Trial Outcomes & Findings for A Study to Evaluate the Efficacy and Safety of X0002 Spray in Subjects With Osteoarthritis (NCT NCT02067611)

NCT ID: NCT02067611

Last Updated: 2018-02-07

Results Overview

The Primary Efficacy Endpoint is change from Baseline in the WOMAC (VAS) pain subscale score for the target knee at 4 weeks of treatment, and will be analyzed using an analysis of covariance (ANCOVA). Treatment will be included as a fixed class effect and WOMAC Baseline pain subscale score as covariates. The primary comparisons of interest will be the difference between active Group A (low dose) and combined placebo, active Group B (middle dose) and combined placebo, and active Group C (high dose) and combined placebo. Safety analyses will be conducted on the SAS. Safety parameters will be listed and summarized using standard descriptive statistics, as appropriate. No formal statistical analyses are planned.

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

216 participants

Primary outcome timeframe

4 weeks of treatment

Results posted on

2018-02-07

Participant Flow

Participant milestones

Participant milestones
Measure
Group A
Low dose of X0002/placebo, twice per day
Group B
Middle dose of X0002/placebo, twice per day.
Group C
High dose of X0002/placebo, twice per day.
Overall Study
STARTED
72
72
72
Overall Study
COMPLETED
66
66
68
Overall Study
NOT COMPLETED
6
6
4

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

In this study, the active drug and placebo were mixed up and we did not have safety and efficacy data and no report at all.

Baseline characteristics by cohort

Baseline data not reported

PRIMARY outcome

Timeframe: 4 weeks of treatment

Population: The labels for X0002 and placebo were mixed up, and the data was mixed up totally.

The Primary Efficacy Endpoint is change from Baseline in the WOMAC (VAS) pain subscale score for the target knee at 4 weeks of treatment, and will be analyzed using an analysis of covariance (ANCOVA). Treatment will be included as a fixed class effect and WOMAC Baseline pain subscale score as covariates. The primary comparisons of interest will be the difference between active Group A (low dose) and combined placebo, active Group B (middle dose) and combined placebo, and active Group C (high dose) and combined placebo. Safety analyses will be conducted on the SAS. Safety parameters will be listed and summarized using standard descriptive statistics, as appropriate. No formal statistical analyses are planned.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: 2, 8, and 12 weeks of treatment

Population: The labels for X0002 and placebo were mixed up, and the data was mixed up totally.

A sensitivity analysis will also be conducted on the Primary Efficacy Endpoint using an ANCOVA with treatment as a fixed class effect and WOMAC baseline pain subscale score as covariates, but the comparisons of interest will be the difference between the active and placebo subjects within each treatment group. The Secondary Efficacy Endpoints, change from Baseline in the WOMAC subscale scores for pain, stiffness, and functional ability, and overall WOMAC score at 2, 8, and 12 weeks of treatment, will be by analyzed using the same methods as the for the Primary Efficacy Endpoint. Safety analyses will be conducted on the SAS. Safety parameters will be listed and summarized using standard descriptive statistics, as appropriate. No formal statistical analyses are planned.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: 2, 4, 8, and 12 weeks of treatment

Population: The labels for X0002 and placebo were mixed up, and the data was mixed up totally.

A sensitivity analysis will also be conducted on the Primary Efficacy Endpoint using an ANCOVA with treatment as a fixed class effect and WOMAC baseline pain subscale score as covariates, but the comparisons of interest will be the difference between the active and placebo subjects within each treatment group. The Secondary Efficacy Endpoints, change from Baseline in the WOMAC subscale scores for pain, stiffness, and functional ability, and overall WOMAC score at 2, 4, 8, and 12 weeks of treatment, will be by analyzed using the same methods as the for the Primary Efficacy Endpoint. Safety analyses will be conducted on the SAS. Safety parameters will be listed and summarized using standard descriptive statistics, as appropriate. No formal statistical analyses are planned.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: at 2, 4, 8, and 12 weeks of treatment

Population: The labels for X0002 and placebo were mixed up, and the data was mixed up totally.

A sensitivity analysis will also be conducted on the Primary Efficacy Endpoint using an ANCOVA with treatment as a fixed class effect and WOMAC baseline pain subscale score as covariates, but the comparisons of interest will be the difference between the active and placebo subjects within each treatment group. The Secondary Efficacy Endpoints, change from Baseline in the WOMAC subscale scores for pain, stiffness, and functional ability, and overall WOMAC score at 2, 8, and 12 weeks of treatment, will be by analyzed using the same methods as the for the Primary Efficacy Endpoint. Safety analyses will be conducted on the SAS. Safety parameters will be listed and summarized using standard descriptive statistics, as appropriate. No formal statistical analyses are planned.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: at the Week 2, week 3, week 4 and Week 12

Population: The labels for X0002 and placebo were mixed up, and the data was mixed up totally.

Cmax, Tmax, AUCs, apparent terminal elimination rate constant, apparent terminal elimination half-life will be calculated.

Outcome measures

Outcome data not reported

OTHER_PRE_SPECIFIED outcome

Timeframe: at 2, 4, 8, and 12 weeks of treatment

Population: The labels for X0002 and placebo were mixed up, and the data was mixed up totally.

Data for the exploratory efficacy endpoints will be summarized using descriptive statistics. Safety analyses will be conducted on the SAS. Safety parameters will be listed and summarized using standard descriptive statistics, as appropriate. No formal statistical analyses are planned.

Outcome measures

Outcome data not reported

OTHER_PRE_SPECIFIED outcome

Timeframe: at 2, 4, 8, and 12 weeks of treatment

Population: The labels for X0002 and placebo were mixed up, and the data was mixed up totally.

Data for the exploratory efficacy endpoints will be summarized using descriptive statistics. Safety analyses will be conducted on the SAS. Safety parameters will be listed and summarized using standard descriptive statistics, as appropriate. No formal statistical analyses are planned.

Outcome measures

Outcome data not reported

OTHER_PRE_SPECIFIED outcome

Timeframe: at 2, 4, 8, and 12 weeks of treatment

Population: The labels for X0002 and placebo were mixed up, and the data was mixed up totally.

Data for the exploratory efficacy endpoints will be summarized using descriptive statistics. Safety analyses will be conducted on the SAS. Safety parameters will be listed and summarized using standard descriptive statistics, as appropriate. No formal statistical analyses are planned.

Outcome measures

Outcome data not reported

OTHER_PRE_SPECIFIED outcome

Timeframe: at 2, 4, 8, and 12 weeks of treatment

Population: The labels for X0002 and placebo were mixed up, and the data was mixed up totally.

Data for the exploratory efficacy endpoints will be summarized using descriptive statistics. Safety analyses will be conducted on the SAS. Safety parameters will be listed and summarized using standard descriptive statistics, as appropriate. No formal statistical analyses are planned.

Outcome measures

Outcome data not reported

OTHER_PRE_SPECIFIED outcome

Timeframe: at 2, 4, 8, and 12 weeks of treatment

Population: The labels for X0002 and placebo were mixed up, and the data was mixed up totally.

Data for the exploratory efficacy endpoints will be summarized using descriptive statistics. Safety analyses will be conducted on the SAS. Safety parameters will be listed and summarized using standard descriptive statistics, as appropriate. No formal statistical analyses are planned.

Outcome measures

Outcome data not reported

OTHER_PRE_SPECIFIED outcome

Timeframe: at 2, 4, 8, and 12 weeks of treatment

Population: The labels for X0002 and placebo were mixed up, and the data was mixed up totally.

Data for the exploratory efficacy endpoints will be summarized using descriptive statistics. Safety analyses will be conducted on the SAS. Safety parameters will be listed and summarized using standard descriptive statistics, as appropriate. No formal statistical analyses are planned.

Outcome measures

Outcome data not reported

Adverse Events

X0002/Placebo

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Adverse event data not reported

Additional Information

Dr. Chongxi Yu

Techfields

Phone: 571 276 5371

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place