Trial Outcomes & Findings for Neurobiological Basis of Response to Vyvanse in Adults With ADHD: an fMRI Study of Brain Activation (NCT NCT01924429)

NCT ID: NCT01924429

Last Updated: 2018-06-06

Results Overview

Performance Measures on the Go/No-Go Task assessed by fMRI as a Function of Trial Type, Face Emotion, and Drug Condition in Adults with Attention-Deficit/Hyperactivity Disorder. The Go/No-Go Task is a neuropsychological test that provides a direct measure of number of responses made that are "correct" or "incorrect". It is not a scale. Reported are the percentage of correct responses on that direct performance measure. 0% correct is worse than 100% correct.

Recruitment status

COMPLETED

Study phase

PHASE4

Target enrollment

30 participants

Primary outcome timeframe

8 weeks

Results posted on

2018-06-06

Participant Flow

Participant milestones

Participant milestones
Measure
On Drug Then Off Drug
Participants receive fMRI #1 on drug, #2 off drug Escalating stepped titration: 30, 50 or 70mg Lisdexamphetamine: Escalating stepped dose titration: 30, 50 or 70mg
Off Drug Then on Drug
Participants receive fMRI #1 off drug, #2 on drug Escalating stepped dose titration: 30, 50, 70mg Lisdexamphetamine: Escalating stepped dose titration: 30, 50 or 70mg
Period 1 - First Intervention (4 Weeks)
STARTED
17
13
Period 1 - First Intervention (4 Weeks)
COMPLETED
17
13
Period 1 - First Intervention (4 Weeks)
NOT COMPLETED
0
0
Washout Period (2 Weeks)
STARTED
17
13
Washout Period (2 Weeks)
COMPLETED
14
11
Washout Period (2 Weeks)
NOT COMPLETED
3
2
Period 2 - Second Intervention (4 Weeks)
STARTED
14
11
Period 2 - Second Intervention (4 Weeks)
COMPLETED
14
11
Period 2 - Second Intervention (4 Weeks)
NOT COMPLETED
0
0

Reasons for withdrawal

Reasons for withdrawal
Measure
On Drug Then Off Drug
Participants receive fMRI #1 on drug, #2 off drug Escalating stepped titration: 30, 50 or 70mg Lisdexamphetamine: Escalating stepped dose titration: 30, 50 or 70mg
Off Drug Then on Drug
Participants receive fMRI #1 off drug, #2 on drug Escalating stepped dose titration: 30, 50, 70mg Lisdexamphetamine: Escalating stepped dose titration: 30, 50 or 70mg
Washout Period (2 Weeks)
Withdrawal by Subject
3
2

Baseline Characteristics

Neurobiological Basis of Response to Vyvanse in Adults With ADHD: an fMRI Study of Brain Activation

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
On Drug, Then Off Drug
n=17 Participants
fMRI #1 on drug, #2 off drug
Off Drug, Then on Drug
n=13 Participants
fMRI #1 off drug, #2 on drug
Total
n=30 Participants
Total of all reporting groups
Age, Continuous
35.46 years
STANDARD_DEVIATION 11.82 • n=5 Participants
37.27 years
STANDARD_DEVIATION 11.81 • n=7 Participants
35.84 years
STANDARD_DEVIATION 10.25 • n=5 Participants
Sex: Female, Male
Female
8 Participants
n=5 Participants
5 Participants
n=7 Participants
13 Participants
n=5 Participants
Sex: Female, Male
Male
9 Participants
n=5 Participants
8 Participants
n=7 Participants
17 Participants
n=5 Participants

PRIMARY outcome

Timeframe: 8 weeks

Population: Performance measures are done while participants are off drug and while on drug.

Performance Measures on the Go/No-Go Task assessed by fMRI as a Function of Trial Type, Face Emotion, and Drug Condition in Adults with Attention-Deficit/Hyperactivity Disorder. The Go/No-Go Task is a neuropsychological test that provides a direct measure of number of responses made that are "correct" or "incorrect". It is not a scale. Reported are the percentage of correct responses on that direct performance measure. 0% correct is worse than 100% correct.

Outcome measures

Outcome measures
Measure
Placebo
n=25 Participants
Participants received fMRI while off drug
Lisdexamfetamine
n=25 Participants
Participants received fMRI while on drug
The Go/No-Go Task Percentage Assessed by fMRI
Happy Correct Responses
91.7 percentage correct responses/inhibitions
Standard Error 2.8
97.0 percentage correct responses/inhibitions
Standard Error 3.8
The Go/No-Go Task Percentage Assessed by fMRI
Happy Correct Inhibitions
88.7 percentage correct responses/inhibitions
Standard Error 9.4
87.9 percentage correct responses/inhibitions
Standard Error 11.5
The Go/No-Go Task Percentage Assessed by fMRI
Sad Correct Responses
90.3 percentage correct responses/inhibitions
Standard Error 7.7
88.5 percentage correct responses/inhibitions
Standard Error 10.6
The Go/No-Go Task Percentage Assessed by fMRI
Sad Correct Inhibitions
84.4 percentage correct responses/inhibitions
Standard Error 12.5
86.7 percentage correct responses/inhibitions
Standard Error 11.3
The Go/No-Go Task Percentage Assessed by fMRI
Neutral Correct Responses
93.2 percentage correct responses/inhibitions
Standard Error 12.2
95.6 percentage correct responses/inhibitions
Standard Error 5.8
The Go/No-Go Task Percentage Assessed by fMRI
Neutral Correct Inhibitions
77.5 percentage correct responses/inhibitions
Standard Error 12.3
79.6 percentage correct responses/inhibitions
Standard Error 11.6

PRIMARY outcome

Timeframe: up to 6 weeks

Reaction-time, as measured by the reaction time test Go/No-Go Task as a Function of Trial Type, Face Emotion, and Drug Condition in Adults with Attention-Deficit/Hyperactivity Disorder

Outcome measures

Outcome measures
Measure
Placebo
n=25 Participants
Participants received fMRI while off drug
Lisdexamfetamine
n=25 Participants
Participants received fMRI while on drug
fMRI Reaction Time
Happy
532 ms
Standard Error 99
519 ms
Standard Error 114
fMRI Reaction Time
Sad
533 ms
Standard Error 110
509 ms
Standard Error 96
fMRI Reaction Time
Neutral
553 ms
Standard Error 109
533 ms
Standard Error 104

SECONDARY outcome

Timeframe: Baseline

Behavior Rating Inventory of Executive Function®-Adult Version (BRIEF-A): Norm Referenced Measure of Impaired Executive Functioning, reported in T-Scores (0 to 100, with 50 +/-1 SD = 'Normal', higher is worse, more impaired)

Outcome measures

Outcome measures
Measure
Placebo
n=14 Participants
Participants received fMRI while off drug
Lisdexamfetamine
n=11 Participants
Participants received fMRI while on drug
BRIEF-A
66.64 t-score
Standard Deviation 11.89
73.5 t-score
Standard Deviation 14.75

SECONDARY outcome

Timeframe: at one week

Population: not collected

Behavior Rating Inventory of Executive Function®-Adult Version (BRIEF-A): Norm Referenced Measure of Impaired Executive Functioning, reported in T-Scores (higher is worse)

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: at 4 weeks

Population: not collected

Behavior Rating Inventory of Executive Function®-Adult Version (BRIEF-A): Norm Referenced Measure of Impaired Executive Functioning, reported in T-Scores (higher is worse)

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Baseline

ADHD and Related Symptoms Measure (ASRS): self report, reported as Sum of Responses (0-4 per item, higher = more impaired) 0-26 (normal range) and \>27 (clinically significant symptoms).

Outcome measures

Outcome measures
Measure
Placebo
n=14 Participants
Participants received fMRI while off drug
Lisdexamfetamine
n=11 Participants
Participants received fMRI while on drug
ASRS - Expanded
83.7 units on a scale
Standard Deviation 25.59
86 units on a scale
Standard Deviation 4.24

SECONDARY outcome

Timeframe: at one week

Population: not collected

ADHD and Related Symptoms Measure (ASRS): self report, reported as Sum of Responses (0-4 per item, higher = more impaired) 0-26 (normal range) and \>27 (clinically significant symptoms).

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: at 4 weeks

Population: not collected

ADHD and Related Symptoms Measure (ASRS): self report, reported as Sum of Responses (0-4 per item, higher = more impaired) 0-26 (normal range) and \>27 (clinically significant symptoms).

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Baseline

The Wender-Reimherr adult attention deficit disorder scale (WRAADS): Symptom measure for emotional functioning/lability, generally reported as Sum of Responses (0-2 per item, higher = more impaired). For this outcome measure, Average scores for particular questions were taken - specifically question 3, question 4, and question 5.

Outcome measures

Outcome measures
Measure
Placebo
n=14 Participants
Participants received fMRI while off drug
Lisdexamfetamine
n=11 Participants
Participants received fMRI while on drug
WRAADS
Question 3
0.80 units on a scale
Standard Deviation 0.86
0.94 units on a scale
Standard Deviation 0.745
WRAADS
Question 4
1.27 units on a scale
Standard Deviation 1.22
1.47 units on a scale
Standard Deviation 1.23
WRAADS
Question 5
1.13 units on a scale
Standard Deviation 1.35
1.82 units on a scale
Standard Deviation 1.19

SECONDARY outcome

Timeframe: Baseline

ADHD symptoms and severity. Norm referenced interview to assess severity and frequency of ADHD symptoms. 18 Items are scored 0-3 to reflect severity and frequency of ADHD symptoms, and a sum is taken. Full range from 0 to 54, with higher number indicating more symptoms and severity.

Outcome measures

Outcome measures
Measure
Placebo
n=14 Participants
Participants received fMRI while off drug
Lisdexamfetamine
n=11 Participants
Participants received fMRI while on drug
ADHD-RS-IV Combined Sum
On Drug
11.00 units on a scale
Standard Deviation 6.98
13.67 units on a scale
Standard Deviation 11.64
ADHD-RS-IV Combined Sum
Placebo
25.65 units on a scale
Standard Deviation 8.53
31.00 units on a scale
Standard Deviation 14.80

SECONDARY outcome

Timeframe: 4 weeks and 8 weeks

ADHD symptoms and severity - subscale for Inattentiveness. 9-item scale, each scored 0-3, with total from 0 to 27. Higher score indicates higher level of inattentiveness.

Outcome measures

Outcome measures
Measure
Placebo
n=14 Participants
Participants received fMRI while off drug
Lisdexamfetamine
n=11 Participants
Participants received fMRI while on drug
ADHD-Inattentive
On drug
7.36 units on a scale
Standard Deviation 4.53
8.83 units on a scale
Standard Deviation 7.63
ADHD-Inattentive
Placebo
18.94 units on a scale
Standard Deviation 6.21
19.2 units on a scale
Standard Deviation 5.07

SECONDARY outcome

Timeframe: Baseline

Clinical Global Impressions - CGI-I: Clinical response was the Clinical Global Impression-Improvement scale (CGI-I). Lower CGI-I scores indicate greater improvement (1=very much improved; 2=much improved; 3=minimally improved; 4=no change; 5=minimally worse; 6=much worse; 7=very much worse).

Outcome measures

Outcome measures
Measure
Placebo
n=14 Participants
Participants received fMRI while off drug
Lisdexamfetamine
n=11 Participants
Participants received fMRI while on drug
CGI-I
1.88 units on a scale
Standard Deviation 1.13
2.00 units on a scale
Standard Deviation 1.41

SECONDARY outcome

Timeframe: baseline

CGI-S: Severity of impairment due to ADHD was measured by the Clinical Global Impressions-Severity scale (CGI-S). Lower scores indicate less severe impairment from symptoms, with a CGI-I=1 indicating the person is "normal" with no impairment. (1= normal, not ill, 2= minimally ill, 3= mildly ill, 4= moderately ill, 5=markedly ill, 6=severely ill, 7= very severely ill)

Outcome measures

Outcome measures
Measure
Placebo
n=14 Participants
Participants received fMRI while off drug
Lisdexamfetamine
n=11 Participants
Participants received fMRI while on drug
CGI-S
4.9 units on a scale
Standard Deviation 1.0
4.95 units on a scale
Standard Deviation 0.9

Adverse Events

On Drug, Then Off Drug

Serious events: 0 serious events
Other events: 14 other events
Deaths: 0 deaths

Off Drug, Then on Drug

Serious events: 0 serious events
Other events: 11 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
On Drug, Then Off Drug
n=14 participants at risk
Participants receive fMRI #1 on drug, #2 off drug Escalating stepped titration: 30, 50 or 70mg Lisdexamphetamine: Escalating stepped dose titration: 30, 50 or 70mg
Off Drug, Then on Drug
n=11 participants at risk
Participants receive fMRI #1 off drug, #2 on drug Escalating stepped dose titration: 30, 50, 70mg Lisdexamphetamine: Escalating stepped dose titration: 30, 50 or 70mg
General disorders
Incidental finding on brain scan
0.00%
0/14
9.1%
1/11
General disorders
Incidental Physical finding
21.4%
3/14
0.00%
0/11
General disorders
Insomnia
14.3%
2/14
9.1%
1/11
General disorders
Heart Racing
7.1%
1/14
0.00%
0/11
General disorders
Dry mouth
7.1%
1/14
18.2%
2/11
General disorders
feeling agitated
7.1%
1/14
0.00%
0/11
General disorders
Tired
7.1%
1/14
0.00%
0/11
General disorders
Anxious
7.1%
1/14
18.2%
2/11
General disorders
Headache
7.1%
1/14
18.2%
2/11
General disorders
Restless
7.1%
1/14
0.00%
0/11
General disorders
Seasonal allergies
0.00%
0/14
18.2%
2/11
General disorders
Subjectively feeling "stuck"
0.00%
0/14
9.1%
1/11
General disorders
Suspiciousness
7.1%
1/14
0.00%
0/11
Musculoskeletal and connective tissue disorders
Backache
7.1%
1/14
0.00%
0/11
General disorders
Reduced Appetite
7.1%
1/14
0.00%
0/11
Skin and subcutaneous tissue disorders
Skin Sores
7.1%
1/14
0.00%
0/11
General disorders
Bruxism
0.00%
0/14
9.1%
1/11

Additional Information

Dr. Jeffrey Newcorn

Icahn School of Medicine at Mount Sinai

Phone: 212-659-8775

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place