Trial Outcomes & Findings for A Multicenter Assessment of LBR-101 in High Frequency Episodic Migraine (NCT NCT02025556)

NCT ID: NCT02025556

Last Updated: 2022-01-24

Results Overview

A migraine day was endorsed when at least 1 of the following situations occurred: 1) A calendar day (0:00 to 23:59) demonstrating at least 4 consecutive hours of a headache endorsing criteria for migraine, or 2) a calendar day (0:00 to 23:59) demonstrating at least 4 consecutive hours of a headache endorsing criteria for probable migraine, a migraine subtype where only one migraine criterion is missing, or 3) the participant used acute migraine medication (triptans and ergot compounds) to treat a headache of any duration, or 4) any of the above days preceded or followed by a day with a headache of any duration. This calculation was defined as the change from baseline in the number of headache days during the 28-day post treatment period ending at week 12. Headache severity was rated daily by the participant as either no pain, mild, moderate, or severe.

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

297 participants

Primary outcome timeframe

Baseline to week 12

Results posted on

2022-01-24

Participant Flow

A total of 297 participants with episodic migraine were enrolled in the study.

Participants were assigned to receive either subcutaneous administration of 675 mg of fremanezumab (LBR-101) for three months, subcutaneous administration of 225 mg of fremanezumab (LBR-101) for three months, or subcutaneous administration of placebo for three months.

Participant milestones

Participant milestones
Measure
Placebo
Participants received subcutaneous placebo injections at one visit per month for three months (Day 1/week 0, Day 29/week 4, and Day 57/week 8).
Low Dose
Participants received 225 mg fremanezumab subcutaneously on Day 1/week 0, Day 29/week 4, and on Day 57/week 8.
High Dose
Participants received 675 mg fremanezumab subcutaneously on Day 1/week 0, Day 29/week 4, and on Day 57/week 8.
Overall Study
STARTED
104
96
97
Overall Study
Safety Analysis Set
104
96
96
Overall Study
Intent-to-treat (ITT) Set
104
95
96
Overall Study
COMPLETED
98
83
88
Overall Study
NOT COMPLETED
6
13
9

Reasons for withdrawal

Reasons for withdrawal
Measure
Placebo
Participants received subcutaneous placebo injections at one visit per month for three months (Day 1/week 0, Day 29/week 4, and Day 57/week 8).
Low Dose
Participants received 225 mg fremanezumab subcutaneously on Day 1/week 0, Day 29/week 4, and on Day 57/week 8.
High Dose
Participants received 675 mg fremanezumab subcutaneously on Day 1/week 0, Day 29/week 4, and on Day 57/week 8.
Overall Study
Adverse Event
0
4
2
Overall Study
Lack of Efficacy
2
1
0
Overall Study
Protocol Violation
2
1
0
Overall Study
Withdrawal by Subject
0
3
6
Overall Study
Lost to Follow-up
2
4
0
Overall Study
Reason not reported
0
0
1

Baseline Characteristics

A Multicenter Assessment of LBR-101 in High Frequency Episodic Migraine

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Placebo
n=104 Participants
Participants received subcutaneous placebo injections at one visit per month for three months (Day 1/week 0, Day 29/week 4, and Day 57/week 8).
Low Dose
n=96 Participants
Participants received 225 mg fremanezumab subcutaneously on Day 1/week 0, Day 29/week 4, and on Day 57/week 8.
High Dose
n=97 Participants
Participants received 675 mg fremanezumab subcutaneously on Day 1/week 0, Day 29/week 4, and on Day 57/week 8.
Total
n=297 Participants
Total of all reporting groups
Age, Continuous
42.0 Years
STANDARD_DEVIATION 11.62 • n=5 Participants
40.8 Years
STANDARD_DEVIATION 12.43 • n=7 Participants
40.7 Years
STANDARD_DEVIATION 12.56 • n=5 Participants
41.2 Years
STANDARD_DEVIATION 12.17 • n=4 Participants
Sex: Female, Male
Female
92 Participants
n=5 Participants
87 Participants
n=7 Participants
82 Participants
n=5 Participants
261 Participants
n=4 Participants
Sex: Female, Male
Male
12 Participants
n=5 Participants
9 Participants
n=7 Participants
15 Participants
n=5 Participants
36 Participants
n=4 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
11 Participants
n=5 Participants
16 Participants
n=7 Participants
17 Participants
n=5 Participants
44 Participants
n=4 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
92 Participants
n=5 Participants
80 Participants
n=7 Participants
79 Participants
n=5 Participants
251 Participants
n=4 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
1 Participants
n=5 Participants
0 Participants
n=7 Participants
1 Participants
n=5 Participants
2 Participants
n=4 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
Race (NIH/OMB)
Asian
2 Participants
n=5 Participants
1 Participants
n=7 Participants
1 Participants
n=5 Participants
4 Participants
n=4 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
Race (NIH/OMB)
Black or African American
13 Participants
n=5 Participants
19 Participants
n=7 Participants
18 Participants
n=5 Participants
50 Participants
n=4 Participants
Race (NIH/OMB)
White
85 Participants
n=5 Participants
74 Participants
n=7 Participants
74 Participants
n=5 Participants
233 Participants
n=4 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
Race (NIH/OMB)
Unknown or Not Reported
4 Participants
n=5 Participants
2 Participants
n=7 Participants
4 Participants
n=5 Participants
10 Participants
n=4 Participants
Years of migraine
21.2 Years
STANDARD_DEVIATION 14.1 • n=5 Participants
18.9 Years
STANDARD_DEVIATION 12.92 • n=7 Participants
16.9 Years
STANDARD_DEVIATION 12.25 • n=5 Participants
19.0 Years
STANDARD_DEVIATION 13.21 • n=4 Participants
Preventive medication use
Yes
28 Participants
n=5 Participants
32 Participants
n=7 Participants
26 Participants
n=5 Participants
86 Participants
n=4 Participants
Preventive medication use
No
76 Participants
n=5 Participants
64 Participants
n=7 Participants
71 Participants
n=5 Participants
211 Participants
n=4 Participants

PRIMARY outcome

Timeframe: Baseline to week 12

Population: Intent-to-treat (ITT) population includes all randomized participants that received at least one dose and obtained at least one endpoint measurement.

A migraine day was endorsed when at least 1 of the following situations occurred: 1) A calendar day (0:00 to 23:59) demonstrating at least 4 consecutive hours of a headache endorsing criteria for migraine, or 2) a calendar day (0:00 to 23:59) demonstrating at least 4 consecutive hours of a headache endorsing criteria for probable migraine, a migraine subtype where only one migraine criterion is missing, or 3) the participant used acute migraine medication (triptans and ergot compounds) to treat a headache of any duration, or 4) any of the above days preceded or followed by a day with a headache of any duration. This calculation was defined as the change from baseline in the number of headache days during the 28-day post treatment period ending at week 12. Headache severity was rated daily by the participant as either no pain, mild, moderate, or severe.

Outcome measures

Outcome measures
Measure
Placebo
n=104 Participants
Participants received subcutaneous placebo injections at one visit per month for three months (Day 1/week 0, Day 29/week 4, and Day 57/week 8).
Low Dose
n=95 Participants
Participants received 225 mg fremanezumab subcutaneously on Day 1/week 0, Day 29/week 4, and on Day 57/week 8.
High Dose
n=96 Participants
Participants received 675 mg fremanezumab subcutaneously on Day 1/week 0, Day 29/week 4, and on Day 57/week 8.
Mean Change From Baseline in the Monthly Migraine Days During the 28-day Post Treatment Period Ending With Week 12
-3.46 Days
Standard Error 0.53
-6.27 Days
Standard Error 0.55
-6.09 Days
Standard Error 0.53

PRIMARY outcome

Timeframe: Baseline to week 12

Population: Safety analysis set included all randomized participants who received at least one dose of study drug.

An AE was defined as any untoward medical occurrence that develops or worsens in severity during the conduct of a clinical study and does not necessarily have a causal relationship to the study drug. Relationship of AE to treatment was determined by the Investigator. Serious AEs include death, a life-threatening adverse event, inpatient hospitalization or prolongation of existing hospitalization, persistent or significant disability or incapacity, a congenital anomaly or birth defect, or an important medical event that jeopardized the participant and required medical intervention to prevent the previously listed serious outcomes. A summary of other non-serious AEs and all serious AEs, regardless of causality is located in Reported AE section.

Outcome measures

Outcome measures
Measure
Placebo
n=104 Participants
Participants received subcutaneous placebo injections at one visit per month for three months (Day 1/week 0, Day 29/week 4, and Day 57/week 8).
Low Dose
n=96 Participants
Participants received 225 mg fremanezumab subcutaneously on Day 1/week 0, Day 29/week 4, and on Day 57/week 8.
High Dose
n=96 Participants
Participants received 675 mg fremanezumab subcutaneously on Day 1/week 0, Day 29/week 4, and on Day 57/week 8.
Number of Participants With at Least One Adverse Event
58 Participants
44 Participants
57 Participants

PRIMARY outcome

Timeframe: Up to week 12

Population: Per planned analysis participants analyzed included all randomized participants who received at least one dose of study drug and reported at least one adverse event.

Adverse events were rated based on the investigator's clinical judgment. Mild: awareness of a sign or symptom that was easily tolerated Moderate: sign or symptom intense enough to interfere with usual activity Severe: interfered significantly with ability to do work or usual activity

Outcome measures

Outcome measures
Measure
Placebo
n=58 Participants
Participants received subcutaneous placebo injections at one visit per month for three months (Day 1/week 0, Day 29/week 4, and Day 57/week 8).
Low Dose
n=44 Participants
Participants received 225 mg fremanezumab subcutaneously on Day 1/week 0, Day 29/week 4, and on Day 57/week 8.
High Dose
n=57 Participants
Participants received 675 mg fremanezumab subcutaneously on Day 1/week 0, Day 29/week 4, and on Day 57/week 8.
Number of Participants Reporting Mild, Moderate, and Severe Adverse Events (AEs)
Mild
29 Participants
20 Participants
31 Participants
Number of Participants Reporting Mild, Moderate, and Severe Adverse Events (AEs)
Moderate
27 Participants
20 Participants
26 Participants
Number of Participants Reporting Mild, Moderate, and Severe Adverse Events (AEs)
Severe
1 Participants
4 Participants
0 Participants
Number of Participants Reporting Mild, Moderate, and Severe Adverse Events (AEs)
Unknown severity
1 Participants
0 Participants
0 Participants

SECONDARY outcome

Timeframe: Baseline to week 12

Population: Intent-to-treat (ITT) population includes all randomized participants who received at least one dose of study medication and obtained at least one endpoint measurement.

A headache day was defined as when at least 1 of the following situations occurred: A calendar day (0:00 to 23:59) demonstrating at least 4 consecutive hours of a headache of any severity or the participant used acute migraine medication (triptans and ergot compounds) to treat a headache. This calculation was defined as the change from baseline in the number of headache days during the 28-day post treatment period ending at week 12. Headache severity was rated daily by the participant as either no pain, mild, moderate, or severe.

Outcome measures

Outcome measures
Measure
Placebo
n=104 Participants
Participants received subcutaneous placebo injections at one visit per month for three months (Day 1/week 0, Day 29/week 4, and Day 57/week 8).
Low Dose
n=95 Participants
Participants received 225 mg fremanezumab subcutaneously on Day 1/week 0, Day 29/week 4, and on Day 57/week 8.
High Dose
n=96 Participants
Participants received 675 mg fremanezumab subcutaneously on Day 1/week 0, Day 29/week 4, and on Day 57/week 8.
Change From Baseline in Number of Days With Headache of Any Severity
-3.52 Days
Standard Error 0.53
-6.14 Days
Standard Error 0.56
-6.10 Days
Standard Error 0.54

Adverse Events

Placebo

Serious events: 0 serious events
Other events: 9 other events
Deaths: 0 deaths

Low Dose

Serious events: 2 serious events
Other events: 9 other events
Deaths: 0 deaths

High Dose

Serious events: 2 serious events
Other events: 11 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Placebo
n=104 participants at risk
Participants received subcutaneous placebo injections at one visit per month for three months (Day 1/week 0, Day 29/week 4, and Day 57/week 8).
Low Dose
n=96 participants at risk
Participants received 225 mg fremanezumab subcutaneously on Day 1/week 0, Day 29/week 4, and on Day 57/week 8.
High Dose
n=96 participants at risk
Participants received 675 mg fremanezumab subcutaneously on Day 1/week 0, Day 29/week 4, and on Day 57/week 8.
Blood and lymphatic system disorders
Antiphospholipid syndrome
0.00%
0/104 • Baseline to week 12
0.00%
0/96 • Baseline to week 12
1.0%
1/96 • Number of events 1 • Baseline to week 12
Injury, poisoning and procedural complications
Fibula fracture
0.00%
0/104 • Baseline to week 12
1.0%
1/96 • Number of events 1 • Baseline to week 12
0.00%
0/96 • Baseline to week 12
Nervous system disorders
Migraine
0.00%
0/104 • Baseline to week 12
1.0%
1/96 • Number of events 1 • Baseline to week 12
0.00%
0/96 • Baseline to week 12
Nervous system disorders
Tremor
0.00%
0/104 • Baseline to week 12
0.00%
0/96 • Baseline to week 12
1.0%
1/96 • Number of events 1 • Baseline to week 12
Vascular disorders
Hypertensive crisis
0.00%
0/104 • Baseline to week 12
1.0%
1/96 • Number of events 1 • Baseline to week 12
0.00%
0/96 • Baseline to week 12

Other adverse events

Other adverse events
Measure
Placebo
n=104 participants at risk
Participants received subcutaneous placebo injections at one visit per month for three months (Day 1/week 0, Day 29/week 4, and Day 57/week 8).
Low Dose
n=96 participants at risk
Participants received 225 mg fremanezumab subcutaneously on Day 1/week 0, Day 29/week 4, and on Day 57/week 8.
High Dose
n=96 participants at risk
Participants received 675 mg fremanezumab subcutaneously on Day 1/week 0, Day 29/week 4, and on Day 57/week 8.
General disorders
Injection site pain
5.8%
6/104 • Number of events 10 • Baseline to week 12
9.4%
9/96 • Number of events 13 • Baseline to week 12
4.2%
4/96 • Number of events 4 • Baseline to week 12
Infections and infestations
Sinusitis
2.9%
3/104 • Number of events 3 • Baseline to week 12
0.00%
0/96 • Baseline to week 12
5.2%
5/96 • Number of events 5 • Baseline to week 12
Nervous system disorders
Dizziness
0.00%
0/104 • Baseline to week 12
1.0%
1/96 • Number of events 2 • Baseline to week 12
5.2%
5/96 • Number of events 6 • Baseline to week 12

Additional Information

Director, Clinical Research

Teva Branded Pharmaceutical Products R&D, Inc.

Phone: 1-888-483-8279

Results disclosure agreements

  • Principal investigator is a sponsor employee Sponsor has the right 60 days before submission for publication to review/provide comments. If the Sponsor's review shows that potentially patentable subject matter would be disclosed, publication or public disclosure shall be delayed for up to 90 additional days in order for the Sponsor, or Sponsor's designees, to file the necessary patent applications. In multicenter trials, each PI will postpone single center publications until after disclosure or publication of multicenter data.
  • Publication restrictions are in place

Restriction type: OTHER