Lubiprostone in Children With Functional Constipation

NCT ID: NCT02042183

Last Updated: 2020-07-21

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

606 participants

Study Classification

INTERVENTIONAL

Study Start Date

2013-12-13

Study Completion Date

2016-07-27

Brief Summary

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Study to determine if children (6-17 years old) with functional constipation will respond to being treated with lubiprostone for 12 weeks.

Detailed Description

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Dose administration details:

* Participants with a body weight \<50 kg at baseline received Lubiprostone 12 mcg BID for 12 weeks. If the dose was safe but did not show any efficacy at Week 1, dosage was increased to 24 mcg BID.
* Participants with a body weight \>50 kg at baseline received Lubiprostone 24 mcg BID for 12 weeks. If the dose was unsafe at Week 1, dosage was decreased to 12 mcg BID.

Conditions

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Constipation - Functional

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Placebo controlled
Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators
While the care provider and outcomes assessor were also blinded, this was classified as a double-blind trial

Study Groups

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Lubiprostone

Participants receive lubiprostone twice daily (BID) up to 12 weeks

Group Type EXPERIMENTAL

Lubiprostone

Intervention Type DRUG

12 or 24 mcg soft capsules of lubiprostone for oral administration, depending on baseline weight and response during week 1

Placebo

Participants receive placebo BID up to 12 weeks

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

0 mcg soft capsules of placebo for oral administration

Interventions

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Lubiprostone

12 or 24 mcg soft capsules of lubiprostone for oral administration, depending on baseline weight and response during week 1

Intervention Type DRUG

Placebo

0 mcg soft capsules of placebo for oral administration

Intervention Type DRUG

Other Intervention Names

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Amitiza Matching Placebo

Eligibility Criteria

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Inclusion Criteria

* Medically-confirmed diagnosis of Functional Constipation per Rome III Diagnostic Criteria for Childhood Functional Constipation
* At least 6 years of age but less than 18 years of age at the time of randomisation
* Only stable dose of selective serotonin re-uptake inhibitors (SSRIs), serotonin-specific reuptake inhibitor (SNRIs), or monoamine oxidase inhibitors (MAO) inhibitors are allowed if subject is taking antidepressants

Exclusion Criteria

* Any gastrointestinal (GI) condition, other than constipation and/or irritable bowel syndrome (IBS), affecting GI motility or defecation
* Untreated faecal impaction at the time of screening
* Medical/surgical condition that might interfere with the absorption, distribution, metabolism, or excretion of the study medication
Minimum Eligible Age

6 Years

Maximum Eligible Age

17 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Sucampo AG

INDUSTRY

Sponsor Role collaborator

Sucampo Pharma Americas, LLC

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clinical Team Leader

Role: STUDY_DIRECTOR

Mallinckrodt

Locations

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University of Alabama Pediatric Gastroenterology

Birmingham, Alabama, United States

Site Status

University of South Alabama Women's and Children's Hospital

Mobile, Alabama, United States

Site Status

Arizona Children's Center at Maricopa Medical Center

Phoenix, Arizona, United States

Site Status

Phoenix Children's Hospital

Phoenix, Arizona, United States

Site Status

Northwest Arkansas Pediatric Clinic

Fayetteville, Arkansas, United States

Site Status

Arkansas Children's Hospital Research Institute

Little Rock, Arkansas, United States

Site Status

Applied Clinical Research of Arkansas

Little Rock, Arkansas, United States

Site Status

WCCT Global

Costa Mesa, California, United States

Site Status

Loma Linda University Health Care

Loma Linda, California, United States

Site Status

Children's Hospital Los Angeles

Los Angeles, California, United States

Site Status

Children's Hospital of Orange County

Orange, California, United States

Site Status

University of California, San Francisco

San Francisco, California, United States

Site Status

MCB Clinical Research

Colorado Springs, Colorado, United States

Site Status

Nemours/Alfred I. duPont Hospital for Children

Wilmington, Delaware, United States

Site Status

Emmerson Clinical Research

Washington D.C., District of Columbia, United States

Site Status

University of Florida

Gainesville, Florida, United States

Site Status

Palmetto Professional Research

Hialeah, Florida, United States

Site Status

Nemours Children's Clinic

Jacksonville, Florida, United States

Site Status

Acevedo Clinical Research Associates

Miami, Florida, United States

Site Status

Savin Medical Group Research Center

Miami Lakes, Florida, United States

Site Status

Digestive & Liver Center of Florida

Orlando, Florida, United States

Site Status

Nemours Childrens Clinic

Pensacola, Florida, United States

Site Status

Children's Center for Digestive Healthcare/GI Care for Kids

Atlanta, Georgia, United States

Site Status

Center For Children's Digestive Health

Park Ridge, Illinois, United States

Site Status

Methodist Medical Center

Peoria, Illinois, United States

Site Status

PediaResearch, LLC - Newburgh

Newburgh, Indiana, United States

Site Status

UnityPoint Health Des Moines/ Blank Children's Clinic

Des Moines, Iowa, United States

Site Status

University of Iowa Children's Hospital

Iowa City, Iowa, United States

Site Status

Heartland Research Associates

Wichita, Kansas, United States

Site Status

University of Louisville Research Foundation Inc. Kosair Charities Pediatric Clinical Research Unit

Louisville, Kentucky, United States

Site Status

PediaResearch, LLC - Owensboro

Owensboro, Kentucky, United States

Site Status

Children's Hospital

New Orleans, Louisiana, United States

Site Status

Willis-Knighton Physician Network

Shreveport, Louisiana, United States

Site Status

Johns Hopkins Children's Center

Baltimore, Maryland, United States

Site Status

Virgo-Carter Pediatrics

Silver Spring, Maryland, United States

Site Status

Boston Children's Hospital

Boston, Massachusetts, United States

Site Status

Mayo Clinic

Rochester, Minnesota, United States

Site Status

Gastrointestinal Associates, PA

Jackson, Mississippi, United States

Site Status

University of Mississippi Medical Center

Jackson, Mississippi, United States

Site Status

The Children's Mercy Hospital

Kansas City, Missouri, United States

Site Status

Pioneer Clinical Research

Bellevue, Nebraska, United States

Site Status

Midwest Children's Health Research Institute

Lincoln, Nebraska, United States

Site Status

Digestive Diseases and Nutrition Center Women and Childrens Hospital of Buffalo

Buffalo, New York, United States

Site Status

Smart Medical Research, Inc.

Jackson Heights, New York, United States

Site Status

NY Presbyterian Weill Cornell

New York, New York, United States

Site Status

Morgan Stanley Children's Hospital of New York Presbyterian

New York, New York, United States

Site Status

UNC School of Medicine

Chapel Hill, North Carolina, United States

Site Status

PriMed Clinical Research

Beavercreek, Ohio, United States

Site Status

Nationwide Children's Hospital

Columbus, Ohio, United States

Site Status

Toledo Children's Hospital

Toledo, Ohio, United States

Site Status

University of Oklahoma Health Sciences Center

Oklahoma City, Oklahoma, United States

Site Status

Cyn3rgy Research

Gresham, Oregon, United States

Site Status

Square-1 Clinical Research, Inc.

Erie, Pennsylvania, United States

Site Status

Children's Hospital of Philadelphia

Philadelphia, Pennsylvania, United States

Site Status

St. Christopher's Hospital for Children/Drexel University

Philadelphia, Pennsylvania, United States

Site Status

Children's Hospital of Pittsburgh UPMC

Pittsburgh, Pennsylvania, United States

Site Status

AAPRI Clinical Research

Warwick, Rhode Island, United States

Site Status

Coastal Pediatric Associates - James Island

Charleston, South Carolina, United States

Site Status

Coastal Clinical Research

Charleston, South Carolina, United States

Site Status

Greenville Health System

Greenville, South Carolina, United States

Site Status

Coastal Pediatrics Associates - Mount Pleasant

Mt. Pleasant, South Carolina, United States

Site Status

Spartanburg Medical Research

Spartanburg, South Carolina, United States

Site Status

The Jackson Clinic, P.C.

Jackson, Tennessee, United States

Site Status

Le Bonheur Children's Hospital

Memphis, Tennessee, United States

Site Status

Monroe Carell Junior Children's Hospital at Vanderbilt

Nashville, Tennessee, United States

Site Status

Texas Tech University Health Sciences Center

Amarillo, Texas, United States

Site Status

Austin Center for Clinical Research

Austin, Texas, United States

Site Status

A1 Clinical Research

Baytown, Texas, United States

Site Status

3rd Coast Research Associates

Corpus Christi, Texas, United States

Site Status

Childrens Medical Center Dallas

Dallas, Texas, United States

Site Status

Cook Children's Medical Center

Fort Worth, Texas, United States

Site Status

Baylor College of Medicine

Houston, Texas, United States

Site Status

Envision Clinical Research, LLC

Laredo, Texas, United States

Site Status

DCOL Center for Clinical Research

Longview, Texas, United States

Site Status

Medical Clinics of Sealy

Sealy, Texas, United States

Site Status

Bridgerland Clinical Research

Logan, Utah, United States

Site Status

Primary Children's Medical Center

Salt Lake City, Utah, United States

Site Status

Wee Care Pediatrics

Syracuse, Utah, United States

Site Status

University of Vermont Medical Center

Burlington, Vermont, United States

Site Status

Pediatric Research of Charlottesville, LLC

Charlottesville, Virginia, United States

Site Status

INOVA Pediatric Digestive Diseases Center

Fairfax, Virginia, United States

Site Status

The Children's Hospital of the King's Daughter

Norfolk, Virginia, United States

Site Status

Pediatric Gastroenterology Carilion Medical Center

Roanoke, Virginia, United States

Site Status

Northwest Clinicial Research Center

Bellevue, Washington, United States

Site Status

Zain Research LLC

Richland, Washington, United States

Site Status

MultiCare Health System Institute for Research and Innovation

Tacoma, Washington, United States

Site Status

Medical College of Wisconsin

Milwaukee, Wisconsin, United States

Site Status

Universitair Kinderziekenhuis Brussel

Brussels, , Belgium

Site Status

University Hospital Gasthuisberg

Leuven, , Belgium

Site Status

CHC - Clinique Saint-Joseph

Montegnée, , Belgium

Site Status

London Health Sciences Centre

London, Ontario, Canada

Site Status

Centre de recherche du CHUS

Sherbrooke, Quebec, Canada

Site Status

Sainte Justine University Health Center

Montreal, , Canada

Site Status

CHU-Bordeaux

Bordeaux, , France

Site Status

Groupe Hospitalier Est

Bron, , France

Site Status

Armand-Trousseau Teaching Hospital

Paris, , France

Site Status

Hôpital Necker

Paris, , France

Site Status

Emma Children's Hospital

Amsterdam, , Netherlands

Site Status

Amphia Ziekenhuis

Breda, , Netherlands

Site Status

Maasstad Hospital Rotterdam

Rotterdam, , Netherlands

Site Status

Isala Klinieken

Zwolle, , Netherlands

Site Status

Medical University of Bialystok

Bialystok, , Poland

Site Status

Szpital Uniwersytecki

Bydgoszcz, , Poland

Site Status

ATOPIA Poradnie Specjalistyczne

Krakow, , Poland

Site Status

Medical University of Lodz

Lodz, , Poland

Site Status

Szpital Pediatryczny ICZMP

Lodz, , Poland

Site Status

Gabinet Lekarski Bartosc Korczowski

Rzeszów, , Poland

Site Status

Children's Memorial Health Institute

Warsaw, , Poland

Site Status

Przychodnia Specjalistyczna PROSEN

Warsaw, , Poland

Site Status

Children's Memorial Health Institute

Warsaw, , Poland

Site Status

Kent and Canterbury Hospital

Canterbury, , United Kingdom

Site Status

Darlington Memorial Hospital

Darlington, , United Kingdom

Site Status

Royal Hospital for Sick Children

Glasgow, , United Kingdom

Site Status

Royal London Hospital

London, , United Kingdom

Site Status

Chelsea and Westminster Hospital NHS Foundation Trust

London, , United Kingdom

Site Status

Great Ormond Street Hospital for children NHS Foundation Trust

London, , United Kingdom

Site Status

Sheffield Children Hospital

Sheffield, , United Kingdom

Site Status

Countries

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United States Belgium Canada France Netherlands Poland United Kingdom

References

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Benninga MA, Hussain SZ, Sood MR, Nurko S, Hyman P, Clifford RA, O'Gorman M, Losch-Beridon T, Mareya S, Lichtlen P, Di Lorenzo C. Lubiprostone for Pediatric Functional Constipation: Randomized, Controlled, Double-Blind Study With Long-term Extension. Clin Gastroenterol Hepatol. 2022 Mar;20(3):602-610.e5. doi: 10.1016/j.cgh.2021.04.005. Epub 2021 Apr 7.

Reference Type DERIVED
PMID: 33838349 (View on PubMed)

Other Identifiers

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2013-004384-31

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

EMEA-000245-PIP01-08

Identifier Type: OTHER

Identifier Source: secondary_id

SAG/0211PFC-1131

Identifier Type: -

Identifier Source: org_study_id

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