Trial Outcomes & Findings for Study to Evaluate Efficacy/Safety of Combination Budesonide/Indacaterol vs Fluticasone/Salmeterol in Patients With COPD (NCT NCT02055352)

NCT ID: NCT02055352

Last Updated: 2017-04-18

Results Overview

Forced Expiratory Volume in 1 second (FEV1) is the amount of air which can be forcibly exhaled from the lungs in the first second of a forced exhalation.

Recruitment status

COMPLETED

Study phase

PHASE4

Target enrollment

222 participants

Primary outcome timeframe

Baseline and week 12

Results posted on

2017-04-18

Participant Flow

Participant milestones

Participant milestones
Measure
Budesonide/Indacaterol
Participants will receive a fixed combination of fluticasone and salmeterol during 4 weeks followed by a free combination of budesonide and indacaterol for the remainig of study.
Fluticasone / Salmeterol
Fixed combination of fluticasone and salmeterol
Overall Study
STARTED
109
113
Overall Study
Per-Protocol Set (PPS)
108
111
Overall Study
COMPLETED
103
96
Overall Study
NOT COMPLETED
6
17

Reasons for withdrawal

Reasons for withdrawal
Measure
Budesonide/Indacaterol
Participants will receive a fixed combination of fluticasone and salmeterol during 4 weeks followed by a free combination of budesonide and indacaterol for the remainig of study.
Fluticasone / Salmeterol
Fixed combination of fluticasone and salmeterol
Overall Study
Adverse Event
0
1
Overall Study
Non-eligible
0
1
Overall Study
Poor compliance
1
1
Overall Study
Death
1
2
Overall Study
Patient decision
1
1
Overall Study
Use of prohibited treatment
0
3
Overall Study
AE, study drug would be detrimental
1
3
Overall Study
Withdrawal of informed consent
1
0
Overall Study
Reason unknown
1
5

Baseline Characteristics

Study to Evaluate Efficacy/Safety of Combination Budesonide/Indacaterol vs Fluticasone/Salmeterol in Patients With COPD

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Budesonide/Indacaterol
n=109 Participants
Participants will receive a fixed combination of fluticasone and salmeterol during 4 weeks followed by a free combination of budesonide and indacaterol for the remainig of study.
Fluticasone / Salmeterol
n=113 Participants
Fixed combination of fluticasone and salmeterol
Total
n=222 Participants
Total of all reporting groups
Age, Continuous
67.1 Years
STANDARD_DEVIATION 9 • n=5 Participants
67.3 Years
STANDARD_DEVIATION 8.45 • n=7 Participants
67.2 Years
STANDARD_DEVIATION 8.70 • n=5 Participants
Sex: Female, Male
Female
41 Participants
n=5 Participants
54 Participants
n=7 Participants
95 Participants
n=5 Participants
Sex: Female, Male
Male
68 Participants
n=5 Participants
59 Participants
n=7 Participants
127 Participants
n=5 Participants

PRIMARY outcome

Timeframe: Baseline and week 12

Population: Per-protocol set (PPS) included all patients in the FAS without any major protocol deviations. Major protocol deviations were defined in the validation analysis plan prior to database lock and the unblinding of the study. Patients were analyzed according to the treatment they are randomized to

Forced Expiratory Volume in 1 second (FEV1) is the amount of air which can be forcibly exhaled from the lungs in the first second of a forced exhalation.

Outcome measures

Outcome measures
Measure
Budesonide/Indacaterol
n=108 Participants
Participants will receive a fixed combination of fluticasone and salmeterol during 4 weeks followed by a free combination of budesonide and indacaterol for the remainig of study.
Fluticasone / Salmeterol
n=111 Participants
Fixed combination of fluticasone and salmeterol
Change From Baseline in Trough Forced Expiratory Volume in 1 Second (Non-inferiority Analysis).
0.080 Liters
Standard Error 0.027
0.019 Liters
Standard Error 0.028

SECONDARY outcome

Timeframe: Baseline, week 12 and week 24

Population: Per-protocol set (PPS) included all patients in the FAS without any major protocol deviations. Major protocol deviations were defined in the validation analysis plan prior to database lock and the unblinding of the study. Patients were analyzed according to the treatment they are randomized to

Modified Medical Research Council scale (mMRC) questionnaire will be completed by participants. 0 Not troubled with breathlessness except with strenuous exercise; 1 Troubled by shortness of breath when hurrying on the level or walking up a slight hill; 2 Walks slower than people of the same age on the level because of breathlessness or has to stop for breath when walking at own pace on the level; 3 Stops for breath after walking about 100 yards or after a few minutes on the level; 4 Too breathless to leave the house or breathless when dressing or undressing

Outcome measures

Outcome measures
Measure
Budesonide/Indacaterol
n=108 Participants
Participants will receive a fixed combination of fluticasone and salmeterol during 4 weeks followed by a free combination of budesonide and indacaterol for the remainig of study.
Fluticasone / Salmeterol
n=111 Participants
Fixed combination of fluticasone and salmeterol
Change in Health Status - mMRC
Week 12
1.452 Score on a scale
Standard Error 0.111
1.623 Score on a scale
Standard Error 0.113
Change in Health Status - mMRC
Week 24
1.315 Score on a scale
Standard Error 0.112
1.414 Score on a scale
Standard Error 0.115

SECONDARY outcome

Timeframe: 24 weeks

Population: Per-protocol set (PPS) included all patients in the FAS without any major protocol deviations. Major protocol deviations were defined in the validation analysis plan prior to database lock and the unblinding of the study. Patients that were not discontinued before Visit 3 (day 28±3).

A day with no rescue medication use is defined from the diary data as any day where the patient recorded no rescue medicine use during the previous 12 hours.

Outcome measures

Outcome measures
Measure
Budesonide/Indacaterol
n=105 Participants
Participants will receive a fixed combination of fluticasone and salmeterol during 4 weeks followed by a free combination of budesonide and indacaterol for the remainig of study.
Fluticasone / Salmeterol
n=105 Participants
Fixed combination of fluticasone and salmeterol
Change From Baseline in Mean Daily Number of Puffs of Rescue Medication Used Over the 24 Week Treatment
10.5 Puffs
Standard Deviation 9.53
12.9 Puffs
Standard Deviation 12.34

SECONDARY outcome

Timeframe: Baseline and week 24

Population: Per-protocol set (PPS) included all patients in the FAS without any major protocol deviations. Major protocol deviations were defined in the validation analysis plan prior to database lock and the unblinding of the study. Patients were analyzed according to the treatment they are randomized to

Forced Expiratory Volume in 1 second (FEV1) is the amount of air which can be forcibly exhaled from the lungs in the first second of a forced exhalation, measured through spirometry testing.

Outcome measures

Outcome measures
Measure
Budesonide/Indacaterol
n=108 Participants
Participants will receive a fixed combination of fluticasone and salmeterol during 4 weeks followed by a free combination of budesonide and indacaterol for the remainig of study.
Fluticasone / Salmeterol
n=111 Participants
Fixed combination of fluticasone and salmeterol
Change From Baseline in Trough Forced Expiratory Volume in 1 Second at Week 24 (Analysis of Superiority)
0.063 Liters
Standard Error 0.033
0.020 Liters
Standard Error 0.034

SECONDARY outcome

Timeframe: Baseline, week 12 and week 24

Population: Per-protocol set (PPS) included all patients in the FAS without any major protocol deviations. Major protocol deviations were defined in the validation analysis plan prior to database lock and the unblinding of the study. Patients were analyzed according to the treatment they are randomized to

St George's Respiratory Questionnaire short version questionnaire will be completed by participants. The SGRQ ranges from 0 (no impairment of quality of life) to 100 (highest impairment of quality of life)

Outcome measures

Outcome measures
Measure
Budesonide/Indacaterol
n=108 Participants
Participants will receive a fixed combination of fluticasone and salmeterol during 4 weeks followed by a free combination of budesonide and indacaterol for the remainig of study.
Fluticasone / Salmeterol
n=111 Participants
Fixed combination of fluticasone and salmeterol
Change in Health Status - SGRQ-C
Week 12
-8.703 Score on a scale
Standard Error 2.006
-2.334 Score on a scale
Standard Error 2.053
Change in Health Status - SGRQ-C
Week 24
-7.787 Score on a scale
Standard Error 2.308
-2.523 Score on a scale
Standard Error 2.384

Adverse Events

Budesonide / Indacaterol (A)

Serious events: 10 serious events
Other events: 24 other events
Deaths: 0 deaths

Fluticasone / Salmeterol (B)

Serious events: 9 serious events
Other events: 39 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Budesonide / Indacaterol (A)
n=109 participants at risk
Budesonide / Indacaterol (A)
Fluticasone / Salmeterol (B)
n=113 participants at risk
Fluticasone / Salmeterol (B)
Cardiac disorders
Acute myocardial infarction
0.00%
0/109
0.88%
1/113
Cardiac disorders
Bradycardia
0.00%
0/109
0.88%
1/113
Cardiac disorders
Cor pulmonale
0.00%
0/109
0.88%
1/113
Cardiac disorders
Nodal arrhythmia
0.00%
0/109
0.88%
1/113
Infections and infestations
Cellulitis
0.00%
0/109
0.88%
1/113
Infections and infestations
Pneumonia
2.8%
3/109
0.88%
1/113
Injury, poisoning and procedural complications
Hip fracture
0.00%
0/109
0.88%
1/113
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Bronchial carcinoma
0.92%
1/109
0.00%
0/113
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Hepatocellular carcinoma
0.00%
0/109
0.88%
1/113
Respiratory, thoracic and mediastinal disorders
Acute pulmonary oedema
0.00%
0/109
0.88%
1/113
Respiratory, thoracic and mediastinal disorders
Chronic obstructive pulmonary disease
5.5%
6/109
1.8%
2/113
Respiratory, thoracic and mediastinal disorders
Haemoptysis
0.92%
1/109
0.00%
0/113
Respiratory, thoracic and mediastinal disorders
Pulmonary embolism
0.92%
1/109
0.00%
0/113
Vascular disorders
Peripheral arterial occlusive disease
0.00%
0/109
0.88%
1/113
Vascular disorders
Vascular insufficiency
0.00%
0/109
0.88%
1/113
Vascular disorders
Venous thrombosis limb
0.00%
0/109
0.88%
1/113

Other adverse events

Other adverse events
Measure
Budesonide / Indacaterol (A)
n=109 participants at risk
Budesonide / Indacaterol (A)
Fluticasone / Salmeterol (B)
n=113 participants at risk
Fluticasone / Salmeterol (B)
Infections and infestations
Influenza
5.5%
6/109
8.8%
10/113
Infections and infestations
Nasopharyngitis
10.1%
11/109
8.8%
10/113
Infections and infestations
Urinary tract infection
2.8%
3/109
6.2%
7/113
Musculoskeletal and connective tissue disorders
Arthralgia
0.92%
1/109
6.2%
7/113
Musculoskeletal and connective tissue disorders
Back pain
0.92%
1/109
5.3%
6/113
Nervous system disorders
Headache
0.92%
1/109
8.0%
9/113
Respiratory, thoracic and mediastinal disorders
Dysphonia
2.8%
3/109
7.1%
8/113

Additional Information

Study Director

Novartis Pharmaceuticals

Phone: 862-778-8300

Results disclosure agreements

  • Principal investigator is a sponsor employee The terms and conditions of Novartis' agreements with its investigators may vary. However, Novartis does not prohibit any investigator from publishing. Any publications from a single-site are postponed until the publication of the pooled data (i.e., data from all sites) in the clinical trial or disclosure of trial results in their entirety.
  • Publication restrictions are in place

Restriction type: OTHER