Trial Outcomes & Findings for Genistein in Treatment of Metastatic Colorectal Cancer (NCT NCT01985763)

NCT ID: NCT01985763

Last Updated: 2019-05-10

Results Overview

Number of adverse events to assess tolerability of genistein treatment. Evaluation of side effects conducted every 14 days before each chemotherapy/genistein cycle.

Recruitment status

COMPLETED

Study phase

PHASE1/PHASE2

Target enrollment

13 participants

Primary outcome timeframe

up to 6 months

Results posted on

2019-05-10

Participant Flow

Participant milestones

Participant milestones
Measure
Genistein
Genistein combined with FOLFOX or FOLFOX-Avastin Genistein 60mg/day orally for 7 days every 2 weeks. Genistein administered beginning 4 days prior to FOLFOX or FOLFOX-Avastin and continuing the 3 days of chemotherapy.
Overall Study
STARTED
13
Overall Study
COMPLETED
13
Overall Study
NOT COMPLETED
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Genistein in Treatment of Metastatic Colorectal Cancer

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Genistein
n=13 Participants
Genistein combined with FOLFOX or FOLFOX-Avastin Genistein 60mg/day orally for 7 days every 2 weeks. Genistein administered beginning 4 days prior to FOLFOX or FOLFOX-Avastin and continuing the 3 days of chemotherapy.
Age, Continuous
61 years
n=5 Participants
Sex: Female, Male
Female
4 Participants
n=5 Participants
Sex: Female, Male
Male
9 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
Race (NIH/OMB)
Asian
2 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
1 Participants
n=5 Participants
Race (NIH/OMB)
White
3 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
7 Participants
n=5 Participants
ECOG
0
8 Participants
n=5 Participants
ECOG
1
5 Participants
n=5 Participants
Tumor Location
Right Colon
3 Participants
n=5 Participants
Tumor Location
Left Colon
10 Participants
n=5 Participants
KRAS/NRAS
Wild Type (WT)
5 Participants
n=5 Participants
KRAS/NRAS
Mutated
6 Participants
n=5 Participants
KRAS/NRAS
Unknown
2 Participants
n=5 Participants
BRAF V600F
WT
11 Participants
n=5 Participants
BRAF V600F
Mutated
0 Participants
n=5 Participants
BRAF V600F
Unknown
2 Participants
n=5 Participants
Number of Metastatic Sites
1
8 Participants
n=5 Participants
Number of Metastatic Sites
2
5 Participants
n=5 Participants

PRIMARY outcome

Timeframe: up to 6 months

Number of adverse events to assess tolerability of genistein treatment. Evaluation of side effects conducted every 14 days before each chemotherapy/genistein cycle.

Outcome measures

Outcome measures
Measure
Genistein
n=13 Participants
Genistein combined with FOLFOX or FOLFOX-Avastin Genistein 60mg/day orally for 7 days every 2 weeks. Genistein administered beginning 4 days prior to FOLFOX or FOLFOX-Avastin and continuing the 3 days of chemotherapy.
Number of Adverse Events
Grade 1
250 events
Number of Adverse Events
Grade 2
119 events
Number of Adverse Events
Grade 3
24 events
Number of Adverse Events
Grade 4
0 events

PRIMARY outcome

Timeframe: end of Cycle 6

Percent change in tumor size after cycle 6. Each cycle is 21 days.

Outcome measures

Outcome measures
Measure
Genistein
n=13 Participants
Genistein combined with FOLFOX or FOLFOX-Avastin Genistein 60mg/day orally for 7 days every 2 weeks. Genistein administered beginning 4 days prior to FOLFOX or FOLFOX-Avastin and continuing the 3 days of chemotherapy.
Percent Change in Tumor Size
-43.0 Percent change
Interval -49.8 to -1.3

SECONDARY outcome

Timeframe: end of Cycle 6

Response Rate (RR) as measured by radiologic RECIST criteria. Complete Response (CR): Disappearance of all target lesions. Any pathological lymph nodes (whether target or non-target) must have reduction in short axis to \<10 mm. Partial Response (PR): At least a 30% decrease in the sum of diameters of target lesions, taking as reference the baseline sum diameters. Progressive Disease (PD): At least a 20% increase in the sum of diameters of target lesions, taking as reference the smallest sum on study (this includes the baseline sum if that is the smallest on study). In addition to the relative increase of 20%, the sum must also demonstrate an absolute increase of at least 5 mm. (Note: the appearance of one or more new lesions is also considered progression). Stable Disease (SD): Neither sufficient shrinkage to qualify for PR nor sufficient increase to qualify for PD, taking as reference the smallest sum diameters while on study.

Outcome measures

Outcome measures
Measure
Genistein
n=13 Participants
Genistein combined with FOLFOX or FOLFOX-Avastin Genistein 60mg/day orally for 7 days every 2 weeks. Genistein administered beginning 4 days prior to FOLFOX or FOLFOX-Avastin and continuing the 3 days of chemotherapy.
Response Rate RECIST Criteria
PR
8 Participants
Response Rate RECIST Criteria
SD
1 Participants
Response Rate RECIST Criteria
PD
2 Participants
Response Rate RECIST Criteria
Not evaluable
2 Participants

SECONDARY outcome

Timeframe: up to 50 months

Number of participants with an ORR - the portion of patients with a tumor size reduction of a predefined amount for a minimum time period

Outcome measures

Outcome measures
Measure
Genistein
n=13 Participants
Genistein combined with FOLFOX or FOLFOX-Avastin Genistein 60mg/day orally for 7 days every 2 weeks. Genistein administered beginning 4 days prior to FOLFOX or FOLFOX-Avastin and continuing the 3 days of chemotherapy.
Number of Participants With an Overall Response Rate (ORR)
6 Participants

SECONDARY outcome

Timeframe: up to 50 months

Best Overall Response Rate (ORR) as measured by radiologic RECIST criteria. The best overall response is the best response recorded from the start of the treatment until disease progression/recurrence (taking as reference for PD the smallest measurements recorded since the treatment started). In general, the patient's best response assignment will depend on the achievement of both measurement and confirmation criteria. SD - target lesion SD, non target lesions Non-PD, and no new lesions. PR - target lesion CR, non target lesions Incomplete response/SD and no new lesions; or target lesion PR, non target lesions Non-PD, and no new lesions. PD - target lesions PD, non target lesions Any, can have new lesions; or target lesions Any, non target lesions PD, can have new lesions; or target lesions Any, non target lesions Any, have new lesions.

Outcome measures

Outcome measures
Measure
Genistein
n=13 Participants
Genistein combined with FOLFOX or FOLFOX-Avastin Genistein 60mg/day orally for 7 days every 2 weeks. Genistein administered beginning 4 days prior to FOLFOX or FOLFOX-Avastin and continuing the 3 days of chemotherapy.
Best Overall Response Rate RECIST Criteria
PR
6 Participants
Best Overall Response Rate RECIST Criteria
SD
3 Participants
Best Overall Response Rate RECIST Criteria
PD
2 Participants
Best Overall Response Rate RECIST Criteria
Not evaluable
2 Participants

SECONDARY outcome

Timeframe: up to 50 months

The number of participants with best overall response is the best response recorded from the start of the treatment until disease progression/recurrence (taking as reference for PD the smallest measurements recorded since the treatment started). In general, the patient's best response assignment will depend on the achievement of both measurement and confirmation criteria.

Outcome measures

Outcome measures
Measure
Genistein
n=13 Participants
Genistein combined with FOLFOX or FOLFOX-Avastin Genistein 60mg/day orally for 7 days every 2 weeks. Genistein administered beginning 4 days prior to FOLFOX or FOLFOX-Avastin and continuing the 3 days of chemotherapy.
Number of Participants With Best Overall Response Rate (ORR)
8 Participants

SECONDARY outcome

Timeframe: up to 50 months

Patients monitored for progression. Progression-free survival (PFS) is the length of time during and after the treatment that a patient lives with the disease but it does not get worse.

Outcome measures

Outcome measures
Measure
Genistein
n=13 Participants
Genistein combined with FOLFOX or FOLFOX-Avastin Genistein 60mg/day orally for 7 days every 2 weeks. Genistein administered beginning 4 days prior to FOLFOX or FOLFOX-Avastin and continuing the 3 days of chemotherapy.
Progression Free Survival (PFS)
11.5 months
Interval 4.9 to 21.7

SECONDARY outcome

Timeframe: 6 month and 12 month

Patients monitored for progression during the study period and 1 year following. Progression-free survival (PFS) is the length of time during and after the treatment that a patient lives with the disease but it does not get worse.

Outcome measures

Outcome measures
Measure
Genistein
n=13 Participants
Genistein combined with FOLFOX or FOLFOX-Avastin Genistein 60mg/day orally for 7 days every 2 weeks. Genistein administered beginning 4 days prior to FOLFOX or FOLFOX-Avastin and continuing the 3 days of chemotherapy.
Percent of Patients With Progression Free Survival (PFS) at 6 Months and 12 Months
6 months
69 percentage of participants
Interval 48.0 to 99.0
Percent of Patients With Progression Free Survival (PFS) at 6 Months and 12 Months
12 months
38 percentage of participants
Interval 19.0 to 76.0

SECONDARY outcome

Timeframe: up to 50 months

Overall Survival - Number of months still living since baseline

Outcome measures

Outcome measures
Measure
Genistein
n=13 Participants
Genistein combined with FOLFOX or FOLFOX-Avastin Genistein 60mg/day orally for 7 days every 2 weeks. Genistein administered beginning 4 days prior to FOLFOX or FOLFOX-Avastin and continuing the 3 days of chemotherapy.
Overall Survival (OS)
36.5 months
Interval 29.5 to 50.0

Adverse Events

Genistein

Serious events: 0 serious events
Other events: 13 other events
Deaths: 0 deaths

Genistein and Chemotherapy

Serious events: 0 serious events
Other events: 13 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
Genistein
n=13 participants at risk
Genistein 60mg/day orally for 4 days before chemotherapy.
Genistein and Chemotherapy
n=13 participants at risk
Genistein combined with FOLFOX or FOLFOX-Avastin Genistein 60mg/day orally for 7 days every 2 weeks. Genistein administered beginning 4 days prior to chemotherapy.
General disorders
Fatigue
15.4%
2/13 • Number of events 6 • 6 months
AEs collected for when subjects on Genistein alone and when subjects on Genistein and Chemotherapy
84.6%
11/13 • Number of events 55 • 6 months
AEs collected for when subjects on Genistein alone and when subjects on Genistein and Chemotherapy
General disorders
Hot Flashes
15.4%
2/13 • Number of events 8 • 6 months
AEs collected for when subjects on Genistein alone and when subjects on Genistein and Chemotherapy
7.7%
1/13 • Number of events 1 • 6 months
AEs collected for when subjects on Genistein alone and when subjects on Genistein and Chemotherapy
General disorders
Mucositis
0.00%
0/13 • 6 months
AEs collected for when subjects on Genistein alone and when subjects on Genistein and Chemotherapy
38.5%
5/13 • Number of events 11 • 6 months
AEs collected for when subjects on Genistein alone and when subjects on Genistein and Chemotherapy
Cardiac disorders
Hypertension
7.7%
1/13 • Number of events 2 • 6 months
AEs collected for when subjects on Genistein alone and when subjects on Genistein and Chemotherapy
92.3%
12/13 • Number of events 88 • 6 months
AEs collected for when subjects on Genistein alone and when subjects on Genistein and Chemotherapy
Skin and subcutaneous tissue disorders
Rash
15.4%
2/13 • Number of events 4 • 6 months
AEs collected for when subjects on Genistein alone and when subjects on Genistein and Chemotherapy
0.00%
0/13 • 6 months
AEs collected for when subjects on Genistein alone and when subjects on Genistein and Chemotherapy
Gastrointestinal disorders
Diarrhea
0.00%
0/13 • 6 months
AEs collected for when subjects on Genistein alone and when subjects on Genistein and Chemotherapy
46.2%
6/13 • Number of events 23 • 6 months
AEs collected for when subjects on Genistein alone and when subjects on Genistein and Chemotherapy
Gastrointestinal disorders
Nausea
15.4%
2/13 • Number of events 10 • 6 months
AEs collected for when subjects on Genistein alone and when subjects on Genistein and Chemotherapy
61.5%
8/13 • Number of events 27 • 6 months
AEs collected for when subjects on Genistein alone and when subjects on Genistein and Chemotherapy
Gastrointestinal disorders
Vomiting
0.00%
0/13 • 6 months
AEs collected for when subjects on Genistein alone and when subjects on Genistein and Chemotherapy
15.4%
2/13 • Number of events 9 • 6 months
AEs collected for when subjects on Genistein alone and when subjects on Genistein and Chemotherapy
Blood and lymphatic system disorders
Bleeding
7.7%
1/13 • Number of events 1 • 6 months
AEs collected for when subjects on Genistein alone and when subjects on Genistein and Chemotherapy
46.2%
6/13 • Number of events 12 • 6 months
AEs collected for when subjects on Genistein alone and when subjects on Genistein and Chemotherapy
Blood and lymphatic system disorders
Neutropenia
0.00%
0/13 • 6 months
AEs collected for when subjects on Genistein alone and when subjects on Genistein and Chemotherapy
7.7%
1/13 • Number of events 1 • 6 months
AEs collected for when subjects on Genistein alone and when subjects on Genistein and Chemotherapy
Blood and lymphatic system disorders
Thromboembolism
0.00%
0/13 • 6 months
AEs collected for when subjects on Genistein alone and when subjects on Genistein and Chemotherapy
7.7%
1/13 • Number of events 1 • 6 months
AEs collected for when subjects on Genistein alone and when subjects on Genistein and Chemotherapy
Nervous system disorders
Cold Sensitivity
0.00%
0/13 • 6 months
AEs collected for when subjects on Genistein alone and when subjects on Genistein and Chemotherapy
92.3%
12/13 • Number of events 55 • 6 months
AEs collected for when subjects on Genistein alone and when subjects on Genistein and Chemotherapy
Nervous system disorders
Headache
30.8%
4/13 • Number of events 11 • 6 months
AEs collected for when subjects on Genistein alone and when subjects on Genistein and Chemotherapy
7.7%
1/13 • Number of events 1 • 6 months
AEs collected for when subjects on Genistein alone and when subjects on Genistein and Chemotherapy
Nervous system disorders
Neuropathy
15.4%
2/13 • Number of events 2 • 6 months
AEs collected for when subjects on Genistein alone and when subjects on Genistein and Chemotherapy
53.8%
7/13 • Number of events 34 • 6 months
AEs collected for when subjects on Genistein alone and when subjects on Genistein and Chemotherapy
Gastrointestinal disorders
Intestinal Obstruction
0.00%
0/13 • 6 months
AEs collected for when subjects on Genistein alone and when subjects on Genistein and Chemotherapy
7.7%
1/13 • Number of events 2 • 6 months
AEs collected for when subjects on Genistein alone and when subjects on Genistein and Chemotherapy
Gastrointestinal disorders
Abdominal Pain
0.00%
0/13 • 6 months
AEs collected for when subjects on Genistein alone and when subjects on Genistein and Chemotherapy
7.7%
1/13 • 6 months
AEs collected for when subjects on Genistein alone and when subjects on Genistein and Chemotherapy
Renal and urinary disorders
Acute Kidney Injury
0.00%
0/13 • 6 months
AEs collected for when subjects on Genistein alone and when subjects on Genistein and Chemotherapy
61.5%
8/13 • 6 months
AEs collected for when subjects on Genistein alone and when subjects on Genistein and Chemotherapy
Gastrointestinal disorders
Anorexia
0.00%
0/13 • 6 months
AEs collected for when subjects on Genistein alone and when subjects on Genistein and Chemotherapy
61.5%
8/13 • 6 months
AEs collected for when subjects on Genistein alone and when subjects on Genistein and Chemotherapy
Musculoskeletal and connective tissue disorders
Back Pain
7.7%
1/13 • 6 months
AEs collected for when subjects on Genistein alone and when subjects on Genistein and Chemotherapy
61.5%
8/13 • 6 months
AEs collected for when subjects on Genistein alone and when subjects on Genistein and Chemotherapy
Gastrointestinal disorders
Constipation
7.7%
1/13 • 6 months
AEs collected for when subjects on Genistein alone and when subjects on Genistein and Chemotherapy
15.4%
2/13 • 6 months
AEs collected for when subjects on Genistein alone and when subjects on Genistein and Chemotherapy
Infections and infestations
Fever
0.00%
0/13 • 6 months
AEs collected for when subjects on Genistein alone and when subjects on Genistein and Chemotherapy
7.7%
1/13 • 6 months
AEs collected for when subjects on Genistein alone and when subjects on Genistein and Chemotherapy
Gastrointestinal disorders
GERD
0.00%
0/13 • 6 months
AEs collected for when subjects on Genistein alone and when subjects on Genistein and Chemotherapy
61.5%
8/13 • 6 months
AEs collected for when subjects on Genistein alone and when subjects on Genistein and Chemotherapy

Additional Information

Dr. Sofya Pintova

Icahn School of Medicine at Mount Sinai

Phone: 212-824-8461

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place