Phase 1 Dose-escalating Study of MM-398 (Irinotecan Sucrosofate Liposome Injection) Plus Intravenous Cyclophosphamide in Recurrent or Refractory Pediatric Solid Tumors

NCT ID: NCT02013336

Last Updated: 2022-03-31

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

UNKNOWN

Clinical Phase

PHASE1

Total Enrollment

30 participants

Study Classification

INTERVENTIONAL

Study Start Date

2013-12-31

Study Completion Date

2023-12-31

Brief Summary

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This is a Phase 1 study of the combination of two drugs: MM-398 and Cyclophosphamide. The goal is to find the highest dose of MM-398 that can be given safely when it is used together with the chemotherapy drug Cyclophosphamide.

Detailed Description

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Conditions

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Recurrent or Refractory Solid Tumors Ewing Sarcoma Rhabdomyosarcoma Neuroblastoma Osteosarcoma

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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MM-398 + cyclophosphamide

MM-398+cyclophosphamide

Group Type EXPERIMENTAL

MM-398 (Irinotecan Sucrosofate Liposome Injection) plus cyclophosphamide

Intervention Type DRUG

chemotherapy

Interventions

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MM-398 (Irinotecan Sucrosofate Liposome Injection) plus cyclophosphamide

chemotherapy

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Histologically or cytologically-confirmed Ewing sarcoma, rhabdomyosarcoma, neuroblastoma, or osteosarcoma
* Disease progression after prior therapy in locally advanced or metastatic setting
* Measurable or evaluable disease based on the Response Evaluation Criteria in Solid Tumors (RECIST v1.1) criteria
* Age 12 months to \<21 years
* Adequate bone marrow reserves, hepatic function, and renal function
* Recovered from effects of any prior surgery or cancer therapy
* Patients 18 years or older will provide written consent. A parent or legal guardian of a patient \<18 years of age will provide informed consent and patients 11 to 18 years of age will provide written assent or as per participating institutional policy.

Exclusion Criteria

* Clinically significant gastrointestinal disorders
* NYHA Class III or IV congestive heart failure, ventricular arrhythmias or uncontrolled blood pressure
* Active infection or unexplained fever
* Known hypersensitivity to any of the components of MM-398 or other liposomal products
* Recent Investigational therapy
* Pregnant or breast feeding; females of child-bearing potential must test negative for pregnancy at the time of enrollment
Minimum Eligible Age

12 Months

Maximum Eligible Age

20 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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South Plains Oncology Consortium

NETWORK

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Paul Harker-Murray, MD

Role: STUDY_CHAIR

Midwest Children's Hospital

Locations

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Cincinnati Children's Hospital Medical Center

Cincinnati, Ohio, United States

Site Status RECRUITING

University Of Oklahoma Health Sciences Center

Oklahoma City, Oklahoma, United States

Site Status RECRUITING

UT Southwestern

Dallas, Texas, United States

Site Status RECRUITING

MD Anderson Children's Cancer Hospital

Houston, Texas, United States

Site Status RECRUITING

Texas Tech University Health Sciences Center

Lubbock, Texas, United States

Site Status RECRUITING

Midwest Children's Hospital

Milwaukee, Wisconsin, United States

Site Status RECRUITING

Countries

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United States

Central Contacts

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Amanda Knight, RN, BSN

Role: CONTACT

806-743-2690

Facility Contacts

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Role: primary

513-636-4200

Haley Jones

Role: primary

Alison Patterson

Role: primary

Jonathan Gill, MD

Role: primary

Angie Cervantez

Role: primary

Olivia Tarnowske

Role: primary

References

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Hattinger CM, Patrizio MP, Magagnoli F, Luppi S, Serra M. An update on emerging drugs in osteosarcoma: towards tailored therapies? Expert Opin Emerg Drugs. 2019 Sep;24(3):153-171. doi: 10.1080/14728214.2019.1654455. Epub 2019 Aug 14.

Reference Type DERIVED
PMID: 31401903 (View on PubMed)

Other Identifiers

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SPOC-2012-001

Identifier Type: -

Identifier Source: org_study_id

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