Phase 1b Trial of BGJ398/BYL719 in Solid Tumors

NCT ID: NCT01928459

Last Updated: 2020-12-09

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE1

Total Enrollment

62 participants

Study Classification

INTERVENTIONAL

Study Start Date

2013-10-31

Study Completion Date

2016-08-31

Brief Summary

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To study the safety and efficacy of the combination of BGJ398 with BYL719 in patients whose tumors express mutations to PIK3CA with or without alterations to FGFR 1-3.

Detailed Description

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This dose escalation/dose expansion study will evaluate the combination of orally administered BGJ398 in combination with orally administered BYL719. During the dose escalation part, the MTD of the combination will be determined in patients whose advanced or metastatic tumors express mutations to PIK3CA. Once the MTD has been determined, the expansion part will begin. Patients will be addd to one of three arms based on the disease type and genetic changes. Patients with metastatic colorectal cancer are not eligible for participation in the expansion part.

Conditions

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Advanced Solid Tumors Metastatic Solid Tumors

Keywords

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BGJ398 BYL719 advanced solid tumor metastatic breast cancer PK3CA FGFR fibroblast growth factor receptor

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Metastatic breast cancer

Evaluation of safety and efficacy in patients with metastatic breast cancer whose tumors contain mutations to PIK3CA and alterations FGFR 1-3.

Group Type EXPERIMENTAL

BGJ398

Intervention Type DRUG

BGJ398 will be administered orally once daily for the first 21 days of each 28-day cycle.

BYL719

Intervention Type DRUG

BYL719 will be administered orally once daily on each day of the 28-day cycle.

Solid tumor arm 1

Patients with solid tumors (except for colorectal cancer) whose tumors express mutations to PIK3CA.

Group Type EXPERIMENTAL

BGJ398

Intervention Type DRUG

BGJ398 will be administered orally once daily for the first 21 days of each 28-day cycle.

BYL719

Intervention Type DRUG

BYL719 will be administered orally once daily on each day of the 28-day cycle.

Solid tumor arm 2

Patients with solid tumors (except for colorectal cancer) whose tumomrs express mutations to PIK3CA and alterations to FGFR 1-3

Group Type EXPERIMENTAL

BGJ398

Intervention Type DRUG

BGJ398 will be administered orally once daily for the first 21 days of each 28-day cycle.

BYL719

Intervention Type DRUG

BYL719 will be administered orally once daily on each day of the 28-day cycle.

Dose escalation

To determine the MTD or RDE of the combination of BGJ398 with BYL719 in patients with advanced or metastastic solid tumors that express mutations to PIK3CA.

Group Type EXPERIMENTAL

BGJ398

Intervention Type DRUG

BGJ398 will be administered orally once daily for the first 21 days of each 28-day cycle.

BYL719

Intervention Type DRUG

BYL719 will be administered orally once daily on each day of the 28-day cycle.

Interventions

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BGJ398

BGJ398 will be administered orally once daily for the first 21 days of each 28-day cycle.

Intervention Type DRUG

BYL719

BYL719 will be administered orally once daily on each day of the 28-day cycle.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Histologically/cytologically confirmed advanced or metastatic solid tumors who have failed standard therapy or for whom no effective standard anti-cancer therapy exists
* Documented PIK3CA mutations in all patients in dose escalation and expansion with or without documented genetic alterations in FGFR depending upon dose expansion cohort (either local or central determination)
* Measurable disease defined by RECIST v1.1
* ECOG performance status of ≤2

Exclusion Criteria

* Prior PI3Ki or selective FGFR inhibitor treatment (for patients enrolled to expansion part)
* Colorectal cancer (for patients enrolled to expansion part)
* Patients with diabetes mellitus requiring insulin treatment and/or with clinical signs or with fasting glucose ≥ 140 mg/dL / 7.8 mmol/L, history of clinically significant gestational diabetes mellitus or documented steroid-induced diabetes mellitus
* Use of medications that increase serum levels of phosphorus and/or calcium
* Inorganic phosphorus outside of normal limits
* Total and ionized serum calcium outside of normal limits
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Novartis Pharmaceuticals

Role: STUDY_DIRECTOR

Novartis Pharmaceuticals

Locations

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H. Lee Moffitt Cancer Center & Research Institute Moffitt 4

Tampa, Florida, United States

Site Status

University of Michigan Comprehensive Cancer Center SC

Ann Arbor, Michigan, United States

Site Status

Karmanos Cancer Institute Dept of Onc

Detroit, Michigan, United States

Site Status

Washington University School of Medicine Onc Dept

St Louis, Missouri, United States

Site Status

Memorial Sloan Kettering Cancer Center Onc Dept

New York, New York, United States

Site Status

Vanderbilt University Medical Center Dept of Onc

Nashville, Tennessee, United States

Site Status

Cancer Therapy & Research Center / UT Health Science Center SC

San Antonio, Texas, United States

Site Status

Novartis Investigative Site

Parkville, Victoria, Australia

Site Status

Novartis Investigative Site

Brussels, , Belgium

Site Status

Novartis Investigative Site

Toronto, Ontario, Canada

Site Status

Novartis Investigative Site

Lyon, , France

Site Status

Novartis Investigative Site

Saint-Herblain, , France

Site Status

Novartis Investigative Site

Cologne, North Rhine-Westphalia, Germany

Site Status

Novartis Investigative Site

Milan, MI, Italy

Site Status

Novartis Investigative Site

Modena, MO, Italy

Site Status

Novartis Investigative Site

Amsterdam, , Netherlands

Site Status

Novartis Investigative Site

Singapore, , Singapore

Site Status

Novartis Investigative Site

Seoul, Korea, South Korea

Site Status

Novartis Investigative Site

Seville, Andalusia, Spain

Site Status

Novartis Investigative Site

Barcelona, Catalonia, Spain

Site Status

Novartis Investigative Site

Madrid, , Spain

Site Status

Novartis Investigative Site

Bellinzona, , Switzerland

Site Status

Countries

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United Kingdom United States Australia Belgium Canada France Germany Italy Netherlands Singapore South Korea Spain Switzerland

Related Links

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https://www.novctrd.com/ctrdweb/trialresult/trialresults/pdf?trialResultId=16593

Results for CBGJ398X2102 from the Novartis Clinical Trials website

Other Identifiers

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CBGJ398X2102

Identifier Type: -

Identifier Source: org_study_id