Efficacy and Safety Study of TissueGene-C to Degenerative Arthritis

NCT ID: NCT02072070

Last Updated: 2017-11-17

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

163 participants

Study Classification

INTERVENTIONAL

Study Start Date

2013-11-30

Study Completion Date

2015-08-31

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

The purpose of this study is to determine whether TissueGene-C, an allogeneic human chondrocytes expressing Transforming Growth Factor(TGF)-b1, is effective and safe in patients with degenerative arthritis.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

TissueGene-C is a biological new drug which consists of normal chondrocyte cells and transduced chondrocyte cells that express growth factor to modify osteoarthritis symptom for long term period.

During the Phase 3 clinical trial , we will compare TissueGene-C to placebo in 26, 52 weeks trial with 156 outpatients who have osteoarthritis. The outpatients are randomized to TissueGene-C or placebo in 1:1 ratio, and they will be monitored and recorded in terms of alleviating symptoms, sports activities, function of the knee, and the presence of adverse events.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Degenerative Arthritis

Keywords

Explore important study keywords that can help with search, categorization, and topic discovery.

chondrocyte cells, Osteoarthritis, gene therapy

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

TissueGene-C

Single intra-articular injection to the damaged knee joint at a dose of 1.8 x 10\^7 cells

Group Type EXPERIMENTAL

TissueGene-C

Intervention Type BIOLOGICAL

TissueGene-C at 1.8 x 10\^7 cells

Placebo

Single intra-articular injection to the damaged knee joint

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo control(Normal Saline)

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

TissueGene-C

TissueGene-C at 1.8 x 10\^7 cells

Intervention Type BIOLOGICAL

Placebo

Placebo control(Normal Saline)

Intervention Type DRUG

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

1. Male or female patients at least 19 years of age
2. Patients diagnosed with degenerative arthritis
3. Patients with IKDC(Knee Documentation Committee subjective score) score of 60 or below
4. Patients with 100 mm VAS(Visual Analog Scale) score of 40 or above
5. With Grade 3 osteoarthritis as determined by the radiographic criteria of Kellgren and Lawrence
6. With an International Cartilage Repair Society(ICRS) Grade III or IV cartilage damage in the major lesions, as confirmed through an MRI scan
7. With a Body Mass Index(BMI) of higher than18.5 and lower than 30
8. Patients who satisfies the clinical/radiational criteria by the American College of Rheumatology (ACR) guidelines, and applies to one of the following.

* Older than 50
* Morning stiffness for less than 30 minutes
* Crepitus and Osteophytes
9. With major lesions concentrated in one section of the knee, and with the major lesions considered the main cause of the clinical symptoms
10. With no alleviation of the symptoms even after at least three months of non-surgical treatment
11. Healthy, with no major findings from the physical examination, hematology, serum chemistry, and urine tests, and no significant medical history
12. Agreed to use an effective contraceptive method during the study period
13. Voluntarily agreed to participate in this study, and signed the informed consent form


* patients with a major lesion of ICRS grade 4 which is larger than 6cm2(for patient with ICRS grade 4)
* patients with a major lesion of ICRS grade 3 which is larger than 6cm2(for patient without a ICRS grade 4),
3. Patient who had skin disease around target knee
4. patients who have a positive skin reaction to CS-10
5. Patients who had been administered with drugs such as oriental medicine, glucosamine and chondroitin within 14 days of baseline visit
6. Patients taking steroidal anti-inflammatory medications within 14 days of baseline visit
7. Patients with severe pain in other areas that could effect the diagnosis of the symptoms of the
8. History of surgery like arthroendoscopy within the past 6 months on the target knee
9. Patients who had been administered with immunosuppressants, including antirheumatic drugs (including methotrexate or antimetabolite), within the past 3 months
10. Patients who had been treated with physical therapy or herbal remedy (acupuncture, heat etc.) within 2 weeks of baseline visit
11. History of injection within the past 3 months on the target knee
12. Pregnant or breastfeeding female
13. With another joint disease apart from degenerative arthritis (e.g., systemic rheumatic inflammatory disease associated with the knee or chondrocalcinosis, hemachromatosis, inflammatory arthritis, necrosis of the trochanter, Paget's disease adjacent to a joint in the femur or tibia, ochronosis, hemophilic arthropathy, infectious arthritis, Charcot's disease in the knee joint, villonodular synovitis, synovial chondromas)
14. With an infectious disease, including HIV or hepatitis
15. With any of the following clinically significant diseases:

* heart disease (e.g., myocardial infarction, arrhythmia, other serious heart diseases, coronary artery bypass graft)
* kidney disease (e.g., chronic renal failure, glomerulonephritis)
* liver disease (e.g., liver cirrhosis, fatty liver, acute or chronic liver disease)
* endocrine disease (e.g., hyperthyroidism, hypothyroidism, thyroiditis, diabetes insipidus, Cushing's disease)
* insulin-dependent diabetes mellitus
* medical history of past or current malignant tumor
* In particular, the tumors that TissueGene-C may aggravate can be screened using the following tests:

* Leukemia (White Blood Cell level in the hematology)
* Osteochondroma, Chondromas, Chondroblastoma, Chondromyxoid fibroma, Chondrosarcoma (Alkaline phosphatase level in the hematology)
16. Participated in another clinical trial (using the investigational drug or a medical device) within 30 days before enrollment in this study
17. Patients who administered the TissueGene-C from past clinical trial
18. Considered inappropriate by the investigator for participation in this study

Exclusion Criteria

1. Showed clinically significant hematology, serum chemistry, and urine test results at the screening visit
Minimum Eligible Age

19 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Kolon Life Science

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Jin Gu Kim, MD, PhD

Role: PRINCIPAL_INVESTIGATOR

Inje University

Su Hee Kyung, MD, PhD

Role: PRINCIPAL_INVESTIGATOR

Kyungpook National University Hospital

Chul Won Ha, MD, PhD

Role: PRINCIPAL_INVESTIGATOR

Samsung Medical Center

Myung Chul Lee, MD, PhD

Role: STUDY_CHAIR

Seoul National University Hospital

Yong In, MD, PhD

Role: PRINCIPAL_INVESTIGATOR

The Catholic University of Korea Seoul ST. Mary's Hospita

Seong Il Bin, MD, PhD

Role: PRINCIPAL_INVESTIGATOR

Asan Medical Center

Seong Do Cho, MD, PhD

Role: PRINCIPAL_INVESTIGATOR

Ulsan University Hospital

Jae Doo Yoo, MD, PhD

Role: PRINCIPAL_INVESTIGATOR

Ewha Womans University Mokdong

Myung Gu Kim, MD, PhD

Role: PRINCIPAL_INVESTIGATOR

Inha University Hospital

Ju Hong Lee, MD, PhD

Role: PRINCIPAL_INVESTIGATOR

Chonbuk National University Hospital

Ui Seong Choi, MD, PhD

Role: PRINCIPAL_INVESTIGATOR

Chungbuk National University Hospital

Chung Hyeok Choi, MD, PhD

Role: PRINCIPAL_INVESTIGATOR

Hanyang University

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Chungbuk National University Hospital

Cheongju-si, , South Korea

Site Status

Kyungpook National Univ. Hospital

Daegu, , South Korea

Site Status

Inha University Hospital

Incheon, , South Korea

Site Status

Chonbuk National University Hospital

Jeonju, , South Korea

Site Status

Inje University Seoul Paik Hospital

Seoul, , South Korea

Site Status

Seoul National University Hospital

Seoul, , South Korea

Site Status

Hanyang University Medical Center

Seoul, , South Korea

Site Status

Samsung Medical Center

Seoul, , South Korea

Site Status

The Catholic University of Korea Seoul St. Mary's Hospital

Seoul, , South Korea

Site Status

ASAN Medical Center

Seoul, , South Korea

Site Status

Ewha Womans University Mokdong Hospital

Seoul, , South Korea

Site Status

Ulsan University Hospital

Ulsan, , South Korea

Site Status

Countries

Review the countries where the study has at least one active or historical site.

South Korea

References

Explore related publications, articles, or registry entries linked to this study.

Chen L, Huang FL, Tang Q, Zhao ZK, Ye ZY, Liang JH. Targeted therapy for knee osteoarthritis: From basic to clinics. Medicine (Baltimore). 2025 Aug 15;104(33):e43686. doi: 10.1097/MD.0000000000043686.

Reference Type DERIVED
PMID: 40826764 (View on PubMed)

Kim MK, Ha CW, In Y, Cho SD, Choi ES, Ha JK, Lee JH, Yoo JD, Bin SI, Choi CH, Kyung HS, Lee MC. A Multicenter, Double-Blind, Phase III Clinical Trial to Evaluate the Efficacy and Safety of a Cell and Gene Therapy in Knee Osteoarthritis Patients. Hum Gene Ther Clin Dev. 2018 Mar;29(1):48-59. doi: 10.1089/humc.2017.249.

Reference Type DERIVED
PMID: 29641281 (View on PubMed)

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

KS-TGC-01-3

Identifier Type: -

Identifier Source: org_study_id