90 days, to allow Sponsor to file patent applications. If a multicenter publication isn't submitted for publication within 12 months of the conclusion of the Study at all sites, or is published in a shorter period, the results from the institution's site may be published individually.
  • Publication restrictions are in place

Restriction type: OTHER