Trial Outcomes & Findings for Efficacy and Safety of Lucentis® Use in Patients With Diabetic Macular Edema Evaluating a Spaced Out Follow-up After Intensive Treatment Phase (NCT NCT02032173)

NCT ID: NCT02032173

Last Updated: 2020-10-22

Results Overview

Best-Corrected Visual Acuity (BCVA) letters were measured using Early Treatment Diabetic Retinopathy Study (EDTRS)-like chart while participants were in a sitting position at a testing distance of 4 meters. The range of EDTRS is 0 to 100 letters. A positive change from baseline of BCVA indicates improvement. Best value on the scale 100, worst 0. The number of participants with a stable BCVA (BCVA score at 6 months minus BCVA score at 24 months ≤4 letters) were reported.

Recruitment status

TERMINATED

Study phase

PHASE3

Target enrollment

31 participants

Primary outcome timeframe

Month 6 and 24

Results posted on

2020-10-22

Participant Flow

Participants were recruited from 10 centers across France.

Participant milestones

Participant milestones
Measure
Ranibizumab
Intravitreal injection with standard dose of 0.5 mg/0.05mL Pro re nata (PRN)
Overall Study
STARTED
31
Overall Study
Included Population - Main Group
31
Overall Study
Rescue Group
1
Overall Study
COMPLETED
0
Overall Study
NOT COMPLETED
31

Reasons for withdrawal

Reasons for withdrawal
Measure
Ranibizumab
Intravitreal injection with standard dose of 0.5 mg/0.05mL Pro re nata (PRN)
Overall Study
Discontinuation due to sponsor decision
31

Baseline Characteristics

Efficacy and Safety of Lucentis® Use in Patients With Diabetic Macular Edema Evaluating a Spaced Out Follow-up After Intensive Treatment Phase

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Ranibizumab
n=31 Participants
Intravitreal injection with standard dose of 0.5 mg/0.05mL Pro re nata (PRN)
Age, Continuous
64.7 Years
STANDARD_DEVIATION 7.08 • n=5 Participants
Sex: Female, Male
Female
10 Participants
n=5 Participants
Sex: Female, Male
Male
21 Participants
n=5 Participants

PRIMARY outcome

Timeframe: Month 6 and 24

Population: Included population: No subjects included as analysis required data at month 24 and trial terminated before any subject reached month 12

Best-Corrected Visual Acuity (BCVA) letters were measured using Early Treatment Diabetic Retinopathy Study (EDTRS)-like chart while participants were in a sitting position at a testing distance of 4 meters. The range of EDTRS is 0 to 100 letters. A positive change from baseline of BCVA indicates improvement. Best value on the scale 100, worst 0. The number of participants with a stable BCVA (BCVA score at 6 months minus BCVA score at 24 months ≤4 letters) were reported.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Month 11 and 24

Population: Included population: No subjects included as analysis required data at month 24 and trial terminated before any subject reached month 12

Best-Corrected Visual Acuity (BCVA) letters were measured using Early Treatment Diabetic Retinopathy Study (EDTRS)-like chart while participants were in a sitting position at a testing distance of 4 meters. The range of EDTRS is 0 to 100 letters. A positive change from baseline of BCVA indicates improvement. Best value on the scale 100, worst 0. The number of participants with a stable BCVA (BCVA score at 11 months minus BCVA score at 24 months ≤4 letters) was calculated as well as its confidence interval at 95%.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Baseline, Month 3, 6, 8 and 11

Population: Included population with evaluable patients at specific time points.

Best-Corrected Visual Acuity (BCVA) letters was measured using Early Treatment Diabetic Retinopathy Study (EDTRS)-like chart while participants were in a sitting position at a testing distance of 4 meters. The range of EDTRS is 0 to 100 letters. A positive change from baseline of BCVA indicates improvement. Best value on the scale 100, worst 0. The number of participants maintaining ≥10 letters gains in BCVA (compared to the baseline BCVA \[Day 0\]) value for each visit from Month 3 onwards were reported.

Outcome measures

Outcome measures
Measure
Ranibizumab
n=21 Participants
Intravitreal injection with standard dose of 0.5 mg/0.05mL Pro re nata (PRN)
Visual Acuity: Number of Participants Keeping a BCVA Score Gain ≥10 Letters
Month 3
8 Participants
Visual Acuity: Number of Participants Keeping a BCVA Score Gain ≥10 Letters
Month 6
4 Participants
Visual Acuity: Number of Participants Keeping a BCVA Score Gain ≥10 Letters
Month 8
3 Participants
Visual Acuity: Number of Participants Keeping a BCVA Score Gain ≥10 Letters
Month 11
1 Participants

SECONDARY outcome

Timeframe: Baseline, Months 3, 6, 8 and 11

Population: Included population with evaluable patients at specific time points.

Best-Corrected Visual Acuity (BCVA) letters was measured using Early Treatment Diabetic Retinopathy Study (EDTRS)-like chart while participants were in a sitting position at a testing distance of 4 meters. The range of EDTRS is 0 to 100 letters. A positive change from baseline of BCVA indicates improvement. Best value on the scale 100, worst 0. The number of participants maintaining ≥15 letters gains in BCVA (compared to the baseline BCVA \[Day 0\]) value for each visit from Month 3 onwards were reported.

Outcome measures

Outcome measures
Measure
Ranibizumab
n=21 Participants
Intravitreal injection with standard dose of 0.5 mg/0.05mL Pro re nata (PRN)
Visual Acuity: Number of Participants Keeping a BCVA Score Gain ≥15 Letters
Month 3
4 Participants
Visual Acuity: Number of Participants Keeping a BCVA Score Gain ≥15 Letters
Month 6
3 Participants
Visual Acuity: Number of Participants Keeping a BCVA Score Gain ≥15 Letters
Month 8
1 Participants
Visual Acuity: Number of Participants Keeping a BCVA Score Gain ≥15 Letters
Month 11
0 Participants

SECONDARY outcome

Timeframe: Months 6, 8 and 11

Population: Included population with evaluable patients at specific time points.

Best-Corrected Visual Acuity (BCVA) letters were measured using Early Treatment Diabetic Retinopathy Study (EDTRS)-like chart while participants were in a sitting position at a testing distance of 4 meters. The range of EDTRS is 0 to 100 letters. A positive change from baseline of BCVA indicates improvement. Best value on the scale 100, worst 0. Number of participants presenting with a ≥15 letter loss in BCVA (compared to the value observed at 6 months) and leading to a treatment change (Rescue Group) for month 8 and 11 were analyzed.

Outcome measures

Outcome measures
Measure
Ranibizumab
n=5 Participants
Intravitreal injection with standard dose of 0.5 mg/0.05mL Pro re nata (PRN)
Visual Acuity: Number of Participants With a BCVA Loss ≥15 Letters at Months 8 and 11 Compared to Month 6 in the Study Eye.
Month 6 to Month 8
0 Participants
Visual Acuity: Number of Participants With a BCVA Loss ≥15 Letters at Months 8 and 11 Compared to Month 6 in the Study Eye.
Month 6 to Month 11
0 Participants

SECONDARY outcome

Timeframe: Baseline, months 1, 2, 3, 4, 5, 6, 8 and 11

Population: Included population with evaluable patients at specific time points.

Best-Corrected Visual Acuity (BCVA) letters was measured using Early Treatment Diabetic Retinopathy Study (EDTRS)-like chart while participants were in a sitting position at a testing distance of 4 meters. The range of EDTRS is 0 to 100 letters. A positive change from baseline of BCVA indicates improvement. Best value on the scale 100, worst 0. The mean variation in BCVA was compared to the baseline BCVA value \[Day 0\] over a period of 24 months for patients in the Main Group.

Outcome measures

Outcome measures
Measure
Ranibizumab
n=31 Participants
Intravitreal injection with standard dose of 0.5 mg/0.05mL Pro re nata (PRN)
Visual Acuity : Change of BCVA From Baseline in the Study Eye (ETDRS)
Month 1
5.45 Letters
Standard Deviation 6.444
Visual Acuity : Change of BCVA From Baseline in the Study Eye (ETDRS)
Month 2
5.81 Letters
Standard Deviation 7.328
Visual Acuity : Change of BCVA From Baseline in the Study Eye (ETDRS)
Month 3
8.05 Letters
Standard Deviation 6.704
Visual Acuity : Change of BCVA From Baseline in the Study Eye (ETDRS)
Month 4
9.94 Letters
Standard Deviation 5.805
Visual Acuity : Change of BCVA From Baseline in the Study Eye (ETDRS)
Month 5
9.88 Letters
Standard Deviation 5.290
Visual Acuity : Change of BCVA From Baseline in the Study Eye (ETDRS)
Month 6
11.00 Letters
Standard Deviation 8.485
Visual Acuity : Change of BCVA From Baseline in the Study Eye (ETDRS)
Month 8
10.40 Letters
Standard Deviation 5.413
Visual Acuity : Change of BCVA From Baseline in the Study Eye (ETDRS)
Month 11
10.00 Letters
Standard Deviation NA
standard deviation not calculated for n=1

SECONDARY outcome

Timeframe: Baseline, months 1, 2, 3, 4, 5, 6, 8 and 11

Population: Included population: No subjects included as analysis required data at month 24 and trial terminated before any subject reached month 12

Retinal thickness is assessed by optical coherence tomography (OCT) in the study eye. The retina is the light-sensitive part of the eye. OCT is a laser-based, noninvasive, diagnostic system providing high-resolution, three-dimensional images of the retina. A negative mean change from baseline indicates an improvement and a positive mean change from baseline indicates a worsening.The absolute variations of the Central Retinal Thickness (CRT) was measured using a Spectral Domain-Optical Coherence Tomography (SD-OCT) at each visit. Values were calculated as a log OCT (=log\[CRT/200\]).

Outcome measures

Outcome measures
Measure
Ranibizumab
n=31 Participants
Intravitreal injection with standard dose of 0.5 mg/0.05mL Pro re nata (PRN)
Central Retinal Thickness : Change of Log OCT From Baseline in the Study Eye
Month 1
-0.10 log[μm/200]
Standard Deviation 0.117
Central Retinal Thickness : Change of Log OCT From Baseline in the Study Eye
Month 2
-0.12 log[μm/200]
Standard Deviation 0.122
Central Retinal Thickness : Change of Log OCT From Baseline in the Study Eye
Month 3
-0.13 log[μm/200]
Standard Deviation 0.123
Central Retinal Thickness : Change of Log OCT From Baseline in the Study Eye
Month 4
-0.13 log[μm/200]
Standard Deviation 0.104
Central Retinal Thickness : Change of Log OCT From Baseline in the Study Eye
Month 5
-0.16 log[μm/200]
Standard Deviation 0.096
Central Retinal Thickness : Change of Log OCT From Baseline in the Study Eye
Month 6
-0.15 log[μm/200]
Standard Deviation 0.120
Central Retinal Thickness : Change of Log OCT From Baseline in the Study Eye
Month 8
-0.12 log[μm/200]
Standard Deviation 0.062
Central Retinal Thickness : Change of Log OCT From Baseline in the Study Eye
Month 11
-0.13 log[μm/200]
Standard Deviation NA
standard deviation not calculated for n=1

SECONDARY outcome

Timeframe: Baseline, Months 3, 6, 8 and 11

Population: Included population for subjects entering Rescue Group: No subjects provided evaluable data after switching to the Rescue Group

Best-Corrected Visual Acuity (BCVA) letters was measured using Early Treatment Diabetic Retinopathy Study (EDTRS)-like chart while participants were in a sitting position at a testing distance of 4 meters. The range of EDTRS is 0 to 100 letters. A positive change from baseline of BCVA indicates improvement. Best value on the scale 100, worst 0. The mean variation in BCVA was compared to the baseline BCVA value \[Day 0\] over a period of 24 months for patients in the Rescue Group.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Baseline, Months 3, 6, 8 and 11

Population: Included population for subjects entering Rescue Group: No subjects provided evaluable data after switching to the Rescue Group

Retinal thickness is assessed by optical coherence tomography (OCT) in the study eye. The retina is the light-sensitive part of the eye. OCT is a laser-based, noninvasive, diagnostic system providing high-resolution, three-dimensional images of the retina. A negative mean change from baseline indicates an improvement and a positive mean change from baseline indicates a worsening.The absolute variations of the Central Retinal Thickness (CRT) measured using a Spectral Domain-Optical Coherence Tomography (SD-OCT) at each visit. Values were calculated as a log OCT (=log\[CRT/200\]).

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: baseline, months 11, 12 and 24

Population: Included population: No subjects included as analysis required data at month 24 and trial terminated before any subject reached month 12

The global score obtained on the Visual Function Questionnaire 25 (VFQ 25) was compared from baseline to months 11 and 24 for the Main group and from baseline to months 12 and 24 for the Rescue group.

Outcome measures

Outcome data not reported

Adverse Events

Ranibizumab

Serious events: 2 serious events
Other events: 12 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Ranibizumab
n=31 participants at risk
Intravitreal injection with standard dose of 0.5 mg/0.05mL Pro re nata (PRN)
Metabolism and nutrition disorders
Diabetes mellitus inadequate control
3.2%
1/31 • Adverse events (AEs) were collected from the patient screening onwards. However, a safety observation period which started from first injection until 4 weeks after discontinuation - up to 11 months.
Musculoskeletal and connective tissue disorders
Osteonecrosis
3.2%
1/31 • Adverse events (AEs) were collected from the patient screening onwards. However, a safety observation period which started from first injection until 4 weeks after discontinuation - up to 11 months.

Other adverse events

Other adverse events
Measure
Ranibizumab
n=31 participants at risk
Intravitreal injection with standard dose of 0.5 mg/0.05mL Pro re nata (PRN)
Cardiac disorders
Coronary artery stenosis
3.2%
1/31 • Adverse events (AEs) were collected from the patient screening onwards. However, a safety observation period which started from first injection until 4 weeks after discontinuation - up to 11 months.
Eye disorders
Eye allergy (Both eyes)
3.2%
1/31 • Adverse events (AEs) were collected from the patient screening onwards. However, a safety observation period which started from first injection until 4 weeks after discontinuation - up to 11 months.
Eye disorders
Halo vision (Study eye)
3.2%
1/31 • Adverse events (AEs) were collected from the patient screening onwards. However, a safety observation period which started from first injection until 4 weeks after discontinuation - up to 11 months.
Eye disorders
Macular oedema (Contralateral eye)
3.2%
1/31 • Adverse events (AEs) were collected from the patient screening onwards. However, a safety observation period which started from first injection until 4 weeks after discontinuation - up to 11 months.
Eye disorders
Posterior capsule opacification (Contralateral eye)
3.2%
1/31 • Adverse events (AEs) were collected from the patient screening onwards. However, a safety observation period which started from first injection until 4 weeks after discontinuation - up to 11 months.
Eye disorders
Vitreous haemorrhage (Study eye)
3.2%
1/31 • Adverse events (AEs) were collected from the patient screening onwards. However, a safety observation period which started from first injection until 4 weeks after discontinuation - up to 11 months.
Gastrointestinal disorders
Abdominal pain upper
3.2%
1/31 • Adverse events (AEs) were collected from the patient screening onwards. However, a safety observation period which started from first injection until 4 weeks after discontinuation - up to 11 months.
General disorders
Chills
3.2%
1/31 • Adverse events (AEs) were collected from the patient screening onwards. However, a safety observation period which started from first injection until 4 weeks after discontinuation - up to 11 months.
General disorders
Oedema peripheral
3.2%
1/31 • Adverse events (AEs) were collected from the patient screening onwards. However, a safety observation period which started from first injection until 4 weeks after discontinuation - up to 11 months.
General disorders
Pyrexia
3.2%
1/31 • Adverse events (AEs) were collected from the patient screening onwards. However, a safety observation period which started from first injection until 4 weeks after discontinuation - up to 11 months.
Infections and infestations
Conjunctivitis (Both eyes)
3.2%
1/31 • Adverse events (AEs) were collected from the patient screening onwards. However, a safety observation period which started from first injection until 4 weeks after discontinuation - up to 11 months.
Infections and infestations
Conjunctivitis viral (Study eye)
3.2%
1/31 • Adverse events (AEs) were collected from the patient screening onwards. However, a safety observation period which started from first injection until 4 weeks after discontinuation - up to 11 months.
Infections and infestations
Gastroenteritis
9.7%
3/31 • Adverse events (AEs) were collected from the patient screening onwards. However, a safety observation period which started from first injection until 4 weeks after discontinuation - up to 11 months.
Infections and infestations
Nasopharyngitis
3.2%
1/31 • Adverse events (AEs) were collected from the patient screening onwards. However, a safety observation period which started from first injection until 4 weeks after discontinuation - up to 11 months.
Injury, poisoning and procedural complications
Wound
3.2%
1/31 • Adverse events (AEs) were collected from the patient screening onwards. However, a safety observation period which started from first injection until 4 weeks after discontinuation - up to 11 months.
Nervous system disorders
Paraesthesia
3.2%
1/31 • Adverse events (AEs) were collected from the patient screening onwards. However, a safety observation period which started from first injection until 4 weeks after discontinuation - up to 11 months.
Renal and urinary disorders
Microalbuminuria
3.2%
1/31 • Adverse events (AEs) were collected from the patient screening onwards. However, a safety observation period which started from first injection until 4 weeks after discontinuation - up to 11 months.
Respiratory, thoracic and mediastinal disorders
Cough
3.2%
1/31 • Adverse events (AEs) were collected from the patient screening onwards. However, a safety observation period which started from first injection until 4 weeks after discontinuation - up to 11 months.
Respiratory, thoracic and mediastinal disorders
Epistaxis
3.2%
1/31 • Adverse events (AEs) were collected from the patient screening onwards. However, a safety observation period which started from first injection until 4 weeks after discontinuation - up to 11 months.
Vascular disorders
Peripheral arterial occlusive disease
3.2%
1/31 • Adverse events (AEs) were collected from the patient screening onwards. However, a safety observation period which started from first injection until 4 weeks after discontinuation - up to 11 months.

Additional Information

Study Director

Novartis Pharmaceuticals

Phone: 862-778-1873

Results disclosure agreements

  • Principal investigator is a sponsor employee The terms and conditions of Novartis' agreements with its investigators may vary. However, Novartis does not prohibit any investigator from publishing. Any publications from a single-site are postponed until the publication of the pooled data (i.e., data from all sites) in the clinical trial or disclosure of trial results in their entirety.
  • Publication restrictions are in place

Restriction type: OTHER