Telotristat Etiprate for Carcinoid Syndrome Therapy

NCT ID: NCT02063659

Last Updated: 2018-02-26

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

76 participants

Study Classification

INTERVENTIONAL

Study Start Date

2014-03-11

Study Completion Date

2016-03-29

Brief Summary

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The purpose of the study is to evaluate the effect of telotristat etiprate versus placebo on the incidence of treatment-emergent adverse events and on 5-hydroxyindoleacetic acid (5-HIAA) levels.

Detailed Description

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Conditions

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Carcinoid Syndrome

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators

Study Groups

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250 mg Telotristat Etiprate

Following a 3 to 4-week run-in period, participants were randomized to receive one 250 mg telotristat etiprate tablet and one placebo-matching telotristat etiprate tablet administered three times daily for 12 weeks, followed by a 36 week open-label extension period.

Group Type EXPERIMENTAL

Telotristat etiprate

Intervention Type DRUG

Telotristat etiprate tablets

Placebo

Intervention Type DRUG

Placebo-matching telotristat etiprate tablets

500 mg Telotristat Etiprate

Following a 3 to 4-week run-in period, participants were randomized to receive one 250 mg telotristat etiprate tablet and one placebo-matching telotristat etiprate tablet administered three times daily for one week, followed by two 250 mg telotristat etiprate tablets administered three times daily for 11 weeks in the 12 week double-blind treatment period, followed by a 36 week open-label extension period.

Group Type EXPERIMENTAL

Telotristat etiprate

Intervention Type DRUG

Telotristat etiprate tablets

Placebo

Intervention Type DRUG

Placebo-matching telotristat etiprate tablets

Placebo

Following a 3 to 4-week run-in period, participants were randomized to receive two placebo-matching telotristat etiprate tablets administered three times daily for 12 weeks, followed by a 36 week open-label extension period.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo-matching telotristat etiprate tablets

Interventions

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Telotristat etiprate

Telotristat etiprate tablets

Intervention Type DRUG

Placebo

Placebo-matching telotristat etiprate tablets

Intervention Type DRUG

Other Intervention Names

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LX1606

Eligibility Criteria

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Inclusion Criteria

* Patients ≥ 18 years of age
* All patients of reproductive potential must agree to use an adequate method of contraception during the study and for 12 weeks after the Follow-up visit.
* Histopathologically-confirmed, well-differentiated metastatic neuroendocrine tumor
* Documented history of carcinoid syndrome
* Patient is able and willing to provide written informed consent prior to participation

Exclusion Criteria

* Presence of diarrhea attributed to any condition other than carcinoid syndrome.
* Presence of 12 or more watery bowel movements per day
* Positive stool examination for enteric pathogens, pathogenic ova or parasites, of Clostridium difficile at Screening
* Karnofsky Performance Status ≤ 60%
* Presence of any clinically significant laboratory, medical history, or physical examination findings deemed unacceptable by the Investigator
* A history of short bowel syndrome
* History of constipation within 2 years of Screening
* Life expectancy \< 12 months from Screening
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Lexicon Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Pablo Lapuerta, MD

Role: STUDY_DIRECTOR

Lexicon Pharmaceuticals, Inc.

Locations

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Lexicon Investigational Site

Stanford, California, United States

Site Status

Lexicon Investigational Site

Orlando, Florida, United States

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Lexicon Investigational Site

Iowa City, Iowa, United States

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Lexicon Investigational Site

Lexington, Kentucky, United States

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Lexicon Investigational Site

Boston, Massachusetts, United States

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Lexicon Investigational Site

Buffalo, New York, United States

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Lexicon Investigational Site

New York, New York, United States

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Lexicon Investigational Site

Philadelphia, Pennsylvania, United States

Site Status

Lexicon Investigational Site

Kogara, New South Wales, Australia

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Lexicon Investigational Site

St Leonards, New South Wales, Australia

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Lexicon Investigational Site

Herston, Queensland, Australia

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Lexicon Investigational Site

East Melbourne, Victoria, Australia

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Lexicon Investigational Site

Edegem, , Belgium

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Lexicon Investigational Site

Ghent, , Belgium

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Lexicon Investigational Site

Yvoir, , Belgium

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Lexicon Investigational Site

Calgary, Alberta, Canada

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Lexicon Investigational Site

Halifax, Nova Scotia, Canada

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Lexicon Investigational Site

Clichy, , France

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Lexicon Investigational Site

Lille, , France

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Lexicon Investigational Site

Lyon, , France

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Marseille, , France

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Strasbourg, , France

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Lexicon Investigational Site

Villejuif, , France

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Lexicon Investigational Site

Bad Berka, , Germany

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Lexicon Investigational Site

Berlin, , Germany

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Lexicon Investigational Site

Hamburg, , Germany

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Lexicon Investigational Site

Heidelberg, , Germany

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Lexicon Investigational Site

Lübeck, , Germany

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Lexicon Investigational Site

Mainz, , Germany

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Lexicon Investigational Site

Marburg, , Germany

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Munich, , Germany

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Lexicon Investigational Site

Neuss, , Germany

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Lexicon Investigational Site

Jerusalem, , Israel

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Lexicon Investigational Site

Amsterdam, North Holland, Netherlands

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Lexicon Investigational Site

Amsterdam, North Holland, Netherlands

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Lexicon Investigational Site

Noord Brahant, , Netherlands

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Lexicon Investigative Site

Rotterdam, , Netherlands

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Lexicon Investigational Site

Barcelona, , Spain

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Lexicon Investigational Site

Barcelona, , Spain

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Lexicon Investigational Site

Madrid, , Spain

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Lexicon Investigational Site

Madrid, , Spain

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Lexicon Investigational Site

Seville, , Spain

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Lexicon Investigational Site

Uppsala, , Sweden

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Lexicon Investigational Site

Basingstoke Hampshire, , United Kingdom

Site Status

Lexicon Investigational Site

Coventry, , United Kingdom

Site Status

Lexicon Investigational Site

London, , United Kingdom

Site Status

Lexicon Investigational Site

London, , United Kingdom

Site Status

Lexicon Investigational Site

London, , United Kingdom

Site Status

Lexicon Investigational Site

Manchester, , United Kingdom

Site Status

Lexicon Investigational Site

Newcastle upon Tyne, , United Kingdom

Site Status

Countries

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United States Australia Belgium Canada France Germany Israel Netherlands Spain Sweden United Kingdom

References

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Srirajaskanthan R, Pavel M, Kulke M, Clement D, Houchard A, Keeber L, Weickert MO. Weight Maintenance up to 48 Weeks in Patients With Carcinoid Syndrome Treated With Telotristat Ethyl: Pooled Data From the Open-Label Extensions of the Phase III Clinical Trials TELESTAR and TELECAST. Clin Ther. 2021 Oct;43(10):1779-1785. doi: 10.1016/j.clinthera.2021.08.014. Epub 2021 Sep 28.

Reference Type DERIVED
PMID: 34598813 (View on PubMed)

Dillon JS, Kulke MH, Horsch D, Anthony LB, Warner RRP, Bergsland E, Welin S, O'Dorisio TM, Kunz PL, McKee C, Lapuerta P, Banks P, Pavel M. Time to Sustained Improvement in Bowel Movement Frequency with Telotristat Ethyl: Analyses of Phase III Studies in Carcinoid Syndrome. J Gastrointest Cancer. 2021 Mar;52(1):212-221. doi: 10.1007/s12029-020-00375-2.

Reference Type DERIVED
PMID: 32146619 (View on PubMed)

Pavel M, Gross DJ, Benavent M, Perros P, Srirajaskanthan R, Warner RRP, Kulke MH, Anthony LB, Kunz PL, Horsch D, Weickert MO, Lapuerta P, Jiang W, Kassler-Taub K, Wason S, Fleming R, Fleming D, Garcia-Carbonero R. Telotristat ethyl in carcinoid syndrome: safety and efficacy in the TELECAST phase 3 trial. Endocr Relat Cancer. 2018 Mar;25(3):309-322. doi: 10.1530/ERC-17-0455. Epub 2018 Jan 12.

Reference Type DERIVED
PMID: 29330194 (View on PubMed)

Other Identifiers

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LX1606.303

Identifier Type: OTHER

Identifier Source: secondary_id

2013-001543-31

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

LX1606.1-303-CS

Identifier Type: -

Identifier Source: org_study_id

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