A Phase 1a/1b Study of PPI-383 in Healthy Adults and Hepatitis C Patients

NCT ID: NCT01928147

Last Updated: 2015-11-26

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE1

Total Enrollment

114 participants

Study Classification

INTERVENTIONAL

Study Start Date

2013-08-31

Study Completion Date

2015-11-30

Brief Summary

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PPI-383 is an antiviral agent (an inhibitor of the hepatitis C virus NS5B polymerase) that is being developed as a potential treatment for hepatitis C virus infection. This study is being done to assess the dose-related safety and tolerance of PPI-383 when given to healthy volunteers for up to 5 days (Part I of the study) and to hepatitis C patients for up to 3 days (Part II). In addition, the study will assess how much PPI-383 is absorbed into the bloodstream. In Part II, the dose-related effect of PPI-383 on the amount of hepatitis C virus in patients' bloodstream (serum HCV RNA levels) also will be assessed.

Detailed Description

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Conditions

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Hepatitis C, Chronic

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators

Study Groups

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PPI-383 single dose escalation in healthy volunteers

There will be up to 10 sequential single dose cohorts to assess the bioavailability of different doses and formulations; a food effect cohort will be included.

Group Type EXPERIMENTAL

PPI-383

Intervention Type DRUG

Placebo

Intervention Type DRUG

PPI-383 multiple doses in healthy volunteers

Upon completion of the single dose cohorts, an additional cohort will receive the highest well-tolerated dose from the single dose cohorts or placebo once daily for five days; up to additional cohorts may receive multiple doses of different formulations or different regimens

Group Type EXPERIMENTAL

PPI-383

Intervention Type DRUG

Placebo

Intervention Type DRUG

PPI-383 multiple dose escalation in HCV Subjects

Upon completion of the single and multiple dose healthy volunteer cohorts, there will be 3, and potentially 4, sequential cohorts of HCV patients

Group Type EXPERIMENTAL

PPI-383

Intervention Type DRUG

Placebo

Intervention Type DRUG

Interventions

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PPI-383

Intervention Type DRUG

Placebo

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Healthy males
* Age 18 to 55 years
* Body mass index (BMI)18 to 32 kg/m2


* Males, or females of non-childbearing potential
* Age 18 to 65 years
* Chronic hepatitis C, and absence of other known liver disease
* Seropositive for HCV antibody (HCV Ab) or HCV RNA at least once previously
* Seropositive for HCV Ab at screening
* Serum HCV RNA \> 5 log10 IU/mL at screening
* HCV gt-1
* Treatment-naïve for hepatitis C:
* BMI 18 to 35 kg/m2
* Otherwise in good health, without severe or clinically significant chronic or recurrent conditions requiring frequent medical intervention or continual pharmacologic management, except for anti-hypertensive use
* No medical or psychosocial conditions that would potentially interfere with the subject's ability to comply with the study assessments or visit schedule.

Exclusion Criteria

* Seropositive for human immunodeficiency virus (HIV) antibody or hepatitis B virus (HBV) surface antigen (HBsAg)
* Signs or symptoms of decompensated liver disease
* Evidence of cirrhosis or hepatocellular carcinoma
* Diabetes Mellitus treated with insulin or hypoglycemic agents
* Asthma requiring hospital admission within the preceding 12 months
* History of alcohol abuse or illicit drug use which could interfere with a patient's compliance with the protocol requirements
* Any of the following laboratory values at screening

* Haemoglobin (Hgb) \<11 g/dL in women or 12 g/dL in men
* White blood cell count \<4,000/mm3
* Absolute neutrophil count (ANC) \< 1800 per mm3
* Platelet count \<100,000 per mm3
* Serum creatinine \> upper limit of normal (ULN) at the central study laboratory
* Serum albumin \<3.4 g/dL
* Total bilirubin \>2.0 mg/dL
* Clinically significant abnormality in the electrocardiograms (ECGs) at screening
Minimum Eligible Age

18 Years

Maximum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

Yes

Sponsors

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Presidio Pharmaceuticals, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Nathaniel Brown, M.D.

Role: STUDY_DIRECTOR

Presidio Pharmaceuticals

Locations

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Investigational site

Phoenix, , Mauritius

Site Status

Investigational site

London, , United Kingdom

Site Status

Investigational site

London, , United Kingdom

Site Status

Investigational site

London, , United Kingdom

Site Status

Investigational site

London, , United Kingdom

Site Status

Investigational site

Nottingham, , United Kingdom

Site Status

Countries

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Mauritius United Kingdom

Other Identifiers

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PPI-383-101

Identifier Type: -

Identifier Source: org_study_id