A Study of Abemaciclib (LY2835219) Combined With Fulvestrant in Women With Hormone Receptor Positive HER2 Negative Breast Cancer

NCT ID: NCT02107703

Last Updated: 2025-10-21

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

669 participants

Study Classification

INTERVENTIONAL

Study Start Date

2014-07-22

Study Completion Date

2027-12-31

Brief Summary

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The main purpose of this study is to compare progression-free survival for women with hormone receptor positive (HR+), human epidermal growth factor receptor (HER2) negative advanced breast cancer receiving either abemaciclib + fulvestrant or fulvestrant alone. Participants will be randomized to abemaciclib or placebo in a 2:1 ratio. The study will last about 9 months for each participant.

For the endocrine naïve cohort, all participants will received abemaciclib + fulvestrant.

Detailed Description

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Conditions

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Breast Neoplasms

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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Abemaciclib + Fulvestrant

Abemaciclib 150 milligram (mg) administered orally every 12 hours on Days 1 to 28 of a 28-day cycle in combination with fulvestrant 500mg administered intramuscularly (IM) on Days 1 and 15 of Cycle 1, then on Day 1 of Cycle 2 and beyond. Participants received treatment until discontinuation were met.

Group Type EXPERIMENTAL

Abemaciclib

Intervention Type DRUG

Administered Orally

Fulvestrant

Intervention Type DRUG

Administered IM

Placebo + Fulvestrant

Placebo administered orally every 12 hours on Days 1 to 28 of a 28-day cycle in combination with fulvestrant 500mg administered IM on Days 1 and 15 of Cycle 1, then on Day 1 of Cycle 2 and beyond. Participants received treatment until discontinuation were met.

Group Type PLACEBO_COMPARATOR

Fulvestrant

Intervention Type DRUG

Administered IM

Placebo

Intervention Type DRUG

Administered Orally

Interventions

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Abemaciclib

Administered Orally

Intervention Type DRUG

Fulvestrant

Administered IM

Intervention Type DRUG

Placebo

Administered Orally

Intervention Type DRUG

Other Intervention Names

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LY2835219

Eligibility Criteria

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Inclusion Criteria

* Have a diagnosis of HR+, HER2- breast cancer
* Have locally advanced disease not amenable to curative treatment by surgery or metastatic disease. In addition, participants must fulfill 1 of the following criteria:

* relapsed with radiologic evidence of progression while receiving neoadjuvant or adjuvant endocrine therapy, with no subsequent endocrine therapy received following progression
* relapsed with radiologic evidence of progression within 1 year from completion of adjuvant endocrine therapy, with no subsequent endocrine therapy received following progression
* relapsed with radiologic evidence of progression more than 1 year from completion of adjuvant endocrine therapy and then subsequently relapsed with radiologic evidence of progression after receiving treatment with either an antiestrogen or an aromatase inhibitor as first-line endocrine therapy for metastatic disease. Participants may not have received more than 1 line of endocrine therapy or any prior chemotherapy for metastatic disease
* presented de novo with metastatic disease and then relapsed with radiologic evidence of progression after receiving treatment with either an antiestrogen or an aromatase inhibitor as first line endocrine therapy for metastatic disease. Participants may not have received more than 1 line of endocrine therapy or any prior chemotherapy for metastatic disease
* for the endocrine naïve cohort: Must not have received prior endocrine therapy in current or prior disease setting
* Have postmenopausal status due to either surgical/natural menopause or ovarian suppression (initiated at least 28 days prior to Day 1 of Cycle 1) with a gonadotropin-releasing hormone (GnRH) agonist such as goserelin
* Have a negative serum pregnancy test at baseline (within 14 days prior to randomization) and agree to use medically approved precautions to prevent pregnancy during the study and for 12 weeks following the last dose of abemaciclib if postmenopausal status is due to ovarian suppression with a GnRH agonist
* Have either measurable disease or nonmeasurable bone only disease
* Have a performance status ≤1 on the Eastern Cooperative Oncology Group (ECOG) scale
* Have discontinued previous therapies for cancer (including specifically, aromatase inhibitors, anti-estrogens, chemotherapy, radiotherapy, and immunotherapy) for at least 21 days for myelosuppressive agents or 14 days for nonmyelosuppressive agents prior to receiving study drug, and recovered from the acute effects of therapy (until the toxicity resolves to either baseline or at least Grade 1) except for residual alopecia or peripheral neuropathy

Exclusion Criteria

* Are currently receiving an investigational drug in a clinical trial or participating in any other type of medical research judged not to be scientifically or medically compatible with this study
* Have visceral crisis, lymphangitic spread, or leptomeningeal carcinomatosis visceral crisis is not the mere presence of visceral metastases but implies severe organ dysfunction as assessed by symptoms and signs, laboratory studies, and rapid progression of the disease
* Have clinical evidence or history of central nervous system metastasis
* Have received prior treatment with chemotherapy (except for neoadjuvant/ adjuvant chemotherapy), fulvestrant, everolimus, or any CDK4/6 inhibitor. For the endocrine naïve cohort: In addition, have received treatment with any prior endocrine therapy
* Have received treatment with a drug that has not received regulatory approval for any indication within 14 or 21 days prior to randomization of study drug for a nonmyelosuppressive or myelosuppressive agent, respectively
* Have received recent (within 28 days prior to randomization) yellow fever vaccination
* Have had major surgery within 14 days prior to randomization of study drug to allow for post-operative healing of the surgical wound and site(s)
* Have a personal history within the last 12 months of any of the following conditions: syncope of cardiovascular etiology, ventricular tachycardia, ventricular fibrillation, or sudden cardiac arrest
* Have inflammatory breast cancer or a history of any other cancer (except nonmelanoma skin cancer or carcinoma in-situ of the cervix), unless in complete remission with no therapy for a minimum of 3 years
* Have received an autologous or allogeneic stem-cell transplant
* Have active bacterial or fungal infection, or detectable viral infection
* Have initiated bisphosphonates or approved Receptor activator of nuclear factor kappa-B (RANK) ligand targeted agents \<7 days prior to randomization
Minimum Eligible Age

18 Years

Eligible Sex

FEMALE

Accepts Healthy Volunteers

No

Sponsors

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Eli Lilly and Company

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Call 1-877-CTLILLY (1-877-285-4559) or 1-317-615-4559 Mon - Fri 9 AM - 5 PM Eastern time (UTC/GMT - 5 hours, EST)

Role: STUDY_DIRECTOR

Eli Lilly and Company

Locations

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St. Bernards Medical Center

Jonesboro, Arkansas, United States

Site Status

Highlands Oncology Group

Springdale, Arkansas, United States

Site Status

University of California - San Diego

La Jolla, California, United States

Site Status

Kaiser Permanente

Riverside, California, United States

Site Status

Univ of California San Francisco

San Francisco, California, United States

Site Status

Stanford University Clinic

Stanford, California, United States

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Palm Beach Cancer Institue

Atlantis, Florida, United States

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Holy Cross Hospital

Fort Lauderdale, Florida, United States

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Florida Cancer Specialists - South

Fort Myers, Florida, United States

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Palm Beach Cancer Institue

Palm Beach Gardens, Florida, United States

Site Status

Florida Cancer Specialists - North

St. Petersburg, Florida, United States

Site Status

Moffitt Cancer Center, Richard M. Shulze Family Foundation Outpatient Center

Tampa, Florida, United States

Site Status

Palm Beach Cancer Institue

Wellington, Florida, United States

Site Status

Palm Beach Cancer Institue

West Palm Beach, Florida, United States

Site Status

University Cancer & Blood Center, LLC

Athens, Georgia, United States

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Harbin Clinic

Rome, Georgia, United States

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Quincy Medical Group

Quincy, Illinois, United States

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Pharmasite Research, Inc.

Baltimore, Maryland, United States

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Dana Farber Cancer Institute

Boston, Massachusetts, United States

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Breslin Cancer Center

Lansing, Michigan, United States

Site Status

Minnesota Oncology/Hematology PA

Minneapolis, Minnesota, United States

Site Status

Washington University Medical School

City of Saint Peters, Missouri, United States

Site Status

Washington University Medical School

Creve Coeur, Missouri, United States

Site Status

Freeman Cancer Institute

Joplin, Missouri, United States

Site Status

St Lukes Hospital

Kansas City, Missouri, United States

Site Status

Washington University Medical School

St Louis, Missouri, United States

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Washington University Medical School

St Louis, Missouri, United States

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Billings Clinic

Billings, Montana, United States

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Dartmouth-Hitchcock Medical Center

Lebanon, New Hampshire, United States

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Icahn School of Medicine at Mount Sinai

New York, New York, United States

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Columbia University Medical Center

New York, New York, United States

Site Status

Rochester General Hospital

Rochester, New York, United States

Site Status

Rochester General Hospital

Rochester, New York, United States

Site Status

Novant Health, Oncology Research Institute

Winston-Salem, North Carolina, United States

Site Status

Oklahoma Cancer Specialists & Research Institute, LLC

Tulsa, Oklahoma, United States

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Sanford Research/USD

Sioux Falls, South Dakota, United States

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The Boston Baskin Cancer Group

Memphis, Tennessee, United States

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SMO Sarah Cannon Research Inst.

Nashville, Tennessee, United States

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Baylor College of Medicine

Houston, Texas, United States

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Oncology Consultants P.A.

Houston, Texas, United States

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Utah Cancer Specialists

Salt Lake City, Utah, United States

Site Status

Kadlec Clinic Hematology and Oncology

Kennewick, Washington, United States

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St Mary Regional Cancer Center

Walla Walla, Washington, United States

Site Status

Icon Cancer Centre South Brisbane

South Brisbane, Queensland, Australia

Site Status

Gold Coast University Hospital

Southport, Queensland, Australia

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Ashford Cancer Centre Research

Kurralta Park, South Australia, Australia

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Monash Cancer Centre

East Bentleigh, Victoria, Australia

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St. John of God Subiaco Hospital

Subiaco, Western Australia, Australia

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Antwerp University Hospital

Edegem, Antwerpen, Belgium

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UZ Brussel

Brussels, Bruxelles-Capitale, Région de, Belgium

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UZ Leuven

Leuven, Vlaams-Brabant, Belgium

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Centre Hospitalier Universitaire de Liège - Domaine Universitaire du Sart Tilman

Liège, , Belgium

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Tom Baker Cancer Center

Calgary, Alberta, Canada

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London Regional Cancer Program

London, Ontario, Canada

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Humber River Hospital

Toronto, Ontario, Canada

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Unity Health Toronto, St. Michael's Hospital

Toronto, Ontario, Canada

Site Status

Herlev and Gentofte Hospital

Copenhagen, Capital Region, Denmark

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Aalborg Universitets hospital

Aalborg, , Denmark

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Roskilde Sygehus

Roskilde, , Denmark

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Tampereen yliopistollinen sairaala

Tampere, Pirkanmaa, Finland

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Helsinki University Hospital - Comprehensive Cancer Center (HYKS - Syöpäkeskus)

Helsinki, Uusimaa, Finland

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Turun Yliopistollinen Keskussairaala

Turku, , Finland

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CHU Besançon

Besançon, Doubs, France

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Centre Jean Perrin - Centre Régional de Lutte contre le Cancer d'Auvergne

Clermont-Ferrand, Puy-de-Dôme, France

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Polyclinique De Blois

La Chaussée-Saint-Victor, , France

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Clinique Victor Hugo - Centre Jean Bernard

Le Mans, , France

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Klinikum Ludwigsburg

Ludwigsburg, Baden-Wurttemberg, Germany

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Universitaetsklinikum Tuebingen

Tübingen, Baden-Wurttemberg, Germany

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Gemeinschaftspraxis hop-augsburg

Augsburg, Bavaria, Germany

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Klinikum der Ludwig-Maximilians-Universitaet Muenchen

München, Bavaria, Germany

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Facharztzentrum Eppendorf

Hamburg, , Germany

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University Hospital of Patras

Pátrai, Achaḯa, Greece

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Agios Savvas Regional Cancer Hospital

Athens, Attikí, Greece

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University General Hospital of Heraklion

Heraklion, Krítí, Greece

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Chania General Hospital 'Agios Georgios'

Chania, , Greece

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Azienda Ospedaliero Universitaria S.Anna

Cona, Emilia-Romagna, Italy

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Istituto Nazionale Tumori Regina Elena

Rome, Roma, Italy

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Ospedale Bellaria - Azienda USL di Bologna

Bologna, , Italy

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Istituto Oncologico Veneto IRCCS

Padua, , Italy

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Aichi Cancer Center Hospital

Nagoya, Aichi-ken, Japan

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Chiba cancer center

Chiba, Chiba, Japan

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National Cancer Center Hospital East

Kashiwa, Chiba, Japan

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National Hospital Organization Shikoku Cancer Center

Matsuyama, Ehime, Japan

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Kurume General Hospital

Kurume, Fukuoka, Japan

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National Hospital Organization Hokkaido Cancer Center

Sapporo, Hokkaido, Japan

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Hyogo College of Medicine

Nishinomiya, Hyōgo, Japan

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St. Marianna University School of Medicine Hospital

Kawasaki, Kanagawa, Japan

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Niigata Cancer Center Hospital

Niigata, Niigata, Japan

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Saitama Prefectural Cancer Center

Ina-machi, Saitama, Japan

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Jichi Medical University Hospital

Shimotsuke, Tochigi, Japan

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Tokyo Met Cancer & Infectious Diseases Center Komagome Hp

Bunkyo-ku, Tokyo, Japan

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National Cancer Center Hospital

Chuo-ku, Tokyo, Japan

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Japanese Foundation for Cancer Research

Koto, Tokyo, Japan

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National Hospital Organization Kyushu Cancer Center

Fukuoka, , Japan

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Sagara Hospital

Kagoshima, , Japan

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Kyoto University Hospital

Kyoto, , Japan

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National Hospital Organization Osaka Medical Center

Osaka, , Japan

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Osaka International Cancer Institute

Osaka, , Japan

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Hospital Angeles

Tijuana, Estado de Baja California, Mexico

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Preparaciones Oncológicas S.C.

León, Guanajuato, Mexico

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Centro Oncológico Internacional (COI)

Guadalajara, Jalisco, Mexico

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Grupo Medico Camino Sc

Mexico City, Mexico City, Mexico

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Instituto Nacional de Cancerologia

Mexico City, Mexico City, Mexico

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OCA Hospital

Monterrey, Nuevo León, Mexico

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Tecnologico de Monterrey

Monterrey, Nuevo León, Mexico

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Uniwersyteckie Centrum Kliniczne

Gdansk, Pomeranian Voivodeship, Poland

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Bialostockie Centrum Onkologii, Oddzial Onkologii Klinicznej

Bialystok, , Poland

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Centrum Terapii Wspolczesnej J. M. Jasnorzewska Spolka Komandytowo-Akcyjna

Lodz, Łódź Voivodeship, Poland

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Puerto Rico Hematology/Oncology Group

Bayamón, PR, Puerto Rico

Site Status

S.C. MedisProf SRL

Cluj-Napoca, Cluj, Romania

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Centrul de Oncologie "Sfântul Nectarie"

Craiova, Dolj, Romania

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Ianuli Med Consult SRL

Bucharest, , Romania

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Arkhangelsk Clinical Oncological Dispensary

Arkhangelsk, Arkhangelskaya oblast, Russia

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Regional Budgetary Healthcare Institution 'Ivanovo Regional Oncology Dispensary'

Ivanovo, Ivanovo Oblast, Russia

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Fed State Budgetary Inst "N.N. Blokhin Med Center of Oncology" MHRF

Moscow, Moscow, Russia

Site Status

Kursk Regional Oncology Dispensary

Kursk, Russian Federation, Russia

Site Status

N.N.Petrov Research Institute of Oncology

Saint Petersburg, Sankt-Peterburg, Russia

Site Status

Saint-Petersburg City Clinical Oncology Dispensary

Saint Petersburg, Sankt-Peterburg, Russia

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Chungbuk National University Hospital

Cheongju-si, Chungcheongbuk-do [Chungbuk], South Korea

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Inha University Hospital

Incheon, Incheon-gwangyeoksi [Incheon], South Korea

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Gachon University Gil Medical Center

Namdong-gu, Incheon-gwangyeoksi [Incheon], South Korea

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Seoul National University Bundang Hospital

Seongnam, Kyǒnggi-do, South Korea

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Seoul National University Hospital

Seoul, Seoul-teukbyeolsi [Seoul], South Korea

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Severance Hospital, Yonsei University Health System

Seoul, Seoul-teukbyeolsi [Seoul], South Korea

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Asan Medical Center

Seoul, Seoul-teukbyeolsi [Seoul], South Korea

Site Status

Samsung Medical Center

Seoul, Seoul-teukbyeolsi [Seoul], South Korea

Site Status

The Catholic Univ. of Korea Seoul St. Mary's Hospital

Seoul, Seoul-teukbyeolsi [Seoul], South Korea

Site Status

Ulsan University Hospital

Ulsan, Ulsan-Kwangyǒkshi, South Korea

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Hospital General Universitario de Elche

Elche, Alicante, Spain

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Hospital Universitari Vall d'Hebron

Barcelona, Barcelona [Barcelona], Spain

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Hospital Universitario Arnau de Vilanova de Lleida

Lleida, Lleida [Lérida], Spain

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Hospital Universitario 12 de Octubre

Madrid, Madrid, Comunidad de, Spain

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Hospital General Universitario Morales Meseguer

Murcia, Murcia, Región de, Spain

Site Status

Hospital Quirónsalud Valencia

Valencia, València, Spain

Site Status

Hospital Clinico San Carlos

Madrid, , Spain

Site Status

Universitätsspital Basel

Basel, Canton of Basel-City, Switzerland

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Spital Thun

Thun, Canton of Bern, Switzerland

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HUG-Hôpitaux Universitaires de Genève

Geneva, , Switzerland

Site Status

Chang Gung Memorial Hospital at Kaohsiung

Kaohsiung Niao Sung Dist, Kaohsiung, Taiwan

Site Status

Kaohsiung Medical University Hospital

Kaohsiung City, , Taiwan

Site Status

Kaohsiung Veterans General Hospital

Kaohsiung City, , Taiwan

Site Status

China Medical University Hospital

Taichung, , Taiwan

Site Status

Taichung Veterans General Hospital

Taichung, , Taiwan

Site Status

National Taiwan University Hospital

Taipei, , Taiwan

Site Status

Taipei Veterans General Hospital

Taipei, , Taiwan

Site Status

Chang Gung Medical Foundation-Linkou Branch

Taoyuan District, , Taiwan

Site Status

Countries

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United States Australia Belgium Canada Denmark Finland France Germany Greece Italy Japan Mexico Poland Puerto Rico Romania Russia South Korea Spain Switzerland Taiwan

References

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Neven P, Rugo HS, Tolaney SM, Iwata H, Toi M, Goetz MP, Kaufman PA, Lu Y, Haddad N, Hurt KC, Sledge GW Jr. Abemaciclib plus fulvestrant in hormone receptor-positive, human epidermal growth factor receptor 2-negative advanced breast cancer in premenopausal women: subgroup analysis from the MONARCH 2 trial. Breast Cancer Res. 2021 Aug 23;23(1):87. doi: 10.1186/s13058-021-01463-2.

Reference Type DERIVED
PMID: 34425869 (View on PubMed)

Inoue K, Masuda N, Iwata H, Takahashi M, Ito Y, Miyoshi Y, Nakayama T, Mukai H, van der Walt JS, Mori J, Sakaguchi S, Kawaguchi T, Tanizawa Y, Llombart-Cussac A, Sledge GW Jr, Toi M. Japanese subpopulation analysis of MONARCH 2: phase 3 study of abemaciclib plus fulvestrant for treatment of hormone receptor-positive, human epidermal growth factor receptor 2-negative breast cancer that progressed on endocrine therapy. Breast Cancer. 2021 Sep;28(5):1038-1050. doi: 10.1007/s12282-021-01239-8. Epub 2021 Apr 1.

Reference Type DERIVED
PMID: 33797023 (View on PubMed)

Goetz MP, Okera M, Wildiers H, Campone M, Grischke EM, Manso L, Andre VAM, Chouaki N, San Antonio B, Toi M, Sledge GW Jr. Safety and efficacy of abemaciclib plus endocrine therapy in older patients with hormone receptor-positive/human epidermal growth factor receptor 2-negative advanced breast cancer: an age-specific subgroup analysis of MONARCH 2 and 3 trials. Breast Cancer Res Treat. 2021 Apr;186(2):417-428. doi: 10.1007/s10549-020-06029-y. Epub 2021 Jan 3.

Reference Type DERIVED
PMID: 33392835 (View on PubMed)

Sledge GW Jr, Toi M, Neven P, Sohn J, Inoue K, Pivot X, Burdaeva O, Okera M, Masuda N, Kaufman PA, Koh H, Grischke EM, Conte P, Lu Y, Barriga S, Hurt K, Frenzel M, Johnston S, Llombart-Cussac A. The Effect of Abemaciclib Plus Fulvestrant on Overall Survival in Hormone Receptor-Positive, ERBB2-Negative Breast Cancer That Progressed on Endocrine Therapy-MONARCH 2: A Randomized Clinical Trial. JAMA Oncol. 2020 Jan 1;6(1):116-124. doi: 10.1001/jamaoncol.2019.4782.

Reference Type DERIVED
PMID: 31563959 (View on PubMed)

Sledge GW Jr, Toi M, Neven P, Sohn J, Inoue K, Pivot X, Burdaeva O, Okera M, Masuda N, Kaufman PA, Koh H, Grischke EM, Frenzel M, Lin Y, Barriga S, Smith IC, Bourayou N, Llombart-Cussac A. MONARCH 2: Abemaciclib in Combination With Fulvestrant in Women With HR+/HER2- Advanced Breast Cancer Who Had Progressed While Receiving Endocrine Therapy. J Clin Oncol. 2017 Sep 1;35(25):2875-2884. doi: 10.1200/JCO.2017.73.7585. Epub 2017 Jun 3.

Reference Type DERIVED
PMID: 28580882 (View on PubMed)

Provided Documents

Download supplemental materials such as informed consent forms, study protocols, or participant manuals.

Document Type: Study Protocol: JPBL 05 Protocol_Redacted

View Document

Document Type: Study Protocol: JPBL 05 Protocol (a)_Redacted

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Document Type: Study Protocol: JPBL 05 Protocol (b)_Redacted

View Document

Document Type: Study Protocol: JPBL 05 Protocol (c)_Redacted

View Document

Document Type: Study Protocol: JPBL 05 Protocol (d)_Redacted

View Document

Document Type: Study Protocol: JPBL 05 Protocol (g)_Redacted

View Document

Document Type: Statistical Analysis Plan: version 4

View Document

Document Type: Statistical Analysis Plan: Addendum for Overall Survival Analyses

View Document

Other Identifiers

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I3Y-MC-JPBL

Identifier Type: OTHER

Identifier Source: secondary_id

2013-004728-13

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

15362

Identifier Type: -

Identifier Source: org_study_id

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