MAD Study Evaluating the Safety, Tolerability, and Pharmacokinetic Effects of N91115 in Healthy Subjects

NCT ID: NCT02013388

Last Updated: 2016-12-21

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE1

Total Enrollment

49 participants

Study Classification

INTERVENTIONAL

Study Start Date

2014-02-28

Study Completion Date

2015-02-28

Brief Summary

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A study in healthy subjects to assess the safety, tolerability, and pharmacokinetics of N91115.

Detailed Description

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This Phase 1 study in healthy subjects is being conducted to assess the safety, tolerability, and pharmacokinetics of N91115. Also, a comparison of the fasted versus fed with a high fat meal were compared for PK.

Conditions

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Healthy

Keywords

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N91115 GSNORi SNO Cavosonstat

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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10 mg

single oral daily dose of 10 mg N91115 for 14 days

Group Type EXPERIMENTAL

N91115

Intervention Type DRUG

Given PO daily for 14 days

Placebo

single oral daily dose of placebo for 14 days

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Given PO daily for 14 days

50 mg

single oral daily dose of 50 mg N91115 for 14 days

Group Type EXPERIMENTAL

N91115

Intervention Type DRUG

Given PO daily for 14 days

50 mg (single dose)

single oral dose of 50 mg N91115

Group Type EXPERIMENTAL

N91115

Intervention Type DRUG

Given PO only on Day 1

250 mg

single oral daily dose of 250 mg N91115 for 14 days (fasted)

Group Type EXPERIMENTAL

N91115

Intervention Type DRUG

Given PO daily for 14 days

250 mg (Fed)

single oral daily dose of 250 mg N91115 for 1 day (fed fat meal)

Group Type EXPERIMENTAL

N91115

Intervention Type DRUG

Given PO only on Day 1

500 mg

single oral daily dose of 500 mg N91115 for 14 days

Group Type EXPERIMENTAL

N91115

Intervention Type DRUG

Given PO daily for 14 days

Placebo-Day 1 only

Single oral dose of placebo (Day 1 only)

Group Type PLACEBO_COMPARATOR

Placebo-Day 1 only

Intervention Type DRUG

Given PO- only on Day 1 (single dosed to match single dose treatments)

Interventions

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N91115

Given PO daily for 14 days

Intervention Type DRUG

Placebo

Given PO daily for 14 days

Intervention Type DRUG

N91115

Given PO only on Day 1

Intervention Type DRUG

Placebo-Day 1 only

Given PO- only on Day 1 (single dosed to match single dose treatments)

Intervention Type DRUG

Other Intervention Names

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Cavosonstat Cavosonstat Placebo

Eligibility Criteria

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Inclusion Criteria

* Subject voluntarily agrees to participate in this study and signs an Institutional Review Board (IRB)-approved informed consent prior to performing any of the screening procedures and in the opinion of the PI complies with all the requirements of the study.
* Subject is healthy, determined at the screening medical evaluation (including but not limited to medical history, physical examination and clinical laboratory evaluations).
* Subject is Caucasian.
* Female subject must be of non-childbearing potential (surgically sterile \[hysterectomy or bilateral tubal ligation\] or post-menopausal ≥ 1 year with follicle stimulating hormone \[FSH\] \> 40 U/L). Women receiving hormone replacement therapy (HRT) are eligible to enroll.
* Male subject must agree to use condoms and refrain from sperm donation from Day 1 until 30 days post last dose or have documentation of vasectomy.
* Subject has a body weight \> 50 kg and body mass index (BMI) between 19.5 and 32 kg/m2, inclusive, at screening.
* Subject has no clinically significant abnormal findings related to their systolic or diastolic blood pressure (BP), per the investigator's judgment, at screening or Day 1.
* Subject has no clinically significant abnormal findings in 12 lead ECG, per the investigator's judgment, at screening.

Exclusion Criteria

* Subject has clinically significant history or evidence of cardiovascular, respiratory, hepatic, renal, gastrointestinal, endocrine, neurological, immunological, or psychiatric disorder(s) as determined by the investigator or designee.
* Subject has clinically significant abnormalities on a 12 lead ECG done at screening
* Subject has clinically significant abnormalities on a 48-hour ambulatory ECG done at screening
* Subject has any disorder that would interfere with the absorption, distribution, metabolism, or excretion of drugs.
* Subject has any concurrent disease or condition that, in the opinion of the investigator, would make the subject unsuitable for participation in the clinical study.
* Subject is unlikely to comply with the protocol requirements, instructions, and study related restrictions; e.g., uncooperative attitude, unavailable for follow-up call, and/or improbability of completing the clinical study.
Minimum Eligible Age

18 Years

Maximum Eligible Age

55 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

Yes

Sponsors

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Nivalis Therapeutics, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Christopher Galloway, MD

Role: PRINCIPAL_INVESTIGATOR

Davita Clinical Research

Steven A Shoemaker, MD

Role: STUDY_DIRECTOR

Nivalis Therapeutics, Inc.

Locations

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DaVita Clinical Research

Lakewood, Colorado, United States

Site Status

Countries

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United States

References

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Donaldson SH, Solomon GM, Zeitlin PL, Flume PA, Casey A, McCoy K, Zemanick ET, Mandagere A, Troha JM, Shoemaker SA, Chmiel JF, Taylor-Cousar JL. Pharmacokinetics and safety of cavosonstat (N91115) in healthy and cystic fibrosis adults homozygous for F508DEL-CFTR. J Cyst Fibros. 2017 May;16(3):371-379. doi: 10.1016/j.jcf.2017.01.009. Epub 2017 Feb 13.

Reference Type DERIVED
PMID: 28209466 (View on PubMed)

Related Links

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Other Identifiers

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N91115-1H-01

Identifier Type: -

Identifier Source: org_study_id