Reversal of Type 1 Diabetes in Children by Stem Cell Educator Therapy

NCT ID: NCT01996228

Last Updated: 2019-02-05

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

UNKNOWN

Clinical Phase

PHASE1/PHASE2

Total Enrollment

20 participants

Study Classification

INTERVENTIONAL

Study Start Date

2013-11-30

Study Completion Date

2019-10-31

Brief Summary

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Type 1 diabetes (T1D) is an autoimmune disease that usually occurs in children and reduces their pancreatic islet beta cells and thereby limits insulin production. Millions of individuals worldwide have T1D, and the number of children with diagnosed or undiagnosed T1D is increasing annually. Insulin supplementation is not a cure. It does not halt the persistent autoimmune response, nor can it reliably prevent devastating complications such as neuronal and cardiovascular diseases, blindness, and kidney failure. A true cure has proven elusive despite intensive research pressure over the past 25 years. Notably, Dr.Zhao and his team have successfully developed a groundbreaking technology Stem Cell Educator therapy (Zhao Y, et al.BMC Medicine 2011, 2012). To date, clinical trials in adult patients have demonstrated the safety and efficacy of Stem Cell Educator therapy for the treatment of T1D and other autoimmune-associated diseases. Here, the investigators will evaluate the safety and efficacy of Stem Cell Educator therapy in children with type 1 diabetes.

Detailed Description

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Conditions

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Type 1 Diabetes

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Cord Blood-derived multipotent stem cells

Human cord blood-derived multipotent stem cells (CB-SC) display unique phenotypes, such as the expression of embryonic stem (ES) cell markers, multipotential of differentiations, very low immunogenecity, and immune modulations in patients.

Group Type EXPERIMENTAL

Stem Cell Educator

Intervention Type DEVICE

Interventions

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Stem Cell Educator

Intervention Type DEVICE

Other Intervention Names

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Procedure: Apharesis and Stem Cell Educator Therapy Biological: Cord blood

Eligibility Criteria

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Inclusion Criteria

* 1\. T1D patients are screened for enrollment in the study if both clinical signs and laboratory tests meet the diagnosis standards of American Diabetes Association.

2\. Children from 3 through 18 years old and body weight \> 15 kg.

3\. Presence of at least one autoantibody to the pancreatic islet β cells (IA-2, GAD, ICA, ZnT8, or IAA).

4\. Written informed consent from the child and child's parents or legal representative.

Exclusion Criteria

* 1\. Any clinically significant diseases in liver, kidney, and heart.


3\. Significantly abnormal hematology results at screening.

4\. Presence of any infection diseases or inflammation conditions, including active skin infections, flu, fever, upper or lower respiratory track infections.
Minimum Eligible Age

6 Years

Maximum Eligible Age

14 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Second Xiangya Hospital of Central South University

OTHER

Sponsor Role collaborator

Throne Biotechnologies Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Yong Zhao, MD, PhD

Associate Scientist

Responsibility Role PRINCIPAL_INVESTIGATOR

Principal Investigators

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Yong Zhao, MD,PhD

Role: STUDY_CHAIR

Tianhe Stem Cell Biotechnologies

Zhiguang Zhou, Md,PhD

Role: PRINCIPAL_INVESTIGATOR

Second Xiangya Hospital of Central South University

Locations

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The Second Xiangya Hospital

Changsha, Hunan, China

Site Status RECRUITING

Countries

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China

Central Contacts

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Yong Zhao, MD, PhD

Role: CONTACT

001 630 723 1968

Facility Contacts

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Xia Li, MD, PhD

Role: primary

References

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Zhao Y, Jiang Z, Zhao T, Ye M, Hu C, Yin Z, Li H, Zhang Y, Diao Y, Li Y, Chen Y, Sun X, Fisk MB, Skidgel R, Holterman M, Prabhakar B, Mazzone T. Reversal of type 1 diabetes via islet beta cell regeneration following immune modulation by cord blood-derived multipotent stem cells. BMC Med. 2012 Jan 10;10:3. doi: 10.1186/1741-7015-10-3.

Reference Type BACKGROUND
PMID: 22233865 (View on PubMed)

Zhao Y, Jiang Z, Zhao T, Ye M, Hu C, Zhou H, Yin Z, Chen Y, Zhang Y, Wang S, Shen J, Thaker H, Jain S, Li Y, Diao Y, Chen Y, Sun X, Fisk MB, Li H. Targeting insulin resistance in type 2 diabetes via immune modulation of cord blood-derived multipotent stem cells (CB-SCs) in stem cell educator therapy: phase I/II clinical trial. BMC Med. 2013 Jul 9;11:160. doi: 10.1186/1741-7015-11-160.

Reference Type BACKGROUND
PMID: 23837842 (View on PubMed)

Zhao Y. Stem cell educator therapy and induction of immune balance. Curr Diab Rep. 2012 Oct;12(5):517-23. doi: 10.1007/s11892-012-0308-1.

Reference Type BACKGROUND
PMID: 22833322 (View on PubMed)

Zhao Y, Mazzone T. Human cord blood stem cells and the journey to a cure for type 1 diabetes. Autoimmun Rev. 2010 Dec;10(2):103-7. doi: 10.1016/j.autrev.2010.08.011. Epub 2010 Aug 20.

Reference Type BACKGROUND
PMID: 20728583 (View on PubMed)

Related Links

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http://www.tianhecell.com

Tianhe Stem Cell Biotechnologies

Other Identifiers

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2013-0002

Identifier Type: -

Identifier Source: org_study_id

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