Efficacy, Safety and Tolerability of Sexelaxin When Added to Standard Therapy in AHF

NCT ID: NCT02007720

Last Updated: 2019-08-02

Study Results

Results available

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

876 participants

Study Classification

INTERVENTIONAL

Study Start Date

2014-03-12

Study Completion Date

2017-06-16

Brief Summary

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The purpose of the study was to evaluate the efficacy, safety and tolerability of intravenous infusion of serelaxin, when added to standard therapy, in acute heart failure (AHF) patients.

Detailed Description

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Conditions

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Acute Heart Failure

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Placebo

Patients will receive continuous intravenous infusion of matching placebo serelaxin for 48 hours.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Intravenous infusion

Standard of CareTherapy

Intervention Type OTHER

This treatment can include but is not limited to intravenous and/or oral diuretics, ACE inhibitors/angiotensin receptor antagonists, β blockers, and aldosterone receptor antagonists, etc.

Serelaxin

Patients will receive continuous intravenous infusion of serelaxin(30 µg/kg/day) for 48 hours.

Group Type EXPERIMENTAL

Standard of CareTherapy

Intervention Type OTHER

This treatment can include but is not limited to intravenous and/or oral diuretics, ACE inhibitors/angiotensin receptor antagonists, β blockers, and aldosterone receptor antagonists, etc.

Serelaxin

Intervention Type DRUG

Intravenous infusion

Interventions

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Placebo

Intravenous infusion

Intervention Type DRUG

Standard of CareTherapy

This treatment can include but is not limited to intravenous and/or oral diuretics, ACE inhibitors/angiotensin receptor antagonists, β blockers, and aldosterone receptor antagonists, etc.

Intervention Type OTHER

Serelaxin

Intravenous infusion

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Male or female ≥ 18 years of age, with body weight ≤160 kg
* Hospitalized for AHF; AHF is defined as including all of the following measured at any time between presentation (including the emergency department and outpatient clinic) and at the end of screening:

* Persistent dyspnea at rest or with minimal exertion at screening and at the time of randomization
* Pulmonary congestion on chest radiograph
* Brain natriuretic peptide (BNP) ≥500 pg/mL or NT-proBNP ≥2,000 pg/mL
* Systolic BP ≥125 mmHg at the start and at the end of screening
* Able to be randomized within 16 hours from presentation to the hospital, including the emergency department and outpatient clinic
* Received intravenous furosemide of at least 40 mg total (or equivalent) at any time between presentation (this includes outpatient clinic, ambulance, or hospital including emergency department) and the start of screening for the study for the treatment of the current acute HF episode
* Renal impairment defined as an estimate glomerular filtration rate using the between presentation and randomization of ≥ 25 and ≤75mL/min/1.73m2, calculated using the Modification of Diet in Renal Disease formula (or modified sMDRD formula according to specific ethnic groups and local practice guidelines).

Exclusion Criteria

* Dyspnea primarily due to non-cardiac causes
* Temperature \>38.5°C (oral or equivalent), sepsis, active and clinically significant infection requiring IV anti-microbial treatment or known presence or evidence of Human Immunodeficiency Virus (HIV) infection (based on history and/or clinical findings, including laboratory results obtained during screening period).
* Clinical evidence of acute coronary syndrome currently or within 30 days prior to enrollment

\*Patients with systolic blood pressure \>180 mmHg at the end of screening
* AHF due to significant arrhythmias, which include any of the following: sustained ventricular tachycardia, bradycardia with sustained ventricular rate \<45 beats per minute, or atrial fibrillation/flutter with sustained ventricular response of \>130 beats per minute
* Hepatic disease unrelated to Heart Failure etiology and as determined by any one of the following: AST and/or ALT values exceeding 3 X ULN and/or bilirubin \> 1.5 X ULN at screening or history of hepatic encephalopathy, esophageal varices, or portacaval shunt, or a diagnosis of cirrhosis by any means, or evidence of chronic Hepatitis B (presence of hepatitis B surface antigen production: positive HBsAg), or chronic Hepatitis C infection (presence of Hepatitis C genetic replication: positive Hepatitis C viral RNA, based on history and/or clinical findings, including laboratory results obtained during screening period).

\*Significant uncorrected left ventricular outflow obstruction, such as obstructive hypertrophic cardiomyopathy or severe aortic stenosis (i.e., aortic valve area \<1.0 cm2 or mean gradient \>50 mmHg on prior or current echocardiogram), and severe mitral stenosis
* History of malignancy of any organ system (other than localized basal cell carcinoma of the skin), treated or untreated, within the past year with a life expectancy less than 1 year
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Novartis Pharmaceuticals

Role: STUDY_DIRECTOR

Novartis Pharmaceuticals

Locations

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Novartis Investigative Site

Beijing, Beijing Municipality, China

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Beijing, Beijing Municipality, China

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Lanzhou, Gansu, China

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Guangzhou, Guangdong, China

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Guangzhou, Guangdong, China

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Suzhou, Jiangsu, China

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Yangzhou, Jiangsu, China

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Shenyang, Liaoning, China

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Shenyang, Liaoning, China

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Shanghai, Shanghai Municipality, China

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Zhujing, Shanghai Municipality, China

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Xian, Shanxi, China

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Tianjin, Tianjin Municipality, China

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Hangzhou, Zhejiang, China

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Wenzhou, Zhejiang, China

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Beijing, , China

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Chongqing, , China

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Shanghai, , China

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Ahmedabad, Gujarat, India

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Vadodara, Gujarat, India

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Rajasthan, India, India

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Nagpur, Maharashtra, India

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Nagpur, Maharashtra, India

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New Delhi, National Capital Territory of Delhi, India

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Chennai, Tamil Nadu, India

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Hyderabad, Telangana, India

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Nagakute, Aichi-ken, Japan

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Seto, Aichi-ken, Japan

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Kamogawa, Chiba, Japan

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Saijō, Ehime, Japan

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Chikushino-shi, Fukuka, Japan

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Fukuoka, Fukuoka, Japan

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Fukuoka, Fukuoka, Japan

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Fukuoka, Fukuoka, Japan

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Iizuka, Fukuoka, Japan

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Kurume, Fukuoka, Japan

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Kurume, Fukuoka, Japan

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Ōgaki, Gifu, Japan

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Kushiro, Hokkaido, Japan

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Sapporo, Hokkaido, Japan

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Amagasaki, Hyōgo, Japan

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Kobe, Hyōgo, Japan

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Mito, Ibaraki, Japan

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Kanazawa, Ishikawa-ken, Japan

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Kan’onjichō, Kagawa-ken, Japan

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Takamatsu, Kagawa-ken, Japan

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Kawasaki, Kanagawa, Japan

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Yokohama, Kanagawa, Japan

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Yokohama, Kanagawa, Japan

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Yokohama, Kanagawa, Japan

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Yokohama, Kanagawa, Japan

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Kochi, Kochi, Japan

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Kumamoto, Kumamoto, Japan

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Yatsushiro, Kumamoto, Japan

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Kyoto, Kyoto, Japan

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Uji, Kyoto, Japan

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Sendai, Miyagi, Japan

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Nakano, Nagano, Japan

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Saku, Nagano, Japan

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Ueda, Nagano, Japan

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Niigata, Niigata, Japan

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Osaka, Osaka, Japan

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Kawaguchi, Saitama, Japan

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Sayama, Saitama, Japan

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Wako, Saitama, Japan

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Kusatsu, Shiga, Japan

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Hamamatsu, Shizuoka, Japan

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Kakegawa, Shizuoka, Japan

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Akishima, Tokyo, Japan

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Chuo Ku, Tokyo, Japan

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Hachiōji, Tokyo, Japan

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Itabashi-ku, Tokyo, Japan

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Musashino, Tokyo, Japan

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Shinagawa Ku, Tokyo, Japan

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Shinagawa-ku, Tokyo, Japan

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Tanabe, Wakayama, Japan

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Osaka, , Japan

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Saitama, , Japan

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Amman, JOR, Jordan

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Amman, , Jordan

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Amman, , Jordan

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Beirut, , Lebanon

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Beirut, , Lebanon

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El Achrafiyé, , Lebanon

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Hazmiyeh, , Lebanon

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Kuala Lumpur, MYS, Malaysia

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Kota Kinabalu, Sabah, Malaysia

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Kuching, Sarawak, Malaysia

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Kuala Lumpur, Selangor, Malaysia

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Sungai Buloh, Selangor, Malaysia

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Kuala Lumpur, , Malaysia

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Kuala Lumpur, , Malaysia

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Quezon City, Manila, Philippines

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Manila, National Capital Region, Philippines

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Makati City, , Philippines

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Manila, , Philippines

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Pasig, , Philippines

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Quezon City, , Philippines

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Quezon City, , Philippines

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San Juan City, , Philippines

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Singapore, , Singapore

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Singapore, , Singapore

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Gyeonggi-do, Bucheon Si, South Korea

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Wŏnju, Gangwon-do, South Korea

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Bundang Gu, Gyeonggi-do, South Korea

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Seoul, Korea, South Korea

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Seoul, Korea, South Korea

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Seoul, Korea, South Korea

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Cheongju-si, North Chungcheong, South Korea

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Seoul, Seocho Gu, South Korea

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Busan, , South Korea

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Gwangju, , South Korea

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Incheon, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Changhua, , Taiwan

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Kaohsiung City, , Taiwan

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Kaohsiung City, , Taiwan

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New Taipei City, , Taiwan

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Taichung, , Taiwan

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Taipei, , Taiwan

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Taipei, , Taiwan

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Taipei, , Taiwan

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Taoyuan District, , Taiwan

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Yilan, , Taiwan

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Songkhla, Hat Yai, Thailand

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Bangkok, , Thailand

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Bangkok, , Thailand

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Bangkok, , Thailand

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Chiang Mai, , Thailand

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Muang, , Thailand

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Countries

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China India Japan Jordan Lebanon Malaysia Philippines Singapore South Korea Taiwan Thailand

References

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Grand J, Miger K, Sajadieh A, Kober L, Torp-Pedersen C, Ertl G, Lopez-Sendon J, Pietro Maggioni A, Teerlink JR, Sato N, Gimpelewicz C, Metra M, Holbro T, Nielsen OW. Blood Pressure Drops During Hospitalization for Acute Heart Failure Treated With Serelaxin: A Patient-Level Analysis of 4 Randomized Controlled Trials. Circ Heart Fail. 2022 Apr;15(4):e009199. doi: 10.1161/CIRCHEARTFAILURE.121.009199. Epub 2022 Feb 21.

Reference Type DERIVED
PMID: 35184572 (View on PubMed)

Grand J, Miger K, Sajadieh A, Kober L, Torp-Pedersen C, Ertl G, Lopez-Sendon J, Pietro Maggioni A, Teerlink JR, Sato N, Gimpelewicz C, Metra M, Holbro T, Nielsen OW. Systolic Blood Pressure and Outcome in Patients Admitted With Acute Heart Failure: An Analysis of Individual Patient Data From 4 Randomized Clinical Trials. J Am Heart Assoc. 2021 Sep 21;10(18):e022288. doi: 10.1161/JAHA.121.022288. Epub 2021 Sep 13.

Reference Type DERIVED
PMID: 34514815 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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CRLX030A2302

Identifier Type: -

Identifier Source: org_study_id

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